A Study of CYP-001 in Combination With Corticosteroids in Adults With High-risk aGvHD

NCT ID: NCT05643638

Last Updated: 2025-12-05

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE2

Total Enrollment

60 participants

Study Classification

INTERVENTIONAL

Study Start Date

2024-03-04

Study Completion Date

2027-12-31

Brief Summary

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This study is a prospective randomized placebo-controlled phase 2 study to compare CYP-001 plus corticosteroids (CS) to placebo plus CS in allogeneic hematologic stem cell transplant recipients with HR-aGvHD. Severity of GvHD will be assessed at screening and throughout the study using Mount Sinai Acute GvHD International Consortium (MAGIC) guidelines. Eligible subjects will be randomized to receive either CYP-001 IV infusion on Days 0 and 4 or placebo on the same days. All subjects will receive ongoing CS therapy as appropriate per institutional guidelines. Subjects will have study visits up to Day 100 during the Primary Evaluation Period. During the Follow-Up Period, subjects will have study visits up to 24 months.

Detailed Description

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Conditions

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Graft Versus Host Disease, Acute

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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CYP-001 plus corticosteroids

Group Type EXPERIMENTAL

CYP-001: Cymerus induced pluripotent stem cell (iPSC)-derived mesenchymal stem cells (MSCs)

Intervention Type BIOLOGICAL

Cymerus MSCs are derived from iPSCs using the proprietary Cymerus platform technology.

Corticosteroids

Intervention Type DRUG

All enrolled subjects in this trial must receive corticosteroids at a minimum dose of oral prednisone 2 mg/kg/day (or methylprednisolone 1.6 mg/kg/day IV) as therapy for aGvHD for at least for 72 hours post enrollment.

Placebo plus corticosteroids

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type BIOLOGICAL

The placebo product is identical to CYP-001, except that it contains no active agent

Corticosteroids

Intervention Type DRUG

All enrolled subjects in this trial must receive corticosteroids at a minimum dose of oral prednisone 2 mg/kg/day (or methylprednisolone 1.6 mg/kg/day IV) as therapy for aGvHD for at least for 72 hours post enrollment.

Interventions

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CYP-001: Cymerus induced pluripotent stem cell (iPSC)-derived mesenchymal stem cells (MSCs)

Cymerus MSCs are derived from iPSCs using the proprietary Cymerus platform technology.

Intervention Type BIOLOGICAL

Placebo

The placebo product is identical to CYP-001, except that it contains no active agent

Intervention Type BIOLOGICAL

Corticosteroids

All enrolled subjects in this trial must receive corticosteroids at a minimum dose of oral prednisone 2 mg/kg/day (or methylprednisolone 1.6 mg/kg/day IV) as therapy for aGvHD for at least for 72 hours post enrollment.

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Undergone allogeneic hematopoietic stem cell transplant (HSCT)
* Clinically diagnosed with acute GvHD requiring systemic therapy with corticosteroids.
* HR-aGvHD must meet one of the following clinical features within 72 hours prior to randomization: (a) high-risk as per Refined Minnesota Criteria; OR (b) One of the following: (i) isolated stage 2 involvement of the lower GI tract; (ii) Stage 1 lower GI tract disease with skin involvement
* Evidence of myeloid engraftment post allogeneic HSCT
* Life expectancy of at least one month

Exclusion Criteria

* Received any systemic treatment for aGvHD other than corticosteroids +/- calcineurin inhibitors
* Chronic GvHD or overlap syndrome with both acute and chronic features of GvHD
* Relapsed primary malignancy since
* received more than one allogeneic HSCT
* Clinically significant respiratory, renal or cardiac disease
* Cholestatic disorders or sinusoidal obstructive syndrome/veno-occlusive disease of the liver
* Any active uncontrolled infection requiring treatment and likely to impact on the ability of the subject to participate in the trial.
* Known infection with CMV, EBV, HHV-6, HBV, HCV, HIV or Tuberculosis. If the treatment for CMV, EBV, HHV-6, HBV, HCV has commenced the subject is eligible.
* Known sensitivity to dimethylsulfoxide (DMSO) or any other component of CYP-001.
* Received any investigational treatment agent within 30 days or within 5 half-lives of Screening, whichever is greater.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Cynata Therapeutics Limited

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Jolanta Airey, MD

Role: STUDY_DIRECTOR

Cynata Therapeutics Limited

Locations

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Banner MD Anderson

Phoenix, Arizona, United States

Site Status COMPLETED

Mayo Clinic Hospital

Phoenix, Arizona, United States

Site Status RECRUITING

University of Arkansas Medical Center

Little Rock, Arkansas, United States

Site Status RECRUITING

Mayo Clinic Hospital

Jacksonville, Florida, United States

Site Status RECRUITING

Memorial healthcare System

Pembroke Pines, Florida, United States

Site Status RECRUITING

BMT Group of Georgia

Atlanta, Georgia, United States

Site Status RECRUITING

Northwestern University

Evanston, Illinois, United States

Site Status RECRUITING

Karmanos Cancer Institute

Detroit, Michigan, United States

Site Status RECRUITING

University Of Nebrasaka Medical Center

Omaha, Nebraska, United States

Site Status RECRUITING

Weill Cornell Medicine - New York Presbyterian Hospital

New York, New York, United States

Site Status COMPLETED

Cleveland Clinic

Cleveland, Ohio, United States

Site Status RECRUITING

Penn State Health

Hershey, Pennsylvania, United States

Site Status RECRUITING

University of Utah

Salt Lake City, Utah, United States

Site Status RECRUITING

Royal Prince Alfred Hospital

Sydney, New South Wales, Australia

Site Status COMPLETED

Westmead Hospital

Westmead, New South Wales, Australia

Site Status COMPLETED

Royal Brisbane and Women's Hospital

Herston, Queensland, Australia

Site Status ACTIVE_NOT_RECRUITING

Hospital Claude Huriez

Lille, , France

Site Status RECRUITING

Hôpital Necker Enfants Malades

Paris, , France

Site Status RECRUITING

Hôpital Universitaire Pitié-Salpêtrière

Paris, , France

Site Status RECRUITING

Azienda Ospedaliero Universitaria delle Marche

Ancona, , Italy

Site Status RECRUITING

ASST Grande Ospedale Metropolitano Niguarda

Milan, , Italy

Site Status RECRUITING

Fondazione Policlinico Universitario Agostino Gemelli IRCCS

Roma, , Italy

Site Status RECRUITING

Istituto Clinico Humanitas

Rozzano, , Italy

Site Status RECRUITING

IRCCS Ospedale Casa Sollievo della Sofferenza

San Giovanni Rotondo, , Italy

Site Status RECRUITING

Ospedale dell'Angelo di Mestre

Venezia, , Italy

Site Status RECRUITING

Vilnius University Hospital Santaros Klinikos

Vilnius, , Lithuania

Site Status RECRUITING

ICO l'Hospitalet - Hospital Duran i Reynals

Barcelona, , Spain

Site Status RECRUITING

Hospital Universitario Fundacion Jimenez Diaz

Madrid, , Spain

Site Status RECRUITING

Hospital Universitario Ramon y Cajal

Madrid, , Spain

Site Status RECRUITING

Hospital Universitato De La Princesa

Madrid, , Spain

Site Status COMPLETED

Hospital Universitario Virgen de la Arrixaca

Murcia, , Spain

Site Status RECRUITING

Clínica Universidad de Navarra

Pamplona, , Spain

Site Status RECRUITING

Anadolu Medical Center

Eskişehir, , Turkey (Türkiye)

Site Status RECRUITING

Gayrettepe Florence Nightingale Hastanesi

Istanbul, , Turkey (Türkiye)

Site Status COMPLETED

Koc University

Istanbul, , Turkey (Türkiye)

Site Status RECRUITING

Memorial Bahcelievler Hospital

Istanbul, , Turkey (Türkiye)

Site Status COMPLETED

Izmir Medicalpark Hospital

Izmir, , Turkey (Türkiye)

Site Status RECRUITING

İnonu University

Malatya, , Turkey (Türkiye)

Site Status RECRUITING

Dr Abdurrahman Yurtaslan Ankara Onkoloji Egitim ve Arastirma Hastanesi

Yenimahalle, , Turkey (Türkiye)

Site Status RECRUITING

Countries

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United States Australia France Italy Lithuania Spain Turkey (Türkiye)

Central Contacts

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Cynata Project Manager

Role: CONTACT

+61 3 7067 6940

Other Identifiers

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CYP-GvHD-P2-01

Identifier Type: -

Identifier Source: org_study_id

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