Whole Exome Screening of Newborns

NCT ID: NCT05325749

Last Updated: 2022-04-13

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

UNKNOWN

Total Enrollment

7000 participants

Study Classification

OBSERVATIONAL

Study Start Date

2021-07-10

Study Completion Date

2022-12-31

Brief Summary

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The aim of the study is to obtain the initial experience of the inclusive genetic screening of newborn.

Two groups of newborns born in RCOGP will be enlisted to the study:

1. newborns without developmental features having no variations according to an inherited diseases screening;
2. newborns showing either phenotypic features or deviations according to MS screening.

The residual volume of the cord blood of all newborns form both groups will be collected and subjected to the whole exome sequencing. The sequencing data will be analyzed in "screening" mode for the first group while for the second group analysis will be performed taking the respective phenotype into account.

The study is planned to cover 7000 newborns in total.

Detailed Description

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Conditions

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Infant, Newborn

Study Design

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Observational Model Type

COHORT

Study Time Perspective

CROSS_SECTIONAL

Study Groups

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unaffected

newborns without developmental features having no variations according to an inherited diseases screening;

Screening

Intervention Type GENETIC

Whole exome sequencing will be done and all infants will receive a report which will include pathogenic or likely pathogenic variants identified in genes associated with childhood-onset diseases for which specific care or prevention protocols are available. Families signed additional informed consent will receive an advanced report including variants with no care or prevention available, mid or low risk variants, and variants with late onset or those suggesting relatives to undergo screening.

Family history record

Intervention Type GENETIC

Families enrolled to the study will receive a genetic consult during which a family history will be taken concerning the inherited conditions.

Questionnaire survey

Intervention Type OTHER

Families invited to the study will be asked to undergo a questionnaire survey regarding the reasons to accept or refuse the study, the familiarity of the aims, methods and outcomes of the study as well as the satisfaction.

affected

newborns showing either phenotypic features or deviations according to MS screening

Screening

Intervention Type GENETIC

Whole exome sequencing will be done and all infants will receive a report which will include pathogenic or likely pathogenic variants identified in genes associated with childhood-onset diseases for which specific care or prevention protocols are available. Families signed additional informed consent will receive an advanced report including variants with no care or prevention available, mid or low risk variants, and variants with late onset or those suggesting relatives to undergo screening.

Family history record

Intervention Type GENETIC

Families enrolled to the study will receive a genetic consult during which a family history will be taken concerning the inherited conditions.

Questionnaire survey

Intervention Type OTHER

Families invited to the study will be asked to undergo a questionnaire survey regarding the reasons to accept or refuse the study, the familiarity of the aims, methods and outcomes of the study as well as the satisfaction.

Diagnostic

Intervention Type GENETIC

The results of whole exome sequencing will be analysed according to the infant's phenotype in addition the the general screening pipeline

refused families

parents refused to enroll their newborns to the study

Questionnaire survey

Intervention Type OTHER

Families invited to the study will be asked to undergo a questionnaire survey regarding the reasons to accept or refuse the study, the familiarity of the aims, methods and outcomes of the study as well as the satisfaction.

unaffected born prematurely

newborns without specific developmental features having no variations according to an inherited diseases screening, born before term

Screening

Intervention Type GENETIC

Whole exome sequencing will be done and all infants will receive a report which will include pathogenic or likely pathogenic variants identified in genes associated with childhood-onset diseases for which specific care or prevention protocols are available. Families signed additional informed consent will receive an advanced report including variants with no care or prevention available, mid or low risk variants, and variants with late onset or those suggesting relatives to undergo screening.

Family history record

Intervention Type GENETIC

Families enrolled to the study will receive a genetic consult during which a family history will be taken concerning the inherited conditions.

Questionnaire survey

Intervention Type OTHER

Families invited to the study will be asked to undergo a questionnaire survey regarding the reasons to accept or refuse the study, the familiarity of the aims, methods and outcomes of the study as well as the satisfaction.

Selective screening

Intervention Type GENETIC

The results of whole exome sequencing will be analysed according to the data of prenatal ultrasound examination, family history and other available alarming information in addition the the general screening pipeline

unaffected wirh family history

newborns without developmental features having no variations according to an inherited diseases screening but with affected relative(s)

Screening

Intervention Type GENETIC

Whole exome sequencing will be done and all infants will receive a report which will include pathogenic or likely pathogenic variants identified in genes associated with childhood-onset diseases for which specific care or prevention protocols are available. Families signed additional informed consent will receive an advanced report including variants with no care or prevention available, mid or low risk variants, and variants with late onset or those suggesting relatives to undergo screening.

Family history record

Intervention Type GENETIC

Families enrolled to the study will receive a genetic consult during which a family history will be taken concerning the inherited conditions.

Questionnaire survey

Intervention Type OTHER

Families invited to the study will be asked to undergo a questionnaire survey regarding the reasons to accept or refuse the study, the familiarity of the aims, methods and outcomes of the study as well as the satisfaction.

Selective screening

Intervention Type GENETIC

The results of whole exome sequencing will be analysed according to the data of prenatal ultrasound examination, family history and other available alarming information in addition the the general screening pipeline

unaffected wirh prenatal phenotype

newborns without developmental features at birth and on, having no variations according to an inherited diseases screening which had been observed to show signs of developmental features during prenatal ultrasound examination

Screening

Intervention Type GENETIC

Whole exome sequencing will be done and all infants will receive a report which will include pathogenic or likely pathogenic variants identified in genes associated with childhood-onset diseases for which specific care or prevention protocols are available. Families signed additional informed consent will receive an advanced report including variants with no care or prevention available, mid or low risk variants, and variants with late onset or those suggesting relatives to undergo screening.

Family history record

Intervention Type GENETIC

Families enrolled to the study will receive a genetic consult during which a family history will be taken concerning the inherited conditions.

Questionnaire survey

Intervention Type OTHER

Families invited to the study will be asked to undergo a questionnaire survey regarding the reasons to accept or refuse the study, the familiarity of the aims, methods and outcomes of the study as well as the satisfaction.

Selective screening

Intervention Type GENETIC

The results of whole exome sequencing will be analysed according to the data of prenatal ultrasound examination, family history and other available alarming information in addition the the general screening pipeline

Interventions

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Screening

Whole exome sequencing will be done and all infants will receive a report which will include pathogenic or likely pathogenic variants identified in genes associated with childhood-onset diseases for which specific care or prevention protocols are available. Families signed additional informed consent will receive an advanced report including variants with no care or prevention available, mid or low risk variants, and variants with late onset or those suggesting relatives to undergo screening.

Intervention Type GENETIC

Family history record

Families enrolled to the study will receive a genetic consult during which a family history will be taken concerning the inherited conditions.

Intervention Type GENETIC

Questionnaire survey

Families invited to the study will be asked to undergo a questionnaire survey regarding the reasons to accept or refuse the study, the familiarity of the aims, methods and outcomes of the study as well as the satisfaction.

Intervention Type OTHER

Diagnostic

The results of whole exome sequencing will be analysed according to the infant's phenotype in addition the the general screening pipeline

Intervention Type GENETIC

Selective screening

The results of whole exome sequencing will be analysed according to the data of prenatal ultrasound examination, family history and other available alarming information in addition the the general screening pipeline

Intervention Type GENETIC

Eligibility Criteria

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Inclusion Criteria

* Infants born in the RCOGP, showing no development features and with no inherited diseases revealed by common screening
* Informed consent signed by a newborn's representative


* Infants showing either phenotypic features or deviations according to MS screening
* Informed consent signed by a newborn's representative

Exclusion Criteria

* Parents refuse to participate
* Parent(s) younger 18 years
* Parent(s) unable to make decisions
* The infant is older 30 d
* Blood cannot be collected from the infant

Group 2 (newborns with phenotypic features)


* Parents refuse to participate
* Parent(s) younger 18 years
* Parent(s) unable to make decisions
* Blood cannot be collected from the infant
* Detailed description of the phenotype is not available
* The infant's exome has been already sequenced
Eligible Sex

ALL

Accepts Healthy Volunteers

Yes

Sponsors

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Federal State Budget Institution Research Center for Obstetrics, Gynecology and Perinatology Ministry of Healthcare

OTHER_GOV

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Dmitriy Y Trofimov, DSc

Role: STUDY_DIRECTOR

Federal State Budget Institution Research Center for Obstetrics, Gynecology and Perinatology Ministry of Healthcare

Locations

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Federal State Budget Institution Research Center for Obstetrics, Gynecology and Perinatology Ministry of Healthcare

Moscow, , Russia

Site Status RECRUITING

Countries

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Russia

Central Contacts

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Jekaterina Shubina, PhD

Role: CONTACT

+7 926 721-87-17

Andrey A Bystritskiy, PhD

Role: CONTACT

+7 903 722-10-34

Facility Contacts

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Elena A Gorodnova, PhD

Role: primary

+7 (495) 531-44-44

References

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Kochetkova TO, Maslennikov DN, Tolmacheva ER, Shubina J, Bolshakova AS, Suvorova DI, Degtyareva AV, Orlovskaya IV, Kuznetsova MV, Rachkova AA, Sukhikh GT, Rebrikov DV, Trofimov DY. De Novo Variant in the KCNJ9 Gene as a Possible Cause of Neonatal Seizures. Genes (Basel). 2023 Jan 31;14(2):366. doi: 10.3390/genes14020366.

Reference Type DERIVED
PMID: 36833293 (View on PubMed)

Other Identifiers

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Examen

Identifier Type: -

Identifier Source: org_study_id

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