A Trial to Evaluate the Safety of Long Term Treatment With Nintedanib in Patients With Scleroderma Related Lung Fibrosis

NCT ID: NCT03313180

Last Updated: 2024-02-20

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

444 participants

Study Classification

INTERVENTIONAL

Study Start Date

2017-11-27

Study Completion Date

2023-01-25

Brief Summary

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The main objective is to assess long term safety of treatment with oral nintedanib in patients with Systemic Sclerosis associated Interstitial Lung Disease (SSc-ILD).

Detailed Description

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Conditions

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Lung Diseases, Interstitial

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Nintedanib

Patients with Systemic Sclerosis associated Interstitial Lung Disease (SSc-ILD) who took part in the parent trials 1199.214 (Nintedanib or Placebo) or 1199-0340 (Nintedanib). Patients continued in this trial and received Nintedanib 150 mg (milligram) twice daily (bid) unless they had reduced their dose to 100 mg bid trial medication (Nintedanib or Placebo) in the parent trial.

Patients receiving 100 mg bid trial medication at the end of the parent trial could receive either Nintedanib 100 mg bid or 150 mg bid at the discretion of the investigator.

Group Type EXPERIMENTAL

Nintedanib

Intervention Type DRUG

Administered twice daily

Interventions

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Nintedanib

Administered twice daily

Intervention Type DRUG

Other Intervention Names

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OVEF

Eligibility Criteria

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Inclusion Criteria

* Patients who completed the parent trial 1199.214/1199-0340 per protocol and did not permanently discontinue study treatment
* Signed and dated written informed consent in accordance with International Conference on Harmonisation - Good Clinical Practice (ICH-GCP) and local legislation prior to admission to the trial
* Women of childbearing potential must be ready and able to use highly effective methods of birth control per ICH M3 (R2) that result in a low failure rate of less than 1% per year when used consistently and correctly as well as one barrier method for 28 days prior to nintedanib treatment initiation, during the trial and for 3 months after last intake of nintedanib.

Exclusion Criteria

* Aspartate Aminotransferase (AST), Alanine Aminotransferase (ALT) \> 3 x Upper Limit of Normal (ULN)
* Bilirubin \> 2 x ULN
* Creatinine clearance \<30 mL/min calculated by Cockcroft-Gault formula.
* Clinically relevant anaemia at investigators discretion.
* Bleeding risk, any of the following

* Known genetic predisposition to bleeding according to the judgement of the investigator
* Patients who require

* Fibrinolysis, full-dose therapeutic anticoagulation
* High dose antiplatelet therapy.
* Hemorrhagic central nervous system (CNS) event after completion of the parent trial 1199.214/1199-0340
* Any of the following after last treatment of 1199.214/1199-0340:

* Haemoptysis or haematuria
* Active gastro-intestinal bleeding or Gastrointestinal (GI) - ulcers
* Gastric antral vascular ectasia (GAVE)
* Major injury or surgery
* Coagulation parameters: International normalised ratio (INR) \>2, prolongation of prothrombin time (PT) and partial thromboplastin time (PTT) by \>1.5 x ULN at Visit 1.
* New major thrombo-embolic events developed after completion of the parent trial 1199.214/1199-0340:

* Stroke;
* Deep vein thrombosis;
* Pulmonary embolism;
* Myocardial infarction.
* Major surgery performed within the next 3 months
* Time period \> 12 weeks between last drug intake in 1199.214 or \> 1 week between last nintedanib intake in trial 1199-0340 and Visit 2 of this trial
* Usage of any investigational drug after completion of 1199.214/1199-0340 or planned usage of an investigational drug during the course of this trial.
* A disease or condition which may put the patient at risk because of participation in this trial (e.g. clinically relevant intestinal pseudoobstruction) or limit the patient's ability to participate in this trial
* Chronic alcohol or drug abuse or any condition that, in the investigator's opinion, makes them an unreliable trial subject or unlikely to complete the trial
* Known hypersensitivity to the trial medication or its components (i.e. soya lecithin).
* Women who are pregnant, nursing, or who plan to become pregnant while in the trial
* Previous enrolment in this trial
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Boehringer Ingelheim

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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University of Alabama at Birmingham

Birmingham, Alabama, United States

Site Status

University of California Los Angeles

Los Angeles, California, United States

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University of California Davis

Sacramento, California, United States

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University of California San Francisco

San Francisco, California, United States

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Stanford University Medical Center

Stanford, California, United States

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University of Colorado Denver

Aurora, Colorado, United States

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Yale University School of Medicine

New Haven, Connecticut, United States

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Georgetown University

Washington D.C., District of Columbia, United States

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University of Florida College of Medicine

Jacksonville, Florida, United States

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University of Miami

Miami, Florida, United States

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The Emory Clinic

Atlanta, Georgia, United States

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Northwestern University

Chicago, Illinois, United States

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University of Iowa Hospitals and Clinics

Iowa City, Iowa, United States

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University of Kansas Medical Center

Kansas City, Kansas, United States

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Tulane University Hospital and Clinic

New Orleans, Louisiana, United States

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Johns Hopkins Hospital

Baltimore, Maryland, United States

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Boston University School of Medicine

Boston, Massachusetts, United States

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University of Minnesota

Minneapolis, Minnesota, United States

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Mayo Clinic, Rochester

Rochester, Minnesota, United States

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Washington University School of Medicine

St Louis, Missouri, United States

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Hospital for Special Surgery

New York, New York, United States

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Icahn School of Medicine at Mount Sinai

New York, New York, United States

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Columbia University Medical Center-New York Presbyterian Hospital

New York, New York, United States

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Duke University Medical Center

Durham, North Carolina, United States

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University of Cincinnati

Cincinnati, Ohio, United States

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Cleveland Clinic

Cleveland, Ohio, United States

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University of Toledo

Toledo, Ohio, United States

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University of Pennsylvania

Philadelphia, Pennsylvania, United States

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Thomas Jefferson University

Philadelphia, Pennsylvania, United States

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Temple University Hospital

Philadelphia, Pennsylvania, United States

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Medical University of South Carolina

Charleston, South Carolina, United States

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Vanderbilt University Medical Center - Vanderbilt Lung Institute at 100 Oaks

Nashville, Tennessee, United States

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University of Texas Southwestern Medical Center

Dallas, Texas, United States

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The University of Texas Health Science Center at Houston

Houston, Texas, United States

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University of Utah Health Sciences Center

Salt Lake City, Utah, United States

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Inova Fairfax Medical Campus

Falls Church, Virginia, United States

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Virginia Mason Medical Center

Seattle, Washington, United States

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University of Washington

Seattle, Washington, United States

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Froedtert and The Medical College of Wisconsin

Milwaukee, Wisconsin, United States

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Hospital Militar Central Cirujano Mayor Dr. Cosme Argerich

Buenos Aires, , Argentina

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APRILLUS-Asistencia e Investigación

Ciudad Autonoma Buenos Aires, , Argentina

Site Status

CEMER-Centro Medico De Enfermedades Respiratorias

Florida, , Argentina

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Royal Prince Alfred Hospital

Camperdown, New South Wales, Australia

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Liverpool Hospital

Sydney, New South Wales, Australia

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Royal Adelaide Hospital

Adelaide, South Australia, Australia

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St Vincent's Hospital Melbourne

Fitzroy, Victoria, Australia

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Medical University of Innsbruck

Innsbruck, , Austria

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UNIV UZ Gent

Ghent, , Belgium

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UZ Leuven

Leuven, , Belgium

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Centre Hospitalier Universitaire de Liège

Liège, , Belgium

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Edumed - Educacao e Saude SA

Curitiba, , Brazil

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HSCM

Montreal, Quebec, Canada

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Hospital Clínico Reg. de Concepción "Dr. G. Grant Benavente"

Concepción, , Chile

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Centro de Investigación del Maule

Talca, , Chile

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Peking Union Medical College Hospital

Beijing, , China

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The First Hospital of Jilin University

Changchun, , China

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West China Hospital

Chengdu, , China

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The First Affiliated Hospital of Anhui Medical University

Hefei, , China

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Huashan Hospital, Fudan University

Shanghai, , China

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The First Hospital of China Medical University

Shenyang, , China

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Institute of Rheumathology Prague

Prague, , Czechia

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Aarhus University Hospital

Aarhus N, , Denmark

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Odense University Hospital

Odense, , Denmark

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HYKS Keuhkosairauksien tutkimusyksikkö

Helsinki, , Finland

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TYKS

Turku, , Finland

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HOP Avicenne

Bobigny, , France

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HOP Louis Pradel

Bron, , France

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CHRU Lille

Lille, , France

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HOP Claude Huriez

Lille, , France

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HOP Arnaud de Villeneuve

Montpellier, , France

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HOP Hôtel-Dieu

Nantes, , France

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HOP Pasteur

Nice, , France

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HOP Bichat

Paris, , France

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HOP Pontchaillou

Rennes, , France

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HOP Charles Nicolle

Rouen, , France

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HOP Larrey

Toulouse, , France

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HOP Bretonneau

Tours, , France

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Klinik Donaustauf

Donaustauf, , Germany

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Universitätsklinikum Carl Gustav Carus Dresden

Dresden, , Germany

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Universitätsklinikum Erlangen

Erlangen, , Germany

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Universitätsmedizin Greifswald

Greifswald, , Germany

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Asklepios Klinik Altona

Hamburg, , Germany

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Medizinische Hochschule Hannover

Hanover, , Germany

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Thoraxklinik-Heidelberg gGmbH am Universitätsklinikum Heidelberg

Heidelberg, , Germany

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Universitätsklinikum Schleswig-Holstein, Campus Kiel

Kiel, , Germany

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Universitätsklinikum Münster

Münster, , Germany

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Universitätsklinikum Tübingen

Tübingen, , Germany

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General Hospital of Athens "Laiko"

Athens, , Greece

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Ramaiah Medical College and Hospitals

Bangalore, , India

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Post Graduate Institute of Medical Education and Research

Chandigarh, , India

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Sir Gangaram Hospital

Delhi, , India

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Care Hospital

Hyderabad, , India

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Nizam's Institute of Medical Sciences

Hyderabad, , India

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Asthma Bhawan

Jaipur, , India

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Getwell Hospital & Research Institute

Nagpur, , India

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All India Institute of Medical Sciences

New Delhi, , India

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B.J. Medical College and Sasoon General Hospital

Pune, , India

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Bnei Zion Medical Center, Haifa

Haifa, , Israel

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Rambam Medical Center

Haifa, , Israel

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Rabin Medical Center Beilinson

Petah Tikva, , Israel

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Sourasky Medical Center

Tel Aviv, , Israel

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Università degli Studi di Genova

Genova, , Italy

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A.O. San Gerardo di Monza

Monza, , Italy

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A.O Universitaria - Università degli Studi della Campania Luigi Vanvitelli

Napoli, , Italy

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Università degli Studi Padova

Padua, , Italy

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Azienda Universitaria-Universita' La Sapienza

Roma, , Italy

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Tosei General Hospital

Aichi, Seto, , Japan

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Kurume University Hospital

Fukuoka, Kurume, , Japan

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Sapporo Medical University Hospital

Hokkaido, Sapporo, , Japan

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National Hospital Organization Himeji Medical Center

Hyogo, Himeji, , Japan

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St. Marianna University Hospital

Kanagawa, Kawasaki, , Japan

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Kitasato University Hospital

Kanagawa, Sagamihara, , Japan

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Kanagawa Cardiovascular and Respiratory Center

Kanagawa, Yokohama, , Japan

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Nagasaki University Hospital

Nagasaki, Nagasaki, , Japan

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Kindai University Hospital

Osaka, Osakasayama, , Japan

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National Hospital Organization Kinki-Chuo Chest Medical Center

Osaka, Sakai, , Japan

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Osaka Medical College Hospital

Osaka, Takatsuki, , Japan

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Saitama Medical University Hospital

Saitama, Iruma-gun, , Japan

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Hamamatsu University Hospital

Shizuoka, Hamamatsu, , Japan

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Tokushima University Hospital

Tokushima, Tokushima, , Japan

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Juntendo University Hospital

Tokyo, Bunkyo-Ku, , Japan

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Nippon Medical School Hospital

Tokyo, Bunkyo-Ku, , Japan

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Toho University Omori Medical Center

Tokyo, Ota-ku, , Japan

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Institute of Rheumatology Tokyo Women's Medical University

Tokyo, Shinjyuku-ku, , Japan

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Hospital Pulau Pinang

Georgetown Pulau Pinang, , Malaysia

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University of Malaya Medical Centre

Kuala Lumpur, , Malaysia

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Instituto Nacional de Enfermedades Respiratorias Ismael Cosío Villegas

Mexico City, , Mexico

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Amsterdam UMC Locatie VUMC

Amsterdam, , Netherlands

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Leids Universitair Medisch Centrum (LUMC)

Leiden, , Netherlands

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Radboud Universitair Medisch Centrum

Nijmegen, , Netherlands

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Erasmus Medisch Centrum

Rotterdam, , Netherlands

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Oslo Universitetssykehus HF, Rikshospitalet

Oslo, , Norway

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Universitetssykehuset Nord-Norge, Tromsø

Tromsø, , Norway

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Dr.Biziel UnivHosp#2,Rheumat&Connec.Tissue Disease,Bydgoszcz

Bydgoszcz, , Poland

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Specialist Allergy-Internist Center ALL-MED

Krakow, , Poland

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EMED, Center of Medical Services,Private Prac,Rzeszow

Rzeszów, , Poland

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Indep.Pblic Clin.Hosp#1,Dermatol,Venereol&Allerg.dep,Wroclaw

Wroclaw, , Poland

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Hospital Garcia de Orta, EPE

Almada, , Portugal

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Hospital Fernando Fonseca, EPE

Amadora, , Portugal

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CHUC - Centro Hospitalar e Universitário de Coimbra, EPE

Coimbra, , Portugal

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ULSAM, EPE - Hospital Conde de Bertiandos

Ponte de Lima, , Portugal

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Centro Hospitalar Universitário São João,EPE

Porto, , Portugal

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Centro Hospitalar de Vila Nova de Gaia

Vila Nova de Gaia, , Portugal

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Hospital Santa Creu i Sant Pau

Barcelona, , Spain

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Hospital Vall d'Hebron

Barcelona, , Spain

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Hospital General Universitario Gregorio Marañón

Madrid, , Spain

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Hospital Universitario 12 de Octubre

Madrid, , Spain

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Hospital Dr. Peset

Valencia, , Spain

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Hospital Politècnic La Fe

Valencia, , Spain

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Hospital Álvaro Cunqueiro

Vigo, , Spain

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Clinical Rheumatology Research Center Sahlgrenska

Gothenburg, , Sweden

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University Hospital Zurich

Zurich, , Switzerland

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Ramathibodi Hospital

Bangkok, , Thailand

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Srinagarind Hospital

Muang, , Thailand

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Songklanagarind Hospital

Songkhla, , Thailand

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Royal Free Hospital

London, , United Kingdom

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Guy's Hospital

London, , United Kingdom

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Royal Brompton Hospital

London, , United Kingdom

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Salford Royal Hospital

Salford, , United Kingdom

Site Status

Countries

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United States Argentina Australia Austria Belgium Brazil Canada Chile China Czechia Denmark Finland France Germany Greece India Israel Italy Japan Malaysia Mexico Netherlands Norway Poland Portugal Spain Sweden Switzerland Thailand United Kingdom

References

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Allanore Y, Khanna D, Smith V, Aringer M, Hoffmann-Vold AM, Kuwana M, Merkel PA, Stock C, Sambevski S, Denton CP; SENSCIS Trial Investigators. Effects of nintedanib in patients with limited cutaneous systemic sclerosis and interstitial lung disease. Rheumatology (Oxford). 2024 Mar 1;63(3):639-647. doi: 10.1093/rheumatology/kead280.

Reference Type DERIVED
PMID: 37294870 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Related Links

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Other Identifiers

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2016-003403-66

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

1199-0225

Identifier Type: -

Identifier Source: org_study_id

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