Study of ARO-APOC3 in Adults With Mixed Dyslipidemia

NCT ID: NCT04998201

Last Updated: 2025-10-03

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

353 participants

Study Classification

INTERVENTIONAL

Study Start Date

2021-09-28

Study Completion Date

2023-08-14

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

Participants who have met all protocol eligibility criteria will be randomly assigned to treatment (ARO-APOC3 or placebo) in a double-blind fashion and will be evaluted for safety and efficacy over 48 weeks. Participants will be counseled to remain on a specified diet throughout the study, as recommended by the Investigator in accordance with local standard of care. After week 48, participants will be eligible and invited to consent and continue in an open-label extension study. All placebo participants who opt to continue will switch to active drug (ARO-APOC3) during the extension study.

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

Mixed Dyslipidemia

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

ARO-APOC3 10 mg, Day 1 and Week 12

2 doses of ARO-APOC3 by subcutaneous (sc) injection

Group Type EXPERIMENTAL

ARO-APOC3

Intervention Type DRUG

ARO-APOC3 Injection

ARO-APOC3 25 mg, Day 1 and Week 12

2 doses of ARO-APOC3 by subcutaneous (sc) injection

Group Type EXPERIMENTAL

ARO-APOC3

Intervention Type DRUG

ARO-APOC3 Injection

ARO-APOC3 50 mg, Day 1 and Week 12

2 doses of ARO-APOC3 by subcutaneous (sc) injection

Group Type EXPERIMENTAL

ARO-APOC3

Intervention Type DRUG

ARO-APOC3 Injection

ARO-APOC3 50 mg, Day 1 and Week 24

2 doses of ARO-APOC3 by subcutaneous (sc) injection

Group Type EXPERIMENTAL

ARO-APOC3

Intervention Type DRUG

ARO-APOC3 Injection

Placebo, Day 1 and Week 12 or Week 24

calculated volume to match active treatment by sc injection

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Sterile Normal Saline (0.9% NaCl)

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

ARO-APOC3

ARO-APOC3 Injection

Intervention Type DRUG

Placebo

Sterile Normal Saline (0.9% NaCl)

Intervention Type DRUG

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

Based on medical history, evidence of TG ≥ 150 mg/dL but ≤ 499 mg/dL on more than one occasion

* Fasting levels at Screening of non-HDL-C ≥ 100 mg/dL OR LDL-C ≥ 70 mg/dL after at least 4 weeks of stable diet and stable optimal statin therapy
* Mean fasting TG ≥ 150 mg/dL and ≤ 499 mg/dL during Screening collected at two separate and consecutive visits and at least 7 days apart and not more than 14 days apart
* Willing to follow diet counseling as per Investigator judgment based on local standard of care
* Participants of childbearing potential (males \& females) must use highly-effective contraception during the study and for at least 24 weeks following the last dose of study medication. Males must not donate sperm and females must ot donate eggs during the study and for at least 24 weeks following the last dose of study medication.
* Women of childbearing potential must have a negative pregnancy test at Screening and cannot be breastfeeding
* Women of childbearing potential on hormonal contraceptives must be stable on the medication for ≥ 2 menstrual cycles prior to Day 1
* Willing to provide written informed consent and to comply with study requirements

Exclusion Criteria

* Current use or use within 365 days from Day 1 of any hepatocyte targeted siRNA or antisense oligonucleotide molecule
* Active pancreatitis within 12 weeks prior to Day 1
* Any planned bariatric surgery or similar procedures to induce weight loss from consent through end of study
* Acute coronary syndrome event within 24 weeks of Day 1
* Major surgery within 12 weeks of Day 1
* Planned coronary intervention (e.g., stent placement or heart bypass) during the study
* New York Heart Association Class II, III or IV heart failure or last known ejection fraction of \<30%
* Uncontrolled hypertension
* Known history of human immunodeficiency virus (HIV) infection, seropositive for Hepatitis B (HBV), seropositive for Hepatitis C (HCV)
* Uncontrolled hypothyroidism or hyperthyroidism
* Hemorrhagic stroke within 24 weeks of Day 1
* History of bleeding diathesis or coagulopathy
* Current diagnosis of nephrotic syndrome
* Systemic use of corticosteroids or anabolic steroids within 4 weeks prior to Day 1 or planned use during the study
* Malignancy within the last 2 years prior to date of consent requiring systemic treatment (some exceptions apply)
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

Arrowhead Pharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Responsibility Role SPONSOR

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

Research Site 3

Beverly Hills, California, United States

Site Status

Research Site 8

Northridge, California, United States

Site Status

Research Site 2

Boca Raton, Florida, United States

Site Status

Research Site 1

Fort Lauderdale, Florida, United States

Site Status

Research Site 14

Miami Springs, Florida, United States

Site Status

Research Site 5

Pembroke Pines, Florida, United States

Site Status

Research Site 18

Dunwoody, Georgia, United States

Site Status

Research Site 31

Las Vegas, Nevada, United States

Site Status

Research Site 17

New Windsor, New York, United States

Site Status

Research Site 12

Dayton, Ohio, United States

Site Status

Research Site 4

Franklin, Ohio, United States

Site Status

Research Site 7

Greenville, South Carolina, United States

Site Status

Research Site 6

Houston, Texas, United States

Site Status

Research Site 32

Houston, Texas, United States

Site Status

Research Site 13

San Antonio, Texas, United States

Site Status

Research Site 30

Morayfield, Queensland, Australia

Site Status

Research Site 29

Adelaide, South Australia, Australia

Site Status

Research Site 19

Clayton, Victoria, Australia

Site Status

Research Site 27

Joondalup, Western Australia, Australia

Site Status

Research Site 15

Concord, Ontario, Canada

Site Status

Research Site 10

Montreal, Quebec, Canada

Site Status

Research Site 20

Balatonfüred, , Hungary

Site Status

Research Site 21

Debrecen, , Hungary

Site Status

Research Site 22

Nyíregyháza, , Hungary

Site Status

Research Site 11

Auckland, , New Zealand

Site Status

Research Site 16

Christchurch, , New Zealand

Site Status

Research Site 28

Lodz, , Poland

Site Status

Research Site 24

Lodz, , Poland

Site Status

Research Site 25

Poznan, , Poland

Site Status

Research Site 26

Rzeszów, , Poland

Site Status

Countries

Review the countries where the study has at least one active or historical site.

United States Australia Canada Hungary New Zealand Poland

References

Explore related publications, articles, or registry entries linked to this study.

Ballantyne CM, Vasas S, Azizad M, Clifton P, Rosenson RS, Chang T, Melquist S, Zhou R, Mushin M, Leeper NJ, Hellawell J, Gaudet D. Plozasiran, an RNA Interference Agent Targeting APOC3, for Mixed Hyperlipidemia. N Engl J Med. 2024 Sep 12;391(10):899-912. doi: 10.1056/NEJMoa2404143. Epub 2024 May 28.

Reference Type DERIVED
PMID: 38804517 (View on PubMed)

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

2021-000688-57

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

AROAPOC3-2002

Identifier Type: -

Identifier Source: org_study_id

More Related Trials

Additional clinical trials that may be relevant based on similarity analysis.

ALN-APOC3 in Adult Participants With Dyslipidemia
NCT06784349 ACTIVE_NOT_RECRUITING PHASE1