A Study to Asses Efficacy, Safety and Tolerability of Monthly Long-acting IM Injection of GA Depot in Subjects With RMS

NCT ID: NCT04121221

Last Updated: 2023-12-01

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

1016 participants

Study Classification

INTERVENTIONAL

Study Start Date

2019-09-19

Study Completion Date

2023-06-13

Brief Summary

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A multinational, multicenter, randomized, Phase III, double blind, parallel group, placebo controlled study in subjects with Relapsing Forms of Multiple Sclerosis (RMS) to assess the efficacy, safety and tolerability of GA Depot, a long acting IM injection of glatiramer acetate, administered once every four weeks

Detailed Description

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A total of 1000 subjects are planned to be randomized into this study to receive treatment with GA Depot or with matching placebo.

During the placebo controlled period (PC period, the first 52 weeks of the study immediately after randomization) subjects will receive either 40mg of GA Depot or matching placebo, IM, once every 4 weeks, for a total of 13 times.

Subjects who complete the PC period of the study will be offered to continue into the open label period (OL period) for an additional 52 weeks, in which all subjects will receive 40mg of GA Depot IM once every 4 weeks.

Conditions

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Multiple Sclerosis, Relapsing-Remitting

Keywords

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Multiple Sclerosis RMS GA Depot Multiple Sclerosis, Relapsing-Remitting

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

During the placebo controlled period subjects will receive either 40mg of GA Depot or matching placebo, IM, once every 4 weeks, for a total of 13 times.

Subjects who complete the PC period of the study will be offered to continue into the open label period for an additional 52 weeks, in which all subjects will receive 40mg of GA Depot IM once every 4 weeks.
Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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GA Depot

Monthly IM injection

Group Type EXPERIMENTAL

GA Depot

Intervention Type DRUG

Long acting intramuscular injection of glatiramer acetate, once every 4 weeks

Placebo

Monthly IM injection

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type OTHER

IM injection once every 4 weeks

Interventions

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GA Depot

Long acting intramuscular injection of glatiramer acetate, once every 4 weeks

Intervention Type DRUG

Placebo

IM injection once every 4 weeks

Intervention Type OTHER

Eligibility Criteria

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Inclusion Criteria

1. Adult subjects between 18-55 years of age, inclusive.
2. Subjects able to provide signed written informed consent.
3. Subjects must be willing and able to comply with the protocol requirements for the duration of the study.
4. MS diagnosis fulfilling the 2017 McDonald Criteria.
5. Subjects should be ambulatory with an EDSS score of 0-5.5 at screening and baseline visits. EDSS score will be determined by a separate, blinded trained EDSS rater.
6. Subjects should be relapse free and neurologically stable from one month before screening visit and from screening visit to baseline visit.
7. No systemic corticosteroid treatment or ACTH within one month prior to screening visit.
8. Subjects must have experienced at least one of the following:

i. At least one documented relapse in the 12 months prior to screening. ii. At least two documented relapses in the 24 months prior to screening. iii. One documented relapse between 12 and 24 months prior to screening, with at least one documented T1-Gd enhancing lesion in MRI performed within 0-12 months before screening.
9. Women capable of child bearing must have a negative urine pregnancy test at screening and baseline visit and use an adequate contraceptive method throughout the study.

Exclusion Criteria

1. Use of experimental / investigational drug, and / or participation in drug clinical studies within the 6 months prior to screening.
2. Any off-label drug use for MS treatment such as high dose simvastatin and biotin within 6 months prior to screening.
3. Previous use of immunosuppressant including Mitoxantrone, Alemtuzumab, Cladribine or any other cytotoxic agent within 5 years.
4. Previous use of Natalizumab or any anti-B cell agent within 9 months prior to screening.
5. Previous use of Fingolimod or any other sphingosine-1-phosphate receptor modulator, Dimethyl Fumarate, Diroximel Fumarate (DRF), or Monomethyl fumarate within 2 months prior to screening. Subjects will be excluded if they do not have a lymphocyte count of above 1,000/mm3 at screening.
6. Previous use of Teriflunomide within 12 months if no accelerated elimination procedure was used.
7. Previous treatment with immunomodulators (including IFNβ 1a and 1b, and IV Immunoglobulin (IVIg) within 2 months prior to screening.
8. Previous use of GA or any other glatiramoid.
9. Chronic (more than 30 consecutive days) systemic (IV, PO or IM) corticosteroid treatment within 6 months prior to screening visit.
10. Previous total body irradiation or total lymphoid irradiation.
11. Previous stem-cell treatment, autologous bone marrow transplantation or allogeneic bone marrow transplantation.
12. Subjects with a clinically significant or unstable medical, psychiatric, or surgical conditions that would preclude safe and complete study participation, as determined by medical history, physical exams, ECG and/or abnormal laboratory tests; and or subjects with an increased risk of serious Covid-19 related morbidity. Such conditions may include hepatic, renal or metabolic diseases, systemic disease, acute infection, current malignancy, or recent history (5 years) of malignancy, major psychiatric disorder, history of drug and/or alcohol abuse and allergies that could be detrimental according to the investigator's judgment.
13. Subjects who have \>10 T1-Gd enhancing lesions at screening.
14. A known history of sensitivity to Gadolinium.
15. Inability to successfully undergo MRI scanning.
16. Pregnant or breast-feeding women.
17. Abnormal renal function.
18. Abnormal liver function.
19. History of any anaphylactic reaction and/or serious allergic reaction following a vaccination, a proven hypersensitivity to any component of the study article (e.g., GA, Polyglactin, PVA).
20. Positive testing or a history of positive testing for syphilis, HIV, hepatitis, or tuberculosis.
21. Known or suspected history of drug or alcohol abuse.
22. Subjects diagnosed with any systemic autoimmune disease (other than MS) that may impact the CNS with MS like lesions such as Sarcoidosis, Sjögren's syndrome, Systemic Lupus Erythematosus (SLE), Lyme disease, Antiphospholipid antibodies (APLA) syndrome, etc. Subjects with stable local/organ autoimmune disease such as psoriasis, cutaneous lupus erythematosus, thyroiditis (Hashimoto's, Grave's) etc. may be considered eligible upon the investigator's discretion.
23. Any CNS disorder other than MS that may jeopardize the subject's participation in the study.
24. Subjects with uncontrolled diabetes.
25. Subjects with clotting disorders or receiving treatment with anticoagulants.
Minimum Eligible Age

18 Years

Maximum Eligible Age

55 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Mapi Pharma Ltd.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Laura Popper, MD

Role: STUDY_DIRECTOR

Mapi Pharma Ltd.

Aaron E. Miller, Prof. MD

Role: PRINCIPAL_INVESTIGATOR

Mount Sinai School of Medicine, New York, US

Locations

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Mapi Pharma Research site 08

Birmingham, Alabama, United States

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Mapi Pharma Research site 11

Cullman, Alabama, United States

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Mapi Pharma Research site 15

Pasadena, California, United States

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Mapi Pharma Research site 14

Denver, Colorado, United States

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Mapi Pharma Research site 12

Washington D.C., District of Columbia, United States

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Mapi Pharma Research site 17

Homestead, Florida, United States

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Mapi Pharma Research site 09

Miami, Florida, United States

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Mapi Pharma Research site 01

Northbrook, Illinois, United States

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Mapi Pharma Research site 02

Detroit, Michigan, United States

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Mapi Pharma Research site 13

Westerville, Ohio, United States

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Mapi Pharma Research site 04

Round Rock, Texas, United States

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Mapi Pharma Research site 02

Homyel, , Belarus

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Mapi Pharma Research site 04

Minsk, , Belarus

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Mapi Pharma Research site 05

Minsk, , Belarus

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Mapi Pharma Research site 06

Minsk, , Belarus

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Mapi Pharma Research site 01

Vitebsk, , Belarus

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Mapi Pharma Research site 07

Vitebsk, , Belarus

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Mapi Pharma Research site 04

Banja Luka, , Bosnia and Herzegovina

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Mapi Pharma Research site 06

Bihać, , Bosnia and Herzegovina

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Mapi Pharma Research site 01

Sarajevo, , Bosnia and Herzegovina

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Mapi Pharma Research site 03

Tuzla, , Bosnia and Herzegovina

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Mapi Pharma Research site 14

Haskovo, , Bulgaria

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Mapi Pharma Research site 10

Pazardzhik, , Bulgaria

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Mapi Pharma Research site 01

Pleven, , Bulgaria

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Mapi Pharma Research site 02

Pleven, , Bulgaria

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Mapi Pharma Research site 03

Pleven, , Bulgaria

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Mapi Pharma Research site 07

Pleven, , Bulgaria

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Mapi Pharma Research site 12

Plovdiv, , Bulgaria

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Mapi Pharma Research site 18

Rousse, , Bulgaria

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Mapi Pharma Research site 04

Sofia, , Bulgaria

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Mapi Pharma Research site 05

Sofia, , Bulgaria

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Mapi Pharma Research site 06

Sofia, , Bulgaria

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Mapi Pharma Research site 08

Sofia, , Bulgaria

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Mapi Pharma Research site 11

Sofia, , Bulgaria

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Mapi Pharma Research site 13

Sofia, , Bulgaria

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Mapi Pharma Research site 15

Sofia, , Bulgaria

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Mapi Pharma Research site 16

Sofia, , Bulgaria

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Mapi Pharma Research site 19

Sofia, , Bulgaria

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Mapi Pharma Research site 09

Veliko Tarnovo, , Bulgaria

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Mapi Pharma Research site 17

Vratsa, , Bulgaria

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Mapi Pharma Research site 01

Tallinn, , Estonia

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Mapi Pharma Research site 01

Tbilisi, , Georgia

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Mapi Pharma Research site 02

Tbilisi, , Georgia

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Mapi Pharma Research site 03

Tbilisi, , Georgia

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Mapi Pharma Research site 04

Tbilisi, , Georgia

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Mapi Pharma Research site 05

Tbilisi, , Georgia

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Mapi Pharma Research site 06

Tbilisi, , Georgia

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Mapi Pharma Research site 07

Tbilisi, , Georgia

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Mapi Pharma Research site 08

Tbilisi, , Georgia

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Mapi Pharma Research site 09

Tbilisi, , Georgia

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Mapi Pharma Research site 01

Safed, , Israel

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Mapi Pharma Research site 02

Tel Aviv, , Israel

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Mapi Pharma Research site 01

Chisinau, , Moldova

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Mapi Pharma Research site 02

Chisinau, , Moldova

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Mapi Pharma Research site 29

Barnaul, , Russia

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Mapi Pharma Research site 27

Bryansk, , Russia

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Mapi Pharma Research site 23

Chelyabinsk, , Russia

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Mapi Pharma Research site 01

Kazan', , Russia

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Mapi Pharma Research site 19

Kemerovo, , Russia

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Mapi Pharma Research site 24

Krasnodar, , Russia

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Mapi Pharma Research site 03

Moscow, , Russia

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Mapi Pharma Research site 13

Moscow, , Russia

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Mapi Pharma Research site 14

Moscow, , Russia

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Mapi Pharma Research site 21

Moscow, , Russia

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Mapi Pharma Research site 25

Moscow, , Russia

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Mapi Pharma Research site 28

Moscow, , Russia

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Mapi Pharma Research site 02

Nizhny Novgorod, , Russia

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Mapi Pharma Research site 07

Nizhny Novgorod, , Russia

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Mapi Pharma Research site 10

Nizhny Novgorod, , Russia

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Mapi Pharma Research site 11

Novosibirsk, , Russia

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Mapi Pharma Research site 06

Perm, , Russia

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Mapi Pharma Research site 22

Pyatigorsk, , Russia

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Mapi Pharma Research site 08

Rostov-on-Don, , Russia

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Mapi Pharma Research site 09

Saint Petersburg, , Russia

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Mapi Pharma Research site 18

Saint Petersburg, , Russia

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Mapi Pharma Research site 20

Saint Petersburg, , Russia

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Mapi Pharma Research site 05

Samara, , Russia

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Mapi Pharma Research site 26

Saransk, , Russia

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Mapi Pharma Research site 15

Smolensk, , Russia

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Mapi Pharma Research site 16

Tyumen, , Russia

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Mapi Pharma Research site 04

Ufa, , Russia

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Mapi Pharma Research site 17

Ulyanovsk, , Russia

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Mapi Pharma Research site 32

Cherkasy, , Ukraine

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Mapi Pharma Research site 06

Chernihiv, , Ukraine

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Mapi Pharma Research site 11

Chernivtsi, , Ukraine

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Mapi Pharma Research site 03

Dnipro, , Ukraine

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Mapi Pharma Research site 04

Dnipro, , Ukraine

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Mapi Pharma Research site 24

Dnipro, , Ukraine

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Mapi Pharma Research site 18

Ivano-Frankivsk, , Ukraine

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Mapi Pharma Research site 26

Ivano-Frankivsk, , Ukraine

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Mapi Pharma Research site 27

Ivano-Frankivsk, , Ukraine

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Mapi Pharma Research site 09

Kharkiv, , Ukraine

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Mapi Pharma Research site 10

Kharkiv, , Ukraine

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Mapi Pharma Research site 08

Kherson, , Ukraine

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Mapi Pharma Research site 21

Kyiv, , Ukraine

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Mapi Pharma Research site 25

Kyiv, , Ukraine

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Mapi Pharma Research site 28

Kyiv, , Ukraine

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Mapi Pharma Research site 29

Kyiv, , Ukraine

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Mapi Pharma Research site 17

Lutsk, , Ukraine

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Mapi Pharma Research site 12

Lviv, , Ukraine

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Mapi Pharma Research site 13

Lviv, , Ukraine

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Mapi Pharma Research site 23

Lviv, , Ukraine

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Mapi Pharma Research site 05

Odesa, , Ukraine

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Mapi Pharma Research site 14

Poltava, , Ukraine

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Mapi Pharma Research site 34

Ternopil, , Ukraine

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Mapi Pharma Research site 31

Uzhhorod, , Ukraine

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Mapi Pharma Research site 16

Vinnitsa, , Ukraine

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Mapi Pharma Research site 01

Zaporizhzhya, , Ukraine

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Mapi Pharma Research site 02

Zaporizhzhya, , Ukraine

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Mapi Pharma Research site 07

Zaporizhzhya, , Ukraine

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Mapi Pharma Research site 20

Zaporizhzhya, , Ukraine

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Mapi Pharma Research site 33

Zhytomyr, , Ukraine

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Countries

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United States Belarus Bosnia and Herzegovina Bulgaria Estonia Georgia Israel Moldova Russia Ukraine

Other Identifiers

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Mapi GA Depot Phase III - 001

Identifier Type: -

Identifier Source: org_study_id