Mechanistic Studies of Phase III Trial With BAF312 in Secondary Progressive Multiple Sclerosis

NCT ID: NCT02330965

Last Updated: 2020-11-09

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Total Enrollment

36 participants

Study Classification

OBSERVATIONAL

Study Start Date

2014-12-31

Study Completion Date

2017-07-12

Brief Summary

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The primary goal of this study is to evaluate the effects of BAF312 (siponimod) on select immune and neuronal (nerve) cells by examining laboratory specimens (blood and/or spinal fluid) at multiple time points, prior to, and following the initiation of BAF312 or placebo treatment, in patients with Secondary Progressive Multiple Sclerosis (SPMS) who are enrolled in a clinical trial (NCT01665144) to evaluate the effectiveness and safety of BAF312.

Detailed Description

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This study is complementary to a multi-center, randomized, double-blind,parallel-group, placebo-controlled, variable treatment duration study comparing the efficacy and safety of BAF312 to placebo in patients with SPMS (NCT01665144). Investigators will explore both immunological and neuroprotective mechanisms of BAF312 (siponimod), a novel agent in the setting of a SPMS clinical trial.

This study is part of a multi-center study, with the University of Michigan serving as the central site.

Conditions

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Secondary Progressive Multiple Sclerosis

Keywords

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autoimmunity clinical research mechanistic studies blood draw cerebrospinal fluid (CSF) by lumbar puncture (optional)

Study Design

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Observational Model Type

CASE_CONTROL

Study Time Perspective

PROSPECTIVE

Study Groups

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Subjects Assigned to BAF312

Patients with secondary progressive multiple sclerosis (SPMS) randomized to receive BAF312 (siponimod). Refer to ClinicalTrials.gov record NCT01665144 for more information.

Blood Draw

Intervention Type PROCEDURE

Blood draws (65 mLs \[\~4 tablespoons\] per blood draw) at 4 time points: Prior to study medication initiation, and at +6, +12 and+24 months post treatment initiation.

CSF collection by lumbar puncture (Optional)

Intervention Type PROCEDURE

For participants who volunteer to donate CSF samples: up to 25 mLs (\<2 tablespoons): prior to study medication initiation, and at month 24 post treatment initiation.

Subjects Assigned to Placebo (Controls)

Patients with secondary progressive multiple sclerosis (SPMS) randomized to receive placebo. Refer to ClinicalTrials.gov record NCT01665144 for more information.

Blood Draw

Intervention Type PROCEDURE

Blood draws (65 mLs \[\~4 tablespoons\] per blood draw) at 4 time points: Prior to study medication initiation, and at +6, +12 and+24 months post treatment initiation.

CSF collection by lumbar puncture (Optional)

Intervention Type PROCEDURE

For participants who volunteer to donate CSF samples: up to 25 mLs (\<2 tablespoons): prior to study medication initiation, and at month 24 post treatment initiation.

Interventions

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Blood Draw

Blood draws (65 mLs \[\~4 tablespoons\] per blood draw) at 4 time points: Prior to study medication initiation, and at +6, +12 and+24 months post treatment initiation.

Intervention Type PROCEDURE

CSF collection by lumbar puncture (Optional)

For participants who volunteer to donate CSF samples: up to 25 mLs (\<2 tablespoons): prior to study medication initiation, and at month 24 post treatment initiation.

Intervention Type PROCEDURE

Other Intervention Names

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Phlebotomy Venipuncture CSF by LP cerebrospinal fluid collected by lumbar puncture

Eligibility Criteria

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Inclusion Criteria

* Participants enrolled in the multicenter, randomized, double-blind, parallel-group, placebo-controlled, variable treatment duration study comparing the efficacy and safety of BAF312 to placebo in patients with Secondary Progressive Multiple Sclerosis (SPMS) Protocol No. CBAF312A2304 (sponsored by Novartis). Refer to ClinicalTrials.gov record NCT01665144.
* Subjects enrolled at one of the participating AMS04 study sites located in the United States.
* Subject must be able to provide written informed consent.

Exclusion Criteria

* Subjects with severe bleeding disorders, platelet count less than (\<)50,000/microliters (μL), and/or who are currently on full anticoagulant therapy will be excluded from the optional CSF collections.
Minimum Eligible Age

18 Years

Maximum Eligible Age

60 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Autoimmunity Centers of Excellence

OTHER

Sponsor Role collaborator

Novartis Pharmaceuticals

INDUSTRY

Sponsor Role collaborator

National Institute of Allergy and Infectious Diseases (NIAID)

NIH

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Yang Mao-Draayer, MD, PhD

Role: STUDY_CHAIR

Multiple Sclerosis Center - University of Michigan Health System

David Fox, MD

Role: STUDY_CHAIR

Division of Rheumatology - University of Michigan Health System

Locations

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Jordan Research & Education Institute: Sutter Alta Bates Summit

Berkeley, California, United States

Site Status

University of Southern California

Los Angeles, California, United States

Site Status

University of California, Davis

Sacramento, California, United States

Site Status

University of Colorado

Aurora, Colorado, United States

Site Status

University of Michigan Health System -Multiple Sclerosis Center

Ann Arbor, Michigan, United States

Site Status

Henry Ford Health System

Detroit, Michigan, United States

Site Status

Minneapolis Clinic of Neurology

Golden Valley, Minnesota, United States

Site Status

University of New Mexico: Health Sciences Center

Albuquerque, New Mexico, United States

Site Status

South Shore Neurologic Associates - Multiple Sclerosis Care Center

Patchogue, New York, United States

Site Status

Carolinas Medical Center (CMC)

Charlotte, North Carolina, United States

Site Status

Cleveland Clinic: Mellen Center for Multiple Sclerosis

Cleveland, Ohio, United States

Site Status

Providence Multiple Sclerosis Center

Portland, Oregon, United States

Site Status

Swedish Neuroscience Institute

Seattle, Washington, United States

Site Status

Countries

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United States

References

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Wu Q, Mills EA, Wang Q, Dowling CA, Fisher C, Kirch B, Lundy SK, Fox DA, Mao-Draayer Y; AMS04 Study Group. Siponimod enriches regulatory T and B lymphocytes in secondary progressive multiple sclerosis. JCI Insight. 2020 Feb 13;5(3):e134251. doi: 10.1172/jci.insight.134251.

Reference Type RESULT
PMID: 31935197 (View on PubMed)

Related Links

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https://www.niaid.nih.gov/

National Institute of Allergy and Infectious Diseases (NIAID)

https://www.niaid.nih.gov/about/dait

Division of Allergy, Immunology, and Transplantation (DAIT)

Other Identifiers

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DAIT AMS04

Identifier Type: -

Identifier Source: org_study_id