A 12-week Randomized Study to Evaluate Oral Istradefylline in Subjects With Moderate to Severe Parkinson's Disease

NCT ID: NCT01968031

Last Updated: 2024-04-25

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

613 participants

Study Classification

INTERVENTIONAL

Study Start Date

2013-10-31

Study Completion Date

2016-10-31

Brief Summary

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This is a study to assess the efficacy and safety of oral Istradefylline (KW-6002) in patients with moderate to severe Parkinson's Disease. While on this study, participants will continue to take their usual, prescribed, stable regimen of Levodopa/Carbidopa or Levodopa/Benserazide therapy plus adjunct Parkinson's medications. Patients will be randomized 1:1:1 to receive either Istradefylline 20 mg per day, or Istradefylline 40 mg per day or an equivalent placebo. Patients will be treated for a 12 week period to demonstrate the effectiveness of Istradefylline in improving Parkinson's disease symptoms (referred to as improvement in patient OFF time) and that Istradefylline has an acceptable safety profile in this group.

Detailed Description

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Conditions

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Idiopathic Parkinson's Disease

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Istradefylline 20 mg/day

Istradefylline 20 mg and placebo to match istradefylline 40 mg:

A daily, oral, double-blind treatment dose of both tablets will be taken in the morning for 12 weeks.

Group Type EXPERIMENTAL

Istradefylline 20 mg

Intervention Type DRUG

Istradefylline 20 mg and placebo

Placebo

Intervention Type DRUG

Placebo

Istradefylline 40 mg/day

Istradefylline 40 mg and placebo to match istradefylline 20 mg:

A daily, oral, double-blind treatment dose of both tablets will be taken in the morning for 12 weeks.

Group Type EXPERIMENTAL

Istradefylline 40 mg

Intervention Type DRUG

Istradefylline 40 mg and placebo

Placebo

Intervention Type DRUG

Placebo

Placebo

Placebo to match istradefylline 20 mg and placebo to match istradefylline 40 mg:

A daily, oral, double-blind treatment dose of both tablets will be taken in the morning for 12 weeks.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Placebo

Interventions

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Istradefylline 40 mg

Istradefylline 40 mg and placebo

Intervention Type DRUG

Istradefylline 20 mg

Istradefylline 20 mg and placebo

Intervention Type DRUG

Placebo

Placebo

Intervention Type DRUG

Other Intervention Names

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KW-6002 KW-6002

Eligibility Criteria

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Inclusion Criteria

* 30 years of age or older.
* UK Parkinson's Disease Society (UKPDS) brain bank criteria (Step 1 and 2) for PD
* PD Stages 2-4 in the ON state for Modified Hoehn and Yahr Scale.
* On levodopa therapy for at least 1 year with beneficial clinical response at the baseline visit
* Taking at least 400mg levodopa combination daily and on stable regimen of any other anti-Parkinsonian drugs (MAO-B, COMT, DA) for at least 2 weeks prior to randomization
* Stable dopaminergic regimen for at least 4 weeks immediately prior to randomization
* Documented end-of-dose wearing-off and levodopa-induced dyskinesia
* Have an average of two hours of OFF time per day

Exclusion Criteria

* Subjects on apomorphine and/or dopamine receptor antagonists or direct gastrointestinal levodopa infusion.
* Subject who have had neurosurgical operation for PD
* Subjects taking A2a antagonist, potent CYP3A4 inhibitors, potent CYP34A inducers
* Subjects who smoke \> 5 cigarettes/day
Minimum Eligible Age

30 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Kyowa Hakko Kirin Pharma, Inc.

INDUSTRY

Sponsor Role collaborator

Kyowa Kirin Co., Ltd.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Kyowa Hakko Kirin Pharma, Inc.

Role: STUDY_CHAIR

Kyowa Hakko Kirin Pharma, Inc.

Locations

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Kyowa PD Site

Phoenix, Arizona, United States

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Kyowa PD Site

Sun City, Arizona, United States

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Kyowa PD Site

Tucson, Arizona, United States

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Kyowa PD Site

Fountain Valley, California, United States

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Kyowa PD Site

Irvine, California, United States

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Kyowa PD Site

Los Angeles, California, United States

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Kyowa PD Site

Oxnard, California, United States

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Kyowa PD Site

Pasadena, California, United States

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Kyowa PD Site

Reseda, California, United States

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Kyowa PD Site

Sunnyvale, California, United States

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Kyowa PD Site

Torrance, California, United States

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Kyowa PD Site

Englewood, Colorado, United States

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Kyowa PD Site

Danbury, Connecticut, United States

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Kyowa PD Site

Boca Raton, Florida, United States

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Kyowa PD Site

Jacksonville, Florida, United States

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Kyowa PD Site

Panama City, Florida, United States

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Kyowa PD Site

Port Charlotte, Florida, United States

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Kyowa PD Site

Tampa, Florida, United States

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Kyowa PD Site

Atlanta, Georgia, United States

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Kyowa PD Site

Augusta, Georgia, United States

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Kyowa PD Site

Chicago, Illinois, United States

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Chicago, Illinois, United States

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Kyowa PD Site

Des Moines, Iowa, United States

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Kyowa PD Site

Kansas City, Kansas, United States

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Baltimore, Maryland, United States

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Kyowa PD Site

Boston, Massachusetts, United States

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Kyowa PD Site

West Bloomfield, Michigan, United States

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Kyowa PD Site

Minneapolis, Minnesota, United States

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Kyowa PD Site

St Louis, Missouri, United States

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Kyowa PD Site

Albany, New York, United States

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New York, New York, United States

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New York, New York, United States

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Kyowa PD Site

Asheville, North Carolina, United States

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Durham, North Carolina, United States

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Kyowa PD Site

Cincinnati, Ohio, United States

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Cleveland, Ohio, United States

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Toledo, Ohio, United States

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Philadelphia, Pennsylvania, United States

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Charleston, South Carolina, United States

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Dallas, Texas, United States

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Houston, Texas, United States

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Calgary, Alberta, Canada

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Kingston, Ontario, Canada

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Toronto, Ontario, Canada

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Kyowa PD Site

Gatineau, Quebec, Canada

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Québec, Quebec, Canada

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Kyowa PD Site

Brno, , Czechia

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Kyowa PD Site

Litomyšl, , Czechia

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Kyowa PD Site

Olomouc, , Czechia

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Kyowa PD Site

Prague, , Czechia

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Kyowa PD Site

Prague, , Czechia

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Kyowa PD Site

Prague, , Czechia

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Kyowa PD Site

Beelitz-Heilstätten, , Germany

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Kyowa PD Site

Berlin, , Germany

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Kyowa PD Site

Berlin, , Germany

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Kyowa PD Site

Bremerhaven, , Germany

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Kyowa PD Site

Dresden, , Germany

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Kyowa PD Site

Göttingen, , Germany

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Kyowa PD Site

Haag, , Germany

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Kyowa PD Site

Kassel, , Germany

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Kyowa PD Site

Marburg, , Germany

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Kyowa PD Site

Munich, , Germany

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Kyowa PD Site

Tübingen, , Germany

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Kyowa PD Site

Ulm, , Germany

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Kyowa PD Site

Haifa, , Israel

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Kyowa PD Site

Jerusalem, , Israel

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Kyowa PD Site

Petach Tiqva, , Israel

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Kyowa PD Site

Ramat Gan, , Israel

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Kyowa PD Site

Tel Aviv, , Israel

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Kyowa PD Site

Cassino, , Italy

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Kyowa PD Site

Chieti, , Italy

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Kyowa PD Site

Grosseto, , Italy

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Kyowa PD Site

Pavia, , Italy

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Pisa, , Italy

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Kyowa PD Site

Rome, , Italy

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Kyowa PD Site

Rome, , Italy

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Kyowa PD Site

Venezia, , Italy

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Kyowa PD Site

Vicenza, , Italy

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Kyowa PD Site

Bydgoszcz, , Poland

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Kyowa PD Site

Kielce, , Poland

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Kyowa PD Site

Krakow, , Poland

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Kyowa PD Site

Lublin, , Poland

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Kyowa PD Site

Poznan, , Poland

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Kyowa PD Site

Warsaw, , Poland

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Kyowa PD Site

Warsaw, , Poland

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Kyowa PD Site 1

Belgrade, , Serbia

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Kyowa PD Site 2

Belgrade, , Serbia

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Kyowa PD Site 4

Belgrade, , Serbia

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Kyowa PD Site

Novi Sad, , Serbia

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Countries

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United States Canada Czechia Germany Israel Italy Poland Serbia

Related Links

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https://foxtrialfinder.michaeljfox.org/trial/3633/

Fox Trial Finder is a clinical trial matching tool that helps a Parkinson's patient connect with research sites. Volunteers who sign up will receive a list of trials in their area.

Other Identifiers

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2013-002254-70

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

6002-014

Identifier Type: -

Identifier Source: org_study_id

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