Efficacy and Safety of Oral BG00012 in Relapsing-Remitting Multiple Sclerosis

NCT ID: NCT00420212

Last Updated: 2015-01-26

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

1234 participants

Study Classification

INTERVENTIONAL

Study Start Date

2007-01-31

Study Completion Date

2011-02-28

Brief Summary

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To determine if treatment with BG00012 can decrease the number of MS relapses during a certain time period. To determine if, over time, BG00012 treatment can decrease the number of certain types of brain lesions commonly seen in MS patients and slow down the time it takes for the disease to get worse.

The purpose of this study is also to determine the safety of BG00012 and how well it is tolerated. Another goal is to see what effect BG00012 may have on tests and evaluations used to assess MS.

Detailed Description

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Conditions

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Relapsing-Remitting Multiple Sclerosis

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

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Placebo

Participants received two placebo capsules orally three times daily (TID)

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

BG00012 240 mg Twice Daily (BID)

Participants received two 120 mg BG00012 capsules orally twice daily (BID) and two placebo capsules orally once daily (QD)

Group Type EXPERIMENTAL

BG00012

Intervention Type DRUG

BG00012 240 mg 3 Times Daily (TID)

Participants received two 120 mg BG00012 capsules orally three times daily (TID)

Group Type EXPERIMENTAL

BG00012

Intervention Type DRUG

Interventions

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BG00012

Intervention Type DRUG

Placebo

Intervention Type DRUG

Other Intervention Names

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dimethyl fumarate Tecfidera®

Eligibility Criteria

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Inclusion Criteria

* Unless otherwise specified, to be eligible to participate in this study, candidates must meet the following eligibility criteria at the time of the randomization:
* Must have a confirmed diagnosis of RRMS according to McDonald criteria #1-4.
* Must have a baseline EDSS between 0.0 and 5.0, inclusive.
* Must have relapsing-remitting disease course.

Exclusion Criteria

* Other chronic disease of the immune system, malignancies, acute urologic, pulmonary, gastrointestinal disease.
* Pregnant or nursing women.
Minimum Eligible Age

18 Years

Maximum Eligible Age

55 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Biogen

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Medical Director

Role: STUDY_DIRECTOR

Biogen

Locations

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Research Site

Gilbert, Arizona, United States

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Phoenix, Arizona, United States

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San Francisco, California, United States

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New Haven, Connecticut, United States

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Washington D.C., District of Columbia, United States

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Vero Beach, Florida, United States

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Atlanta, Georgia, United States

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Evanston, Illinois, United States

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Palos Heights, Illinois, United States

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Fort Wayne, Indiana, United States

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Indianapolis, Indiana, United States

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Des Moines, Iowa, United States

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Wichita, Kansas, United States

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Lexington, Kentucky, United States

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Brighton, Massachusetts, United States

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Hopedale, Massachusetts, United States

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Lexington, Massachusetts, United States

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Springfield, Massachusetts, United States

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Worcester, Massachusetts, United States

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Farmington Hills, Michigan, United States

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Minneapolis, Minnesota, United States

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Columbia, Missouri, United States

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St Louis, Missouri, United States

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Henderson, Nevada, United States

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Las Vegas, Nevada, United States

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Lebanon, New Hampshire, United States

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Albany, New York, United States

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Staten Island, New York, United States

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Raleigh, North Carolina, United States

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Dayton, Ohio, United States

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Erie, Pennsylvania, United States

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Hershey, Pennsylvania, United States

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Pittsburgh, Pennsylvania, United States

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East Providence, Rhode Island, United States

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Providence, Rhode Island, United States

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San Antonio, Texas, United States

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Newport News, Virginia, United States

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Wien, Virginia, United States

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Seattle, Washington, United States

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Camperdown, New South Wales, Australia

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Chatswood, New South Wales, Australia

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Fitzroy, , Australia

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Geelong, , Australia

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Heidelberg, , Australia

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Kogarah, , Australia

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Liverpool, , Australia

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Melbourne, , Australia

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Newcastle, , Australia

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Vienna, Vienna, Austria

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Graz, , Austria

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Innsbruck, , Austria

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Linz, , Austria

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Antwerp, , Belgium

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Bruges, , Belgium

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Charleroi, , Belgium

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Diepenbeek, , Belgium

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Leuven, , Belgium

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Lommel, , Belgium

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Sijsele-Damme, , Belgium

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Woluwe, , Belgium

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Banja Luka, Republic of Srpksa, Bosnia and Herzegovina

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Burnaby, British Columbia, Canada

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Halifax, Nova Scotia, Canada

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Ottawa, Ontario, Canada

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Lévis, Quebec, Canada

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Québec, Quebec, Canada

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Regina, Saskatchewan, Canada

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Montreal, , Canada

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Zagreb, , Croatia

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Brno, , Czechia

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Jihlava, , Czechia

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Opava, , Czechia

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Ostrava, , Czechia

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Pilsen, , Czechia

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Prague, , Czechia

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Teplice, , Czechia

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Clermont-Ferrand, , France

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Nice, , France

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Paris, , France

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Rennes, , France

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Bad Neustadt-Saale, , Germany

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Berlin, , Germany

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Bochum, , Germany

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Düsseldorf, , Germany

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Essen, , Germany

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Gieben, , Germany

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Halle, , Germany

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Hamburg, , Germany

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Hanover, , Germany

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Leipzig, , Germany

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Minden, , Germany

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München, , Germany

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Münster, , Germany

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Osnabrück, , Germany

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Westerstede, , Germany

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Athens, , Greece

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Ioannina, , Greece

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Thessaloniki, , Greece

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Guatemala City, , Guatemala

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Chenna, , India

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Coimbatore, , India

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Delhi, , India

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Hyderabad, , India

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Kolkata, , India

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Lucknow, , India

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Mangalore, , India

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Mumbai, , India

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New Delhi, , India

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Pune, , India

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Ashkelon, , Israel

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Beer Yaakov, , Israel

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Jerusalem, , Israel

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Tel Litwinsky, , Israel

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Roma, , Italy

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Guadalajara, , Mexico

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Mexico City, , Mexico

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San Luis Potosí City, , Mexico

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Chisinau, , Moldova

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Breda, , Netherlands

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Sittard, , Netherlands

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Christchurch, , New Zealand

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Grafton, , New Zealand

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Hamilton, , New Zealand

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Skopje, , North Macedonia

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Bialystok, , Poland

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Gdansk, , Poland

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Katowice, , Poland

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Krakow, , Poland

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Poznan, , Poland

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Szczecin, , Poland

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Warsaw, , Poland

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Bucharest, , Romania

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Cluj-Napoca, , Romania

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Timișoara, , Romania

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Belgrade, , Serbia

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Kragujevac, , Serbia

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Niš, , Serbia

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Novi Sad, , Serbia

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Bratislava, , Slovakia

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Košice, , Slovakia

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Martin, , Slovakia

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Cape Town, , South Africa

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Durban, , South Africa

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Rosebank, , South Africa

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Basel, , Switzerland

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Sankt Gallen, , Switzerland

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Zurich, , Switzerland

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Kharkiv, , Ukraine

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Kyiv, , Ukraine

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Lviv, , Ukraine

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Odesa, , Ukraine

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Poltava, , Ukraine

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Zaporizhzhya, , Ukraine

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London, , United Kingdom

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Newcastle, , United Kingdom

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Oxford, , United Kingdom

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Sheffield, , United Kingdom

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Staffordshire, , United Kingdom

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Vienna, , Virgin Islands

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Countries

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United States Australia Austria Belgium Bosnia and Herzegovina Canada Croatia Czechia France Germany Greece Guatemala India Israel Italy Mexico Moldova Netherlands New Zealand North Macedonia Poland Romania Serbia Slovakia South Africa Switzerland Ukraine United Kingdom Virgin Islands

References

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Gold R, Arnold DL, Bar-Or A, Fox RJ, Kappos L, Chen C, Parks B, Miller C. Safety and efficacy of delayed-release dimethyl fumarate in patients with relapsing-remitting multiple sclerosis: 9 years' follow-up of DEFINE, CONFIRM, and ENDORSE. Ther Adv Neurol Disord. 2020 May 12;13:1756286420915005. doi: 10.1177/1756286420915005. eCollection 2020.

Reference Type DERIVED
PMID: 32426039 (View on PubMed)

Mehta D, Miller C, Arnold DL, Bame E, Bar-Or A, Gold R, Hanna J, Kappos L, Liu S, Matta A, Phillips JT, Robertson D, von Hehn CA, Campbell J, Spach K, Yang L, Fox RJ. Effect of dimethyl fumarate on lymphocytes in RRMS: Implications for clinical practice. Neurology. 2019 Apr 9;92(15):e1724-e1738. doi: 10.1212/WNL.0000000000007262. Epub 2019 Mar 27.

Reference Type DERIVED
PMID: 30918100 (View on PubMed)

Fox RJ, Gold R, Phillips JT, Okwuokenye M, Zhang A, Marantz JL. Efficacy and Tolerability of Delayed-release Dimethyl Fumarate in Black, Hispanic, and Asian Patients with Relapsing-Remitting Multiple Sclerosis: Post Hoc Integrated Analysis of DEFINE and CONFIRM. Neurol Ther. 2017 Dec;6(2):175-187. doi: 10.1007/s40120-017-0077-5. Epub 2017 Aug 2.

Reference Type DERIVED
PMID: 28770420 (View on PubMed)

Fernandez O, Giovannoni G, Fox RJ, Gold R, Phillips JT, Potts J, Okwuokenye M, Marantz JL. Efficacy and Safety of Delayed-release Dimethyl Fumarate for Relapsing-remitting Multiple Sclerosis in Prior Interferon Users: An Integrated Analysis of DEFINE and CONFIRM. Clin Ther. 2017 Aug;39(8):1671-1679. doi: 10.1016/j.clinthera.2017.06.012. Epub 2017 Jul 25.

Reference Type DERIVED
PMID: 28751099 (View on PubMed)

Fox RJ, Chan A, Zhang A, Xiao J, Levison D, Lewin JB, Edwards MR, Marantz JL. Comparative effectiveness using a matching-adjusted indirect comparison between delayed-release dimethyl fumarate and fingolimod for the treatment of multiple sclerosis. Curr Med Res Opin. 2017 Feb;33(2):175-183. doi: 10.1080/03007995.2016.1248380. Epub 2016 Nov 10.

Reference Type DERIVED
PMID: 27733070 (View on PubMed)

Gold R, Giovannoni G, Phillips JT, Fox RJ, Zhang A, Marantz JL. Sustained Effect of Delayed-Release Dimethyl Fumarate in Newly Diagnosed Patients with Relapsing-Remitting Multiple Sclerosis: 6-Year Interim Results From an Extension of the DEFINE and CONFIRM Studies. Neurol Ther. 2016 Jun;5(1):45-57. doi: 10.1007/s40120-016-0042-8. Epub 2016 Mar 1.

Reference Type DERIVED
PMID: 26932146 (View on PubMed)

Giovannoni G, Gold R, Fox RJ, Kappos L, Kita M, Yang M, Sarda SP, Zhang R, Viglietta V, Havrdova E. Relapses Requiring Intravenous Steroid Use and Multiple-Sclerosis-related Hospitalizations: Integrated Analysis of the Delayed-release Dimethyl Fumarate Phase III Studies. Clin Ther. 2015 Nov 1;37(11):2543-51. doi: 10.1016/j.clinthera.2015.09.011. Epub 2015 Oct 31.

Reference Type DERIVED
PMID: 26526385 (View on PubMed)

Nakamura K, Brown RA, Narayanan S, Collins DL, Arnold DL; Alzheimer's Disease Neuroimaging Initiative. Diurnal fluctuations in brain volume: Statistical analyses of MRI from large populations. Neuroimage. 2015 Sep;118:126-32. doi: 10.1016/j.neuroimage.2015.05.077. Epub 2015 Jun 3.

Reference Type DERIVED
PMID: 26049148 (View on PubMed)

Kita M, Fox RJ, Gold R, Giovannoni G, Phillips JT, Sarda SP, Kong J, Viglietta V, Sheikh SI, Okwuokenye M, Kappos L. Effects of delayed-release dimethyl fumarate (DMF) on health-related quality of life in patients with relapsing-remitting multiple sclerosis: an integrated analysis of the phase 3 DEFINE and CONFIRM studies. Clin Ther. 2014 Dec 1;36(12):1958-1971. doi: 10.1016/j.clinthera.2014.08.013. Epub 2014 Oct 12.

Reference Type DERIVED
PMID: 25315404 (View on PubMed)

Fox RJ, Kita M, Cohan SL, Henson LJ, Zambrano J, Scannevin RH, O'Gorman J, Novas M, Dawson KT, Phillips JT. BG-12 (dimethyl fumarate): a review of mechanism of action, efficacy, and safety. Curr Med Res Opin. 2014 Feb;30(2):251-62. doi: 10.1185/03007995.2013.849236. Epub 2013 Oct 22.

Reference Type DERIVED
PMID: 24131282 (View on PubMed)

Gold R, Kappos L, Arnold DL, Bar-Or A, Giovannoni G, Selmaj K, Tornatore C, Sweetser MT, Yang M, Sheikh SI, Dawson KT; DEFINE Study Investigators. Placebo-controlled phase 3 study of oral BG-12 for relapsing multiple sclerosis. N Engl J Med. 2012 Sep 20;367(12):1098-107. doi: 10.1056/NEJMoa1114287.

Reference Type DERIVED
PMID: 22992073 (View on PubMed)

Other Identifiers

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109MS301

Identifier Type: -

Identifier Source: org_study_id

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