Phase I Study to Assess the Safety and Efficacy of OCU200 for Center-Involved Diabetic Macular Edema (DME)

NCT ID: NCT05802329

Last Updated: 2025-12-03

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE1

Total Enrollment

24 participants

Study Classification

INTERVENTIONAL

Study Start Date

2024-01-13

Study Completion Date

2026-07-31

Brief Summary

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A Phase 1 study to assess the safety and efficacy of OCU200 for center-involved diabetic macular edema

Detailed Description

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This is a multicenter, open-label, dose ranging study with 4 cohorts in the dose-escalation portion of the study. An accelerated 3+3 design with parallel and sequential dosing will be used.

Under the escalation design, 12 subjects will be enrolled if there are no DLTs and up to 24 subjects under the condition that exactly 1 of the 3 subjects of every cohort if determined to have a DLT.

Each subject will receive a total of 2 intravitreal injections of OCU200 6 weeks apart.

The DSMB will review the sentinel subject 1 week safety data post dosing in every cohort of all 3 subjects.

Cohort 1: 3+3 participants will receive intravitreal injection of OCU200.

Cohort 2: 3+3 participants will receive intravitreal injection of OCU200.

Cohort 3: 3+3 participants will receive intravitreal injection of OCU200.

Cohort 4: 3+3 participants will receive intravitreal injection of OCU200.

Conditions

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Center Involved Diabetic Macular Edema Diabetic Macular Edema

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

SEQUENTIAL

3+3 design with parallel and sequential dosing.
Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Cohort 1

3+3 participants will receive intravitreal injection of OCU200 (0.5 mg/mL concentration).

Group Type EXPERIMENTAL

OCU200

Intervention Type DRUG

Intravitreal Injection

Cohort 2

3+3 participants will receive intravitreal injection of OCU200 (1 mg/ML concentration).

Group Type EXPERIMENTAL

OCU200

Intervention Type DRUG

Intravitreal Injection

Cohort 3

3+3 participants will receive intravitreal injection of OCU200 (2 mg/mL concentration).

Group Type EXPERIMENTAL

OCU200

Intervention Type DRUG

Intravitreal Injection

Cohort 4

3+3 participants will receive intravitreal injection of OCU200 (5 mg/mL concentration).

Group Type EXPERIMENTAL

OCU200

Intervention Type DRUG

Intravitreal Injection

Interventions

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OCU200

Intravitreal Injection

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

1. Diagnosis of Type 1 or Type 2 Diabetes Mellitus
2. Decreased visual acuity attributable primarily to DME
3. Central-involved DME with central retinal subfield thickness (CST) values, as assessed with spectral-domain optical coherence tomography (SD-OCT) of:

1. ≥ 320 but ≤ 450µm if male or ≥ 305 but ≤ 435µm if female on Heidelberg Spectralis
2. ≥ 305 but ≤ 435µm if male or ≥ 290 but ≤ 420µm if female on Zeiss Cirrus
4. BCVA ≤ 78 and ≥ 24 letters on ETDRS chart
5. Sufficient ocular media clarity, pupillary dilation and participant cooperation to permit acquisition of good quality retinal imaging
6. No history of prior anti-VEGF injection or history of at least 2 consecutive intravitreal anti-VEGF injection (less than 7 weeks apart) with incomplete resolution of CST within 1 year.

Note: The last anti-VEGF injection must be administered at least six weeks (45 days) prior to the study treatment (Day 1) in the study eye.

Exclusion Criteria

1. Presence of any condition that prevent clear visualization of retina (e.g., significant cataract, vitreous hemorrhage)
2. Uncontrolled hypertension
3. Uncontrolled glaucoma
4. Concurrent disease in the study eye, other than central-involved DME
5. Intravitreal or periocular steroid treatment within 3 months prior to the screening visit
6. Any ocular surgery within 3 months prior to the screening visit in the study eye
7. Uncontrolled/poorly controlled diabetes (Glycated hemoglobin (HbA1c) ≥ 10%)
8. History of retinal detachment in the study eye or other retinal vascular disease in the study eye
9. Focal or pan-retinal laser photocoagulation in the study eye within 3 months prior to the screening visit
10. Presence of any inherited retinal disease or history of proliferative diabetic retinopathy
11. History of Renal disease including stage 3b or worse
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

Yes

Sponsors

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Ocugen

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Huma Qamar, MD, MPH, CMI

Role: STUDY_DIRECTOR

Ocugen

Locations

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Advanced Research LLC

Deerfield Beach, Florida, United States

Site Status RECRUITING

Erie Retina Research, LLC

Erie, Pennsylvania, United States

Site Status RECRUITING

Retina Consultants of Texas Research Centers

Bellaire, Texas, United States

Site Status RECRUITING

Retina Consultants of America

Southlake, Texas, United States

Site Status RECRUITING

Gundersen Health System

La Crosse, Wisconsin, United States

Site Status RECRUITING

Countries

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United States

Central Contacts

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Roshan A George, MD, MPH

Role: CONTACT

845-664-1505

Oscar Cuzzani, MD, PhD

Role: CONTACT

Facility Contacts

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Danahe Navarrete

Role: primary

954-302-3047 ext. 103

Samarth Shah, MD, Ph.D

Role: backup

Bethany Scott

Role: primary

814-737-0203

Rebecca Taing

Role: primary

713-394-7576

Lydia Adams

Role: primary

800-833-5921

Emily Gonzales

Role: backup

Trinity Lee

Role: primary

608-775-9539

Chase Penzkover

Role: backup

Other Identifiers

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OCU200-101

Identifier Type: -

Identifier Source: org_study_id

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