Assessment of Patterns of Patient Reported Outcomes in Adults With Congenital Heart Disease - International Study II

NCT ID: NCT04902768

Last Updated: 2024-05-16

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Total Enrollment

8415 participants

Study Classification

OBSERVATIONAL

Study Start Date

2019-08-01

Study Completion Date

2022-12-31

Brief Summary

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This is an international, cross-sectional and descriptive study that aims to investigate differences in patient-reported outcome measures (PROMs) and patient-reported experience measures (PREMs) and that aims to explore the profile and healthcare needs of adults with congenital heart diseases.

Detailed Description

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The research aims of this study are:

1. To further explore differences in a modified selection of patient-reported outcome measures (PROMs) and (as a new addition in APPROACH-IS II) explore differences in patient-reported experience measures (PREMs), by enrolling adults with congenital heart diseases in low, middle, and high income countries and including new potential explanatory variables ("Part 1").
2. To explore the profile and healthcare needs of a subgroup of older adults with congenital heart disease, with a particular focus on investigating the frailty phenotype ("Part 2").

Conditions

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Congenital Heart Disease

Study Design

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Observational Model Type

CASE_ONLY

Study Time Perspective

CROSS_SECTIONAL

Study Groups

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Adults with congenital heart disease

This is an observational study, there is no intervention

Intervention Type OTHER

This is an observational study, there is no intervention. Hence, this is not applicable.

Interventions

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This is an observational study, there is no intervention

This is an observational study, there is no intervention. Hence, this is not applicable.

Intervention Type OTHER

Eligibility Criteria

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Inclusion Criteria

* Diagnosed with congenital heart disease, defined as: "a gross structural abnormality of the heart and/or intra-thoracic great vessels that is actually or potentially of functional significance (including mild, moderate, and complex heart defects)"
* Aged 18 years of age or older at the moment of study inclusion
* Diagnosed with congenital heart disease before the age of 10 years
* Follow-up at an ACHD center or included in a national/regional registry
* Physical, cognitive, and language abilities to complete self-report questionnaires

Exclusion Criteria

\- Prior heart transplantation
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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KU Leuven

OTHER

Sponsor Role lead

Responsible Party

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Philip Moons

Prof. Dr. Philip Moons

Responsibility Role PRINCIPAL_INVESTIGATOR

Principal Investigators

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Philip Moons, PhD, RN

Role: PRINCIPAL_INVESTIGATOR

Professor in Healthcare Sciences

Locations

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University of California

San Francisco, California, United States

Site Status

Lucile Packard Children's Hospital and Stanford Health Care

Stanford, California, United States

Site Status

University of Florida Health

Gainesville, Florida, United States

Site Status

Taussig Heart Center of Johns Hopkins Hospital

Baltimore, Maryland, United States

Site Status

Boston Children's / Brigham and Women's

Boston, Massachusetts, United States

Site Status

Mount Sinai Heart

New York, New York, United States

Site Status

Nationwide Children's Hospital

Columbus, Ohio, United States

Site Status

Oregon Health and Science University

Portland, Oregon, United States

Site Status

Philadelphia Penn Medicine

Philadelphia, Pennsylvania, United States

Site Status

University of Southwestern Medical Center

Dallas, Texas, United States

Site Status

Hospital San Juan De Dios De La Plata

Buenos Aires, , Argentina

Site Status

Hospital de Niños

Córdoba, , Argentina

Site Status

Melbourne Children's Cardiology

Melbourne, , Australia

Site Status

Vienna General Hospital

Vienna, , Austria

Site Status

Ghent University Hospital

Ghent, , Belgium

Site Status

University Hospitals Leuven

Leuven, , Belgium

Site Status

Princess Marina Hospital

Gaborone, , Botswana

Site Status

Hospital das Clinicas da Faculdade de Medicina de Ribeirão Preto

Ribeirão Preto, , Brazil

Site Status

National Heart Hospital

Sofia, , Bulgaria

Site Status

Clinique Medical Le Jourdain

Yaoundé, , Cameroon

Site Status

Mazankowski Alberta Heart Institute

Edmonton, , Canada

Site Status

Montreal Heart Institute, Université de Montréal

Montreal, , Canada

Site Status

Intituto Nacional Del Torax

Santiago, , Chile

Site Status

Meintegral Clinic

Manizales, , Colombia

Site Status

Copenhagen University Hospital

Copenhagen, , Denmark

Site Status

College of Health sciences, Addis Ababa University

Addis Ababa, , Ethiopia

Site Status

Hôpital cardiologique Haut-Leveque

Bordeaux, , France

Site Status

Montpellier University Hospital

Montpellier, , France

Site Status

Hôpital Européen Georges Pompidou

Paris, , France

Site Status

AHEPA University Hospital

Thessaloniki, , Greece

Site Status

Amrita Institute of Medical Sciences

Kochi, , India

Site Status

Policlinico San Donato (IRCCS)

Milan, , Italy

Site Status

Chiba Cerebral and Cardiovascular Center

Chiba, , Japan

Site Status

Paediatric & Congenital Heart Centre, IJN (National Heart Institute)

Kuala Lumpur, , Malaysia

Site Status

Mater Dei Hospital

Msida, , Malta

Site Status

Centrum voor Congenital Hartafwijkingen

Groningen, , Netherlands

Site Status

Oslo University Hospital, Rikshospitalet

Oslo, , Norway

Site Status

Aga Khan University Hospital

Karachi, , Pakistan

Site Status

Reference Center of Congenital Heart Disease , University Hospital Center of São João

Porto, , Portugal

Site Status

Centre Hospitalier Régional de Thiès

Thiès, , Senegal

Site Status

Samsung Medical Center

Seoul, , South Korea

Site Status

Sahlgrenska University Hospital

Gothenburg, , Sweden

Site Status

Skånes Universitetssjukhus

Lund, , Sweden

Site Status

Karolinska Universitetssjukhuset

Stockholm, , Sweden

Site Status

Umea University Hospital

Umeå, , Sweden

Site Status

Uppsala University Hospital

Uppsala, , Sweden

Site Status

University Hospital Bern

Bern, , Switzerland

Site Status

Hôpitaux Universitaires de Genève

Geneva, , Switzerland

Site Status

Centre Hospitalier universitaire vaudois

Lausanne, , Switzerland

Site Status

National Taiwan University Hospital

Taipei, , Taiwan

Site Status

Ege University Health Application and Research Center, Cardiology Department

Bornova, , Turkey (Türkiye)

Site Status

Royal Brompton Hospital, Royal Brompton & Harefield Hospitals, Guy's and St Thomas' NHS Foundation Trust

London, , United Kingdom

Site Status

Freeman Hospital, Newcastle Upon Tyne Hospitals NHS Foundation Trust

Newcastle, , United Kingdom

Site Status

Countries

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United States Argentina Australia Austria Belgium Botswana Brazil Bulgaria Cameroon Canada Chile Colombia Denmark Ethiopia France Greece India Italy Japan Malaysia Malta Netherlands Norway Pakistan Portugal Senegal South Korea Sweden Switzerland Taiwan Turkey (Türkiye) United Kingdom

References

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Ansari Ramandi MM, Van Bulck L, Ceelen DCH, Voors AA, Goossens E, Kovacs AH, Luyckx K, Van De Bruaene A, Gabriel H, Lykkeberg B, Thomet C, de Hosson M, Ladouceur M, Saidi A, Kosmidis D, Areias ME, Miranda J, Sandberg C, Mandalenakis Z, Coats L, Amedro P, Khairy P, Valente AM, Johansson B, Kaneva A, Andresen B, Christersson C, Reyes FB, Hlebowicz J, Enomoto J, Kim YY, Menahem S, Yang HL, Moon JR, Bredy C, Schmidt A, Callus E, Araujo JJ, Constantine A, Zaidi A, Bouchardy J, Jameson SM, Kutty S, McGrath LB, Leong MC, Ortiz L, Korkmaz FD, Caruana M, Leye M, Moons P, van Melle JP; APPROACH-IS II Consortium; International Society for Adults With Congenital Heart Disease. Quality of Life in Adults With Transposition of the Great Arteries With a Systemic Right or Left Ventricle. Can J Cardiol. 2025 Sep 15:S0828-282X(25)01161-4. doi: 10.1016/j.cjca.2025.09.010. Online ahead of print.

Reference Type DERIVED
PMID: 40962221 (View on PubMed)

Moons P, Kovacs AH, Goossens E, Luyckx K, Ladak L, Leye M, Van De Bruaene A, Leong MC, Kaneva A, Manso PH, Araujo JJ, Sasikumar N, Gabriel H, Yadeta D, Wang JK, Enomoto J, Areias ME, Kosmidis D, Coats L, Valente AM, Moon JR, Ladouceur M, Thomet C, Jackson JL, Sandberg C, Callus E, Kim YY, Lykkeberg B, Alday L, Bredy C, Saidi A, Baraona Reyes F, Menahem S, de Hosson M, Hlebowicz J, Christersson C, Zaidi AN, Johansson B, Andresen B, Ambassa JC, Mattsson E, Constantine A, Amedro P, van Melle JP, Kutty S, Ortiz L, Demir F, Khairy P, Windram J, Bouchardy J, Caruana M, Jameson SM, Mahadevan VS, McGrath LB, Mwita JC, Van Bulck L; APPROACH-IS II consortium, on behalf of the International Society for Adults Congenital Heart Disease (ISACHD). Perceived health, psychological distress and quality of life in 8415 adults with congenital heart disease from 32 countries. Heart. 2025 Aug 12;111(17):818-827. doi: 10.1136/heartjnl-2024-325296.

Reference Type DERIVED
PMID: 40579213 (View on PubMed)

Moons P, Goossens E, Luyckx K, Kovacs AH, Andresen B, Moon JR, Van De Bruaene A, Rassart J, Van Bulck L; APPROACH-IS II consortium and ISACHD. The COVID-19 pandemic as experienced by adults with congenital heart disease from Belgium, Norway, and South Korea: impact on life domains, patient-reported outcomes, and experiences with care. Eur J Cardiovasc Nurs. 2022 Aug 29;21(6):620-629. doi: 10.1093/eurjcn/zvab120.

Reference Type DERIVED
PMID: 34927192 (View on PubMed)

Other Identifiers

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S62537

Identifier Type: -

Identifier Source: org_study_id

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