Long-term Safety Study of Rimegepant in Pediatric Subjects for the Acute Treatment of Migraine

NCT ID: NCT04743141

Last Updated: 2025-11-12

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE3

Total Enrollment

600 participants

Study Classification

INTERVENTIONAL

Study Start Date

2021-04-28

Study Completion Date

2030-07-31

Brief Summary

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The purpose of this study is to test the long-term safety of rimegepant in the acute treatment of migraine in children and adolescents (≥ 6 to \< 18 years of age).

Detailed Description

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Conditions

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Acute Treatment of Migraine

Keywords

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Long-term safety, acute treatment, migraine, phonophobia, photophobia, nausea, pediatric, children, adolescent

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Active

rimegepant 75 mg, 50 mg or 35 mg ODT

Group Type EXPERIMENTAL

Rimegepant (PF-07899801)

Intervention Type DRUG

Rimegepant 75 mg, 50 mg or 35 mg ODT

Interventions

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Rimegepant (PF-07899801)

Rimegepant 75 mg, 50 mg or 35 mg ODT

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

1. History of migraine (with or without aura) for ≥ 6 months before Screening.
2. History of 1 to 8 moderate or severe attacks per month during the 2 months prior to screening.
3. 1 or more migraine days requiring treatment during the Observation Phase.
4. Prophylactic migraine medication is permitted if the dose has been stable for at least 12 weeks prior to the Screening Visit.
5. Ability to distinguish between migraine and other types of headaches.
6. Weight \> 15 kg. For EU countries only: Participants 12 to \< 18 years of age must have a body weight of \>25kg.
7. Adequate venous access for blood sampling.
8. Male and female participants 6 to \< 18 years of age (participants must not reach their 18th birthday on or before the Baseline visit).

Exclusion Criteria

1. History of cluster headache or hemiplegic migraine headache.
2. Confounding and clinically significant pain syndrome.
3. Current uncontrolled and/or untreated psychiatric condition for a minimum of 6 months prior to the Screening Visit (lifetime history of psychosis and/or mania are excluded).
4. History of suicidal behavior or at risk of self-harm/harm to others.
5. History of major psychiatric disorder.
6. Current diagnosis or history of substance abuse
7. Reported current use of or tested positive at Screening for drugs of abuse.
Minimum Eligible Age

6 Years

Maximum Eligible Age

17 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Pfizer

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Pfizer CT.gov Call Center

Role: STUDY_DIRECTOR

Pfizer

Locations

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Perseverance Research Center, LLC

Scottsdale, Arizona, United States

Site Status RECRUITING

Physicians Research Group

Tempe, Arizona, United States

Site Status ACTIVE_NOT_RECRUITING

Advanced Research Center, Inc.

Anaheim, California, United States

Site Status RECRUITING

ProScience Research Group

Culver City, California, United States

Site Status RECRUITING

Neuro-Pain Medical Center

Fresno, California, United States

Site Status RECRUITING

University of California San Diego, Altman Clinical and Translational Research Institute Clinic

La Jolla, California, United States

Site Status RECRUITING

Adult & Child Neurology Medical Associates

Long Beach, California, United States

Site Status RECRUITING

Memorialcare Miller Children's & Women's Hospital Long Beach

Long Beach, California, United States

Site Status RECRUITING

Velocity Clinical Research - North Hollywood

North Hollywood, California, United States

Site Status ACTIVE_NOT_RECRUITING

The Neurology Group

Pomona, California, United States

Site Status RECRUITING

UC Davis Medical Center, Investigational Drug Service (IDS) Pharmacy

Sacramento, California, United States

Site Status RECRUITING

University of California, Davis Clinical and Translational Science Center Clinical Research Center

Sacramento, California, United States

Site Status RECRUITING

University of California, Davis Midtown Clinic

Sacramento, California, United States

Site Status RECRUITING

Velocity Clinical Research- Banning

San Bernardino, California, United States

Site Status RECRUITING

Pacific Clinical Research Management Group LLC

Upland, California, United States

Site Status RECRUITING

Sunwise Clinical Research

Walnut Creek, California, United States

Site Status RECRUITING

Children's Hospital Colorado- Investigational Drug Services

Aurora, Colorado, United States

Site Status RECRUITING

Children's Hospital Colorado

Aurora, Colorado, United States

Site Status RECRUITING

Colorado Springs Neurological Associates

Colorado Springs, Colorado, United States

Site Status RECRUITING

Boeson Research GJT

Grand Junction, Colorado, United States

Site Status TERMINATED

Dinosaur Pediatrics

Grand Junction, Colorado, United States

Site Status TERMINATED

Boeson Research GJT

Grand Junction, Colorado, United States

Site Status TERMINATED

CT Clinical Research

Cromwell, Connecticut, United States

Site Status RECRUITING

Ki Health Partners, LLc, dba New England Institute for Clinical Research

Stamford, Connecticut, United States

Site Status RECRUITING

Children's National Medical Center

Washington D.C., District of Columbia, United States

Site Status RECRUITING

AppleMed Research Group, LLC

Miami, Florida, United States

Site Status RECRUITING

Medical Research Center of Miami II, Inc

Miami, Florida, United States

Site Status ACTIVE_NOT_RECRUITING

Brainstorm Research

Miami, Florida, United States

Site Status RECRUITING

South Florida Research Phase I-IV, Inc

Miami Springs, Florida, United States

Site Status RECRUITING

Physicians Group Services, PA d/b/a Coastal Health Research

Orange Park, Florida, United States

Site Status RECRUITING

Clinical Associates of Orlando, LLC

Orlando, Florida, United States

Site Status RECRUITING

ForCare Clinical Research

Tampa, Florida, United States

Site Status RECRUITING

Premiere Research Institute at Palm Beach Neurology

West Palm Beach, Florida, United States

Site Status ACTIVE_NOT_RECRUITING

Childrens Healthcare of Atlanta

Atlanta, Georgia, United States

Site Status RECRUITING

Rare Disease Research LLC

Atlanta, Georgia, United States

Site Status ACTIVE_NOT_RECRUITING

Pivotal Clinical Research & Associates, LLC

Brunswick, Georgia, United States

Site Status RECRUITING

CenExel iResearch, LLC

Decatur, Georgia, United States

Site Status RECRUITING

Chicago Headache Center & Research Institute

Chicago, Illinois, United States

Site Status RECRUITING

AMR-Baber Research Inc

Naperville, Illinois, United States

Site Status NOT_YET_RECRUITING

Options Research Group, LLC

Westfield, Indiana, United States

Site Status RECRUITING

Integrated Clinical Trial Services

West Des Moines, Iowa, United States

Site Status RECRUITING

Clinical Associates Midwest, LLC

Kansas City, Kansas, United States

Site Status RECRUITING

University of Kentucky Hospital

Lexington, Kentucky, United States

Site Status ACTIVE_NOT_RECRUITING

Ochsner Clinic Foundation

New Orleans, Louisiana, United States

Site Status TERMINATED

MedVadis Research Corporation

Waltham, Massachusetts, United States

Site Status ACTIVE_NOT_RECRUITING

Michigan Head Pain and Neurological Institute

Ann Arbor, Michigan, United States

Site Status RECRUITING

Corewell Health, for and on behalf of Spectrum Health Hospital and Corewell Health Medical Group

Grand Rapids, Michigan, United States

Site Status RECRUITING

Corewell Health, Helen DeVos Children's Hospital

Grand Rapids, Michigan, United States

Site Status RECRUITING

Wellnow Urgent Care and Research

Kalamazoo, Michigan, United States

Site Status TERMINATED

Beaumont Hospital, Royal Oak Campus

Royal Oak, Michigan, United States

Site Status RECRUITING

Sharlin Health Neuroscience Research Center

Ozark, Missouri, United States

Site Status RECRUITING

Clinvest Research, LLC

Springfield, Missouri, United States

Site Status ACTIVE_NOT_RECRUITING

Boeson Research

Great Falls, Montana, United States

Site Status RECRUITING

Heart & Hands Midwifery

Kalispell, Montana, United States

Site Status RECRUITING

Blue Moose Pediatrics

Missoula, Montana, United States

Site Status RECRUITING

Boeson Research Laboratory

Missoula, Montana, United States

Site Status RECRUITING

Boeson Research

Missoula, Montana, United States

Site Status RECRUITING

Alivation Research, LLC

Lincoln, Nebraska, United States

Site Status TERMINATED

Children's Hospital & Medical Center

Omaha, Nebraska, United States

Site Status RECRUITING

HMH Jersey Shore University Medical Center

Neptune City, New Jersey, United States

Site Status NOT_YET_RECRUITING

Dent Neurosciences Research Center

Amherst, New York, United States

Site Status RECRUITING

True North Neurology

Commack, New York, United States

Site Status RECRUITING

New York Neurology Associates

New York, New York, United States

Site Status RECRUITING

Mount Sinai Hospital - Pharmacy Department

New York, New York, United States

Site Status ACTIVE_NOT_RECRUITING

Columbia University Irving Medical Center

New York, New York, United States

Site Status RECRUITING

Irving Center for Clinical and Translational Research, Outpatient Clinical Research Unit

New York, New York, United States

Site Status RECRUITING

The Neurological Institute of New York

New York, New York, United States

Site Status RECRUITING

North Suffolk Neurology

Port Jefferson Station, New York, United States

Site Status ACTIVE_NOT_RECRUITING

Headache Wellness Center, PC

Greensboro, North Carolina, United States

Site Status RECRUITING

WellNow Urgent Care and Research

Cincinnati, Ohio, United States

Site Status ACTIVE_NOT_RECRUITING

Cincinnati Children's Hospital

Cincinnati, Ohio, United States

Site Status RECRUITING

Velocity Clinical Research - Cincinnati

Cincinnati, Ohio, United States

Site Status RECRUITING

University Hospitals Cleveland Medical Center

Cleveland, Ohio, United States

Site Status RECRUITING

Wellnow Urgent Care and Research

Dayton, Ohio, United States

Site Status ACTIVE_NOT_RECRUITING

IPS Research Company

Oklahoma City, Oklahoma, United States

Site Status ACTIVE_NOT_RECRUITING

Velocity Clinical Research, Grants Pass

Grants Pass, Oregon, United States

Site Status ACTIVE_NOT_RECRUITING

Providence Brain & Spine Institute-research coordinator's office

Portland, Oregon, United States

Site Status RECRUITING

Providence Health & Services Investigational Drug Services Westside

Portland, Oregon, United States

Site Status RECRUITING

Providence St. Vincent Medical Center

Portland, Oregon, United States

Site Status RECRUITING

Clario

Philadelphia, Pennsylvania, United States

Site Status RECRUITING

Children's Hospital of Philadelphia

Philadelphia, Pennsylvania, United States

Site Status ACTIVE_NOT_RECRUITING

Velocity Clinical Research-Providence

East Greenwich, Rhode Island, United States

Site Status RECRUITING

Velocity Clinical Research- Greenville

Greenville, South Carolina, United States

Site Status ACTIVE_NOT_RECRUITING

Premier Neurology

Greer, South Carolina, United States

Site Status ACTIVE_NOT_RECRUITING

Novaceut Clinical Research

Clarksville, Tennessee, United States

Site Status ACTIVE_NOT_RECRUITING

Le Bonheur Children's Hospital

Memphis, Tennessee, United States

Site Status RECRUITING

Le Bonheur Childrens Hospital - Childrens Foundation Research Institute

Memphis, Tennessee, United States

Site Status RECRUITING

Le Bonheur Childrens Hospital - Outpatient Building

Memphis, Tennessee, United States

Site Status RECRUITING

Access Clinical Trials, Inc.

Nashville, Tennessee, United States

Site Status TERMINATED

Dell Children's Medical Center

Austin, Texas, United States

Site Status RECRUITING

Child Neurology Consultants of Austin - South Austin

Austin, Texas, United States

Site Status RECRUITING

Child Neurology Consultants of Austin - Central Austin

Austin, Texas, United States

Site Status RECRUITING

Houston Clinical Trials, LLC

Bellaire, Texas, United States

Site Status RECRUITING

Infinite Research Group, LLC

Dallas, Texas, United States

Site Status RECRUITING

Cedar Health Research

Dallas, Texas, United States

Site Status RECRUITING

ANESC Research

El Paso, Texas, United States

Site Status RECRUITING

North Texas Institute of Neurology and Headache

Frisco, Texas, United States

Site Status ACTIVE_NOT_RECRUITING

Trio Clinical Trials, LLC.

Houston, Texas, United States

Site Status ACTIVE_NOT_RECRUITING

Pain and Headache Centers of Texas

Houston, Texas, United States

Site Status RECRUITING

SCLA Management

Houston, Texas, United States

Site Status RECRUITING

Houston Clinical Research,LLC.

Houston, Texas, United States

Site Status TERMINATED

NeuroCare Plus

Houston, Texas, United States

Site Status RECRUITING

AIM Trials, LLC

Plano, Texas, United States

Site Status RECRUITING

JBR Clinical Research

Salt Lake City, Utah, United States

Site Status RECRUITING

Wasatch Clinical Research , LLC(Administrative Location)

Salt Lake City, Utah, United States

Site Status RECRUITING

Children's Hospital of The King's Daughters

Norfolk, Virginia, United States

Site Status RECRUITING

Children's Specialty Group, PLLC , Division of Childhood & Adolescent Neurology

Norfolk, Virginia, United States

Site Status RECRUITING

National Clinical Research, Inc.

Richmond, Virginia, United States

Site Status TERMINATED

Northwest Clinical Research Center

Bellevue, Washington, United States

Site Status RECRUITING

Seattle Children's Hospital Investigational Drug Services

Seattle, Washington, United States

Site Status RECRUITING

Seattle Children's Hospital

Seattle, Washington, United States

Site Status RECRUITING

University Hospital

Madison, Wisconsin, United States

Site Status RECRUITING

NZOZ Wielospecjalistyczna Poradnia Lekarska SYNAPSIS, Lech Szczechowski

Katowice, , Poland

Site Status TERMINATED

Centrum Medyczne Plejady

Krakow, , Poland

Site Status RECRUITING

Wojewodzki Specjalistyczny Szpital Dzieciecy im. Sw. Ludwika w Krakowie Oddzial Kliniczny Dzieci

Krakow, , Poland

Site Status RECRUITING

Clinical Research Center Sp. z o.o.

Poznan, , Poland

Site Status RECRUITING

Pracownia Badan Klinicznych SALUS

Wroclaw, , Poland

Site Status RECRUITING

Centrum Medyczne Oporow

Wroclaw, , Poland

Site Status ACTIVE_NOT_RECRUITING

Centre Atencio Primaria (CAP) Balenya

Balenya, Barcelona, Spain

Site Status ACTIVE_NOT_RECRUITING

Hospital Universitario Vall d'Hebron

Barcelona, , Spain

Site Status RECRUITING

Hospital Universitario Virgen del Rocio

Seville, , Spain

Site Status RECRUITING

Hospital Clinico Universitario de Valladolid

Valladolid, , Spain

Site Status RECRUITING

Countries

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United States Poland Spain

Central Contacts

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Pfizer Pfizer CT.gov Call Center

Role: CONTACT

Phone: 1-800-718-1021

Email: [email protected]

Related Links

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https://pmiform.com/clinical-trial-info-request?StudyID=BHV3000-312

To obtain contact information for a study center near you, click here.

Other Identifiers

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C4951003

Identifier Type: OTHER

Identifier Source: secondary_id

2024-512744-32-00

Identifier Type: REGISTRY

Identifier Source: secondary_id

BHV3000-312

Identifier Type: -

Identifier Source: org_study_id