A Study of the Efficacy and Safety of Belimumab in Adults With Systemic Sclerosis Associated Interstitial Lung Disease

NCT ID: NCT05878717

Last Updated: 2026-01-12

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE2/PHASE3

Total Enrollment

300 participants

Study Classification

INTERVENTIONAL

Study Start Date

2023-09-13

Study Completion Date

2029-07-12

Brief Summary

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This study investigates the efficacy and safety of belimumab compared to placebo, in addition to standard therapy, for the treatment of participants with systemic sclerosis associated interstitial lung disease (SSc-ILD). The study will evaluate the effect of belimumab treatment on lung function as well as on extra-pulmonary disease manifestations, including skin thickening and general symptoms, such as fatigue, that impact quality of life (QoL).

Detailed Description

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Conditions

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Systemic Sclerosis Associated Interstitial Lung Disease Scleroderma, Systemic

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors
This is a double-blind study where participant and investigator are masked.

Study Groups

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Belimumab

Participants will receive belimumab in addition to standard therapy.

Group Type EXPERIMENTAL

Belimumab

Intervention Type BIOLOGICAL

Belimumab will be administered.

Placebo

Participants will receive placebo in addition to standard therapy.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type OTHER

.Placebo will be administered.

Interventions

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Belimumab

Belimumab will be administered.

Intervention Type BIOLOGICAL

Placebo

.Placebo will be administered.

Intervention Type OTHER

Other Intervention Names

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BENLYSTA™, GSK1550188, LymphoStat-B™ BENLYSTATM, GSK1550188, LymphoStat-B™

Eligibility Criteria

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Inclusion Criteria

1. Participant is 18 years of age inclusive, or older at the time of signing the informed consent.
2. Documented diagnosis of SSc as defined by the American College of Rheumatology / European League Against Rheumatism 2013 SSc classification criteria.
3. Diffuse cutaneous disease, defined as presence of thickened skin with mRSS \>0 over at least one skin area proximal to elbows and/or knees in addition to distal areas involvement on Day 1.
4. Total mRSS ≥15 on Day 1.
5. Evidence of interstitial lung disease on centrally read screening HRCT.
6. Anticentromere antibody negative on central test at screening.
7. Evidence for active or progressive disease
8. Participant has an area of uninvolved or mildly thickened skin that, in the opinion of the investigator, would allow SC injection at the abdomen or the front, middle region of the thigh.
9. Participant is capable and willing to self-administer the study medication or has a caregiver who is capable and willing to administer the study medication throughout the study.
10. A female participant is eligible to participate if she is not pregnant or breastfeeding, and one of the following conditions applies:

Is a Woman of Non-Childbearing Potential (WONCBP) OR Is a Woman of Childbearing Potential (WOCBP) and using a contraceptive method that is highly effective.
11. Capable of giving signed informed consent.

Exclusion Criteria

1. Systemic sclerosis-like illness, including but not limited to localized scleroderma (morphoea), eosinophilic fasciitis, sclerodermoid graft-versus-host disease, fibro mucinous conditions (scleroedema, scleromyxoedema), scleroderma-like conditions that are associated with environmental chemical and drug exposure (e.g., toxic rapeseed oil, vinyl chloride, bleomycin, gadolinium-based contrast agents \[nephrogenic systemic fibrosis\], or due to metabolic disease).
2. Primary diagnosis of a rheumatic autoimmune disease other than dcSSc, including but not limited to rheumatoid arthritis, systemic lupus erythematosus, polymyositis, dermatomyositis, systemic vasculitis, Sjogren's syndrome, antisynthetase syndrome, or mixed connective tissue disease, as determined by the investigator.
3. FVC ≤45% of predicted, or a DLco (corrected for hemoglobin) ≤40% of predicted or requiring supplemental oxygen at screening.
4. Pulmonary arterial hypertension, as determined by the investigator at, or prior to first day of dosing (Day 1).
5. SSc renal crisis within 6 months prior to the first day of dosing (Day 1).
6. History or presence of cardiovascular, respiratory, hepatic, renal, gastrointestinal, endocrine, hematologic, or neurological disorders capable of significantly altering the absorption, metabolism, or elimination of drugs; constituting a risk when taking the study intervention or interfering with the interpretation of data.
7. Obstructive pulmonary disease (pre-bronchodilator FEV1/FVC \<0.7).
8. Significant emphysema on screening HRCT (extent of emphysema exceeds extent of ILD).
9. Previous or planned major organ transplant (e.g., heart, lung, kidney, liver) or bone marrow transplant (e.g., autologous stem cell transplant).
10. Treatment with biologic agents, such as intravenous immunoglobulin or monoclonal antibodies, including marketed drugs, within 3 months or 5 half-lives (whichever is longer) prior to dosing.
11. Treatment with rituximab within 6 months prior to Day 1.
12. Treatment with non-biologic systemic immunosuppressive medication, other than mycophenolate, methotrexate or azathioprine (including, but not limited to cyclosporine A, tacrolimus, leflunomide, oral or parenteral gold, Janus kinase (JAK) inhibitors) within 3 months prior to Day 1.
13. Treatment with cyclophosphamide (oral or intravenous) within 6 months prior to Day 1.
14. Use of anti-fibrotic agents including colchicine, D-penicillamine, pirfenidone or tyrosine kinase inhibitors (e.g., nintedanib, nilotinib, imatinib, dasatinib) within 4 weeks prior to Day 1.
15. Cytotoxic drugs such as, chlorambucil, nitrogen mustard, or other alkylating agents within 6 months of Day 1.
16. Treatment with IM or IV corticosteroids within 1 month prior to Day 1.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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GlaxoSmithKline

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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GSK Investigational Site

Phoenix, Arizona, United States

Site Status COMPLETED

GSK Investigational Site

Scottsdale, Arizona, United States

Site Status RECRUITING

GSK Investigational Site

Scottsdale, Arizona, United States

Site Status RECRUITING

GSK Investigational Site

Tucson, Arizona, United States

Site Status RECRUITING

GSK Investigational Site

Los Angeles, California, United States

Site Status RECRUITING

GSK Investigational Site

Los Angeles, California, United States

Site Status RECRUITING

GSK Investigational Site

Los Angeles, California, United States

Site Status RECRUITING

GSK Investigational Site

Upland, California, United States

Site Status RECRUITING

GSK Investigational Site

Aurora, Colorado, United States

Site Status RECRUITING

GSK Investigational Site

Washington D.C., District of Columbia, United States

Site Status RECRUITING

GSK Investigational Site

Jacksonville, Florida, United States

Site Status RECRUITING

GSK Investigational Site

Miami, Florida, United States

Site Status RECRUITING

GSK Investigational Site

Chicago, Illinois, United States

Site Status RECRUITING

GSK Investigational Site

Baltimore, Maryland, United States

Site Status RECRUITING

GSK Investigational Site

Ann Arbor, Michigan, United States

Site Status RECRUITING

GSK Investigational Site

New Brunswick, New Jersey, United States

Site Status RECRUITING

GSK Investigational Site

New York, New York, United States

Site Status RECRUITING

GSK Investigational Site

New York, New York, United States

Site Status RECRUITING

GSK Investigational Site

Potsdam, New York, United States

Site Status RECRUITING

GSK Investigational Site

Cincinnati, Ohio, United States

Site Status RECRUITING

GSK Investigational Site

Philadelphia, Pennsylvania, United States

Site Status RECRUITING

GSK Investigational Site

Philadelphia, Pennsylvania, United States

Site Status RECRUITING

GSK Investigational Site

Denison, Texas, United States

Site Status RECRUITING

GSK Investigational Site

El Paso, Texas, United States

Site Status RECRUITING

GSK Investigational Site

Houston, Texas, United States

Site Status RECRUITING

GSK Investigational Site

Buenos Aires, , Argentina

Site Status RECRUITING

GSK Investigational Site

Ciudad Autonoma Buenos Aires, , Argentina

Site Status RECRUITING

GSK Investigational Site

Ciudad Autonoma de Buenos Aire, , Argentina

Site Status RECRUITING

GSK Investigational Site

Liverpool, New South Wales, Australia

Site Status COMPLETED

GSK Investigational Site

Adelaide, South Australia, Australia

Site Status RECRUITING

GSK Investigational Site

Woodville, South Australia, Australia

Site Status RECRUITING

GSK Investigational Site

Fitzroy, Victoria, Australia

Site Status RECRUITING

GSK Investigational Site

Ghent, , Belgium

Site Status RECRUITING

GSK Investigational Site

Liège, , Belgium

Site Status RECRUITING

GSK Investigational Site

Belo Horizonte, , Brazil

Site Status RECRUITING

GSK Investigational Site

Curitiba, , Brazil

Site Status COMPLETED

GSK Investigational Site

Juiz de Fora, , Brazil

Site Status RECRUITING

GSK Investigational Site

Porto Alegre, , Brazil

Site Status RECRUITING

GSK Investigational Site

Porto Alegre, , Brazil

Site Status RECRUITING

GSK Investigational Site

Salvador, , Brazil

Site Status RECRUITING

GSK Investigational Site

São Paulo, , Brazil

Site Status RECRUITING

GSK Investigational Site

São Paulo, , Brazil

Site Status RECRUITING

GSK Investigational Site

Beijing, , China

Site Status RECRUITING

GSK Investigational Site

Beijing, , China

Site Status RECRUITING

GSK Investigational Site

Beijing, , China

Site Status RECRUITING

GSK Investigational Site

Beijing, , China

Site Status RECRUITING

GSK Investigational Site

Changchun, , China

Site Status RECRUITING

GSK Investigational Site

Chengdu, , China

Site Status RECRUITING

GSK Investigational Site

Chengdu, , China

Site Status RECRUITING

GSK Investigational Site

Luzhou, , China

Site Status RECRUITING

GSK Investigational Site

Mianyang, , China

Site Status RECRUITING

GSK Investigational Site

Nanjing, , China

Site Status RECRUITING

GSK Investigational Site

Nanjing, , China

Site Status RECRUITING

GSK Investigational Site

Nanning, , China

Site Status RECRUITING

GSK Investigational Site

Shanghai, , China

Site Status RECRUITING

GSK Investigational Site

Shanghai, , China

Site Status RECRUITING

GSK Investigational Site

Shenyang, , China

Site Status RECRUITING

GSK Investigational Site

Xi'an, , China

Site Status RECRUITING

GSK Investigational Site

Zhuzhou, , China

Site Status RECRUITING

GSK Investigational Site

Aarhus, , Denmark

Site Status RECRUITING

GSK Investigational Site

Odense C, , Denmark

Site Status WITHDRAWN

GSK Investigational Site

Turku, , Finland

Site Status RECRUITING

GSK Investigational Site

Bobigny, , France

Site Status RECRUITING

GSK Investigational Site

Brest, , France

Site Status RECRUITING

GSK Investigational Site

Paris, , France

Site Status RECRUITING

GSK Investigational Site

Paris, , France

Site Status RECRUITING

GSK Investigational Site

Paris, , France

Site Status RECRUITING

GSK Investigational Site

Toulouse, , France

Site Status RECRUITING

GSK Investigational Site

Cologne, , Germany

Site Status RECRUITING

GSK Investigational Site

Düsseldorf, , Germany

Site Status RECRUITING

GSK Investigational Site

Mainz, , Germany

Site Status RECRUITING

GSK Investigational Site

Minden, , Germany

Site Status RECRUITING

GSK Investigational Site

Tübingen, , Germany

Site Status RECRUITING

GSK Investigational Site

Athens, , Greece

Site Status WITHDRAWN

GSK Investigational Site

Athens, , Greece

Site Status RECRUITING

GSK Investigational Site

Heraklion Crete, , Greece

Site Status RECRUITING

GSK Investigational Site

Larissa, , Greece

Site Status RECRUITING

GSK Investigational Site

Thessaloniki, , Greece

Site Status RECRUITING

GSK Investigational Site

Haifa, , Israel

Site Status RECRUITING

GSK Investigational Site

Holon, , Israel

Site Status WITHDRAWN

GSK Investigational Site

Kfar Saba, , Israel

Site Status WITHDRAWN

GSK Investigational Site

Poria – Neve Oved, , Israel

Site Status RECRUITING

GSK Investigational Site

Ramat Gan, , Israel

Site Status RECRUITING

GSK Investigational Site

Tel Aviv, , Israel

Site Status RECRUITING

GSK Investigational Site

Ancona, , Italy

Site Status RECRUITING

GSK Investigational Site

Bari, , Italy

Site Status RECRUITING

GSK Investigational Site

Cagliari, , Italy

Site Status RECRUITING

GSK Investigational Site

Catania, , Italy

Site Status RECRUITING

GSK Investigational Site

Ferrara, , Italy

Site Status RECRUITING

GSK Investigational Site

Florence, , Italy

Site Status RECRUITING

GSK Investigational Site

Milan, , Italy

Site Status RECRUITING

GSK Investigational Site

Modena, , Italy

Site Status RECRUITING

GSK Investigational Site

Napoli, , Italy

Site Status RECRUITING

GSK Investigational Site

Orbassano to, , Italy

Site Status RECRUITING

GSK Investigational Site

Padua, , Italy

Site Status RECRUITING

GSK Investigational Site

Pavia, , Italy

Site Status RECRUITING

GSK Investigational Site

Roma, , Italy

Site Status RECRUITING

GSK Investigational Site

Roma, , Italy

Site Status RECRUITING

GSK Investigational Site

Verona, , Italy

Site Status RECRUITING

GSK Investigational Site

Gunma, , Japan

Site Status RECRUITING

GSK Investigational Site

Hiroshima, , Japan

Site Status RECRUITING

GSK Investigational Site

Hokkaido, , Japan

Site Status RECRUITING

GSK Investigational Site

Hokkaido, , Japan

Site Status RECRUITING

GSK Investigational Site

Kanagawa, , Japan

Site Status WITHDRAWN

GSK Investigational Site

Miyagi, , Japan

Site Status RECRUITING

GSK Investigational Site

Shizuoka, , Japan

Site Status RECRUITING

GSK Investigational Site

Tokushima, , Japan

Site Status RECRUITING

GSK Investigational Site

Tokyo, , Japan

Site Status RECRUITING

GSK Investigational Site

Chihuahua City, , Mexico

Site Status RECRUITING

GSK Investigational Site

Guadalajara, , Mexico

Site Status RECRUITING

GSK Investigational Site

Mérida, , Mexico

Site Status RECRUITING

GSK Investigational Site

Torreón, , Mexico

Site Status RECRUITING

GSK Investigational Site

Seoul, , South Korea

Site Status RECRUITING

GSK Investigational Site

Seoul, , South Korea

Site Status RECRUITING

GSK Investigational Site

Seoul, , South Korea

Site Status RECRUITING

GSK Investigational Site

Seoul, , South Korea

Site Status RECRUITING

GSK Investigational Site

Suwon Kyunggi-do, , South Korea

Site Status RECRUITING

GSK Investigational Site

Barcelona, , Spain

Site Status RECRUITING

GSK Investigational Site

Barcelona, , Spain

Site Status RECRUITING

GSK Investigational Site

Bilbao, , Spain

Site Status RECRUITING

GSK Investigational Site

Granada, , Spain

Site Status RECRUITING

GSK Investigational Site

Madrid, , Spain

Site Status RECRUITING

GSK Investigational Site

Madrid, , Spain

Site Status RECRUITING

GSK Investigational Site

Seville, , Spain

Site Status RECRUITING

GSK Investigational Site

Valencia, , Spain

Site Status RECRUITING

GSK Investigational Site

VigoPontevedra, , Spain

Site Status RECRUITING

GSK Investigational Site

Birmingham, , United Kingdom

Site Status RECRUITING

GSK Investigational Site

Leeds, , United Kingdom

Site Status RECRUITING

GSK Investigational Site

London, , United Kingdom

Site Status RECRUITING

GSK Investigational Site

Portsmouth, , United Kingdom

Site Status RECRUITING

GSK Investigational Site

Wakefield, , United Kingdom

Site Status RECRUITING

Countries

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United States Argentina Australia Belgium Brazil China Denmark Finland France Germany Greece Israel Italy Japan Mexico South Korea Spain United Kingdom

Central Contacts

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US GSK Clinical Trials Call Center

Role: CONTACT

877-379-3718

EU GSK Clinical Trials Call Center

Role: CONTACT

+44 (0) 20 89904466

Facility Contacts

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US GSK Clinical Trials Call Center

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877-379-3718

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+44 (0) 20 8990 4466

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US GSK Clinical Trials Call Center

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US GSK Clinical Trials Call Center

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US GSK Clinical Trials Call Center

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US GSK Clinical Trials Call Center

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US GSK Clinical Trials Call Center

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US GSK Clinical Trials Call Center

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Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

2023-503219-14-01

Identifier Type: REGISTRY

Identifier Source: secondary_id

218224

Identifier Type: -

Identifier Source: org_study_id

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