Phase II Trial of Neoadjuvant and Adjuvant IO102-IO103 and Pembrolizumab KEYTRUDA® in Patients With Resectable Tumors

NCT ID: NCT05280314

Last Updated: 2024-03-18

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE2

Total Enrollment

60 participants

Study Classification

INTERVENTIONAL

Study Start Date

2023-12-21

Study Completion Date

2027-01-31

Brief Summary

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This is a multicenter, multi-arm trial evaluating anti-tumor activity, safety, and immune infiltration of IO102-IO103 in combination with pembrolizumab KEYTRUDA® as neoadjuvant and post-surgery treatment. This proof-of-concept trial will include patients with resectable tumors in at least 2 indications.

Detailed Description

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This is a multicenter, multi-arm trial evaluating anti-tumor activity, safety, and immune infiltration of IO102-IO103 in combination with pembrolizumab KEYTRUDA® as neoadjuvant and post-surgery treatment. Approximately 60 patients with melanoma or SCCHN will be included (approximately 15 for each indication).During the neoadjuvant period, patients in cohort A, cohort B and Cohort C (Arm A) will receive IO102-IO103 and pembrolizumab KEYTRUDA® Q3W. Patients in Cohort C (Arm B) will receive pembrolizumab KEYTRUDA® Patients with melanoma will receive 3 doses of neoadjuvant treatment. Patients with SCCHN will receive 2 or 3 doses of neoadjuvant treatment, at the investigator's discretion. Surgical resection will be performed 1 to 3 weeks after the last dose of neoadjuvant treatment. All patients in cohort A,B and Cohort C (Arm A)will receive post-surgery treatment with IO102-IO103 and pembrolizumab KEYTRUDA® for a total of 15 cycles (up to 45 weeks). Patients in Cohort C (Arm B) will receive post-surgery treatment with pembrolizumab KEYTRUDA® for a total of 15 cycles (up to 45 weeks).

Patients with melanoma and patients with SCCHN who do not require SOC RT ± cisplatin will start post-surgery treatment after adequate recovery from surgery (approximately 1 to 2 months; no more than 12 weeks).Patients with SCCHN who require postoperative SOC therapy after surgery will start post-surgery IO102-IO103 and pembrolizumab KEYTRUDA® after adequate recovery from SOC therapy (approximately 1 to 2 months; no more than 12 weeks).

Objective response will be based on imaging; pathologic tumor response of the surgical specimens will be assessed at the time of surgery. Safety will be assessed by recording adverse events. The primary endpoint will be the percentage of patients with major pathologic response (MPR) in the resected tumor tissue after neoadjuvant treatment. Secondary endpoints include disease-free survival (DFS) at 2 years after surgery. All patients will have an end-of-treatment visit approximately 4 weeks after their last dose of trial treatment. Follow-up visits will be conducted at 6 and 12 months after the end-of-treatment visit. Following completion of the 12-month follow-up period, long-term follow-up for overall survival (OS) will be conducted every 6 months for at least a further 12 month.

Conditions

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Melanoma Squamous Cell Carcinoma of Head and Neck

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

PARALLEL

Multicenter, Multi-arm, Two indications, One Cohort SCCHN 2 Cohorts melanoma (1 cohort randomized and one cohort not randomized)
Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Cohort A - Melanoma

Cutaneous resectable Stage III melanoma.

Neoadjuvant Treatment (3 cycles): Subcutaneous IO102-IO103 (IO102 85 μg and IO103 85 μg) and intravenous Pembrolizumab KEYTRUDA® 200mg Q3W.

Post-surgery Treatment (15 cycles): Subcutaneous IO102-IO103 (IO102 85 μg and IO103 85 μg) and intravenous Pembrolizumab KEYTRUDA® 200mg Q3W.

Group Type EXPERIMENTAL

IO102-IO103

Intervention Type DRUG

IO102-IO103 is a combination of an indoleamine 2,3-dioxygenase 1 (IDO1) peptide (IO102) and a programmed death-ligand 1 (PD-L1) peptide (IO103), emulsified with an adjuvant (Montanide ISA 51 VG).

Pembrolizumab KEYTRUDA®

Intervention Type DRUG

Pembrolizumab KEYTRUDA® administered intravenously

Cohort B - SCCHN

Stage III or IVA resectable locoregionally advanced Squamous cell carcinoma of the head and neck (SCCHN) of the oral cavity, oropharynx (HPV-negative), hypopharynx, or larynx

Neoadjuvant Treatment (2-3 cycles): Subcutaneous IO102-IO103 (IO102 85 μg and IO103 85 μg) and intravenous Pembrolizumab KEYTRUDA® 200mg Q3W Post-surgery Treatment (15 cycles): Subcutaneous IO102-IO103 (IO102 85 μg and IO103 85 μg) and intravenous Pembrolizumab KEYTRUDA® 200mg Q3W.

Group Type EXPERIMENTAL

IO102-IO103

Intervention Type DRUG

IO102-IO103 is a combination of an indoleamine 2,3-dioxygenase 1 (IDO1) peptide (IO102) and a programmed death-ligand 1 (PD-L1) peptide (IO103), emulsified with an adjuvant (Montanide ISA 51 VG).

Pembrolizumab KEYTRUDA®

Intervention Type DRUG

Pembrolizumab KEYTRUDA® administered intravenously

Cohort C

Cutaneous resectable Stage III melanoma. Neoadjuvant Treatment (3 cycles): Subcutaneous IO102-IO103 (IO102 85 μg and IO103 85 μg) and intravenous Pembrolizumab KEYTRUDA® 200mg Q3W (Arm A) versus intravenous Pembrolizumab KEYTRUDA® 200mg Q3W alone (Arm B) Post-surgery Treatment (15 cycles): Subcutaneous IO102-IO103 (IO102 85 μg and IO103 85 μg) and intravenous Pembrolizumab KEYTRUDA® 200mg Q3W (Arm A) versus Pembrolizumab KEYTRUDA® 200mg Q3W alone (Arm B)

Group Type EXPERIMENTAL

IO102-IO103

Intervention Type DRUG

IO102-IO103 is a combination of an indoleamine 2,3-dioxygenase 1 (IDO1) peptide (IO102) and a programmed death-ligand 1 (PD-L1) peptide (IO103), emulsified with an adjuvant (Montanide ISA 51 VG).

Pembrolizumab KEYTRUDA®

Intervention Type DRUG

Pembrolizumab KEYTRUDA® administered intravenously

Interventions

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IO102-IO103

IO102-IO103 is a combination of an indoleamine 2,3-dioxygenase 1 (IDO1) peptide (IO102) and a programmed death-ligand 1 (PD-L1) peptide (IO103), emulsified with an adjuvant (Montanide ISA 51 VG).

Intervention Type DRUG

Pembrolizumab KEYTRUDA®

Pembrolizumab KEYTRUDA® administered intravenously

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

• Histologically or cytologically confirmed diagnosis of cutaneous stage III melanoma according to the American Joint Committee on Cancer (AJCC) 8th edition.

Patients with resectable tumors are eligible for this trial either at presentation for primary melanoma with concurrent regional nodal metastasis or at the time of clinically detected nodal recurrence; they may belong to any of the following groups:

* Primary cutaneous melanoma with clinically apparent regional lymph node metastases
* Clinically detected recurrent melanoma at the proximal regional lymph node(s) basin
* Clinically detected primary cutaneous melanoma involving multiple regional nodal groups
* Clinically detected nodal melanoma (if single site) arising from an unknown primary
* Relapsed resectable stage III melanoma


• Stage III or IVA resectable locoregionally advanced SCCHN of the oral cavity, oropharynx (with known HPV-negative or p16-negative status assessed per institution standard or centrally), hypopharynx, or larynx.



1. Measurable disease based on Response Evaluation Criteria In Solid Tumors (RECIST) 1.1
2. Candidate for surgical resection with curative intent
3. The patient (or legally acceptable representative if applicable) provides written informed consent for the trial.
4. Age ≥18 years on the day of signing the informed consent form
5. Have provided archival tumor tissue sample or newly obtained core or excisional biopsy of a tumor lesion not previously irradiated. Formalin-fixed, paraffin embedded (FFPE) tissue blocks are preferred to slides.
6. Eastern Cooperative Oncology Group (ECOG) performance score status of 0 or 1
7. Adequate organ function as defined below performed on screening labs obtained within 4 weeks before first dose:

* Absolute neutrophil count (ANC) ≥1500/µL
* Platelets ≥100 000/µL
* Hemoglobin ≥9.0 g/dL or ≥5.6 mmol/L (Note: Criterion must be met without packed red blood cell transfusion within the prior 2 weeks. Patients can be on stable dose of erythropoietin \[≥ approximately 3 months\].)
* Creatinine or measured or calculated creatinine clearance (glomerular filtration rate can also be used in place of creatinine or creatinine clearance) ≤1.5 × upper limit of normal (ULN) or ≥30 mL/min for patient with creatinine levels \>1.5 × institutional ULN
* Serum total bilirubin ≤1.5 × ULN or direct bilirubin ≤ ULN for patients with total bilirubin levels \>1.5 × ULN
* Aspartate aminotransferase (AST) and alanine aminotransferase (ALT) ≤2.5 × ULN
* International normalized ratio (INR) or prothrombin time (PT) ≤1.5 × ULN unless the patient is receiving anticoagulant therapy as long as PT or partial thromboplastin time (PTT) is within the therapeutic range of intended use of anticoagulants
* Activated partial thromboplastin time (aPTT) ≤1.5 × ULN unless the patient is receiving anticoagulant therapy as long as PT or PTT is within the therapeutic range of intended use of anticoagulants
8. Women of childbearing potential: Negative urine or serum pregnancy within 72 hours prior to receiving the first dose of trial medication. If the urine test is positive or cannot be confirmed as negative, a serum pregnancy test will be required.
9. Women of childbearing potential: Willing to use highly effective contraception or abstain from heterosexual activity for the duration of the trial and for at least 120 days after the last dose of trial medication
10. HIV-infected patients must be on anti-retroviral therapy (ART) and have a well-controlled HIV infection/disease defined as:

a Patients on ART must have a CD4+ T-cell count \>350 cells/mm3 at time of screening b Patients on ART must have achieved and maintained virologic suppression defined as confirmed HIV RNA level below 50 copies/mL or the lower limit of qualification (below the limit of detection) using the locally available assay at the time of screening and for at least 12 weeks prior to first dose of trial medication (Day 1) c Patients on ART must have been on a stable regimen, without changes in drugs or dose modification, for at least 4 weeks prior to first dose of trial medication (Day 1) 11. Patients who are hepatitis B surface antigen (HBsAg) positive are eligible if they have received hepatitis B (HBV) antiviral therapy for at least 4 weeks and have undetectable HBV viral load prior to start of trial intervention.

Note: Patients should remain on anti-viral therapy throughout trial intervention and follow local guidelines for HBV anti-viral therapy after completion of trial intervention.

Hepatitis B screening tests are not required unless:

* Known history of HBV infection
* Mandated by local health authority. 12. Patients with a history of hepatitis C (HCV) infection are eligible if HCV viral load is undetectable at screening.

Note: Patients must have completed curative antiviral therapy at least 4 weeks prior to start of trial intervention.

Hepatitis C screening tests are not required unless:

* Known history of HCV infection
* Mandated by local health authority.

Exclusion Criteria

* Current or prior history of uveal, mucosal, or acral melanoma
* Oligometastatic stage IV melanoma
* History of in-transit metastases within the last 6 months
* Prior therapy targeting BRAF and/or MEK


• Nasopharyngeal cancer, unknown primary, nasal cavity or paranasal sinus carcinoma


In addition, patients meeting any of the following criteria must be excluded:

1. Currently participating in or has participated in a trial of an investigational agent or has used an investigational device within 4 weeks of the first dose of trial treatment Note: Patients who have entered the follow-up phase of an investigational trial may participate as long as it has been 4 weeks after the last dose of the previous investigational agent.
2. Any prior treatment for the tumor under study
3. Prior therapy for another tumor with an anti-PD-1, anti-PD-L1, or anti-PD-L2 agent or with an agent directed to another stimulatory or co-inhibitory T-cell receptor (e.g., CTLA-4, OX40, CD137), and discontinued from that treatment due to a grade 3 or higher immune-related adverse event (irAE)
4. Prior chemotherapy, targeted small molecule therapy, or radiation therapy within 2 weeks prior to first dose of trial treatment

* Note: Patients must have recovered from all adverse events (AEs) due to previous therapies (i.e., grade ≤1 at baseline). Patients with grade ≤2 neuropathy are eligible for the trial. Patients with endocrine-related AEs grade ≤2 requiring treatment or hormone replacement are also eligible.
* Note: If the patient has had major surgery, the patient must have recovered adequately from the procedure and/or complications from the surgery prior to starting trial treatment.
5. Live or live-attenuated vaccine within 30 days prior to the first dose of trial treatment. Note: Administration of inactivated vaccines, mRNA-based vaccines \[e.g., COVID-19\] and vector-based vaccines are allowed.
6. Diagnosis of immunodeficiency or receiving systemic steroid therapy or any other form of immunosuppressive therapy within 7 days prior to the first dose of trial treatment. Patients who are currently receiving steroids at a dose equivalent to \<5 mg/day of prednisone do not need to discontinue steroids prior to enrollment. Patients who require topical, ophthalmologic and inhalational steroids will not be excluded from the trial. Patients with hypothyroidism stable on hormone replacement or Sjögren's syndrome will not be excluded from the trial.
7. Additional malignancy that is progressing or requires active treatment. Exceptions include basal cell carcinoma of the skin, squamous cell carcinoma of the skin, or in situ cervical cancer that has undergone potentially curative therapy.
8. History of an allogeneic tissue/solid organ transplant.
9. Active autoimmune disease that has required systemic treatment in past 2 years (i.e., with use of disease modifying agents, corticosteroids or immunosuppressive drugs). Patients with type I diabetes mellitus; hypothyroidism only requiring hormone replacement; skin disorders (such as vitiligo, psoriasis, or alopecia) not requiring systemic treatment; or conditions not expected to recur in the absence of an external trigger are permitted to enroll.
10. History of radiation pneumonitis
11. History of (non-infectious) pneumonitis/interstitial lung disease that required steroids or has current pneumonitis/interstitial lung disease
12. Active infection requiring systemic therapy
13. HIV-infected patients with a history of Kaposi sarcoma and/or Multicentric Castleman Disease
14. Has known active hepatitis B virus (HBV; defined as hepatitis B surface antigen \[HBsAg\] reactive and/or detectable HBV DNA) or known active hepatitis C virus (HCV) (defined as anti HCV Ab positive and detectable HCV ribonucleic acid \[RNA\] \[qualitative\]) infection.

Note: Testing for hepatitis B and hepatitis C is not required unless
1. Known history of HBV or HCV infection
2. Mandated by local health authority. Patients with a history of hepatitis will be screened using serology to confirm status.
15. History or current evidence of any condition, therapy, or laboratory abnormality that might confound the results of the trial, interfere with the patient's participation for the full duration of the trial, or is not in the best interest of the patient to participate, in the opinion of the treating investigator
16. Psychiatric or substance abuse disorders that would interfere with the patient's ability to cooperate with the trial requirements
17. Severe hypersensitivity (grade ≥3) to pembrolizumab and/or any of its excipients
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Theradex

INDUSTRY

Sponsor Role collaborator

Almac

INDUSTRY

Sponsor Role collaborator

Merck Sharp & Dohme LLC

INDUSTRY

Sponsor Role collaborator

IO Biotech

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Barbara Burtness, MD, Prof

Role: PRINCIPAL_INVESTIGATOR

Yale New Haven Hospital - Yale Cancer Center

Locations

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Yale

New Haven, Connecticut, United States

Site Status RECRUITING

Dana Farber Cancer Institute

Boston, Massachusetts, United States

Site Status RECRUITING

Massey Cancer Center

Richmond, Virginia, United States

Site Status RECRUITING

Melanoma Institute Australia The Uiniversity of Sydney, and Royal North Shore Hospital

Sydney, New South Wales, Australia

Site Status RECRUITING

Peter MacCallum Cancer Centre

Melbourne, Victoria, Australia

Site Status RECRUITING

Aarhus University Hospital

Aarhus, , Denmark

Site Status RECRUITING

Copenhagen University Hospital Herlev

Copenhagen, , Denmark

Site Status RECRUITING

CHRU Lille

Lille, , France

Site Status RECRUITING

Hôpital Ambroise-Paré

Paris, , France

Site Status RECRUITING

Institut Gustave Roussy

Paris, , France

Site Status RECRUITING

Universitätsklinikum Essen & Research Alliance Ruhr

Essen, , Germany

Site Status RECRUITING

Universität Heidelberg, Medizinische Fakultät

Heidelberg, , Germany

Site Status RECRUITING

Hospital Universitario Quirón Dexeus

Barcelona, , Spain

Site Status RECRUITING

Hospital Universitario Ramón y Cajal

Madrid, , Spain

Site Status RECRUITING

Hospital Clínico Universitario de Valencia -INCLIVA

Valencia, , Spain

Site Status RECRUITING

Countries

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United States Australia Denmark France Germany Spain

Central Contacts

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Diane McDowell SVP, Clinical Development and Medical Affairs, MD

Role: CONTACT

+1 267 252 7296

Shane O'Neill Clinical Program Director

Role: CONTACT

+44 790 433 7285

Facility Contacts

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Stacy Severin

Role: primary

Barry Anderson

Role: primary

Kartik Sehgal

Role: backup

Carrie Donovan

Role: primary

Karen Bush

Role: primary

Maria Vassiliou, Dr

Role: primary

(03)85595000

Caroline Suhr

Role: backup

Mona Kjaer

Role: primary

Tina Kusk

Role: backup

Signe Reinhold

Role: primary

Sylvie Brice

Role: primary

Veronique Clerisse

Role: primary

Myriam Maalej-Chaari

Role: primary

Katharina Metz

Role: primary

Melanie Leieren

Role: primary

Carlos Esparre

Role: primary

Alba Silvestre

Role: backup

Lucia Castillon

Role: primary

Pardo de Vera

Role: backup

Inma Blasco

Role: primary

Silvia Moreno

Role: backup

Other Identifiers

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MK-3475-E40

Identifier Type: OTHER

Identifier Source: secondary_id

IO102-IO103-032/IOB-032

Identifier Type: -

Identifier Source: org_study_id

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