A Study of PER-001 in Participants With Open-Angle Glaucoma

NCT ID: NCT05822245

Last Updated: 2025-04-15

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

ACTIVE_NOT_RECRUITING

Clinical Phase

PHASE1/PHASE2

Total Enrollment

36 participants

Study Classification

INTERVENTIONAL

Study Start Date

2023-05-25

Study Completion Date

2026-04-04

Brief Summary

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This clinical study has two phases: Phase 1 and Phase 2a. Phase 1 is an open-label, single ascending dose (SAD), while Phase 2a is a randomized, single-masked (participant) with a sham control.

Detailed Description

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This clinical study has two phases: Phase 1 and Phase 2a. Phase 1 is an open-label, SAD study to investigate the ocular and systemic safety and tolerability of two dose levels of PER-001, in participants with advanced OAG. Phase 1 will enroll up to approximately 12 participants.

Phase 2a is a randomized, single-masked (participant) study to further investigate the ocular and systemic safety and tolerability of the two dose levels of PER-001 Intravitreal Implants in participants with progressing glaucoma. Participants who meet entry criteria will be randomized to receive either dose of PER-001 or sham control. In Phase 2a, a total of approximately 24 participants (12 in each Cohort, will be randomized).

Conditions

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Open-angle Glaucoma

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

SEQUENTIAL

Dose escalation.
Primary Study Purpose

TREATMENT

Blinding Strategy

SINGLE

Participants
Placebo sham

Study Groups

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Phase 1 Cohort A

Cohort A - Low Dose

Group Type EXPERIMENTAL

PER-001 Intravitreal Implant - Low Dose

Intervention Type DRUG

PER-001 Low Dose Intravitreal Implant

Phase 1 Cohort B

Cohort B - High Dose

Group Type EXPERIMENTAL

PER-001 Intravitreal Implant - High Dose

Intervention Type DRUG

PER-001 High Dose Intravitreal Implant

Phase 2 Cohort C

Cohort C - Low Dose or Sham

Group Type EXPERIMENTAL

PER-001 Intravitreal Implant - Low Dose

Intervention Type DRUG

PER-001 Low Dose Intravitreal Implant

PER-001 Intravitreal Implant - Sham

Intervention Type DRUG

PER-001 Intravitreal Sham

Phase 2 Cohort D

Cohort D - High Dose or Sham

Group Type EXPERIMENTAL

PER-001 Intravitreal Implant - High Dose

Intervention Type DRUG

PER-001 High Dose Intravitreal Implant

PER-001 Intravitreal Implant - Sham

Intervention Type DRUG

PER-001 Intravitreal Sham

Interventions

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PER-001 Intravitreal Implant - Low Dose

PER-001 Low Dose Intravitreal Implant

Intervention Type DRUG

PER-001 Intravitreal Implant - High Dose

PER-001 High Dose Intravitreal Implant

Intervention Type DRUG

PER-001 Intravitreal Implant - Sham

PER-001 Intravitreal Sham

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

For Phase 1 and Phase 2a:

* Must be ≥ 18 years of age at the time of signing the informed consent
* A negative pregnancy test for females of childbearing potential at Screening (serum) and Day 1 (urine).
* IOP 6 to 25 mmHg (inclusive) at Screening in potentially eligible eye(s)

Phase 1:

* Best corrected visual acuity (BCVA) LogMAR score 1.0 or better at Screening in at least one eye and prior to randomization at Day 1 in the study eye
* Diagnosis of advanced or severe primary OAG including normal tension, pseudoexfoliation and pigment dispersion

Phase 2:

* BCVA LogMAR score 0.5 or better at Screening in at least one eye and prior to randomization at Day 1 in the study eye
* Primary OAG that is progressing in the study eye

Exclusion Criteria

* Blood pressure \>140/90 mmHg or \<90/60 mmHg at Screening
* Any condition which, in the opinion of the investigator, would preclude the participant's ability to comply with study requirements including completion of the study (including but not limited to diagnosis of dementia, Alzheimer's, and/or other neurological disease or physical incapacity)
* Females who are pregnant, nursing, or planning a pregnancy during the study
* Any significant media opacity which precludes clinical evaluation and imaging of the retina
* History of vitrectomy surgery or retinal detachment or macular hole (Stage 3 or 4)
* Retinal laser within 3 months prior to Day 1
* Intraocular surgery, including cataract surgery and Minimally Invasive Glaucoma
* Surgery (MIGS), within 3 months prior to Day 1
* Aphakia or absence of posterior capsule
* Change in IOP lowering therapy within 6 weeks prior to Screening and/or anticipated change in IOP lowering therapy or treatment during the study Worse than mild non-proliferative diabetic retinopathy (Note: stable mild background diabetic retinopathy is permitted)
* Any active uveitis and/or vitritis or history of idiopathic or autoimmune-associated uveitis
* Active infectious conjunctivitis, keratitis, scleritis, or endophthalmitis (Note: mild blepharitis is permitted if stable)
* History of recurrent infectious or inflammatory ocular disease
* Central serous retinopathy
* Non-glaucomatous optic neuropathy
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Perfuse Therapeutics, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Phillip Lai, MD

Role: STUDY_DIRECTOR

Perfuse Therapeutics, Inc.

Locations

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Perfuse Therapeutics, Inc.

San Francisco, California, United States

Site Status

Countries

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United States

Other Identifiers

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PER001-201

Identifier Type: -

Identifier Source: org_study_id

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