A Study to Evaluate the Efficacy and Safety of Faricimab in Participants With Neovascular Age-Related Macular Degeneration (LUCERNE)

NCT ID: NCT03823300

Last Updated: 2025-07-11

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

658 participants

Study Classification

INTERVENTIONAL

Study Start Date

2019-03-11

Study Completion Date

2022-01-07

Brief Summary

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This study will evaluate the efficacy, safety, durability, and pharmacokinetics of faricimab administered at intervals as specified in the protocol, compared with aflibercept once every 8 weeks (Q8W), in participants with neovascular age-related macular degeneration (nAMD).

Detailed Description

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Conditions

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Wet Macular Degeneration

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Investigators Outcome Assessors

Study Groups

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Arm A: Faricimab

Group Type EXPERIMENTAL

Faricimab

Intervention Type DRUG

Faricimab will be administered by intravitreal injection into the study eye at intervals as specified in the study protocol.

Sham Procedure

Intervention Type PROCEDURE

The sham is a procedure that mimics an intravitreal injection, but involves the blunt end of an empty syringe (without a needle) being pressed against the anesthetized eye. It will be administered to participants in both treatment arms at applicable visits to maintain masking.

Arm B: Aflibercept

Group Type ACTIVE_COMPARATOR

Aflibercept

Intervention Type DRUG

Aflibercept will be administered by intravitreal injection into the study eye once every 4 weeks for 3 consecutive months, followed by once every 8 weeks (Q8W).

Sham Procedure

Intervention Type PROCEDURE

The sham is a procedure that mimics an intravitreal injection, but involves the blunt end of an empty syringe (without a needle) being pressed against the anesthetized eye. It will be administered to participants in both treatment arms at applicable visits to maintain masking.

Interventions

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Faricimab

Faricimab will be administered by intravitreal injection into the study eye at intervals as specified in the study protocol.

Intervention Type DRUG

Aflibercept

Aflibercept will be administered by intravitreal injection into the study eye once every 4 weeks for 3 consecutive months, followed by once every 8 weeks (Q8W).

Intervention Type DRUG

Sham Procedure

The sham is a procedure that mimics an intravitreal injection, but involves the blunt end of an empty syringe (without a needle) being pressed against the anesthetized eye. It will be administered to participants in both treatment arms at applicable visits to maintain masking.

Intervention Type PROCEDURE

Other Intervention Names

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VABYSMO™ RO6867461 RG7716 Eylea

Eligibility Criteria

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Inclusion Criteria

* Treatment-naïve choroidal neovascularization (CNV) secondary to age-related macular degeneration (nAMD) in the study eye
* Ability to comply with the study protocol, in the investigator's judgment
* For women of childbearing potential: agreement to remain abstinent (refrain from heterosexual intercourse) or use acceptable contraceptive measures that result in failure rate \<1% per year during the treatment period and for at least 3 months after the final dose of study treatment

Exclusion Criteria

* Uncontrolled blood pressure, defined as systolic blood pressure \>180 millimeters of mercury (mmHg) and/or diastolic blood pressure \>100 mmHg while a patient is at rest on Day 1
* Pregnancy or breastfeeding, or intention to become pregnant during the study
* CNV due to causes other than AMD in the study eye
* Any history of macular pathology unrelated to AMD affecting vision or contributing to the presence of intraretinal or subretinal fluid in the study eye
* Any concurrent intraocular condition in the study eye that, in the opinion of the investigator, could either reduce the potential for visual improvement or require medical or surgical intervention during the study
* Uncontrolled glaucoma in the study eye
* Any prior or concomitant treatment for CNV or vitreomacular-interface abnormalities in the study eye
* Prior IVT administration of faricimab in either eye
* History of idiopathic or autoimmune-associated uveitis in either eye
* Active ocular inflammation or suspected or active ocular or periocular infection in either eye
Minimum Eligible Age

50 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Hoffmann-La Roche

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Clinical Trials

Role: STUDY_DIRECTOR

Hoffmann-La Roche

Locations

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Associated Retina Consultants

Phoenix, Arizona, United States

Site Status

Arizona Retina and Vitreous Consultants

Phoenix, Arizona, United States

Site Status

Northern California Retina Vitreous Associates

Mountain View, California, United States

Site Status

Retinal Consultants Med Group

Sacramento, California, United States

Site Status

Orange County Retina Med Group

Santa Ana, California, United States

Site Status

California Retina Consultants

Santa Barbara, California, United States

Site Status

Colorado Retina Associates, PC

Golden, Colorado, United States

Site Status

Retina Group of Florida

Fort Lauderdale, Florida, United States

Site Status

Retina Care Specialists

Palm Beach Gardens, Florida, United States

Site Status

Southern Vitreoretinal Assoc

Tallahassee, Florida, United States

Site Status

Retina Associates of Florida, LLC

Tampa, Florida, United States

Site Status

Southeast Retina Center

Augusta, Georgia, United States

Site Status

Georgia Retina PC

Marietta, Georgia, United States

Site Status

Retina Consultants of Hawaii

‘Aiea, Hawaii, United States

Site Status

University Retina and Macula Associates, PC

Oak Forest, Illinois, United States

Site Status

Prairie Retina Center

Springfield, Illinois, United States

Site Status

Raj K. Maturi, MD PC

Indianapolis, Indiana, United States

Site Status

Wolfe Eye Clinic

West Des Moines, Iowa, United States

Site Status

Maine Eye Center

Portland, Maine, United States

Site Status

The Retina Care Center

Baltimore, Maryland, United States

Site Status

Cumberland Valley Retina PC

Hagerstown, Maryland, United States

Site Status

Retina Specialists

Towson, Maryland, United States

Site Status

Ophthalmic Consultants of Boston

Boston, Massachusetts, United States

Site Status

VitreoRetinal Surgery, PLLC.

Minneapolis, Minnesota, United States

Site Status

Mid Atlantic Retina - Wills Eye Hospital

Cherry Hill, New Jersey, United States

Site Status

Island Retina

Shirley, New York, United States

Site Status

Retina Assoc of Cleveland Inc

Cleveland, Ohio, United States

Site Status

The Ohio State University Havener Eye Institute

Columbus, Ohio, United States

Site Status

Midwest Retina

Dublin, Ohio, United States

Site Status

Palmetto Retina Center

West Columbia, South Carolina, United States

Site Status

Southeastern Retina Associates Chattanooga

Chattanooga, Tennessee, United States

Site Status

Retina Res Institute of Texas

Abilene, Texas, United States

Site Status

Austin Retina Associates

Austin, Texas, United States

Site Status

Austin Clinical Research LLC

Austin, Texas, United States

Site Status

Retina Center of Texas

Grapevine, Texas, United States

Site Status

Retina Consultants of Houston

The Woodlands, Texas, United States

Site Status

Strategic Clinical Research Group, LLC

Willow Park, Texas, United States

Site Status

Retina Associates of Utah, PLLC

Murray, Utah, United States

Site Status

Piedmont Eye Center

Lynchburg, Virginia, United States

Site Status

Wagner Kapoor Institute

Norfolk, Virginia, United States

Site Status

Pacific Northwest Retina

Silverdale, Washington, United States

Site Status

Organizacion Medica de Investigacion

Buenos Aires, , Argentina

Site Status

Fundacion Zambrano

CABA, , Argentina

Site Status

Centro Oftalmológico Dr. Charles S.A.

Capital Federal, , Argentina

Site Status

Oftalmos

Capital Federal, , Argentina

Site Status

Buenos Aires Mácula

Ciudad Autonoma Buenos Aires, , Argentina

Site Status

Oftar

Mendoza, , Argentina

Site Status

Grupo Laser Vision

Rosario, , Argentina

Site Status

Eyeclinic Albury Wodonga

Albury, New South Wales, Australia

Site Status

Marsden Eye Research Centre

Parramatta, New South Wales, Australia

Site Status

Strathfield Retina Clinic

Strathfield, New South Wales, Australia

Site Status

Sydney Eye Hospital

Sydney, New South Wales, Australia

Site Status

Sydney Retina Clinic and Day Surgery

Sydney, New South Wales, Australia

Site Status

Sydney West Retina

Westmead, New South Wales, Australia

Site Status

Centre For Eye Research Australia

East Melbourne, Victoria, Australia

Site Status

Retina Specialists Victoria

Rowville, Victoria, Australia

Site Status

The Lions Eye Institute

Nedlands, Western Australia, Australia

Site Status

LKH-Univ.Klinikum Graz

Graz, , Austria

Site Status

Medizinische Universität Wien

Vienna, , Austria

Site Status

Hospital de Olhos de Aparecida - HOA

Aparecida de Goiânia, Goiás, Brazil

Site Status

Universidade Federal de Sao Paulo - UNIFESP*X

São Paulo, São Paulo, Brazil

Site Status

Specialized Hospital for Active Treatment of Eye Diseases Zora

Sofia, , Bulgaria

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Pentagram Eye Hospital (Medical Center "Pentagram")

Sofia, , Bulgaria

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Beijing Friendship Hospital

Beijing, , China

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Beijing Tongren Hospital

Beijing, , China

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Peking Union Medical College Hospital

Beijing, , China

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The Second Hospital of Jilin University

Changchun, , China

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West China Hospital, Sichuan University

Chengdu, , China

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Southwest Hospital , Third Military Medical University

Chongqing, , China

Site Status

Army Medical Center of PLA(Daping Hospital)

Chongqing, , China

Site Status

Zhongshan Ophthalmic Center, Sun Yat-sen University

Guangzhou, , China

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The Second Affiliated Hospital of Harbin Medical University

Harbin, , China

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The Affiliated Eye Hospital of Nanjing Medical University

Nanjing, , China

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Shanghai First People's Hospital

Shanghai, , China

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He Eye Specialist Shenyang Hospital

Shenyang, , China

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Tianjin Eye Hospital

Tianjin, , China

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Eye Hospital, Wenzhou Medical University

Wenzhou, , China

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Wuxi No.2 People's Hospital

Wuxi, , China

Site Status

Rigshospitalet Glostrup

Glostrup Municipality, , Denmark

Site Status

Sjællands Universitetshospital, Roskilde

Roskilde, , Denmark

Site Status

Chi De Creteil

Créteil, , France

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Pole Vision Val d'Ouest

Écully, , France

Site Status

Hopital de la croix rousse

Lyon, , France

Site Status

Centre Paradis Monticelli

Marseille, , France

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CHU Nantes - Hôtel Dieu

Nantes, , France

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Centre Odeon

Paris, , France

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Hopital Lariboisiere

Paris, , France

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Centre Ophtalmologique

Paris, , France

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Centres Ophtalmologique St Exupéry

Saint-Cyr-sur-Loire, , France

Site Status

Universitätsklinikum Köln

Cologne, , Germany

Site Status

Universitätkslinikum Düsseldorf, Augenklinik

Düsseldorf, , Germany

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Augenabteilung am St. Franziskus-Hospital

Münster, , Germany

Site Status

Universitätsklinikum Münster

Münster, , Germany

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The University of Hong Kong

Hong Kong, , Hong Kong

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Hong Kong Eye Hospital

Mong Kok, , Hong Kong

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Bajcsy-Zsilinszky Hospital

Budapest, , Hungary

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Magyar Honvedseg Egeszsegugyi Kozpont

Budapest, , Hungary

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Szegedi Tudományegyetem ÁOK

Szeged, , Hungary

Site Status

Fondazione Ptv Policlinico Tor Vergata Di Roma

Rome, Lazio, Italy

Site Status

UNIVERSITA' DEGLI STUDI DI GENOVA - Di.N.O.G.

Genoa, Liguria, Italy

Site Status

Asst Fatebenefratelli Sacco

Milan, Lombardy, Italy

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Azienda Ospedaliero-Universitaria Careggi

Florence, Tuscany, Italy

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Nuovo Ospedale S. Chiara - A.O.U.P Presidio Ospedaliero di Cisanello

Pisa, Tuscany, Italy

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A.O. Universitaria S. Maria Della Misericordia Di Udine

Udine, Veneto, Italy

Site Status

OFTALMIKA Sp. z o.o

Bydgoszcz, , Poland

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Optimum Profesorskie Centrum Okulistyki

Gdansk, , Poland

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SP ZOZ Szpital Uniwersytecki w Krakowie Oddzia? Kliniczny Okulistyki i Onkologii Okulistycznej

Krakow, , Poland

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Caminomed

Tarnowskie Góry, , Poland

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Centro Hospitalar E Universitário de Coimbra EPE - Serviço Oftalmologia

Coimbra, , Portugal

Site Status

Hospital de Sao Joao

Porto, , Portugal

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Intersec Research and Technology Complex ?Eye Microsurgery? n.a. S.N. Fyodorov

Cheboksary, Mariy-El Republic, Russia

Site Status

1 Saint-Petersburg St. Med. University named after academician I.P.Pavlov

Saint Petersburg, Sankt-Peterburg, Russia

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?Intersec. Research and Technology Complex ?Eye Microsurgery? n a Fyodorov Irkutsk branch

Irkutsk, , Russia

Site Status

?Intersec Research and Technology Complex Eye Microsurgery n a Fyodorov Novosibirsk Branch

Novosibirsk, , Russia

Site Status

National University Hospital

Singapore, , Singapore

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Singapore Eye Research Institute

Singapore, , Singapore

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Pusan National University Hospital

Busan, , South Korea

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Yeungnam University Medical Center

Daegu, , South Korea

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Seoul National University Bundang Hospital

Gyeonggi-do, , South Korea

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Kyung Hee University Hospital

Seoul, , South Korea

Site Status

Seoul National University Hospital

Seoul, , South Korea

Site Status

Nune Eye Hospital

Seoul, , South Korea

Site Status

Asan Medical Center.

Seoul, , South Korea

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Samsung Medical Center

Seoul, , South Korea

Site Status

Hospital Universitario de Bellvitge

L'Hospitalet de Llobregat, Barcelona, Spain

Site Status

Instituto Oftalmologico Fernandez Vega

Oviedo, Principality of Asturias, Spain

Site Status

Institut de la Macula i la retina

Barcelona, , Spain

Site Status

Hospital Clinic de Barcelona

Barcelona, , Spain

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Hospital Universitario Rio Hortega

Valladolid, , Spain

Site Status

Hospital Universitario Miguel Servet

Zaragoza, , Spain

Site Status

Changhua Christian Hospital

Changhua, , Taiwan

Site Status

Taipei Veterans General Hospital

Taipei, , Taiwan

Site Status

Chang Gung Medical Foundation - Linkou

Taoyuan District, , Taiwan

Site Status

Hacettepe University Medical Faculty

Ankara, , Turkey (Türkiye)

Site Status

Ankara University Medical Faculty

Ankara, , Turkey (Türkiye)

Site Status

Gazi University Faculty of Medicine

Ankara, , Turkey (Türkiye)

Site Status

Ege University Medical Faculty

Izmir, , Turkey (Türkiye)

Site Status

Countries

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United States Argentina Australia Austria Brazil Bulgaria China Denmark France Germany Hong Kong Hungary Italy Poland Portugal Russia Singapore South Korea Spain Taiwan Turkey (Türkiye)

References

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Khanani AM, Kotecha A, Chang A, Chen SJ, Chen Y, Guymer R, Heier JS, Holz FG, Iida T, Ives JA, Lim JI, Lin H, Michels S, Quezada Ruiz C, Schmidt-Erfurth U, Silverman D, Singh R, Swaminathan B, Willis JR, Tadayoni R; TENAYA and LUCERNE Investigators. TENAYA and LUCERNE: Two-Year Results from the Phase 3 Neovascular Age-Related Macular Degeneration Trials of Faricimab with Treat-and-Extend Dosing in Year 2. Ophthalmology. 2024 Aug;131(8):914-926. doi: 10.1016/j.ophtha.2024.02.014. Epub 2024 Feb 19.

Reference Type RESULT
PMID: 38382813 (View on PubMed)

Takahashi K, Cheung CMG, Iida T, Lai TYY, Ohji M, Yanagi Y, Kawano M, Ohsawa S, Suzuki T, Kotecha A, Lin H, Patel V, Swaminathan B, Lee WK; TENAYA, LUCERNE Investigators. Efficacy, durability, and safety of faricimab in patients from Asian countries with neovascular age-related macular degeneration: 1-Year subgroup analysis of the TENAYA and LUCERNE trials. Graefes Arch Clin Exp Ophthalmol. 2023 Nov;261(11):3125-3137. doi: 10.1007/s00417-023-06071-8. Epub 2023 Jun 9.

Reference Type DERIVED
PMID: 37294433 (View on PubMed)

Khanani AM, Guymer RH, Basu K, Boston H, Heier JS, Korobelnik JF, Kotecha A, Lin H, Silverman D, Swaminathan B, Willis JR, Yoon YH, Quezada-Ruiz C. TENAYA and LUCERNE: Rationale and Design for the Phase 3 Clinical Trials of Faricimab for Neovascular Age-Related Macular Degeneration. Ophthalmol Sci. 2021 Nov 17;1(4):100076. doi: 10.1016/j.xops.2021.100076. eCollection 2021 Dec.

Reference Type DERIVED
PMID: 36246941 (View on PubMed)

Heier JS, Khanani AM, Quezada Ruiz C, Basu K, Ferrone PJ, Brittain C, Figueroa MS, Lin H, Holz FG, Patel V, Lai TYY, Silverman D, Regillo C, Swaminathan B, Viola F, Cheung CMG, Wong TY; TENAYA and LUCERNE Investigators. Efficacy, durability, and safety of intravitreal faricimab up to every 16 weeks for neovascular age-related macular degeneration (TENAYA and LUCERNE): two randomised, double-masked, phase 3, non-inferiority trials. Lancet. 2022 Feb 19;399(10326):729-740. doi: 10.1016/S0140-6736(22)00010-1. Epub 2022 Jan 24.

Reference Type DERIVED
PMID: 35085502 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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2018-004042-42

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

GR40844

Identifier Type: -

Identifier Source: org_study_id

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