HERTHENA-Lung02: A Study of Patritumab Deruxtecan Versus Platinum-based Chemotherapy in Metastatic or Locally Advanced EGFRm NSCLC After Failure of EGFR TKI Therapy

NCT ID: NCT05338970

Last Updated: 2025-01-31

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

ACTIVE_NOT_RECRUITING

Clinical Phase

PHASE3

Total Enrollment

586 participants

Study Classification

INTERVENTIONAL

Study Start Date

2022-07-08

Study Completion Date

2026-06-30

Brief Summary

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Disease progression is typical for patients with epidermal growth factor receptor mutated (EGFRm) non-small cell lung cancer (NSCLC). Standard platinum-based chemotherapy offers limited efficacy and an unfavorable safety profile.There is an urgent need for more effective and tolerable therapies for patients with EGFRm NSCLC who have exhausted available targeted therapies. Clinical evidence suggest that patritumab deruxtecan constitutes a promising investigational therapy for patients with EGFRm NSCLC.

Detailed Description

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Patritumab deruxtecan (HER3-DXd, U3-1402) is an antibody-drug conjugate (ADC) comprising an anti-HER3 mAb linked to a topoisomerase I inhibitor that is in clinical development for patients with NSCLC, metastatic breast cancer, and colorectal cancer.

The primary objective of the current study is to compare the efficacy of patritumab deruxtecan versus platinum-based chemotherapy, as measured by progression-free survival (PFS) and the key secondary endpoint of overall survival (OS), in participants with metastatic or locally advanced NSCLC with an EGFR-activating mutation (exon 19 deletion or L858R) after failure of third-generation (eg, osimertinib, lazertinib, aumolertinib, alflutinib) EGFR TKI therapy.

Conditions

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Nonsquamous Non-small Cell Lung Cancer EGFR L858R EGFR Exon 19 Deletion

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Patritumab deruxtecan

Participants who will be randomized to receive patritumab deruxtecan (HER3-DXd) 5.6 mg/kg q3W.

Group Type EXPERIMENTAL

Patritumab Deruxtecan

Intervention Type DRUG

Intravenous administration, 5.6 mg/kg every 3 weeks (q3W)

Platinum-based chemotherapy

Participants who will be randomized to receive platinum-based chemotherapy for 4 cycles: pemetrexed plus either cisplatin or carboplatin. Participants without disease progression after 4 cycles of platinum plus pemetrexed therapy may continue treatment with maintenance pemetrexed with no restriction on the number of cycles.

Group Type ACTIVE_COMPARATOR

Platinum-based chemotherapy

Intervention Type DRUG

Intravenous, pemetrexed 500 mg/m\^2 plus either cisplatin (75 mg/m\^2) or carboplatin (target area under the plasma concentration time curve of 5 \[AUC5\] by using the Calvert formula) q3W

Interventions

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Patritumab Deruxtecan

Intravenous administration, 5.6 mg/kg every 3 weeks (q3W)

Intervention Type DRUG

Platinum-based chemotherapy

Intravenous, pemetrexed 500 mg/m\^2 plus either cisplatin (75 mg/m\^2) or carboplatin (target area under the plasma concentration time curve of 5 \[AUC5\] by using the Calvert formula) q3W

Intervention Type DRUG

Other Intervention Names

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HER3-DXd U3-1402

Eligibility Criteria

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Inclusion Criteria

1. Is a male or female subject aged ≥18 years (follow local regulatory requirements if the legal age of consent for study participation is \>18 years old).
2. Has histologically or cytologically documented metastatic or locally advanced non-squamous NSCLC not amenable to curative surgery or radiation.
3. Has documentation of an EGFR-activating mutation detected from tumor tissue or blood sample: exon 19 deletion or L858R at diagnosis or thereafter.
4. Received 1 or 2 prior line(s) of an approved EGFR TKI treatment in the metastatic or locally advanced setting, which must include a third -generation EGFR TKI
5. May have received either neoadjuvant and/or adjuvant treatment if progression to metastatic or locally advanced disease occurred at least 12 months after the last dose of such therapy and subsequently experienced disease progression on or after third-generation EGFR TKI treatment administered in the metastatic or locally advanced setting.
6. Has not received any other prior systemic therapies in the metastatic or locally advanced setting (including chemotherapy, immunotherapy etc) (even if administered in combination with EGFR TKI).
7. Has documentation of radiographic disease progression while receiving or after receiving a third generation EGFR TKI for metastatic or locally advanced disease.
8. Has at least 1 measurable lesion as per RECIST v1.1 by Investigator assessment.
9. Is willing to have a tumor biopsy or provide recently obtained tumor tissue.
10. Has an Eastern Cooperative Oncology Group performance status (ECOG PS) of 0 or 1 at Screening.
11. Has adequate bone marrow reserve and organ function based on local laboratory evaluation within 14 days prior to randomization:

* Platelet count: ≥100,000/mm\^3 or ≥100 × 10\^9/L within 14 days prior to the assessment of platelet count during the Screening Period
* Absolute neutrophil count: ≥1500/mm\^3 or ≥1.5 × 10\^9/L within 14 days prior to the assessment of absolute neutrophil count during the Screening Period
* Hemoglobin (Hgb): ≥9.0 g/dL within 14 days prior to the assessment of hemoglobin during the Screening Period
* Creatine clearance (CrCl): CrCl ≥45 mL/min calculated by using the Cockcroft-Gault equation or measured CrCl
* Aspartate aminotransferase (AST)/Alanine aminotransferase (ALT): AST/ALT ≤3× Upper limit of normal (ULN)
* Total bilirubin (TBL): TBL ≤1.5 × ULN
* Serum albumin: ≥2.5 g/dL
* Prothrombin time (PT) or Prothrombin time-International normalized ratio (PT-INR) and activated partial thromboplastin time (aPTT)/partial thromboplastin time (PTT): ≤1.5 × ULN, except for participants receiving coumarin-derivative anticoagulants or other similar anticoagulant therapy who must have PT-INR within therapeutic range as deemed appropriate by the Investigator

Exclusion Criteria

1. Has any previous histologic or cytologic evidence of small cell OR combined small cell/non-small cell disease in the archival tumor tissue or pretreatment tumor biopsy, or squamous NSCLC histology
2. Has any history of interstitial lung disease (ILD) (including pulmonary fibrosis or radiation pneumonitis), has current ILD, or is suspected to have such disease by imaging during Screening
3. Has clinically severe respiratory compromise (based on the Investigator's assessment) resulting from intercurrent pulmonary illnesses including, but not limited to the following:

* Any underlying pulmonary disorder, restrictive lung disease, or pleural effusion
* Any autoimmune, connective tissue, or inflammatory disorders where there is documented, or a suspicion of pulmonary involvement at the time of Screening
* OR prior complete pneumonectomy
4. Is receiving chronic systemic corticosteroids dosed at \>10 mg prednisone or equivalent anti-inflammatory activity or any form of immunosuppressive therapy prior to randomization
5. Has any history of or evidence of current leptomeningeal disease
6. Has evidence of clinically active spinal cord compression or brain metastases, defined as being symptomatic and untreated, or requiring therapy with corticosteroids or anticonvulsants to control associated symptoms
7. Any prior treatment with any agent including an antibody drug conjugate (ADC) containing a chemotherapeutic agent targeting topoisomerase I, human epidermal growth factor receptor 3 (HER3) antibody, and any systemic therapies (other than EGFR TKIs) in the metastatic/locally advanced setting, including chemotherapy or any other systemic therapy in combination with an EGFR TKI
8. Has history of other active malignancy within 3 years prior to randomization, except for adequately resected nonmelanoma skin cancer, adequately treated intraepithelial carcinoma of the cervix, and any other curatively treated in situ disease
9. Has uncontrolled or significant cardiovascular disease prior to randomization
10. Has active hepatitis B and/or hepatitis C infection, such as those with serologic evidence of active viral infection within 28 days of randomization
11. Has a known human immunodeficiency virus (HIV) infection that is not well controlled
12. Has clinically significant corneal disease
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Merck Sharp & Dohme LLC

INDUSTRY

Sponsor Role collaborator

Daiichi Sankyo

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Global Clinical Leader

Role: STUDY_DIRECTOR

Daiichi Sankyo

Clinical Scientist

Role: STUDY_CHAIR

Daiichi Sankyo

Locations

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Alaska Oncology and Hematology LLC

Anchorage, Alaska, United States

Site Status

Highlands Oncology

Springdale, Arkansas, United States

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City of Hope

Duarte, California, United States

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Moores Cancer Center at the UC San Diego Health

La Jolla, California, United States

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Scripps MD Anderson Cancer Center

La Jolla, California, United States

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USC Norris Comprehensive Cancer Center

Los Angeles, California, United States

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Kaiser Permanente - Vallejo Medical Center

Vallejo, California, United States

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Innovative Clinical Research Institute

Whittier, California, United States

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Sarah Cannon/Florida Cancer Specialists - FCS South

Port Charlotte, Florida, United States

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Emory University

Atlanta, Georgia, United States

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St Luke's Cancer Institute

Boise, Idaho, United States

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American Oncology Partners of Maryland

Bethesda, Maryland, United States

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Dana-Farber Cancer Institute

Boston, Massachusetts, United States

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Dartmouth Hitchcock Medical Center

Lebanon, New Hampshire, United States

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Hackensack Meridian Health-Southern Ocean Medical Center

Manahawkin, New Jersey, United States

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Memorial Sloan Kettering Cancer Center

New York, New York, United States

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Montefiore Medical Center

The Bronx, New York, United States

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Providence Portland Medical Center

Portland, Oregon, United States

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Sarah Cannon Research Institute

Nashville, Tennessee, United States

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University of Texas Southwestern Medical Center

Dallas, Texas, United States

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Inova Schar Cancer Institute

Fairfax, Virginia, United States

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Virginia Cancer Specialists

Fairfax, Virginia, United States

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University of Wisconsin Carbone Cancer Center

Madison, Wisconsin, United States

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The Chris O'Brien Lifehouse

Camperdown, , Australia

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St George Public Hospital

Kogarah, , Australia

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Liverpool Hospital

Liverpool, , Australia

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Austin Hospital

Melbourne, , Australia

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St John of God Subiaco Hospital

Subiaco, , Australia

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Princess Alexandra Hospital

Woolloongabba, , Australia

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Landeskrankenhaus Feldkirch

Feldkirch, , Austria

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Medizinische Universitaet Innsbruck

Innsbruck, , Austria

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Klinikum Klagenfurt Pulmologie

Klagenfurt, , Austria

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Karl Landsteiner Institut fur Lungenforschung und pneumologische Onkologie c/o Klinik Floridsdorf

Vienna, , Austria

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Klinikum Wels-Grieskirchen

Wels, , Austria

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Cliniques Universitaires Saint-Luc

Brussels, , Belgium

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UZ Leuven

Leuven, , Belgium

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AZ Sint Maarten Mechelen

Mechelen, , Belgium

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AZ Delta

Roeselare, , Belgium

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William Osler Health System - Brampton Civic Hospital

Brampton, , Canada

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Peking University Cancer Hospital

Beijing, , China

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Jilin Cancer Hospital

Changchun, , China

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Hunan Cancer Hospital

Changsha, , China

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University of Electronic Science Technology of China UESTC - Sichuan Cancer Hospital Institute Sichuan Provincial Tumor Hospital

Chengdu, , China

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National Cancer Center Hospital East

Chibi, , China

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Fujian Medical University - Union Hospital Foochow Christian Union Hospital

Fuzhou, , China

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Guangdong Academy of Medical Science (GAMS) - Guangdong Provincial Peoples Hospital

Guangzhou, , China

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The First Affiliated Hospital Sun-Yat-Sen University

Guangzhou, , China

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Pecking University Third Hospital

Haidian, , China

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The First Affiliated Hospital of College of Medicine Zhejiang University

Hangzhou, , China

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Zhejiang Cancer hospital

Hangzhou, , China

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Harbin Medical University - Tumor Hospital The Third Affiliated Hospital

Harbin, , China

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The First Affiliated Hospital - Anhui Medical University Dept of Medical Oncology

Hefei, , China

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Henan Provincial Peoples Hospital

Henan, , China

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The Second Affiliated Hospital of Kunming Medical University

Kunming, , China

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Lin Yi Cancer Hospital

Linyi, , China

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General Hospital of Eastern Theater Command

Nanjing, , China

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The First Affiliated Hospital of Guangxi Medical University

Nanning, , China

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Fudan University - Shanghai Cancer Center FUSCC

Shanghai, , China

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Cancer Hospital of Shantou University Medical College

Shantou, , China

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The First Hospital of China Medical University

Shenyang, , China

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Affiliated Cancer Hospital of Xinjiang Medical University

Ürümqi, , China

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Union Hospital of Tongji Medical College Huazhong University of Science and Technology

Wuhan, , China

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Huazhong University of Science and Technology - Tongji Medical College - Tongji Hospital TJH

Wuhan, , China

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The First Affiliate Hospital of Xi'an Jiaotong University

Xi'an, , China

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Henan Cancer Hospital

Zhengzhou, , China

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Hopital Morvan CHU de Brest

Brest, , France

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Centre Francois Baclesse

Caen, , France

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Centre Francois Baclesse

Caen, , France

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Centre Leon Berard

Lyon, , France

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Montpellier Cancer Institute ICM

Montpellier, , France

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Institut Curie

Paris, , France

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APHP - Hopital Saint Louis

Paris, , France

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Centre Hospitalier Lyon Sud

Pierre-Bénite, , France

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Centre Hospitalier Universitaire (CHU) de Rennes - Hopital de Pontchaillou

Rennes, , France

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Institut de Cancrologie de lOuest ICO

Saint-Herblain, , France

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Gustave Roussy

Villejuif, , France

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Universitaetsklinikum Essen

Essen, , Germany

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Klinikum Esslingen GmbH

Esslingen am Neckar, , Germany

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IKF Krankenhaus Nordwest

Frankfurt am Main, , Germany

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Asklepios Fachklinik Muenchen-Gauting

Gauting, , Germany

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Universitatsklinik Giessen und Marburg

Giessen, , Germany

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LungenClinic Grosshansdorf

Großhansdorf, , Germany

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Thoraxklinik Heidelberg gGmbH

Heidelberg, , Germany

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LKI Lungenfachklinik Immenhausen

Immenhausen, , Germany

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Klinikverbund Allgaeu

Kempten, , Germany

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Pius-Hospital Oldenburg

Oldenburg, , Germany

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Pamela Youde Nethersole Eastern Hospital

Hong Kong, , Hong Kong

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Prince of Wales Hospital

Hong Kong, , Hong Kong

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University of Hong Kong/Queen Mary Hospital

Hong Kong, , Hong Kong

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Queen Elizabeth Hospital

Hong Kong, , Hong Kong

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IRCCS Istituto Oncologico Giovanni Paolo II

Bari, , Italy

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University G. D'Annunzio Chieti

Chieti, , Italy

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Ospedale San Luca

Lucca, , Italy

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IRCCS Istituto Europeo di Oncologia

Milan, , Italy

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Asst Grande Ospedale Metropolitano Niguarda

Milan, , Italy

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Azienda Ospedaliero-Universitaria San Luigi Gonzaga

Orbassano, , Italy

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Azienda Ospedaliero Universitaria di Parma

Parma, , Italy

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Ospedale Santa Maria della Misericordia

Perugia, , Italy

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IFO Regina Elena

Roma, , Italy

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IRCCS Humanitas Research Hospital

Rozzano, , Italy

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ASST Sette Laghi

Varese, , Italy

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Hyogo Cancer Center

Akashi, , Japan

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Kyushu University Hospital

Fukuoka, , Japan

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Saitama Medical University International Medical Center

Hidaka, , Japan

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Kansai Medical University Hospital

Hirakata, , Japan

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Iwakuni Clinical Center

Iwakuni, , Japan

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Izumi City General Hospital

Izumi, , Japan

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Kanazawa University Hospital

Kanazawa, , Japan

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The Cancer Institute Hospital of JFCR

Kōtoku, , Japan

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Saiseikai Kumamoto Hospital

Kumamoto, , Japan

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Kurashiki Central Hospital

Kurashiki, , Japan

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Kurume University Hospital

Kurume, , Japan

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Matsusaka Municipal Hospital

Matsusaka, , Japan

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NHO Shikoku Cancer Center

Matsuyama, , Japan

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National Hospital Organization Nagoya Medical Center

Nagoya, , Japan

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Niigata Cancer Center Hospital

Niigata, , Japan

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Okayama University Hospital

Okayama, , Japan

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Kindai University Hospital

Ōsaka-sayama, , Japan

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National Hospital Organization Hokkaido Cancer Center

Sapporo, , Japan

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Sendai Kousei Hospital

Sendai, , Japan

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Tokyo Metropolitan Cancer and Infectious Diseases Center Komagome Hospital

Tokyo, , Japan

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Fujita Health University Hospital

Toyoake, , Japan

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Wakayama Medical University Hospital

Wakayama, , Japan

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Netherlands Cancer Institute

Amsterdam, , Netherlands

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Rijnstate Ziekenhuis

Arnhem, , Netherlands

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St. Jansdal Ziekenhuis

Harderwijk, , Netherlands

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Leiden University Medical Center

Leiden, , Netherlands

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Erasmus MC

Rotterdam, , Netherlands

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University Medical Center Utrecht

Utrecht, , Netherlands

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Akershus University Hospital

Nordbyhagen, , Norway

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Oslo University Hospital-The Norwegian Radium Hospital

Oslo, , Norway

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Stavanger University Hospital

Stavanger, , Norway

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II Klinika Chorob Pluc i Gruzlicy

Bialystok, , Poland

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Onko-Centrum Sp. z o.o.

Lublin, , Poland

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Med Polonia Sp. z o.o.

Poznan, , Poland

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Centro Clinico Champalimaud

Lisbon, , Portugal

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Instituto Portugues de Oncologio de Lisboa

Lisbon, , Portugal

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Centro Hospitalar Universitario do Porto - Hospital de Santo Antonio

Porto, , Portugal

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Centro Hospitalar de Vila Nova de Gaia - Espinho

Porto, , Portugal

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National University Cancer Institute National University Hospital

Singapore, , Singapore

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National Cancer Centre Singapore NCCS

Singapore, , Singapore

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Tan Tock Seng Hospital

Singapore, , Singapore

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ICON Cancer Centre

Singapore, , Singapore

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Chungbuk National University Hospital

Cheongju-si, , South Korea

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National Cancer Center

Goyang, , South Korea

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Seoul National University Bundang Hospital

Seongnam, , South Korea

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Seoul National University Hospital

Seoul, , South Korea

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Severance Hospital

Seoul, , South Korea

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Asan Medical Center

Seoul, , South Korea

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Samsung Medical Center

Seoul, , South Korea

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The Catholic University of Korea, Seoul St. Marys Hospital

Seoul, , South Korea

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Samsung Medical Center

Seoul, , South Korea

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Hospital Teresa Herrera C.H.U.A.C.

A Coruña, , Spain

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Hospital del Mar

Barcelona, , Spain

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Hospital Universitari Vall d'Hebron

Barcelona, , Spain

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Hospital Clinic i Provincial de Barcelona

Barcelona, , Spain

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Complejo Hospitalario Materno-Insular - Hospital Insular de Gran Canaria

Las Palmas de Gran Canaria, , Spain

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Hospital General Universitario Gregorio Maranon

Madrid, , Spain

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MD Anderson Cancer Center

Madrid, , Spain

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Hospital Universitario Fundacion Jimenez Diaz

Madrid, , Spain

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Hospital Universitario 12 de Octubre

Madrid, , Spain

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Hospital Regional Universitario Malaga

Málaga, , Spain

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Hospital Univeritario Marques de Valdecilla

Santander, , Spain

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Hospital Universitario Virgen Macarena

Seville, , Spain

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Hospital Universitario Virgen Macarena

Seville, , Spain

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Kantonsspital Graubuenden - Hauptstandort

Chur, , Switzerland

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Kantonsspital Winterthur KSW

Winterthur, , Switzerland

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E-Da Hospital

Kaohsiung City, , Taiwan

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Taichung Veterans General Hospital

Taichung, , Taiwan

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National Cheng Kung University Hospital NCKUH

Tainan City, , Taiwan

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National Taiwan University Hospital NTUH

Taipei, , Taiwan

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Taipei Veterans General Hospital

Taipei, , Taiwan

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Chang Gung Memorial Hospital-Linkou Branch

Taoyuan District, , Taiwan

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University Hospital Birmingham NHS Trust

Birmingham, , United Kingdom

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Beatson West of Scotland Cancer Centre

Glasgow, , United Kingdom

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Leeds Cancer Centre

Leeds, , United Kingdom

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University Hospitals of Leicester

Leicester, , United Kingdom

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Barts and The London NHS Trust - St Bartholomew s hospital - PET CT Centre

London, , United Kingdom

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The Royal Marsden Hospital NHS Foundation Trust

London, , United Kingdom

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The Royal Marsden NHS Foundation Trust

London, , United Kingdom

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The Christie Hospital

Manchester, , United Kingdom

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The Royal Wolverhampton NHS Trust

Wolverhampton, , United Kingdom

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Countries

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United States Australia Austria Belgium Canada China France Germany Hong Kong Italy Japan Netherlands Norway Poland Portugal Singapore South Korea Spain Switzerland Taiwan United Kingdom

References

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Mok T, Janne PA, Nishio M, Novello S, Reck M, Steuer C, Wu YL, Fougeray R, Fan PD, Meng J, Sternberg DW, Esker S, Yu HA. HERTHENA-Lung02: phase III study of patritumab deruxtecan in advanced EGFR-mutated NSCLC after a third-generation EGFR TKI. Future Oncol. 2024 May;20(15):969-980. doi: 10.2217/fon-2023-0602. Epub 2023 Dec 14.

Reference Type DERIVED
PMID: 38095056 (View on PubMed)

Yu HA, Goto Y, Hayashi H, Felip E, Chih-Hsin Yang J, Reck M, Yoh K, Lee SH, Paz-Ares L, Besse B, Bironzo P, Kim DW, Johnson ML, Wu YL, John T, Kao S, Kozuki T, Massarelli E, Patel J, Smit E, Reckamp KL, Dong Q, Shrestha P, Fan PD, Patel P, Sporchia A, Sternberg DW, Sellami D, Janne PA. HERTHENA-Lung01, a Phase II Trial of Patritumab Deruxtecan (HER3-DXd) in Epidermal Growth Factor Receptor-Mutated Non-Small-Cell Lung Cancer After Epidermal Growth Factor Receptor Tyrosine Kinase Inhibitor Therapy and Platinum-Based Chemotherapy. J Clin Oncol. 2023 Dec 10;41(35):5363-5375. doi: 10.1200/JCO.23.01476. Epub 2023 Sep 10.

Reference Type DERIVED
PMID: 37689979 (View on PubMed)

Other Identifiers

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2021-005879-40

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

jRCT 2021220002

Identifier Type: OTHER

Identifier Source: secondary_id

U31402-A-U301

Identifier Type: -

Identifier Source: org_study_id

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