Safety and Efficacy Study of VNX001 Compared to Its Individual Components (Lidocaine and Heparin) or Placebo in Subjects With IC/BPS

NCT ID: NCT05737121

Last Updated: 2026-01-22

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE2

Total Enrollment

120 participants

Study Classification

INTERVENTIONAL

Study Start Date

2023-05-22

Study Completion Date

2026-06-30

Brief Summary

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This is a Phase 2, prospective, randomized, double-blind, placebo-controlled, multi-center, single-dose, pharmacodynamic study designed to evaluate the efficacy and safety of the combination product (VNX001) versus placebo and its individual components (heparin sodium and lidocaine hydrochloride (HCl)) for the reduction of bladder pain in patients with interstitial cystitis (IC) / bladder pain syndrome (BPS), Who Have an Episode of Acute Bladder Pain of Moderate to Severe Intensity.

Detailed Description

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This is a Phase 2, prospective, randomized, double-blind, placebo-controlled, multi-center, single-dose, pharmacodynamic study designed to evaluate the efficacy and safety of the combination product (VNX001) versus placebo and its individual components (heparin sodium and lidocaine hydrochloride) for the reduction of bladder pain in patients with IC/BPS, Who Have an Episode of Acute Bladder Pain of Moderate to Severe Intensity. The study will enroll a target of 120 subjects, with a maximum of 180 subjects, across approximately 12 sites in the United States. Each study subject will receive a single dose of VNX001, placebo (alkalinized phosphate buffer), alkalinized lidocaine, or alkalinized heparin by random assignment. The randomization ratio will be 3:1:3:1, respectively. At 24-48-hours post-dose, all subjects will be given the option of requesting a single dose of VNX001.

Conditions

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Interstitial Cystitis Bladder Pain Syndrome

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

IC/BPS patients will be randomly assigned to receive a single dose of one of the following treatments in a ratio of 3:1:3:1:

* VNX001 (n=45): alkalinized buffered lidocaine HCl (200 mg) and heparin sodium (50,000 USPU), administered as an intravesical instillation
* Placebo (n=15): alkalinized buffer, administered as an intravesical instillation
* Lidocaine (n=45): alkalinized buffered lidocaine HCl (200 mg), administered as an intravesical instillation
* Heparin (n=15): alkalinized buffered heparin sodium (50,000 USPU), administered as an intravesical instillation
* At 24-48-hours post-dose, all subjects will be given the option of requesting a single open-label dose of VNX001.
Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators
Double-blind

Study Groups

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VNX001

VNX001 (lidocaine HCl \[200 mg\] and heparin sodium \[50,000 USPU\] in alkalinized buffer), administered as a single dose via intravesical instillation; n=45 (anticipated)

Group Type EXPERIMENTAL

VNX001

Intervention Type DRUG

VNX001 (alkalinized lidocaine HCl and heparin sodium)

Placebo

Alkalinized buffer, administered as a single dose via intravesical instillation; n=15 (anticipated)

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Inactive placebo for VNX001

Lidocaine

Lidocaine HCl (200 mg) in alkalinized buffer, administered as a single dose via intravesical instillation; n=45 (anticipated)

Group Type EXPERIMENTAL

Lidocaine

Intervention Type DRUG

Alkalinized lidocaine hydrochloride

Heparin

Heparin sodium (50,000 USPU) in alkalinized buffer, administered as a single dose via intravesical instillation; n=15 (anticipated)

Group Type EXPERIMENTAL

Heparin

Intervention Type DRUG

Alkalinized heparin sodium

Interventions

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VNX001

VNX001 (alkalinized lidocaine HCl and heparin sodium)

Intervention Type DRUG

Placebo

Inactive placebo for VNX001

Intervention Type DRUG

Lidocaine

Alkalinized lidocaine hydrochloride

Intervention Type DRUG

Heparin

Alkalinized heparin sodium

Intervention Type DRUG

Other Intervention Names

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Alkalinized lidocaine HCl and heparin sodium Placebo (for VNX001) Alkalinized lidocaine HCl Alkalinized heparin sodium

Eligibility Criteria

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Inclusion Criteria

* Be able and willing to give a signed informed consent and to follow study instructions
* Be male or female, ≥ 18 years of age
* Have a history of IC/BPS for at least 9 months prior to the study
* Have a score of ≥ 16 and ≤ 30 on the Pelvic Pain and Urgency/Frequency (PUF) questionnaire, completed at screening
* Have an episode of acute bladder pain of moderate to severe intensity with a minimum score of 5 on the 11-point bladder pain NRS at time of screening and 15 minutes post void immediately prior to study drug administration.
* Have previously received a therapeutic intravesicular anesthetic treatment according to medication history

Exclusion Criteria

* For females, have a positive pregnancy test at screening or be pregnant or lactating
* Males who are sexually active with females and are not willing to commit to an acceptable method of birth control for the duration of the
* Postmenopausal women who, if taking hormone replacement therapy, have not been stabilized on a regimen of hormone replacement therapy within 3 months of screening
* Have a known hypersensitivity to heparin or lidocaine
* Have used any local anesthetic by any route within 48-hours prior to study drug administration, or used a lidocaine patch or lidocaine containing topical compounds within 14 days prior to study drug administration
* Have used a tricyclic antidepressant, or a gamma-aminobutyric acid (GABA) analogue (gabapentin or pregabalin), unless taking a stable dose of the medication for ≥ 3 weeks. The stable dose of gabapentin may not exceed 1,200 mg per day, and the stable dose of pregabalin may not exceed 150 mg per day
* Have used any pain medication within 6 hours prior to study drug administration
* Have used narcotics or medical marijuana ≤ 3 weeks prior to study entry
* Have used prohibited drugs as determined by self-report, positive urine drug screen, or in the opinion of the investigator be under the influence of drugs affecting mentation precluding their ability to follow the study protocol or bias study results
* Have a known abnormal laboratory test value that, in the investigator's judgement, is clinically significant.
* Have a neurogenic bladder or other disorder that, in the opinion of the investigator, may cause neurogenic bladder (including Parkinson's disease, multiple sclerosis, epilepsy, myasthenia gravis, movement disorders, spinal cord damage)
* Have pain or a pain disorder that, in the opinion of the investigator, would make it difficult to discriminate pelvic pain of bladder origin from the other pain
* Have any of the following central nervous system (CNS) conditions that in the opinion of the investigator would impact the subject's study participation due to their ability to follow the study protocol or bias study results, severe diagnosed: major depressive disorder, bipolar disorder, schizophrenia, general anxiety disorder, attention deficit disorder, obsessive compulsive disorder, or other major central nervous system disorder
* Have history of arrhythmias, conduction disturbances, or cardiac disease, or any coexisting medical condition that, in the opinion of the investigator, may be significant or interfere with study procedures or interpretation of study results
* Had anesthetic bladder instillation therapy within 14 days prior to study entry
* Had an in-office cystoscopy within 7 days of study drug administration
* Had dilatation (hydrodistension) of bladder within 3 months of study entry
* Evidence or suspected presence of cancer detected during cystoscopy 7 days prior to or at time of initial screening
* Has received any investigational drug or device within 30 days prior to screening
* Is currently enrolled in another investigational drug or device study
* Is unwilling or unable to abide by the requirements of the study
* Have an actively bleeding lesion or area in the bladder as detected by dipstick urinalysis and investigator assessment, immediately prior to randomization
* Have a history of coagulopathy or taking anticoagulants.
* Are taking any of the following medications, which are inducers of CYP1A2 and/or CYP3A4: Phenytoin, Carbamazepine, St. John's Wort, Phenobarbital, Rifampin
* Have had any of the following:

* Bacterial cystitis within 30 days as demonstrated by a positive urine culture (≥ 105 bacteria per mL)
* History of pelvic irradiation or radiation cystitis
* History or presence of uterine, cervical, pelvic, rectal, ovarian, or vaginal cancer
* History of benign or malignant bladder tumors
* Current chemotherapy
* History or presence of tuberculous cystitis
* History or presence of chemical cystitis, including that due to cyclophosphamide
* History or presence of urinary schistosomiasis
* Bladder or ureteral calculi
* Clinically significant infectious vaginitis
* Currently uncontrolled genital herpes
* History or presence of urethral diverticulum
* Presence of bladder fistulae
* History of ketamine use
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Prevail Infoworks

INDUSTRY

Sponsor Role collaborator

Vaneltix Pharma, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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IC Study LLC

Escondido, California, United States

Site Status SUSPENDED

University of California Los Angeles Center for Women's Pelvic Health

Los Angeles, California, United States

Site Status COMPLETED

The Clark Center for Urogynecology

Newport Beach, California, United States

Site Status RECRUITING

The Continence Center Medical Group, Inc dba Southern California Continence Center

Newport Beach, California, United States

Site Status COMPLETED

University of California San Diego Medical Center

San Diego, California, United States

Site Status RECRUITING

Prestige Medical Group

Tustin, California, United States

Site Status RECRUITING

United Research Institute

Hialeah, Florida, United States

Site Status RECRUITING

Florida Urology Partners

Tampa, Florida, United States

Site Status RECRUITING

Georgia Urology

Cartersville, Georgia, United States

Site Status RECRUITING

Southern Clinical Research Associates LLC

Metairie, Louisiana, United States

Site Status RECRUITING

Bay State Clinical Trials

Watertown, Massachusetts, United States

Site Status RECRUITING

Sheldon Freedman MD LTD

Las Vegas, Nevada, United States

Site Status RECRUITING

Northwell Health

Lake Success, New York, United States

Site Status RECRUITING

The Wake Forest Institute of Regenerative Medicine

Winston-Salem, North Carolina, United States

Site Status RECRUITING

Countries

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United States

Central Contacts

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Vaneltix Pharma, Inc.

Role: CONTACT

732-354-3217

Related Links

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https://engage-24.com/

ENGAGE2024 Study Website

Other Identifiers

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VNX001-111; Engage 2024

Identifier Type: -

Identifier Source: org_study_id

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