Telitacicept for the Treatment of Connective Tissue Disease-associated Thrombocytopenia

NCT ID: NCT05998759

Last Updated: 2025-05-06

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE2

Total Enrollment

296 participants

Study Classification

INTERVENTIONAL

Study Start Date

2023-12-02

Study Completion Date

2025-12-31

Brief Summary

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The goal of this clinical trial is to evaluate the efficacy and safety of Telitacicept for the treatment of connective tissue disease-associated thrombocytopenia.

Detailed Description

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In this randomized, double-blind placebo-controlled study, the investigators aim to evaluate the efficacy and safety of Telitacicept for the treatment of connective tissue disease-associated thrombocytopenia. After screening, eligible participants will be randomized at a 1: 1 ratio to receive either subcutaneous Telitacicept 160 mg or placebo once a week for 24 weeks. The background standard therapy is maintained stable during the whole treatment period.

Conditions

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Connective Tissue Diseases Thrombocytopenia

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Telitacicept plus standard therapy

Telitacicept (160mg ih qw for 24 weeks) combined with standard therapy. Standard therapy refers to the following treatment (monotherapy or in combination): glucocorticoid, hydroxychloroquine, and other immunosuppressants (i.e. cyclophosphamide, cyclosporine, mycophenolate mofetil, azathioprine, tacrolimus, methotrexate and leflunomide, et al.).

Group Type EXPERIMENTAL

Telitacicept

Intervention Type BIOLOGICAL

subcutaneous telitacicept 160 mg weekly for 24 weeks.

Placebo plus standard therapy

Placebo combined with standard therapy. Standard therapy refers to the following treatment (monotherapy or in combination): glucocorticoid, hydroxychloroquine, and other immunosuppressants (i.e. cyclophosphamide, cyclosporine, mycophenolate mofetil, azathioprine, tacrolimus, methotrexate and leflunomide, et al.).

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

subcutaneous placebo weekly for 24 weeks.

Interventions

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Telitacicept

subcutaneous telitacicept 160 mg weekly for 24 weeks.

Intervention Type BIOLOGICAL

Placebo

subcutaneous placebo weekly for 24 weeks.

Intervention Type DRUG

Other Intervention Names

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recombinant human B lymphocyte stimulating factor receptor-Fc fusion protein Recombinant Human B Lymphocyte(RC18) Tai'ai® Placebo control control

Eligibility Criteria

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Inclusion Criteria

* Subjects who have been diagnosed with connective tissue disease (CTD)-associated thrombocytopenia. And CTD includes primary Sjögren syndrome (according to the 2002 American College of Rheumatology (ACR)/ European League against Rheumatism (EULAR) classification criteria), systemic lupus erythematosus (SLE, according to the 1997 or the 2009 ACR classification criteria), and undifferentiated connective tissue disease (according to the 1999 international classification criteria)
* Refractory thrombocytopenia defined as:

Either: Failure to maintain sustained remission after treatment by glucocorticoid and at least one immunosuppressant (i.e. cyclophosphamide, cyclosporine, mycophenolate mofetil, azathioprine, tacrolimus, methotrexate, leflunomide and hydroxychloroquine, et al.) Or: Relapse during oral glucocorticoid tapering or after withdrawal

* 50×10\^9/L\>PLT
* anti-nuclear antibody (ANA) positive (≥1:80, any karyotype) detected in the laboratory of each research center
* Standard therapy should be maintained stable for at least 14 days prior to the first dose of the experimental drug or placebo. Standard therapy refers to the following treatment (monotherapy or in combination): glucocorticoid, hydroxychloroquine, and other immunosuppressants (i.e. cyclophosphamide, cyclosporine, mycophenolate mofetil, azathioprine, tacrolimus, methotrexate and leflunomide, et al.)
* Signed informed consent form, willing or able to participate in all required study evaluations and procedures

Exclusion Criteria

* Vital organ lethal bleeding (including but not limited to central nervous system bleeding, digestive tract bleeding) at screening, or intracranial bleeding 6 months prior to screening
* Antiphospholipid syndrome, thrombotic thrombocytopenia purpura, hemolytic uremic syndrome, or thrombocytopenia secondary to other causes (such as sepsis, Epstein-Barr virus infection, cytomegalovirus infection, Corona Virus Disease-19 (COVID-19) infection, drugs, etc.)
* Hematopoietic system disorders, such as myelodysplastic syndrome, paroxysmal sleep hemoglobinuria, aplastic anemia, leukemia, lymphoma, myelofibrosis and so on
* Severe cardiovascular system disease, including: unstable or uncontrollable disease or condition affecting the function of the heart (such as angina pectoris, congestive heart failure, uncontrolled hypertension or arrhythmia)
* Arteriovenous thromboembolism events
* Receiving antiplatelet or anticoagulant therapy at screening
* Clinically significant electrocardiogram changes
* corrected Q-T interval (QTc)\>450ms for male, QTc\>470ms for female
* Severe pulmonary disease, including: unstable or uncontrollable disease or condition affecting respiratory function \[e.g., diffuse alveolar hemorrhage, severe pulmonary hypertension, severe pulmonary interstitial disease (peripheral blood oxygen saturation \<92% at rest without oxygen, or forced vital capacity (FVC)\<50%, or carbon monoxide diffusing capacity (DLCO)\<50%)\]
* Severe kidney disease, including: severe lupus nephritis (urinary protein \> 6 g/24 hours or endogenous creatinine clearance \< 30 ml /min) 8 weeks prior to randomization, active nephritis requiring current protocol disallowed drugs, severe renal insufficiency requiring hemodialysis or prednisone ≥100mg/ day (or equivalent) for ≥14 days
* SLE or non-SLE related central nervous system disease (including epilepsy, psychosis, organic encephalopathy syndrome, cerebrovascular accident, encephalitis, central nervous system vasculitis) 8 weeks prior to randomization
* Active hepatitis, a history of severe liver disease. Subjects positive for hepatitis B surface antigen (HBsAg) or antibodies to hepatitis C virus are excluded. As for subjects with antibodies to hepatitis B core antigen (HBcAb), further hepatitis B virus (HBV)-DNA should be tested. If HBV-DNA is negative, subjects could be enrolled; otherwise, subjects should be excluded
* Abnormal laboratory results (including but not limited to: alanine aminotransferase (ALT) or aspertate aminotransferase (AST)≥3×ULN (upper limit of normal), white blood cell count \<1.5×10\^9/L)
* Subjects with known active infections (e.g., shingles, COVID-19, HIV, active tuberculosis, etc.), and active or recurrent gastrointestinal ulcers
* Pregnant or lactating women, and subjects with a during plan during the trial
* Allergic reaction: history of allergic reactions to human biological products
* Treatment with B cell-targeting agents such as Rituximab or Epratuzumab or Belimumab six months prior to randomization
* Treatment with tumor necrosis factor (TNF) inhibitors or TNF-receptor blockers six months prior to randomization
* Participating in clinical trial 28 days or 5 drug half-lives of the investigational agents prior to randomization
* Received live vaccine 28 days prior to randomization
* Treatment with unstable dosage of thrombopoietin receptor agonists such as Eltrombopag or Romiplostim 14 days prior to randomization
* Subjects with depression or suicidal thoughts
* Previous treatment with telitacicept
* B cell targeting drug therapy is not tolerated or responsive
* Investigator considers candidates not appropriating for the study
Minimum Eligible Age

18 Years

Maximum Eligible Age

75 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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The First Affiliated Hospital of Anhui Medical University

OTHER

Sponsor Role collaborator

The First Affiliated Hospital of China University of Science and Technology (Anhui Provincial)

OTHER

Sponsor Role collaborator

Peking University People's Hospital

OTHER

Sponsor Role collaborator

Peking University Third Hospital

OTHER

Sponsor Role collaborator

First Affiliated Hospital, Sun Yat-Sen University

OTHER

Sponsor Role collaborator

Guangdong Provincial People's Hospital

OTHER

Sponsor Role collaborator

The First Affiliated Hospital of Zhengzhou University

OTHER

Sponsor Role collaborator

Union Hospital, Tongji Medical College, Huazhong University of Science and Technology

OTHER

Sponsor Role collaborator

Second Xiangya Hospital of Central South University

OTHER

Sponsor Role collaborator

Xiangya Hospital of Central South University

OTHER

Sponsor Role collaborator

The Affiliated Hospital of Inner Mongolia Medical University

OTHER

Sponsor Role collaborator

First Hospital of China Medical University

OTHER

Sponsor Role collaborator

Shandong Provincial Hospital

OTHER_GOV

Sponsor Role collaborator

Changhai Hospital

OTHER

Sponsor Role collaborator

RenJi Hospital

OTHER

Sponsor Role collaborator

Shanxi Bethune Hospital

OTHER

Sponsor Role collaborator

West China Hospital

OTHER

Sponsor Role collaborator

Institute of Hematology & Blood Diseases Hospital, China

OTHER

Sponsor Role collaborator

Tianjin First Central Hospital

OTHER

Sponsor Role collaborator

Tianjin Medical University General Hospital

OTHER

Sponsor Role collaborator

People's Hospital of Xinjiang Uygur Autonomous Region

OTHER

Sponsor Role collaborator

The First People's Hospital of Yunnan

OTHER

Sponsor Role collaborator

Beijing Hospital

OTHER_GOV

Sponsor Role lead

Responsible Party

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Yongjing Cheng

Professor

Responsibility Role PRINCIPAL_INVESTIGATOR

Principal Investigators

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Xuan Zhang, MD.

Role: STUDY_CHAIR

Beijing Hospital

Yongjing Cheng, MD.

Role: STUDY_CHAIR

Beijing Hospital

Shengqian Xu, MD.

Role: PRINCIPAL_INVESTIGATOR

The First Affiliated Hospital of Anhui Medical Hospital

Zhu Chen, MD.

Role: PRINCIPAL_INVESTIGATOR

The First Affiliated Hospital of China University of Science and Technology (Anhui Provincial)

Jing He, MD.

Role: PRINCIPAL_INVESTIGATOR

Peking University People's Hospital

Rong Mu, MD.

Role: PRINCIPAL_INVESTIGATOR

Peking University Third Hospital

Niansheng Yang, MD.

Role: PRINCIPAL_INVESTIGATOR

First Affiliated Hospital, Sun Yat-Sen University

Yang Li, MD.

Role: PRINCIPAL_INVESTIGATOR

Guangdong Provincial People's Hospital

Guanmin Gao, MD.

Role: PRINCIPAL_INVESTIGATOR

The First Affiliated Hospital of Zhengzhou University

Anbin Huang, MD.

Role: PRINCIPAL_INVESTIGATOR

Union Hospital, Tongji Medical College, Huazhong University of Science and Technology

Fen Li, MD.

Role: PRINCIPAL_INVESTIGATOR

Second Xiangya Hospital of Central South University

Hui Luo, MD.

Role: PRINCIPAL_INVESTIGATOR

Xiangya Hospital of Central South University

Hongbin Li, MD.

Role: PRINCIPAL_INVESTIGATOR

The Affiliated Hospital of Inner Mongolia Medical University

Pinting Yang, MD.

Role: PRINCIPAL_INVESTIGATOR

First Hospital of China Medical University

Hongsheng Sun, MD.

Role: PRINCIPAL_INVESTIGATOR

Shandong Provincial Hospital

Dongbao Zhao, MD.

Role: PRINCIPAL_INVESTIGATOR

Changhai Hospital

Sheng Chen, MD.

Role: PRINCIPAL_INVESTIGATOR

RenJi Hospital

Liyun Zhang, MD.

Role: PRINCIPAL_INVESTIGATOR

Shanxi Bethune Hospital

Qibing Xie, MD.

Role: PRINCIPAL_INVESTIGATOR

West China Hospital

Lei Zhang, MD.

Role: PRINCIPAL_INVESTIGATOR

Institute of Hematology & Blood Diseases Hospital, China

Wufang Qi, MD.

Role: PRINCIPAL_INVESTIGATOR

Tianjin First Central Hospital

Wei Wei, MD.

Role: PRINCIPAL_INVESTIGATOR

Tianjin Medical University General Hospital

Lijun Wu, MD.

Role: PRINCIPAL_INVESTIGATOR

People's Hospital of Xinjiang Uygur Autonomous Region

Qin Li, MD.

Role: PRINCIPAL_INVESTIGATOR

The First People's Hospital of Yunnan

Locations

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The First Affiliated Hospital of Anhui Medical College

Hefei, Anhui, China

Site Status RECRUITING

The First Affiliated Hospital of China University of Science and Technology (Anhui Provincial)

Hefei, Anhui, China

Site Status RECRUITING

Beijing Hospital

Beijing, Beijing Municipality, China

Site Status RECRUITING

Peking University People's Hospital

Beijing, Beijing Municipality, China

Site Status RECRUITING

Peking University Third Hospital

Beijing, Beijing Municipality, China

Site Status RECRUITING

First Affiliated Hospital, Sun Yat-Sen University

Guangzhou, Guangdong, China

Site Status RECRUITING

Guangdong Provincial People's Hospital

Guangzhou, Guangdong, China

Site Status RECRUITING

The First Affiliated Hospital of Zhengzhou University

Zhengzhou, Henan, China

Site Status RECRUITING

Wuhan Union Hospital, China

Wuhan, Hubei, China

Site Status RECRUITING

Second Xiangya Hospital of Central South University

Changsha, Hunan, China

Site Status RECRUITING

Xiangya Hospital of Central South University

Changsha, Hunan, China

Site Status RECRUITING

The Affiliated Hospital of Inner Mongolia Medical University

Hohhot, Inner Mongolia, China

Site Status RECRUITING

First Hospital of China Medical University

Shenyang, Liaoning, China

Site Status RECRUITING

Shandong Provincial Hospital

Jinan, Shandong, China

Site Status RECRUITING

Changhai Hospital

Shanghai, Shanghai Municipality, China

Site Status RECRUITING

RenJi Hospital

Shanghai, Shanghai Municipality, China

Site Status RECRUITING

Shanxi Bethune Hospital

Taiyuan, Shanxi, China

Site Status RECRUITING

West China Hospital

Chengdu, Sichuan, China

Site Status RECRUITING

Institute of Hematology & Blood Diseases Hospital

Tianjin, Tianjin Municipality, China

Site Status RECRUITING

Tianjin First Central Hospital

Tianjin, Tianjin Municipality, China

Site Status RECRUITING

Tianjin Medical University General Hospital

Tianjin, Tianjin Municipality, China

Site Status RECRUITING

People's Hospital of Xinjiang Uygur Autonomous Region

Ürümqi, Xinjiang Uygur Autonomous Region, China

Site Status RECRUITING

The First People's Hospital of Yunnan

Kunming, Yunnan, China

Site Status RECRUITING

Countries

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China

Central Contacts

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Xuan Zhang, MD.

Role: CONTACT

+86-01085136736

Yongjing Cheng, MD.

Role: CONTACT

+86-01085136736

Facility Contacts

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Shengqian Xu, MD.

Role: primary

Zhu Chen, MD.

Role: primary

Xuan Zhang, MD.

Role: primary

Yongjing Cheng, MD.

Role: backup

Jing He, MD.

Role: primary

Rong Mu

Role: primary

Niansheng Yang, MD.

Role: primary

Yang Li, MD.

Role: primary

Guanmin Gao, MD.

Role: primary

Anbin Huang, MD.

Role: primary

Fen Li, MD.

Role: primary

Hui Luo, MD.

Role: primary

Hongbin Li, MD.

Role: primary

Pinting Yang, MD.

Role: primary

Hongsheng Sun, MD.

Role: primary

Dongbao Zhao, MD.

Role: primary

Sheng Chen, MD.

Role: primary

Liyun Zhang, MD.

Role: primary

Qibing Xie, MD.

Role: primary

Lei Zhang, MD.

Role: primary

Wufang Qi, MD.

Role: primary

Wei Wei, MD.

Role: primary

Lijun Wu, MD.

Role: primary

Qin Li, MD.

Role: primary

Other Identifiers

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BJ-2021-235

Identifier Type: OTHER_GRANT

Identifier Source: secondary_id

RCTAIIRCTD001

Identifier Type: OTHER_GRANT

Identifier Source: secondary_id

BJ-2021-235

Identifier Type: -

Identifier Source: org_study_id

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