A Study of TAK-755 (rADAMTS13) With Little to No Plasma Exchange (PEX) Treatment in Adults With Immune-mediated Thrombotic Thrombocytopenic Purpura (iTTP)

NCT ID: NCT05714969

Last Updated: 2025-09-12

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE2

Total Enrollment

33 participants

Study Classification

INTERVENTIONAL

Study Start Date

2023-03-21

Study Completion Date

2026-06-11

Brief Summary

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This is a study of TAK-755 in adults with immune-mediated thrombotic thrombocytopenic purpura (iTTP). The main aim of this study is to determine the percentage of participants with a clinical (Part 1) or platelet (Part 2) response without plasma exchange during the study. Participants who have an acute attack of iTTP will receive TAK-755 and immunosuppressive therapy during their stay at the hospital until they achieve a clinical response in Part 1 or platelet response in Part 2. Participants will also be treated with TAK-755 for an additional time of up to 6 weeks after the acute phase. In total, participants will stay in the study for approximately 3 months.

Detailed Description

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This study consists of 2-parts. Part 1 is a double-blind, randomized study in which participants were randomized 1:1, in a blinded fashion, into 2 TAK-755 dose groups. Part 1, randomization was stratified based on whether the participant had received pre-study PEX and on the participant's Glasgow Coma Scale. Part 2 is an open-label study in which participants with iTTP experiencing an acute iTTP episode will be enrolled and assigned to a single-arm treatment.

Conditions

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Thrombotic Thrombocytopenic Purpura (TTP)

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors
Part 1 is double-blind, randomization and Part 2 is open-label, single-arm.

Study Groups

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Part 1: TAK-755 Dose 1 in Acute Phase and Dose 2 in Post-acute Phase

TAK-755 Dose 1, IV infusion, in the acute phase until clinical response is achieved. All participants achieving clinical response will receive TAK-755 at Dose 2, for up to 6 weeks during the post-acute phase.

Group Type EXPERIMENTAL

TAK-755

Intervention Type BIOLOGICAL

TAK-755 IV infusion

Part 1: TAK-755 Dose 2 in Both Acute and Post-Acute Phase

TAK-755 Dose 2, IV infusion, in the acute phase until clinical response is achieved. All participants achieving clinical response will receive TAK-755 at Dose 2, for up to 6 weeks during the post-acute phase.

Group Type EXPERIMENTAL

TAK-755

Intervention Type BIOLOGICAL

TAK-755 IV infusion

Part 2: TAK-755 Dose 3 in Acute Phase and Dose 2 in Post-acute Phase

TAK-755 Dose 3, IV infusion, in the acute phase until 48-hour platelet response is achieved. All participants achieving platelet response will receive TAK-755 at Dose 2, 4 times per week for Week 1 and 3 times per week for Week 2 and 3 during the post-acute phase based on investigator judgement as high-risk for developing iTTP recurrence.

Group Type EXPERIMENTAL

TAK-755

Intervention Type BIOLOGICAL

TAK-755 IV infusion

Interventions

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TAK-755

TAK-755 IV infusion

Intervention Type BIOLOGICAL

Other Intervention Names

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rADAMTS13 recombinant ADAMTS13 SHP-655 BAX 930

Eligibility Criteria

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Inclusion Criteria

1. Participant must provide a signed informed consent form. A fully recognized proxy may be used per local laws for participants unable to provide consent.
2. Participant is 18 years or older at time of screening.
3. Participant has been diagnosed with de novo or relapsed iTTP.
4. Participant must be willing to fully comply with study procedures and requirements.
5. Female participants of childbearing potential must present with a negative pregnancy test and agree to employ highly effective birth control measures for duration of study. Sexually active male participants must agree to use an effective method of contraception for the duration of the study.

Exclusion Criteria

1. Participant has received more than 2 pre-study PEX prior to randomization in Part 1 or first dose of investigational product in Part 2.
2. Participant has been diagnosed with cTTP or another cause of thrombotic microangiopathy (TMA).
3. Participant has been exposed to another investigational product within 30 days prior to enrollment or is scheduled to participate in another clinical study involving investigational product or investigational device during the course of the study.
4. Participant has received caplacizumab within 30 days prior to study enrollment.
5. Participant has had a previous iTTP event within the past 30 days.
6. Participant is positive for human immunodeficiency virus (HIV) with unstable disease or cluster of differentiation (CD)4+ count ≤200 cells/mm\^3 within 3 months of screening.
7. Participant has condition of severe immunodeficiency.
8. Participant has a severe systemic acute infection.
9. Participant has another underlying progressive fatal disease and/or life expectancy \<3 months.
10. Participant is identified by the investigator as being unable or unwilling to cooperate with study procedures.
11. Participant is pregnant or lactating.
12. Participant has any condition in which methylprednisolone or other steroid equivalent is contraindicated as per prescribing information.
13. Participant has known life-threatening hypersensitivity reaction, including anaphylaxis, to the parent molecule ADAMTS13, Chinese hamster ovary (CHO) cell proteins, or other constituents of TAK-755.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Takeda Development Center Americas, Inc.

INDUSTRY

Sponsor Role collaborator

Takeda

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Study Director

Role: STUDY_DIRECTOR

Takeda

Locations

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University of Florida - Shands

Gainesville, Florida, United States

Site Status RECRUITING

Massachusetts General Hospital

Boston, Massachusetts, United States

Site Status RECRUITING

Brigham and Women's Hospital

Boston, Massachusetts, United States

Site Status NOT_YET_RECRUITING

Beth Israel Deaconess Medical Center

Boston, Massachusetts, United States

Site Status RECRUITING

University of Minnesota Clinical Research Unit

Minneapolis, Minnesota, United States

Site Status RECRUITING

Rutgers University

New Brunswick, New Jersey, United States

Site Status RECRUITING

Weill Cornell

New York, New York, United States

Site Status RECRUITING

Duke University Medical Center

Durham, North Carolina, United States

Site Status RECRUITING

Leo Jenkins Cancer Center/ECU School of Medicine

Greenville, North Carolina, United States

Site Status RECRUITING

Ohio State University

Columbus, Ohio, United States

Site Status RECRUITING

University of Utah Health Sciences Center

Salt Lake City, Utah, United States

Site Status RECRUITING

Versiti Wisconsin, Inc.

Milwaukee, Wisconsin, United States

Site Status RECRUITING

AKH - Medizinische Universitat Wien

Vienna, , Austria

Site Status NOT_YET_RECRUITING

General Hospital of Thessaloniki "G. Papanikolaou"

Thessaloniki, , Greece

Site Status NOT_YET_RECRUITING

Fondazione IRCCS CA' Granda Ospedale Maggiore Policlinico

Milan, , Italy

Site Status NOT_YET_RECRUITING

Azienda Ospedaliero-Universitaria Citta della Salute e della Scienza di Torino

Torino, , Italy

Site Status NOT_YET_RECRUITING

Hospital Universitario Virgen del Rocio

Seville, Sevilla, Spain

Site Status NOT_YET_RECRUITING

Hospital de Cruces

Barakaldo, Vizcaya, Spain

Site Status NOT_YET_RECRUITING

Hospital General Universitario Gregorio Maranon

Madrid, , Spain

Site Status NOT_YET_RECRUITING

Hospital Universitari i Politecnic La Fe

Valencia, , Spain

Site Status NOT_YET_RECRUITING

University College London Hospital

London, Greater London, United Kingdom

Site Status RECRUITING

Royal Liverpool University Hospital

Liverpool, Merseyside, United Kingdom

Site Status RECRUITING

Countries

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United States Austria Greece Italy Spain United Kingdom

Central Contacts

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Takeda Contact

Role: CONTACT

+1-877-825-3327

Facility Contacts

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Site Contact

Role: primary

352-273-7503

Site Contact

Role: primary

617-724-4000

Site Contact

Role: primary

617-732-5840

Site Contact

Role: primary

617-872-7632

Site Contact

Role: primary

612-625-1529

Site Contact

Role: primary

732-235-6531

Site Contact

Role: primary

646-962-2065

Site Contact

Role: primary

919-684-5350

Site Contact

Role: primary

252-744-3326

Site Contact

Role: primary

614-293-2887

Site Contact

Role: primary

801-213-2076

Site Contact

Role: primary

414-937-6826

Site Contact

Role: primary

+4314040044100

Site Contact

Role: primary

+302313307533

Site Contact

Role: primary

+390255035414

Site Contact

Role: primary

+39116335329

Site Contact

Role: primary

+34955013260

Site Contact

Role: primary

+34946006000

Site Contact

Role: primary

+34914269658

Site Contact

Role: primary

+34961245876

Site Contact

Role: primary

+442034479984

Site Contact

Role: primary

+441517064345

Related Links

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https://clinicaltrials.takeda.com/study-detail/f5b44c8ac8e8425f?idFilter=%5B%22TAK-755-2001%22%5D

To obtain more information on the study, click here/on this link.

Other Identifiers

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2023-507787-39-00

Identifier Type: CTIS

Identifier Source: secondary_id

TAK-755-2001

Identifier Type: -

Identifier Source: org_study_id

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