A Study to Evaluate the Safety, Tolerability, and Pharmacokinetics of RO7303509 in Participants With Systemic Sclerosis

NCT ID: NCT05462522

Last Updated: 2025-07-20

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE1

Total Enrollment

56 participants

Study Classification

INTERVENTIONAL

Study Start Date

2023-01-16

Study Completion Date

2025-07-11

Brief Summary

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The purpose of this study is to evaluate the safety, tolerability, and pharmacokinetics (PK) of RO7303509 treatment in participants with systemic sclerosis (SSc) during a multiple-ascending-dose (MAD) portion of the trial. In the MAD phase, increasing doses of study drug will be tested sequentially. For each dose tested, the MAD stage will consist of a treatment period of 12 weeks followed by either a safety follow-up period of 13 weeks or continued treatment in an optional open-label safety extension (OSE) stage of 52 weeks to assess the long-term safety. All patients in the OSE stage will receive RO7303509 and no patient will receive placebo.

Detailed Description

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Conditions

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Systemic Sclerosis

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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MAD Stage

Participants will be randomized in a ratio of 4:1 to receive RO7303509 or placebo, as subcutaneous (SC) injection, one time per month for 3 months. You have a 20% chance of getting placebo.

Group Type EXPERIMENTAL

RO7303509

Intervention Type DRUG

RO7303509 will be administered as SC injection monthly, as specified in each treatment group.

Placebo

Intervention Type DRUG

RO7303509 matching placebo will be administered as SC injection monthly, during the MAD stage.

OSE Stage

Every participant in the OSE stage will receive study drug and no participant will receive placebo. Participants will receive RO7303509 as SC injection at the same dose as that administered during the MAD stage, one time per month for up to a year.

Group Type EXPERIMENTAL

RO7303509

Intervention Type DRUG

RO7303509 will be administered as SC injection monthly, as specified in each treatment group.

Interventions

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RO7303509

RO7303509 will be administered as SC injection monthly, as specified in each treatment group.

Intervention Type DRUG

Placebo

RO7303509 matching placebo will be administered as SC injection monthly, during the MAD stage.

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Weight of 45-150 kg at screening
* Diagnosis of SSc, as defined by 2013 American College of Rheumatology (ACR)/European League Against Rheumatism (EULAR) criteria and ≤ 10 years disease duration from first non-Raynaud's symptom
* Agreement to remain abstinent or use an effective contraceptive method among males and females with childbearing potential for 4 months after last dose of study drug


* No clinically significant change in eligibility status
* Completion of the MAD and ability to roll over into the OSE within 5 days

Exclusion Criteria

* Active rheumatic autoimmune disease other than SSc requiring treatment with disease-modifying therapy
* Pulmonary disease with forced vital capacity (FVC) ≤ 50% of predicted
* History or clinical manifestations of significant metabolic, hepatic, renal, pulmonary, cardiovascular, hematologic, gastrointestinal, urologic, neurologic, or psychiatric disorders
* History of severe allergic or anaphylactic reactions to human, humanized, or murine monoclonal antibodies
* Pregnant or breastfeeding, or intending to become pregnant during the study or within 4 months after the final dose of study drug
* Major surgery within 8 weeks prior to screening, or major planned surgery during the study or within 3 months after the final dose
* Positive hepatitis C virus (HCV) antibody, hepatitis B surface antigen (HBsAg), or human immunodeficiency virus (HIV) antibody test at screening
* Any serious medical condition or abnormality in clinical laboratory tests
Minimum Eligible Age

18 Years

Maximum Eligible Age

75 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Genentech, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Clinical Trials

Role: STUDY_DIRECTOR

Hoffmann-La Roche

Locations

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Stanford University

Palo Alto, California, United States

Site Status

Hospital For Special Surgery

New York, New York, United States

Site Status

Metroplex Clinical Research Centre

Dallas, Texas, United States

Site Status

Hospital de Alta Complejidad en Red ?El Cruce? Dr. Néstor Kirchner ? S.A.M.I.C.

Buenos Aires, , Argentina

Site Status

Clinica Mayo de U.M.C.B. S.R.L

San Miguel de Tucumán, , Argentina

Site Status

UZ Leuven

Leuven, , Belgium

Site Status

Centre Hospitalier Universitaire de Grenoble - Albert Michallon

La Tronche, , France

Site Status

Hopital Cochin

Paris, , France

Site Status

CHU de Bordeaux

Pessac, , France

Site Status

CHRU Rennes

Rennes, , France

Site Status

Hopitaux Universitaires

Strasbourg, , France

Site Status

Hopital Purpan

Toulouse, , France

Site Status

Rambam Medical Center - PPDS

Haifa, , Israel

Site Status

Meir Medical Center

Kfar Saba, , Israel

Site Status

Szpital Uniwersytecki Nr 2 im. Dr Jana Biziela w Bydgoszczy

Bydgoszcz, , Poland

Site Status

Zespol Poradni Specjalistycznych REUMED

Lublin, , Poland

Site Status

Hospital Garcia de Orta

Almada, , Portugal

Site Status

Centro Hospitalar E Universitário de Coimbra EPE

Coimbra, , Portugal

Site Status

The Alliance Medical Sciences Campus

San Juan, , Puerto Rico

Site Status

Institute of Rheumatology Belgrade - PPDS

Belgrade, , Serbia

Site Status

Military Medical Academy

Belgrade, , Serbia

Site Status

Hospital de la Santa Creu i Sant Pau

Barcelona, , Spain

Site Status

Hospital Universitario Vall d Hebron

Barcelona, , Spain

Site Status

Hospital Quironsalud Infanta Luisa

Seville, , Spain

Site Status

Royal Free Hospital

London, , United Kingdom

Site Status

Countries

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United States Argentina Belgium France Israel Poland Portugal Puerto Rico Serbia Spain United Kingdom

Other Identifiers

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2021-004578-68

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

GA43360

Identifier Type: -

Identifier Source: org_study_id

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