Clinical Study to Evaluate the Possible Efficacy and Safety of L- Carnitine and Sildenafil in Children Having Beta Thalassemia With Increased Tricuspid Regurgitant Jet Velocity

NCT ID: NCT05584956

Last Updated: 2022-10-18

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

UNKNOWN

Clinical Phase

PHASE3

Total Enrollment

44 participants

Study Classification

INTERVENTIONAL

Study Start Date

2022-07-08

Study Completion Date

2024-07-08

Brief Summary

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This study aims to investigate the possible efficacy and safety of L\_Carnitine and Sildenafil on patient with Beta thalassemia complicated with increased Tricuspid Regurgitant Jet Velocity

Detailed Description

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Conditions

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Beta Thalassemia With Increased Tricuspid Regurgitant Jet Velocity

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Group 1

n=22): Patients will receive traditional treatment and L- carnitine 50mg/kg/day orally (maximum dose 3g per day)

Group Type ACTIVE_COMPARATOR

L_carnitine

Intervention Type DRUG

l-carnitine stabilizes red blood cell membranes and thus improves the anemic state\[

Group 2

n=22): Patients will receive traditional treatment and Sildenafil 0.25mg/kg/dose every 6 h orally (maximum dose 60 mg per day)

Group Type ACTIVE_COMPARATOR

Sildenafil

Intervention Type DRUG

selective and potent inhibitor of cGMP-specific phosphodiesterase 5 (PDE5), which promotes smooth muscle relaxation in lung vasculature, has been used successfully in the treatment of primary and secondary PH.

Interventions

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L_carnitine

l-carnitine stabilizes red blood cell membranes and thus improves the anemic state\[

Intervention Type DRUG

Sildenafil

selective and potent inhibitor of cGMP-specific phosphodiesterase 5 (PDE5), which promotes smooth muscle relaxation in lung vasculature, has been used successfully in the treatment of primary and secondary PH.

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Children with Beta thalassemia major who have increased TRJV more than 2.5m/s.
* Children age from 6-18 years

Exclusion Criteria

* Others hemolytic anemia

* Young age before 6 years of age
* Allergy to Sildenafil or L-carnitine
* Patient with documented causes of pulmonary hypertension rather than caused by Beta thalassemia.
* Hepatic dysfunction: serum Alanine Aminotransferase (ALT) 3X.
* Renal dysfunction: Creatinine level greater than or equal to 1.2 mg/dl.
Minimum Eligible Age

6 Years

Maximum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Tanta University

OTHER

Sponsor Role lead

Responsible Party

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Mostafa Zaki Zedan

Clinical pharmacist

Responsibility Role PRINCIPAL_INVESTIGATOR

Principal Investigators

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Sahar Kamal Hegazy, Professor

Role: PRINCIPAL_INVESTIGATOR

Tanta University

Locations

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Tanta University Hospital

Tanta, Gharbia Governorate, Egypt

Site Status RECRUITING

Countries

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Egypt

Central Contacts

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Mostafa Zaki Zedan, Bsc of pharmaceutical science

Role: CONTACT

+0201554676330

Facility Contacts

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Mohamed Ramadan El_shanshory, Professor

Role: primary

Other Identifiers

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Beta thalassemia

Identifier Type: -

Identifier Source: org_study_id

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