Study of ARO-ANG3 in Adults With Mixed Dyslipidemia

NCT ID: NCT04832971

Last Updated: 2025-12-03

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

204 participants

Study Classification

INTERVENTIONAL

Study Start Date

2021-06-28

Study Completion Date

2024-09-25

Brief Summary

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The purpose of AROANG3-2001 is to evaluate the efficacy and safety of ARO-ANG3 in participants with mixed dyslipidemia. Participants will initially receive 2 subcutaneous injections of ARO-ANG3 or placebo. Participants who complete the double-blind treatment period may opt to continue in an open-label extension during which they will receive up to 8 doses of ARO-ANG3.

Detailed Description

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Conditions

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Mixed Dyslipidemia

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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ARO-ANG3 50 mg

Two doses of ARO-ANG3 by subcutaneous (sc) injection at Day 1 and Week 12 during double-blind treatment period. Up to 8 doses of ARO-ANG3 by sc injection during the open-label extension period.

Group Type EXPERIMENTAL

ARO-ANG3

Intervention Type DRUG

ARO-ANG3 Injection

ARO-ANG3 100 mg

Two doses of ARO-ANG3 bysc injection at Day 1 and Week 12 during double-blind treatment period. Up to 8 doses of ARO-ANG3 by sc injection during the open-label extension period.

Group Type EXPERIMENTAL

ARO-ANG3

Intervention Type DRUG

ARO-ANG3 Injection

ARO-ANG3 200 mg

Two doses of ARO-ANG3 by sc injection at Day 1 and Week 12 during double-blind treatment period. Up to 8 doses of ARO-ANG3 by sc injection during the open-label extension period.

Group Type EXPERIMENTAL

ARO-ANG3

Intervention Type DRUG

ARO-ANG3 Injection

Placebo

Calculated volume to match active treatment by sc injection at Day 1 and Week 12 during the double-blind treatment period. Up to 8 doses of ARO-ANG3 by sc injection during the open-label extension period.

Group Type PLACEBO_COMPARATOR

ARO-ANG3

Intervention Type DRUG

ARO-ANG3 Injection

Placebo

Intervention Type DRUG

Sterile Normal Saline (0.9% NaCl)

Interventions

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ARO-ANG3

ARO-ANG3 Injection

Intervention Type DRUG

Placebo

Sterile Normal Saline (0.9% NaCl)

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Based on medical history, evidence of triglycerides (TG) ≥ 150 mg/dL but ≤ 499 mg/dL
* Fasting levels at Screening of LDL-C ≥ 70 mg/dL OR non-HDL-C ≥ 100 mg/dL after at least 4 weeks of stable diet and stable optimal statin therapy
* Mean fasting TG ≥ 150 mg/dL and ≤ 499 mg/dL during Screening collected at two separate and consecutive visits and at least 7 days apart and not more than 17 days apart
* Willing to follow diet counseling and maintain a stable diet per Investigator judgment based on local standard of care
* Participants of childbearing potential must agree to use highly-effective contraception during the study and for at least 24 weeks from last dose of study medication
* Women of childbearing potential must have a negative pregnancy test and cannot be breastfeeding
* Women of childbearing potential on hormonal contraceptives must be stable on the medication for ≥ 2 menstrual cycles prior to Day 1
* Men must not donate sperm during the study and for at least 24 weeks following the last dose of study medication
* Able and willing to provide written informed consent and to comply with study requirements

Exclusion Criteria

* Current use or use within 365 days from Day 1 of any hepatocyte targeted siRNA or antisense oligonucleotide molecule
* Active pancreatitis within 12 weeks prior to Day 1
* Any planned bariatric surgery or similar procedures to induce weight loss from consent to end of study
* Acute coronary syndrome event within 24 weeks of Day 1
* Major surgery within 12 weeks of Day 1 or planned surgery during the study
* Planned coronary intervention (e.g., stent placement or heart bypass) during the study
* Uncontrolled hypertension
* Human immunodeficiency virus (HIV) infection, seropositive for Hepatitis B (HBV), seropositive for Hepatitis C (HCV)
* Uncontrolled hypothyroidism or hyperthyroidism
* Hemorrhagic stroke within 24 weeks of Day 1
* History of bleeding diathesis or coagulopathy
* Current diagnosis of nephrotic syndrome
* Systemic use of corticosteroids or anabolic steroids within 4 weeks prior to Day 1 or planned use during the study
* Malignancy within the last 2 years prior to date of consent requiring systemic treatment (some exceptions apply)
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Arrowhead Pharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Research Site 9

Québec, , Canada

Site Status

Research Site 19

Birkenhead, , New Zealand

Site Status

Research Site 13

Christchurch, , New Zealand

Site Status

Research Site 20

Hamilton, , New Zealand

Site Status

Research Site 14

Rotorua, , New Zealand

Site Status

Research Site 5

Huntington Park, California, United States

Site Status

Research Site 7

Hialeah, Florida, United States

Site Status

Research Site 17

Miami, Florida, United States

Site Status

Research Site 8

Port Orange, Florida, United States

Site Status

Research Site 24

Minneapolis, Minnesota, United States

Site Status

Research Site 10

Omaha, Nebraska, United States

Site Status

Research Site 23

Las Vegas, Nevada, United States

Site Status

Research Site 22

New York, New York, United States

Site Status

Research Site 15

Greensboro, North Carolina, United States

Site Status

Research Site 2

Morehead City, North Carolina, United States

Site Status

Research Site 1

Marion, Ohio, United States

Site Status

Research Site 4

Camp Hill, Pennsylvania, United States

Site Status

Research Site 11

Houston, Texas, United States

Site Status

Research Site 6

Blacktown, New South Wales, Australia

Site Status

Research Site 21

Sippy Downs, Queensland, Australia

Site Status

Research Site 18

Nedlands, , Australia

Site Status

Research Site 25

London, Ontario, Canada

Site Status

Research Site 16

Chicoutimi, Quebec, Canada

Site Status

Research Site 12

Québec, , Canada

Site Status

Countries

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United States Australia Canada New Zealand

References

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Rosenson RS, Gaudet D, Hegele RA, Ballantyne CM, Nicholls SJ, Lucas KJ, San Martin J, Zhou R, Muhsin M, Chang T, Hellawell J, Watts GF; ARCHES-2 Trial Team. Zodasiran, an RNAi Therapeutic Targeting ANGPTL3, for Mixed Hyperlipidemia. N Engl J Med. 2024 Sep 12;391(10):913-925. doi: 10.1056/NEJMoa2404147. Epub 2024 May 29.

Reference Type DERIVED
PMID: 38809174 (View on PubMed)

Dimitriadis K, Theofilis P, Iliakis P, Pyrpyris N, Dri E, Sakalidis A, Soulaidopoulos S, Tsioufis P, Fragkoulis C, Chrysohoou C, Tsiachris D, Tsioufis K. Management of dyslipidemia in coronary artery disease: the present and the future. Coron Artery Dis. 2024 Sep 1;35(6):516-524. doi: 10.1097/MCA.0000000000001375. Epub 2024 Apr 29.

Reference Type DERIVED
PMID: 38682459 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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AROANG3-2001

Identifier Type: -

Identifier Source: org_study_id

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