Substudy 02A: Safety and Efficacy of Pembrolizumab in Combination With Investigational Agents in Participants With Programmed Cell-death 1 (PD-1) Refractory Melanoma (MK-3475-02A/KEYMAKER-U02)

NCT ID: NCT04305041

Last Updated: 2025-08-29

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE1/PHASE2

Total Enrollment

100 participants

Study Classification

INTERVENTIONAL

Study Start Date

2020-06-26

Study Completion Date

2025-08-25

Brief Summary

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Substudy 02A is part of a larger research study that is testing experimental treatments for melanoma, a type of skin cancer. The larger study is the umbrella study.

The goal of substudy 02A is to evaluate the safety and efficacy of investigational treatment arms in participants with PD-1 refractory melanoma to identify the investigational agent(s) that, when used in combination, are superior to the current treatment options/historical control available.

As of Amendment 4 (effective date: 05JAN2022), a third arm has been opened to participant enrollment, treatment with pembrolizumab and all-trans retinoic acid (ATRA). Enrollment into the first two arms, treatment with pembrolizumab + quavonlimab+ vibostolimab and treatment with pembrolizumab + quavonlimab + lenvatinib has been completed per protocol as of September 2021.

Detailed Description

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Conditions

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Melanoma

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Pembrolizumab + Quavonlimab + Vibostolimab

Participants will receive pembrolizumab intravenously (IV) plus quavonlimab IV plus vibostolimab IV at specified doses on specified days for a total treatment duration of up to approximately 2 years.

Group Type EXPERIMENTAL

Pembrolizumab

Intervention Type BIOLOGICAL

Administered via IV infusion at a specified dose on specified days

Quavonlimab

Intervention Type BIOLOGICAL

Administered via IV infusion at a specified dose on specified days

Vibostolimab

Intervention Type BIOLOGICAL

Administered via IV infusion at a specified dose on specified days

Pembrolizumab + Quavonlimab + Lenvatinib

Participants will receive pembrolizumab IV plus quavonlimab IV plus lenvatinib orally at specified doses on specified days for a total treatment duration of up to approximately 2 years.

Group Type EXPERIMENTAL

Pembrolizumab

Intervention Type BIOLOGICAL

Administered via IV infusion at a specified dose on specified days

Quavonlimab

Intervention Type BIOLOGICAL

Administered via IV infusion at a specified dose on specified days

Lenvatinib

Intervention Type DRUG

Administered via oral capsules at a specified dose on specified days

Pembrolizumab + all-trans retinoic acid (ATRA)

Participants will receive pembrolizumab IV plus ATRA orally at specified doses on specified days for a total treatment duration of up to approximately 2 years

Group Type EXPERIMENTAL

ATRA

Intervention Type DRUG

Administered via oral capsules at a specified dose on specified days

Interventions

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Pembrolizumab

Administered via IV infusion at a specified dose on specified days

Intervention Type BIOLOGICAL

Quavonlimab

Administered via IV infusion at a specified dose on specified days

Intervention Type BIOLOGICAL

Vibostolimab

Administered via IV infusion at a specified dose on specified days

Intervention Type BIOLOGICAL

Lenvatinib

Administered via oral capsules at a specified dose on specified days

Intervention Type DRUG

ATRA

Administered via oral capsules at a specified dose on specified days

Intervention Type DRUG

Other Intervention Names

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MK-3475 KEYTRUDA® MK-1308 MK-7684 MK-7902 LENVIMA® VESANOID

Eligibility Criteria

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Inclusion Criteria

* Has histologically or cytologically confirmed melanoma
* Has unresectable Stage III or Stage IV melanoma, not amenable to local therapy
* Has progressed on treatment with an anti-PD-1/L1 monoclonal antibody (mAb) administered either as monotherapy, or in combination with other therapies
* Has imaging documenting progression per RECIST 1.1 and iRECIST after initiation of an anti-PD-1/L1 agent, or by RECIST 1.1 if progression occurred on adjuvant therapy or in the setting of rapid progression.
* Has not received more than 3 lines of therapy for their advanced melanoma
* Has provided a tumor biopsy
* Male participants who receive lenvatinib or ATRA are abstinent from heterosexual intercourse or agree to use contraception during the intervention period and for at least 7 days after the last dose of lenvatinib or ATRA; for male participants who only receive pembrolizumab, quavonlimab, vibostolimab, or a combination, no contraception measures are needed
* Female participant are not pregnant or breastfeeding and are either not a woman of child-bearing potential (WOCBP) OR use a contraceptive method that is highly effective or are abstinent from heterosexual intercourse during the intervention period and for at least 120 days after the last dose of pembrolizumab, quavonlimab, vibostolimab or 30 days after the last dose of lenvatinib or ATRA, whichever occurs last
* Has adequate organ function
* Has resolution of toxic effect(s) of the most recent prior therapy to Grade 1 or less (except alopecia)

Exclusion Criteria

* Has a diagnosis of immunodeficiency or is receiving immunosuppressive therapy within 7 days before the first dose of study intervention
* Has a known additional malignancy that is progressing or requires active treatment within the past 2 years
* Has known central nervous system (CNS) metastases and/or carcinomatous meningitis
* Has ocular or mucosal melanoma
* Has known hypersensitivity including previous clinically significant hypersensitivity reaction to treatment with another mAb
* Has an active autoimmune disease that has required systemic treatment in the past 2 years
* Has an active infection requiring systemic therapy
* Has known history of human immunodeficiency virus (HIV)
* Has known history of hepatitis B
* Has a history of (noninfectious) pneumonitis
* Has a history of active tuberculosis (TB)
* Has received prior systemic anticancer therapy within 4 weeks prior to randomization
* Has received prior radiotherapy within 2 weeks of first dose of study intervention
* Has had major surgery \<3 weeks prior to first dose of study intervention
* Has received a live vaccine within 30 days before the first dose of study intervention
* Has participated in a study of an investigational agent within 4 weeks prior to the first dose of study intervention
* Has had an allogeneic tissue/solid organ transplant
* Has a pre-existing Grade ≥3 gastrointestinal fistula or nongastrointestinal fistula
* Has radiographic evidence of encasement of invasion of major blood vessel or of intratumoral cavitation
* Has clinically significant hemoptysis or tumor bleeding within 2 weeks prior to the first dose of study intervention
* Has clinically significant cardiovascular disease within 12 months from first dose of study intervention
Minimum Eligible Age

18 Years

Maximum Eligible Age

120 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Merck Sharp & Dohme LLC

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Medical Director

Role: STUDY_DIRECTOR

Merck Sharp & Dohme LLC

Locations

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The Angeles Clinic and Research Institute ( Site 1009)

Los Angeles, California, United States

Site Status

UCLA Hematology & Oncology ( Site 1004)

Los Angeles, California, United States

Site Status

Providence Saint John's Health Center ( Site 1010)

Santa Monica, California, United States

Site Status

University of Colorado, Anschutz Cancer Pavilion ( Site 1012)

Aurora, Colorado, United States

Site Status

Sidney Kimmel Comprehensive Cancer Center at Johns Hopkins ( Site 1022)

Baltimore, Maryland, United States

Site Status

NYU Clinical Cancer Center ( Site 1002)

New York, New York, United States

Site Status

Duke Cancer Institute ( Site 1005)

Durham, North Carolina, United States

Site Status

Martha Morehouse Tower ( Site 1020)

Columbus, Ohio, United States

Site Status

Oregon Health & Science University ( Site 1013)

Portland, Oregon, United States

Site Status

University of Pennsylvania Abramson Cancer Center ( Site 1008)

Philadelphia, Pennsylvania, United States

Site Status

West Cancer Center - East Campus ( Site 1014)

Germantown, Tennessee, United States

Site Status

University of Texas MD Anderson Cancer Center ( Site 1006)

Houston, Texas, United States

Site Status

Inova Schar Cancer Institute ( Site 1011)

Fairfax, Virginia, United States

Site Status

Calvary Mater Newcastle-Medical Oncology ( Site 1404)

Waratah, New South Wales, Australia

Site Status

Melanoma Institute Australia ( Site 1402)

Wollstonecraft, New South Wales, Australia

Site Status

Tasman Oncology Research Pty Ltd ( Site 1403)

Southport, Queensland, Australia

Site Status

Fiona Stanley Hospital ( Site 1401)

Murdoch, Western Australia, Australia

Site Status

Hopital La Timone ( Site 1103)

Marseille, Bouches-du-Rhone, France

Site Status

Hopital Saint Andre ( Site 1108)

Bordeaux, Gironde, France

Site Status

Institut Claudius Regaud ( Site 1105)

Toulouse, Haute-Garonne, France

Site Status

Centre Hospitalier Lyon Sud ( Site 1102)

Pierre-Bénite, Rhone, France

Site Status

A.P.H. Paris, Hopital Saint Louis ( Site 1107)

Paris, , France

Site Status

Gustave Roussy ( Site 1101)

Villejuif, Île-de-France Region, France

Site Status

HaEmek Medical Center ( Site 1703)

Afula, , Israel

Site Status

Rambam Health Care Campus-Oncology ( Site 1704)

Haifa, , Israel

Site Status

Hadassah Ein Karem Jerusalem ( Site 1702)

Jerusalem, , Israel

Site Status

Chaim Sheba Medical Center ( Site 1701)

Ramat Gan, , Israel

Site Status

Fondazione IRCCS Istituto Nazionale dei Tumori di Milano ( Site 1399)

Milan, , Italy

Site Status

Istituto Europeo di Oncologia ( Site 1301)

Milan, , Italy

Site Status

Istituto Nazionale Tumori Fondazione Pascale ( Site 1302)

Napoli, , Italy

Site Status

Istituto Oncologico Veneto IRCCS ( Site 1355)

Padua, , Italy

Site Status

Policlinico Le Scotte - A.O. Senese ( Site 1377)

Siena, , Italy

Site Status

CANCERCARE LANGENHOVEN DRIVE ONCOLOGY CENTRE-Clinical Trials Unit ( Site 1865)

Port Elizabeth, Eastern Cape, South Africa

Site Status

Hôpitaux Universitaires de Genève (HUG)-Oncology ( Site 1603)

Geneva, Canton of Geneva, Switzerland

Site Status

CHUV Centre Hospitalier Universitaire Vaudois ( Site 1602)

Lausanne, Canton of Vaud, Switzerland

Site Status

Universitaetsspital Zuerich ( Site 1601)

Zuerich Flughafen, Canton of Zurich, Switzerland

Site Status

Countries

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United States Australia France Israel Italy South Africa Switzerland

Related Links

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Other Identifiers

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MK-3475-02A

Identifier Type: OTHER

Identifier Source: secondary_id

KEYMAKER-U02

Identifier Type: OTHER

Identifier Source: secondary_id

2023-506312-41-00

Identifier Type: REGISTRY

Identifier Source: secondary_id

U1111-1293-5630

Identifier Type: REGISTRY

Identifier Source: secondary_id

2019-003956-35

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

3475-02A

Identifier Type: -

Identifier Source: org_study_id

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