Efficacy and Safety Study of Rimegepant in Episodic Migraine Prevention With Multiple Dosing Regimens

NCT ID: NCT05217927

Last Updated: 2025-12-16

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE4

Total Enrollment

1415 participants

Study Classification

INTERVENTIONAL

Study Start Date

2022-03-04

Study Completion Date

2024-12-11

Brief Summary

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The purpose of this study is to compare the efficacy and safety of daily and every other day dosing of rimegepant to placebo as a preventive treatment for episodic migraine.

Detailed Description

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Conditions

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Migraine

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

SEQUENTIAL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Rimegepant 75mg Orally Disitegrating Tablet (ODT)daily dosing

Double-blind Treatment Phase: Rimegepant 75 mg ODT dosed daily

Open-Label Extension Phase:

Rimegepant 75 mg ODT dosed daily

Group Type EXPERIMENTAL

Rimegepant 75mg daily dosing

Intervention Type DRUG

Daily

Rimegepant 75mg Orally Disintegrating Tablet (ODT)every other day dosing

Double-blind Treatment Phase: Rimegepant 75 mg ODT every other day dosing alternating with matching placebo

Group Type EXPERIMENTAL

Rimegepant 75mg every other day dosing

Intervention Type DRUG

Every other day

Placebo comparator dosing

Double-blind Treatment Phase: matching placebo dosed daily

Group Type PLACEBO_COMPARATOR

Placebo comparator dosing

Intervention Type DRUG

Placebo comparator

Interventions

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Rimegepant 75mg daily dosing

Daily

Intervention Type DRUG

Rimegepant 75mg every other day dosing

Every other day

Intervention Type DRUG

Placebo comparator dosing

Placebo comparator

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

1\) Target Population: Subject has at least 1 year history of episodic migraine (with or without aura) consistent with a diagnosis according to the International Classification of Headache Disorders, 3rd Edition, including the following:

1. Age of onset of migraines prior to 50 years of age
2. Migraine attacks, on average, lasting 4-72 hours if untreated
3. Per subject report, 4-14 migraine attacks per month within the last 3 months prior to the Screening Visit (month is defined as 4 weeks for the purpose of this protocol

Exclusion Criteria

1. Sex and Reproductive Status:

1. WOCBP who are unwilling or unable to use an acceptable contraceptive method or abstinence to avoid pregnancy for the entire study and for 60 days after the last dose of study drug
2. Women who are pregnant or breastfeeding
3. Women with a positive pregnancy test at screening or prior to study drug administration
2. Prohibited Medications:

1. Use of prophylactic migraine medication within 30 days prior to the Screening Visit.
2. History of use of analgesics (e.g., non-steroidal anti-inflammatory drugs \[NSAIDs\] or acetaminophen) on ≥ 15 days per month during the 3 months (12 weeks) prior to the Screening Visit.
3. Use of medication accepted for treatment of acute migraine for a nonmigraine indication on ≥ 15 days per month during the 3 months (12 weeks) prior to the Screening Visit.
4. Subjects who previously discontinued biologic migraine medication must have done so at least 6 months (24 weeks) prior to the Screening Visit.
5. Subjects taking a prohibited medication as defined per protocol
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Pfizer

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Pfizer CT.gov Call Center

Role: STUDY_DIRECTOR

Pfizer

Locations

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AMR Clinical

Tempe, Arizona, United States

Site Status

Axiom Research, Llc

Colton, California, United States

Site Status

Clinical Research Institute

Los Angeles, California, United States

Site Status

Wr-Pri, Llc

Newport Beach, California, United States

Site Status

California Neuroscience Research Medical Group, inc.

Sherman Oaks, California, United States

Site Status

Neurology Offices of South Florida, PLLC

Boca Raton, Florida, United States

Site Status

AppleMed Research Group, LLC

Miami, Florida, United States

Site Status

Clinical Investigation Specialists, Inc.

Gurnee, Illinois, United States

Site Status

MediSphere Medical Research Center, LLC

Evansville, Indiana, United States

Site Status

Collective Medical Research

Overland Park, Kansas, United States

Site Status

Clinvest Research, LLC

Springfield, Missouri, United States

Site Status

Alliance for Multispecialty Research, LLC

Las Vegas, Nevada, United States

Site Status

Dent Neurosciences Research Center, Inc.

Amherst, New York, United States

Site Status

Montefiore Medical Center

The Bronx, New York, United States

Site Status

Upstate Clinical Research Associates, LLC

Williamsville, New York, United States

Site Status

Wellnow Urgent Care and Research

Columbus, Ohio, United States

Site Status

Hometown Urgent Care and Research

Huber Heights, Ohio, United States

Site Status

Velocity Clinical Research, Medford

Medford, Oregon, United States

Site Status

Preferred Primary Care Physicians, Inc.

Pittsburgh, Pennsylvania, United States

Site Status

Velocity Clinical Research - Providence

East Greenwich, Rhode Island, United States

Site Status

Velocity Clinical Research - Columbia

Columbia, South Carolina, United States

Site Status

Velocity Clinical Research, Gaffney

Gaffney, South Carolina, United States

Site Status

Tribe Clinical Research LLC

Greenville, South Carolina, United States

Site Status

Clinical Research Associates, Inc.

Nashville, Tennessee, United States

Site Status

FutureSearch Trials of Neurology

Austin, Texas, United States

Site Status

FutureSearch Trials of Dallas, LP

Dallas, Texas, United States

Site Status

Texas Center for Drug Development, Inc.

Houston, Texas, United States

Site Status

APD Clinical Research

Magnolia, Texas, United States

Site Status

Wasatch Clinical Research , LLC(Administrative Location)

Salt Lake City, Utah, United States

Site Status

Seattle Clinical Research Center

Seattle, Washington, United States

Site Status

Medizinische Universitat Innsbruck

Innsbruck, Tyrol, Austria

Site Status

Christian-Doppler-Klinik

Salzburg, , Austria

Site Status

Calgary Headache & Assessment Management Program (CHAMP)

Calgary, Alberta, Canada

Site Status

OCT Research ULC

Kelowna, British Columbia, Canada

Site Status

James K. Lai MD Inc.

Vancouver, British Columbia, Canada

Site Status

Centricity Research

Halifax, Nova Scotia, Canada

Site Status

Aggarwal and Associates Limited

Brampton, Ontario, Canada

Site Status

Manna Research Inc. (Burlington North)

Burlington, Ontario, Canada

Site Status

Milestone Research Inc.

London, Ontario, Canada

Site Status

Bluewater Clinical Research Group Inc.

Sarnia, Ontario, Canada

Site Status

Mirtorabi Medicine Professional Corporation

Stouffville, Ontario, Canada

Site Status

Toronto Memory Program

Toronto, Ontario, Canada

Site Status

Manna Research (Toronto)

Toronto, Ontario, Canada

Site Status

Diex Recherche Sherbrooke Inc.

Sherbrooke, Quebec, Canada

Site Status

Hopital Gabriel Montpied

Clermont-Ferrand, , France

Site Status

Hopital de La Timone

Marseille, , France

Site Status

Klinische Forschung Karlsruhe GmbH

Karlsruhe, Baden-Wurttemberg, Germany

Site Status

Vitos Orthopaedische Klinik Kassel

Kassel, Hesse, Germany

Site Status

Siteworks - Zentrum fur klinische Studien Hannover

Hanover, Lower Saxony, Germany

Site Status

Arztepartnerschaft Dr. med. J. Springub/ W. Schwarz -Studienzentrum Nord-West

Westerstede, Lower Saxony, Germany

Site Status

Klinische Forschung Schwerin GmbH

Schwerin, Mecklenburg-Vorpommern, Germany

Site Status

Klinische Forschung Dresden GmbH

Dresden, Saxony, Germany

Site Status

Universitatsklinikum Jena

Jena, Thuringia, Germany

Site Status

Studienzentrum Dr. A Schwittay

Böhlen, , Germany

Site Status

Datamed GmbH

Cologne, , Germany

Site Status

Kopfschmerzzentrum Frankfurt

Frankfurt, , Germany

Site Status

Klinische Forschung Hamburg GmbH

Hamburg, , Germany

Site Status

Neurologisch-verhaltensmedizinische Schmerzklinik Kiel

Kiel, , Germany

Site Status

Ospedale Sant Andrea - Facolta Medicina Psicologia - Universita degli Studi di Roma Sapienza

Rome, Lazio, Italy

Site Status

Fondazione Mondino - Istituto Neurologico Nazionale IRCCS

Pavia, Padua, Italy

Site Status

Azienda Ospedaliero Universitaria di Careggi - Cliniche Mediche

Florence, Tuscany, Italy

Site Status

IRCCS Istituto delle Scienze Neurologiche Bologna, Unità Operativa di Neurologia - Ospedale Bellaria

Bologna, , Italy

Site Status

ASST Spedali Civili di Brescia, U.O. Neurologia

Brescia, , Italy

Site Status

Neurorehabilitation Unit-ICOT Istituto Marco Pasquali

Latina, , Italy

Site Status

Istituto Neurologico "Carlo Besta" Fondazione IRCCS

Milan, , Italy

Site Status

IRCCS San Raffaele Roma

Rome, , Italy

Site Status

Solumed Centrum Medyczne

Poznan, Greater Poland Voivodeship, Poland

Site Status

Centrum Medyczne Pratia Bydgoszcz

Bydgoszcz, Kuyavian-Pomeranian Voivodeship, Poland

Site Status

Pratia MCM Krakow

Krakow, Lesser Poland Voivodeship, Poland

Site Status

Krakowska Akademia Neurologii Sp. Z o.o.

Krakow, Lesser Poland Voivodeship, Poland

Site Status

MIGRE Polskie Centrum Leczenia Migreny Anna Gryglas-Dworak

Wroclaw, Lower Silesian Voivodeship, Poland

Site Status

Indywidualna Praktyka Lekarska Dr Hab. Med. Anna Szczepanska-Szerej

Lublin, Lublin Voivodeship, Poland

Site Status

Next Stage Sp. Z o.o.

Warsaw, Masovian Voivodeship, Poland

Site Status

Wojskowy Instytut Medyczny

Warsaw, Masovian Voivodeship, Poland

Site Status

Centrum Medyczne Pratia Czestochowa

Częstochowa, Silesian Voivodeship, Poland

Site Status

Centrum Medyczne Pratia Katowice

Katowice, Silesian Voivodeship, Poland

Site Status

NZOZ Wielospecjalistyczna Poradnia Lekarska SYNAPSIS

Katowice, Silesian Voivodeship, Poland

Site Status

Neurologia Slaska Centrum Medyczne

Katowice, Silesian Voivodeship, Poland

Site Status

NZOZ Neuromed M. i M. Nastaj Sp. P.

Lublin, , Poland

Site Status

MTZ Clinical Research Powered by Pratia

Warsaw, , Poland

Site Status

Neurology Service: Hospital Universitario Marques de Valdecilla

Santander, Cantabria, Spain

Site Status

Hospital Clinico Universitario de Valladolid • HCUV

Valladolid, Castille and León, Spain

Site Status

Hospital Alvaro Cunqueiro

Vigo, Pontevedra, Spain

Site Status

Instituto de Investigaciones del Sueno

Madrid, , Spain

Site Status

Hospital Universitario La Paz

Madrid, , Spain

Site Status

Virgen del Rocio Hospital

Seville, , Spain

Site Status

Hospital Universitario y Politecnico La Fe

Valencia, , Spain

Site Status

Pharmasite

Malmo, Skåne County, Sweden

Site Status

CTC Clinical Trial Consultants AB

Stockholm, Stockholms LÄN [se-01], Sweden

Site Status

Ladulaas Clinical Trials

Borås, , Sweden

Site Status

ProbarE i Lund

Lund, , Sweden

Site Status

ProbarE i Stockholm AB

Stockholm, , Sweden

Site Status

Studieenheten Akademiskt Specialistcentrum SLSO

Stockholm, , Sweden

Site Status

Royal Primary Care Ashgate, Chesterfield Royal Hospital, NHS Foundation Trust

Chesterfield, Derbyshire, United Kingdom

Site Status

Panthera Biopartners

Rochdale, Great Manchester, United Kingdom

Site Status

Re:Cognition Health - Winchester

Winchester, Hampshire, United Kingdom

Site Status

Panthera Bio Partners

Preston, Lancashire, United Kingdom

Site Status

Re:Cognition Health - London

London, Marylebone, United Kingdom

Site Status

Re:Cognition Health-Private Practice

London, Marylebone, United Kingdom

Site Status

Lakeside Healthcare Research

Corby, Northamptonshire, United Kingdom

Site Status

CPS Research

Glasgow, Scotland, United Kingdom

Site Status

Re-Cognition Health - Bristol

Bristol, South WEST, United Kingdom

Site Status

Panthera Biopartners - Sheffield

Sheffield, South Yorkshire, United Kingdom

Site Status

Re-Cognition Health

Guildford, Surrey, United Kingdom

Site Status

Re-Cognition Health

Birmingham, WEST Midlands, United Kingdom

Site Status

Panthera Biopartners Glasgow

Glasgow, , United Kingdom

Site Status

Panthera Biopartners - Enfield

London, , United Kingdom

Site Status

Countries

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United States Austria Canada France Germany Italy Poland Spain Sweden United Kingdom

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Related Links

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https://pmiform.com/clinical-trial-info-request?StudyID=BHV3000-404

To obtain contact information for a study center near you, click here.

Other Identifiers

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2021-005239-22

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

C4951010

Identifier Type: OTHER

Identifier Source: secondary_id

BHV3000-404

Identifier Type: -

Identifier Source: org_study_id