A Study to Evaluate Safety and Efficacy of KM-819 in Healthy Adults and Participants with Parkinson's Disease

NCT ID: NCT05670782

Last Updated: 2025-03-05

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

ACTIVE_NOT_RECRUITING

Clinical Phase

PHASE2

Total Enrollment

314 participants

Study Classification

INTERVENTIONAL

Study Start Date

2022-07-19

Study Completion Date

2025-11-13

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

The goal of this study is to test KM-819 in halting or slowing the progression of Parkinson's disease.

The study evaluates the safety and tolerability of multiple ascending doses of KM-819 in healthy older adults and participants with Parkinson's disease.

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

The overall study will consist of three parts (Part 1a, Part 1b and Part 2).

Part 1 of this study will evaluate the safety, tolerability and plasma PK of multiple ascending doses (MAD) of KM-819 in healthy older adults (Part 1a) and participants with Parkinson's disease (Part 1b).

* Part 1a is a randomized, double-blind, Multiple Ascending Dose (MAD) study in healthy older adults that will include 3 cohorts.
* Part 1b is a randomized, double-blind, MAD study in participants with Parkinson's disease that will include 3 cohorts.

Part 2 of the study is a randomized, double-blind, multiple dose study in participants with Parkinson's disease that will include 2 cohorts. It is designed to test the safety, tolerability, plasma PK and pharmacodynamic effects of KM-819 in participants with Parkinson's disease. The study will also assess the degree to which those treated with KM-819 will experience gains in overall daily function within the context of improved Parkinson's disease motor and non-motor symptoms in comparison to placebo. Participants will be randomized to receive KM-819 or matching placebo at doses to be determined based on the findings from Part 1 in a 2:1 ratio.

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

Parkinson Disease

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Allocation Method

RANDOMIZED

Intervention Model

SEQUENTIAL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators
Double-Blinded

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

Part 1a: Cohort 1.1a Dose 400 mg

Healthy older adult participants will receive oral 400 mg dose of KM-819 or matching placebo once-daily for 7 days, after fasting for 2 hours prior to administration of study intervention and will be required to fast for 1 hour after administration of study intervention.

Group Type EXPERIMENTAL

KM-819

Intervention Type DRUG

Participants will receive oral doses of KM-819 once-daily

Placebo

Intervention Type DRUG

Participants will receive matching placebo once-daily

Part 1a: Cohort 1.2a Dose 600 mg

Healthy older adult participants will receive oral 600 mg dose of KM-819 or matching placebo once-daily for 7 days, after fasting for 2 hours prior to administration of study intervention and will be required to fast for 1 hour after administration of study intervention.

Group Type EXPERIMENTAL

KM-819

Intervention Type DRUG

Participants will receive oral doses of KM-819 once-daily

Placebo

Intervention Type DRUG

Participants will receive matching placebo once-daily

Part 1a: Cohort 1.3a Dose 800 mg

Healthy older adult participants will receive oral 800 mg dose of KM-819 or matching placebo once-daily for 7 days, after fasting for 2 hours prior to administration of study intervention and will be required to fast for 1 hour after administration of study intervention.

Group Type EXPERIMENTAL

KM-819

Intervention Type DRUG

Participants will receive oral doses of KM-819 once-daily

Placebo

Intervention Type DRUG

Participants will receive matching placebo once-daily

Part 1b: Cohort 1.1b Dose 200 mg

Participants with Parkinson's disease will receive oral 200 mg dose of KM-819 or matching placebo once-daily for 7 days, after fasting for 2 hours prior to administration of study intervention and will be required to fast for 1 hour after administration of study intervention.

Group Type EXPERIMENTAL

KM-819

Intervention Type DRUG

Participants will receive oral doses of KM-819 once-daily

Placebo

Intervention Type DRUG

Participants will receive matching placebo once-daily

Part 1b: Cohort 1.2b Dose 400 mg

Participants with Parkinson's disease will receive oral 400 mg dose of KM-819 or matching placebo once-daily for 7 days, after fasting for 2 hours prior to administration of study intervention and will be required to fast for 1 hour after administration of study intervention.

Group Type EXPERIMENTAL

KM-819

Intervention Type DRUG

Participants will receive oral doses of KM-819 once-daily

Placebo

Intervention Type DRUG

Participants will receive matching placebo once-daily

Part 1b: Cohort 1.3b Dose 600 mg

Participants with Parkinson's disease will receive oral 600 mg dose of KM-819 or matching placebo once-daily for 7 days, after fasting for 2 hours prior to administration of study intervention and will be required to fast for 1 hour after administration of study intervention.

Group Type EXPERIMENTAL

KM-819

Intervention Type DRUG

Participants will receive oral doses of KM-819 once-daily

Placebo

Intervention Type DRUG

Participants will receive matching placebo once-daily

Part 2: Cohort 2.1 Dose X

Participants with Parkinson's disease will receive oral doses of KM-819 (dose to be determined based on the findings from Part 1) or matching placebo once-daily for 730 days and will be allowed to take study intervention with or without fasting.

Group Type EXPERIMENTAL

KM-819

Intervention Type DRUG

Participants will receive oral doses of KM-819 once-daily

Placebo

Intervention Type DRUG

Participants will receive matching placebo once-daily

Part 2: Cohort 2.2 Dose Y

Participants with Parkinson's disease will receive oral doses of KM-819 (dose to be determined based on the findings from Part 1) or matching placebo once-daily for 730 days and will be allowed to take study intervention with or without fasting.

Group Type EXPERIMENTAL

KM-819

Intervention Type DRUG

Participants will receive oral doses of KM-819 once-daily

Placebo

Intervention Type DRUG

Participants will receive matching placebo once-daily

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

KM-819

Participants will receive oral doses of KM-819 once-daily

Intervention Type DRUG

Placebo

Participants will receive matching placebo once-daily

Intervention Type DRUG

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

* Participant is a healthy volunteer or has a clinical diagnosis of idiopathic Parkinson's disease.
* Participant is on a stable dose of medications to treat Parkinson's disease at least 8 weeks prior to randomization
* Presence of idiopathic Parkinson's disease Hoehn and Yahr Stage ≤ 4
* History or current use of dopamine/dopaminergic drugs, levodopa with decarboxylase inhibitor or dopaminergic agonists, with a stable dosage for at least 30 days prior to Screening
* Body mass index (BMI) within the range 18.5 to 35 kg/m2 (inclusive)
* A male participant must not have a pregnant or breastfeeding partner and must agree to use a highly effective contraception method starting from Screening and refrain from donating sperm during this period
* A female participant is eligible to participate if she is not pregnant, not breastfeeding

Exclusion Criteria

* Diagnosis of neurodegenerative disorder other than idiopathic Parkinson's disease resulting in dementia or atypical parkinsonism
* Life-time history of a suicide attempt as determined by the Columbia-Suicide Severity Rating Scale (C-SSRS) for the Screening
* Evidence of cognitive decline defined by the Montreal Cognitive Assessment (MoCA) score ≤25 for healthy normal population (Part 1a) and ≤21 for the patient population (Part 1b and Part 2)
* History of levodopa-induced motor fluctuations or dyskinesia
* Prior surgical treatment for Parkinson's disease
* Clinically significant brain abnormalities on or contraindication to a structural magnetic resonance imaging (MRI)
* Significant respiratory, hepatic, renal, gastrointestinal, endocrinological, hematological, pancreatic, musculoskeletal, genitourinary, immunological or dermatological disorders.
Minimum Eligible Age

40 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

Yes

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

Parexel

INDUSTRY

Sponsor Role collaborator

FAScinate Therapeutics Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Responsibility Role SPONSOR

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

Parexel Early Phase Clinical Unit

Glendale, California, United States

Site Status

University California San Diego Medical Center

San Diego, California, United States

Site Status

Quest Research Institute, Rose Cancer Center

Royal Oak, Michigan, United States

Site Status

Countries

Review the countries where the study has at least one active or historical site.

United States

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

FASCP-819-K103

Identifier Type: -

Identifier Source: org_study_id

More Related Trials

Additional clinical trials that may be relevant based on similarity analysis.