A Non-interventional Ambispective Real-world Cohort of rEfractory and reLapsed (R/R) FLT3 Mutated Acute MyEloid Leukemia (AML) Patients Treated With Gilteritinib in FrANCE

NCT ID: NCT05193448

Last Updated: 2023-05-24

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Total Enrollment

177 participants

Study Classification

OBSERVATIONAL

Study Start Date

2021-07-05

Study Completion Date

2022-01-31

Brief Summary

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Gilteritinib is available in early access in France through Temporary Authorisation of Use (or ATU program) since March 2019. The ATU program reflects a real-life treatment situation and the related clinical data would help to better understand the benefit/risk profile of gilteritinib and to better document gilteritinib efficacy and safety in patients who received midostaurine in First Line (1L) setting.

The main objective is to describe gilteritinib effectiveness in FLT3 (Fms Related Tyrosine Kinase 3) -mutated AML patients in Refractory/Relapsed(R/R) situation treated in the context of early access program to gilteritinib in France through Temporary Authorisation of Use, the so-called ATU program, and the post ATU period from marketing authorisation to launch when reimbursement and price are published.

Detailed Description

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Conditions

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Refractory AML Relapsed Adult AML FLT3-TKD Mutation FLT3-ITD

Study Design

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Observational Model Type

COHORT

Study Time Perspective

CROSS_SECTIONAL

Eligibility Criteria

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Inclusion Criteria

* Adult patients ≥ 18 years at AML diagnosis
* Patients that started gilteritinib during ATU and post-ATU period from 19th March 2019 to 30th March2021
* Patients diagnosed with refractory or relapsed AML as defined by the World Health Organization (WHO) Classification
* Patients with FLT3 genetic testing performed at diagnosis and/or at R/R (if available)
* Gilteritinib with or without other drug (chemotherapy, hypomethylating agent, hydroxyurea, etc.)

Exclusion Criteria

* Newly diagnosed AML patients
* Participant opposed to the collection and analysis of their medical data
* Prescription of gilteritinib out of the scope of its marketing authorisation approval such as post HSCT maintenance in patients in first complete remission after intensive chemotherapy
* persons placed in curatorship,guardianship or guardianship orders
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Acute Leukemia French Association

OTHER

Sponsor Role collaborator

French Innovative Leukemia Organisation

OTHER

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Amiens CHU

Amiens, , France

Site Status

Angers CHU

Angers, , France

Site Status

Avignon CH

Avignon, , France

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Bayonne CH

Bayonne, , France

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Besançon CHU

Besançon, , France

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Brest CHU

Brest, , France

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Caen CHU

Caen, , France

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CERGY PONTOISE - CH René Dubos

Cergy-Pontoise, , France

Site Status

CHU Estaing

Clermont-Ferrand, , France

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Corbeil-Essonnes - Ch Sud Francilien

Corbeil-Essonnes, , France

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Créteil CHU HENRI MONDOR

Créteil, , France

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Dijon CHU

Dijon, , France

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Grenoble CHU

Grenoble, , France

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Le Mans CH

Le Mans, , France

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Limoges CHU

Limoges, , France

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Lyon sud CHU

Lyon, , France

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Marseille IPC

Marseille, , France

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Meaux CH de l'Est francilien

Meaux, , France

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METZ-THIONVILLE CHR- Hôpital de Mercy

Metz, , France

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Montpellier - Chu Saint Eloi

Montpellier, , France

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Nantes CHU

Nantes, , France

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Nice CHU

Nice, , France

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Nimes CHU

Nîmes, , France

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Paris La Pitié salpetrière

Paris, , France

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Paris Necker

Paris, , France

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Paris Saint Louis

Paris, , France

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Bordeaux CHU

Pessac, , France

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Reims CHU

Reims, , France

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Rennes CHU

Rennes, , France

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roubaix CH

Roubaix, , France

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Institut de Cancérologie Lucien Neuwirth

Saint-Priest-en-Jarez, , France

Site Status

Saint Quentin CH

Saint-Quentin, , France

Site Status

Toulouse - IUCT Oncopole - Service d'Hématologie

Toulouse, , France

Site Status

Tours CHU

Tours, , France

Site Status

Troyes CH

Troyes, , France

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Nancy CHU

Vandœuvre-lès-Nancy, , France

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Versailles CH

Versailles, , France

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Villejuif IGR

Villejuif, , France

Site Status

Countries

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France

Other Identifiers

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ELEGANCE

Identifier Type: -

Identifier Source: org_study_id

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