A Study to Evaluate the Efficacy and Safety of Faricimab in Participants With Macular Edema Secondary to Branch Retinal Vein Occlusion

NCT ID: NCT04740905

Last Updated: 2024-08-06

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

553 participants

Study Classification

INTERVENTIONAL

Study Start Date

2021-03-02

Study Completion Date

2023-06-12

Brief Summary

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This is a Phase III, multicenter, randomized, double-masked, active comparator-controlled, parallel-group study evaluating the efficacy, safety, and pharmacokinetics of faricimab administered by intravitreal (IVT) injection at 4-week intervals until Week 24, followed by a double-masked period of study without active control to evaluate faricimab administered according to a personalized treatment interval (PTI) dosing regimen in participants with macular edema due to branch retinal vein occlusion (BRVO).

Detailed Description

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Conditions

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Macular Edema Branch Retinal Vein Occlusion

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Investigators Outcome Assessors

Study Groups

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Arm A: Faricimab Q4W (Part 1), Faricimab PTI (Part 2)

In Part 1 (Day 1 through Week 24), participants randomly assigned to Arm A will receive faricimab 6 milligrams (mg) by IVT injection once every 4 weeks (Q4W) from Day 1 through Week 20 (a total of 6 injections). In Part 2 (from Week 24 to Week 72), participants will receive faricimab 6 mg by IVT injection according to a personalized treatment interval (PTI) dosing regimen. To preserve masking for Part 2, a sham procedure will be administered during study visits at which no faricimab treatment is administered (according to the PTI dosing regimen).

Group Type EXPERIMENTAL

Faricimab

Intervention Type DRUG

Faricimab will be administered by intravitreal (IVT) injection as specified in each treatment arm.

Sham Procedure

Intervention Type PROCEDURE

The sham is a procedure that mimics an intravitreal (IVT) injection, but involves the blunt end of an empty syringe (without a needle) being pressed against the anesthetized eye. It will be administered to participants in both treatments arms at applicable visits to maintain masking.

Arm B: Aflibercept Q4W (Part 1), Faricimab PTI (Part 2)

In Part 1 (Day 1 through Week 24), participants randomly assigned to Arm B will receive aflibercept 2 milligrams (mg) by IVT injection once every 4 weeks (Q4W) from Day 1 through Week 20 (a total of 6 injections). In Part 2 (from Week 24 to Week 72), participants will receive faricimab 6 mg by IVT injection according to a personalized treatment interval (PTI) dosing regimen. To preserve masking for Part 2, a sham procedure will be administered during study visits at which no faricimab treatment is administered (according to the PTI dosing regimen).

Group Type ACTIVE_COMPARATOR

Faricimab

Intervention Type DRUG

Faricimab will be administered by intravitreal (IVT) injection as specified in each treatment arm.

Aflibercept

Intervention Type DRUG

Aflibercept 2 mg will be administered by IVT injection once every 4 weeks (Q4W) from Day 1 through Week 20 (a total of 6 injections).

Sham Procedure

Intervention Type PROCEDURE

The sham is a procedure that mimics an intravitreal (IVT) injection, but involves the blunt end of an empty syringe (without a needle) being pressed against the anesthetized eye. It will be administered to participants in both treatments arms at applicable visits to maintain masking.

Interventions

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Faricimab

Faricimab will be administered by intravitreal (IVT) injection as specified in each treatment arm.

Intervention Type DRUG

Aflibercept

Aflibercept 2 mg will be administered by IVT injection once every 4 weeks (Q4W) from Day 1 through Week 20 (a total of 6 injections).

Intervention Type DRUG

Sham Procedure

The sham is a procedure that mimics an intravitreal (IVT) injection, but involves the blunt end of an empty syringe (without a needle) being pressed against the anesthetized eye. It will be administered to participants in both treatments arms at applicable visits to maintain masking.

Intervention Type PROCEDURE

Other Intervention Names

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VABYSMO® faricimab-svoa RO6867461 RG7716 Eylea

Eligibility Criteria

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Inclusion Criteria

* Foveal center-involved macular edema due to branch retinal vein occlusion (BRVO), diagnosed no longer than 4 months prior to the screening visit
* Best-corrected visual acuity (BCVA) of 73 to 19 letters, inclusive (20/40 to 20/400 approximate Snellen equivalent) on Day 1
* Sufficiently clear ocular media and adequate pupillary dilatation to allow acquisition of good quality retinal images to confirm diagnosis
* For women of childbearing potential: agreement to remain abstinent or use contraception, and agreement to refrain from donating eggs during the treatment period and for 3 months after the final dose of study treatment

Exclusion Criteria

* Any major illness or major surgical procedure within 1 month before screening
* Uncontrolled blood pressure
* Stroke (cerebral vascular accident) or myocardial infarction within 6 months prior to Day 1
* Pregnant or breastfeeding, or intending to become pregnant during the study


* History of previous episodes of macular edema due to RVO or persistent macular edema due to RVO diagnosed more than 4 months before screening
* Any current ocular condition which, in the opinion of the investigator, is currently causing or could be expected to contribute to irreversible vision loss due to a cause other than macular edema due to RVO in the study eye (e.g., ischemic maculopathy, Irvine-Gass syndrome, foveal atrophy, foveal fibrosis, pigment abnormalities, dense subfoveal hard exudates, or other non-retinal conditions)
* Macular laser (focal/grid) in the study eye at any time prior to Day 1
* Panretinal photocoagulation in the study eye within 3 months prior to Day 1 or anticipated within 3 months of study start on Day 1
* Any prior or current treatment for macular edema; macular neovascularization, including diabetic macular edema (DME) and neovascular age-related macular degeneration (nAMD); and vitreomacular-interface abnormalities, including, but not restricted to, IVT treatment with anti-VEGF, steroids, tissue plasminogen activator, ocriplasmin, C3F8, air or periocular injection
* Any prior intervention with verteporfin photodynamic therapy, diode laser, transpupillary thermotherapy, or vitreo-retinal surgery including sheatotomy
* Any prior steroid implant use including dexamethasone intravitreal implant (Ozurdex) and fluocinolone acetonide intravitreal implant (Iluvien)


* Prior IVT administration of faricimab in either eye
* History of idiopathic or autoimmune-associated uveitis in either eye
* Active periocular, ocular or intraocular inflammation or infection (including suspected) in either eye on Day 1
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Chugai Pharmaceutical

INDUSTRY

Sponsor Role collaborator

Hoffmann-La Roche

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Clinical Trials

Role: STUDY_DIRECTOR

Hoffmann-La Roche

Locations

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Retinal Research Institute, LLC

Phoenix, Arizona, United States

Site Status

Retina Associates Southwest PC

Tucson, Arizona, United States

Site Status

Retinal Diagnostic Center

Campbell, California, United States

Site Status

The Retina Partners

Encino, California, United States

Site Status

California Eye Specialists Medical group Inc.

Pasadena, California, United States

Site Status

Retina Consultants, San Diego

Poway, California, United States

Site Status

Retina Consultants of Southern Colorado PC

Colorado Springs, Colorado, United States

Site Status

Retina Group of New England

Waterford, Connecticut, United States

Site Status

Florida Eye Associates

Melbourne, Florida, United States

Site Status

Fort Lauderdale Eye Institute

Plantation, Florida, United States

Site Status

Retina Vitreous Assoc of FL

St. Petersburg, Florida, United States

Site Status

Southern Vitreoretinal Assoc

Tallahassee, Florida, United States

Site Status

Retina Associates of Florida, LLC

Tampa, Florida, United States

Site Status

Southeast Retina Center

Augusta, Georgia, United States

Site Status

Georgia Retina PC

Marietta, Georgia, United States

Site Status

Retina Consultants of Hawaii

‘Aiea, Hawaii, United States

Site Status

University Retina and Macula Associates, PC

Oak Forest, Illinois, United States

Site Status

Prairie Retina Center

Springfield, Illinois, United States

Site Status

Cumberland Valley Retina PC

Hagerstown, Maryland, United States

Site Status

Tufts Medical Center; Ophthalmology

Boston, Massachusetts, United States

Site Status

Assoc Retinal Consultants PC

Royal Oak, Michigan, United States

Site Status

VitreoRetinal Surgery, PLLC.; DBA Retina Consultants of Minnesota

Edina, Minnesota, United States

Site Status

Midwest Vision Research Foundation

Chesterfield, Missouri, United States

Site Status

Sierra Eye Associates

Reno, Nevada, United States

Site Status

Retina Associates of NJ

Teaneck, New Jersey, United States

Site Status

Long Is. Vitreoretinal Consult

Hauppauge, New York, United States

Site Status

Retina Vit Surgeons/Central NY

Liverpool, New York, United States

Site Status

Graystone Eye

Hickory, North Carolina, United States

Site Status

Cincinnati Eye Institute

Cincinnati, Ohio, United States

Site Status

Black Hills Eye Institute

Rapid City, South Dakota, United States

Site Status

Charles Retina Institute

Germantown, Tennessee, United States

Site Status

Tennessee Retina PC

Nashville, Tennessee, United States

Site Status

Retina Res Institute of Texas

Abilene, Texas, United States

Site Status

Austin Retina Associates

Austin, Texas, United States

Site Status

Retina & Vitreous of Texas

Bellaire, Texas, United States

Site Status

Texas Retina Associates

Dallas, Texas, United States

Site Status

Retina Consultants of Texas

The Woodlands, Texas, United States

Site Status

Strategic Clinical Research Group, LLC

Willow Park, Texas, United States

Site Status

Retina Associates of Utah, PLLC

Salt Lake City, Utah, United States

Site Status

Fundacion Zambrano

CABA, , Argentina

Site Status

Centro Oftalmológico Dr. Charles S.A.

Capital Federal, , Argentina

Site Status

Oftalmos

Capital Federal, , Argentina

Site Status

Hospital Italiano; Ophtalmology

Capital Federal, , Argentina

Site Status

Buenos Aires Mácula

Ciudad Autonoma Buenos Aires, , Argentina

Site Status

Oftar

Mendoza, , Argentina

Site Status

Centro Oftalmólogos Especialistas

Rosario, , Argentina

Site Status

Grupo Laser Vision

Rosario, , Argentina

Site Status

Organizacion Medica de Investigacion

San Nicolás, , Argentina

Site Status

Strathfield Retina Clinic

Strathfield, New South Wales, Australia

Site Status

Save Sight Institute

Sydney, New South Wales, Australia

Site Status

Sydney Retina Clinic and Day Surgery

Sydney, New South Wales, Australia

Site Status

Centre For Eye Research Australia

East Melbourne, Victoria, Australia

Site Status

Retina Specialists Victoria

Rowville, Victoria, Australia

Site Status

The Lions Eye Institute

Nedlands, Western Australia, Australia

Site Status

LKH-Univ.Klinikum Graz; Universitäts-Augenklinik

Graz, , Austria

Site Status

Hospital das Clinicas - UFRGS

Porto Alegre, Rio Grande do Sul, Brazil

Site Status

Botelho Hospital da Visao

Blumenau, Santa Catarina, Brazil

Site Status

Universidade Federal de Sao Paulo - UNIFESP*X; Oftalmologia

São Paulo, São Paulo, Brazil

Site Status

Hosp de Olhos de Sorocaba

Sorocaba, São Paulo, Brazil

Site Status

Beijing Hospital of Ministry of Health

Beijing, , China

Site Status

The Second Hospital of Jilin University

Changchun, , China

Site Status

West China Hospital, Sichuan University

Chengdu, , China

Site Status

Zhongshan Ophthalmic Center, Sun Yat-sen University

Guangzhou, , China

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The 2nd Affiliated Hospital of Harbin Medical University

Harbin, , China

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The Affiliated Eye Hospital of Nanjing Medical University

Nanjing, , China

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Shanghai Tenth People's Hospital

Shanghai, , China

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Shanghai First People's Hospital

Shanghai, , China

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He Eye Specialist Shenyang Hospital

Shenyang, , China

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Tianjin Eye Hospital

Tianjin, , China

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Tianjin Medical University Eye Hospital

Tianjin, , China

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Eye Hospital, Wenzhou Medical University

Wenzhou, , China

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Renmin Hospital of Wuhan University

Wuhan, , China

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Henan Provincial Eye Hosptial

Zhengzhou, , China

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Faculty Hospital Ostrava; Ophthalmology clinic

Ostrava, , Czechia

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Faculty Hospital Kralovske Vinohrady; Ophthalmology clinic

Prague, , Czechia

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AXON Clinical

Prague, , Czechia

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Nemocnice Sokolov

Sokolov, , Czechia

Site Status

Chi De Creteil; Ophtalmologie

Créteil, , France

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Hopital Lariboisiere; Ophtalmologie

Paris, , France

Site Status

Universitätsklinikum Freiburg, Klinik für Augenheilkunde

Freiburg im Breisgau, , Germany

Site Status

Universitätsmedizin Göttingen Georg-August-Universität; Klinik für Augenheilkunde

Göttingen, , Germany

Site Status

Klinikum der Stadt Ludwigshafen am Rhein gGmbH; Augenklinik

Ludwigshafen, , Germany

Site Status

Queen Mary Hospital; Department of Ophthalmology

Hong Kong, , Hong Kong

Site Status

Hong Kong Eye Hospital; CUHK Eye Centre

Mong Kok, , Hong Kong

Site Status

Budapest Retina Associates Kft.

Budapest, , Hungary

Site Status

Debreceni Egyetem Klinikai Kozpont; Szemeszeti Klinika

Debrecen, , Hungary

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Ganglion Medial Center

Pécs, , Hungary

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Szegedi Tudományegyetem ÁOK; Department of Ophtalmology

Szeged, , Hungary

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Rambam Medical Center; Opthalmology

Haifa, , Israel

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Hadassah MC; Ophtalmology

Jerusalem, , Israel

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Rabin MC; Ophtalmology

Petah Tikva, , Israel

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Kaplan Medical Center; Ophtalmology

Rehovot, , Israel

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Tel Aviv Sourasky MC; Ophtalmology

Tel Aviv, , Israel

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Fondazione Ptv Policlinico Tor Vergata Di Roma;U.O.S.D. Patologie Renitiche

Rome, Lazio, Italy

Site Status

Fondazione Irccs Ca' Granda Ospedale Maggiore Policlinico-Clinica Regina Elena;U.O.C Oculistica

Milan, Lombardy, Italy

Site Status

Azienda Ospedaliero-Universitaria Careggi; S.O.D. Oculistica

Florence, Tuscany, Italy

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Sugita Eye Hospital

Aichi, , Japan

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Nagoya University Hospital

Aichi, , Japan

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Nagoya City University Hospital

Aichi, , Japan

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Aichi Medical University Hospital

Aichi, , Japan

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Toho University Sakura Medical Center

Chiba, , Japan

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Hayashi Eye Hospital

Fukuoka, , Japan

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Southern TOHOKU Eye Clinic

Fukushima, , Japan

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Asahikawa Medical University Hospital

Hokkaido, , Japan

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Hyogo Prefectural Amagasaki General Medical Center (Hyogo AGMC)

Hyōgo, , Japan

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Hyogo Medical University Hospital

Hyōgo, , Japan

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Kozawa eye hospital and diabetes center

Ibaraki, , Japan

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Kyoto University Hospital

Kyoto, , Japan

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Tokushima University Hospital

Tokushima, , Japan

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Nihon University Hospital

Tokyo, , Japan

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Tokyo Medical University Hachioji Medical Center

Tokyo, , Japan

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Specjalistyczny O?rodek Okulistyczny Oculomedica

Bydgoszcz, , Poland

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Szpital Specjalistyczny nr 1; Oddzial Okulistyki

Bytom, , Poland

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Dobry Wzrok Sp Z O O

Gda?sk, , Poland

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Poradnia Okulistyczna i Salon Optyczny w Gliwicach- PRYZMAT

Gliwice, , Poland

Site Status

Gabinet Okulistyczny Prof Edward Wylegala

Katowice, , Poland

Site Status

Centrum Medyczne Dietla 19 Sp. Z O.O.

Krakow, , Poland

Site Status

Centrum Medyczne Pulawska SP. z o.o.

Piaseczno, , Poland

Site Status

Lens Clinic

Rybnik, , Poland

Site Status

Caminomed

Tarnowskie Góry, , Poland

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Centrum Zdrowia MDM

Warsaw, , Poland

Site Status

Centro Hospitalar E Universitário de Coimbra EPE - Serviço Oftalmologia; Serviço Oftalmologia

Coimbra, , Portugal

Site Status

Espaco Medico Coimbra

Coimbra, , Portugal

Site Status

Centro Hospitalar Universitário do Porto ? Hospital de Santo António; Servico de Oftalmologia

Porto, , Portugal

Site Status

Clinic Optimed

Ufa, Bashkortostan Republic, Russia

Site Status

Clinics of Eye Diseases, LLC

Kazan', Tatarstan Republic, Russia

Site Status

?Intersec. Research and Technology Complex ?Eye Microsurgery? n a Fyodorov Irkutsk branch

Irkutsk, , Russia

Site Status

Singapore Eye Research Institute

Singapore, , Singapore

Site Status

Tan Tock Seng Hospital; Ophthalmology Department

Singapore, , Singapore

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Pusan National University Hospital

Busan, , South Korea

Site Status

Yeungnam University Medical Center

Daegu, , South Korea

Site Status

Seoul National University Bundang Hospital

Seongnam-si, , South Korea

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Kyung Hee University Hospital

Seoul, , South Korea

Site Status

Asan Medical Center

Seoul, , South Korea

Site Status

Samsung Medical Center

Seoul, , South Korea

Site Status

Clinica Universitaria de Navarra; Servicio de Oftalmologia

Pamplona, Navarre, Spain

Site Status

Oftalvist Valencia

Burjassot, Valencia, Spain

Site Status

Hospital dos de maig; servicio de oftalmologia

Barcelona, , Spain

Site Status

Clinica Baviera; Servicio Oftalmologia

Madrid, , Spain

Site Status

Hospital Universitario Rio Hortega; Servicio de Oftalmologia

Valladolid, , Spain

Site Status

Changhua Christian Hospital; Department of Ophthalmology

Changhua, , Taiwan

Site Status

Taipei Veterans General Hospital; Ophthalmology

Taipei, , Taiwan

Site Status

Chang Gung Medical Foundation - Linkou; Ophthalmology

Taoyuan District, , Taiwan

Site Status

National Taiwan University Hospital; Ophthalmology

Zhongzheng Dist., , Taiwan

Site Status

Belfast Health and Social Care Trust, ROYAL VICTORIA HOSPITAL

Belfast, , United Kingdom

Site Status

Bristol Eye Hospital;Retinal Treatment and Research Unit

Bristol, , United Kingdom

Site Status

University Hospital of Wales

Cardiff, , United Kingdom

Site Status

Gloucestershire Hospitals NHS Foundation Trust

Gloucestershire, , United Kingdom

Site Status

St James University Hospital

Leeds, , United Kingdom

Site Status

Central Middlesex Hospital

London, , United Kingdom

Site Status

Countries

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United States Argentina Australia Austria Brazil China Czechia France Germany Hong Kong Hungary Israel Italy Japan Poland Portugal Russia Singapore South Korea Spain Taiwan United Kingdom

References

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Romano F, Lamanna F, Gabrielle PH, Teo KYC, Battaglia Parodi M, Iacono P, Fraser-Bell S, Cornish EE, Nassisi M, Viola F, Agarwal A, Samanta A, Chhablani J, Staurenghi G, Invernizzi A. Update on Retinal Vein Occlusion. Asia Pac J Ophthalmol (Phila). 2023 Mar-Apr 01;12(2):196-210. doi: 10.1097/APO.0000000000000598. Epub 2023 Feb 14.

Reference Type DERIVED
PMID: 36912792 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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2020-000440-63

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

GR41984

Identifier Type: -

Identifier Source: org_study_id

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