A Study of Lorcaserin as Adjunctive Treatment in Participants With Dravet Syndrome

NCT ID: NCT04572243

Last Updated: 2025-10-08

Study Results

Results available

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Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE3

Total Enrollment

22 participants

Study Classification

INTERVENTIONAL

Study Start Date

2020-09-23

Study Completion Date

2024-08-15

Brief Summary

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The primary purpose of the study is to demonstrate that lorcaserin has superior efficacy compared to placebo on percent change in frequency of convulsive seizures per 28 days in participants with Dravet syndrome.

Detailed Description

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Conditions

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Epilepsies, Myoclonic

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Lorcaserin (Core Study and Open-label Extension Phase)

Participants will be randomized to receive lorcaserin administered as an oral suspension, twice daily for 14 weeks during the core treatment period. Dose will be based on body weight as follows: target dose for participants weighing 10 to less than (\<) 20, 20 to \<40, and greater than or equal to (\>=) 40 kilogram (kg) will be 5, 10, and 20 milligram per day (mg/day) respectively. Based on clinical response and tolerability and within 2 weeks of treatment, dose can be increased up to 10, 20 mg/day for participants weighing 10 to \<20, 20 to \<40 kg respectively. Participants completing the core treatment period will enter a 12-week extension phase and will receive lorcaserin.

Group Type EXPERIMENTAL

Lorcaserin

Intervention Type DRUG

Lorcaserin oral tablet, administered as oral suspension.

Placebo (Core Study) + Lorcaserin (Open-label Extension Phase)

Participants will be randomized to receive lorcaserin matching placebo administered as an oral suspension, twice daily for 14 weeks during the core treatment period. Dose will be based on body weight as follows: target dose for participants weighing 10 to \<20, 20 to \<40, and \>=40 kg will be 5, 10, and 20 mg/day respectively. Based on clinical response and tolerability and within 2 weeks of treatment, dose can be increased up to 10, 20 mg/day for participants weighing 10 to \<20, 20 to \<40 kg respectively. Participants completing the core treatment period will enter a 12-week extension phase and will receive lorcaserin.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Placebo matching to lorcaserin oral tablet, administered as oral suspension.

Lorcaserin

Intervention Type DRUG

Lorcaserin oral tablet, administered as oral suspension.

Interventions

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Placebo

Placebo matching to lorcaserin oral tablet, administered as oral suspension.

Intervention Type DRUG

Lorcaserin

Lorcaserin oral tablet, administered as oral suspension.

Intervention Type DRUG

Other Intervention Names

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E2023

Eligibility Criteria

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Inclusion Criteria

Participants must meet all of the following criteria to be included in this study:

1. Male or female, age 2 years and older at the time of informed consent
2. Diagnosis of epilepsy with Dravet syndrome
3. Has at least 4 convulsive seizures during the 4 weeks of baseline
4. Current treatment with antiepileptic drugs must be stable for at least 4 weeks before screening, and be expected to remain stable throughout the study

Exclusion Criteria

Participants who meet any of the following criteria will be excluded from this study:

1. Use of lorcaserin within 4 weeks before screening, or any history of it being discontinued due to lack of efficacy or adverse reactions
2. Use of fenfluramine within 2 months before screening, any history of lack of fenfluramine efficacy, or any history of valvulopathy at baseline with history of fenfluramine use
3. Recent or concomitant use of serotonergic medications or monoamine oxidase inhibitors
4. Presence of progressive central nervous system disease other than Dravet syndrome
Minimum Eligible Age

2 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Eisai Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Children's of Alabama / University of Alabama at Birmingham

Birmingham, Alabama, United States

Site Status

University of California Los Angeles (UCLA)

Los Angeles, California, United States

Site Status

UCSD Rady's Children's Hosptial

San Diego, California, United States

Site Status

Children's Hospital Colorado

Aurora, Colorado, United States

Site Status

Northwest Florida Clinical Research Group

Gulf Breeze, Florida, United States

Site Status

Joe DiMaggio Children's Hospital

Hollywood, Florida, United States

Site Status

Miami Children's Hospital - Nicklaus Children's Hospital

Miami, Florida, United States

Site Status

Pediatric Neurology, P.A.

Winter Park, Florida, United States

Site Status

Rare Disease Research Center Pediatrics, LLC

Atlanta, Georgia, United States

Site Status

Mid-Atlantic Epilepsy and Sleep Center - Bethesda

Bethesda, Maryland, United States

Site Status

Spectrum Health/ Helen DeVos Children's Hospital

Grand Rapids, Michigan, United States

Site Status

University of Missouri, Department of Child Health, Division of Neurology

Columbia, Missouri, United States

Site Status

Institute of Neurology and Neurosurgery at Saint Barnabas

Livingston, New Jersey, United States

Site Status

Northwell Health - Neuroscience Institute at Great Neck

New Hyde Park, New York, United States

Site Status

NYU Langone Comprehensive Epilepsy Center

New York, New York, United States

Site Status

New York Medical College

New York, New York, United States

Site Status

NorthWell Health - Lennox Hill Hospital

New York, New York, United States

Site Status

University of Rochester Medical Center

Rochester, New York, United States

Site Status

University of North Carolina

Chapel Hill, North Carolina, United States

Site Status

Duke University Hospital Center

Durham, North Carolina, United States

Site Status

University Hospitals Cleveland Medical Center

Cleveland, Ohio, United States

Site Status

Children's Hospital of Pittsburgh of UPMC

Pittsburgh, Pennsylvania, United States

Site Status

The University of Texas Health Science Center at Houston

Houston, Texas, United States

Site Status

Seattle Children's Hospital

Seattle, Washington, United States

Site Status

MultiCare Institute for Research & Innovation

Tacoma, Washington, United States

Site Status

Alberta Children's Hospital

Calgary, Alberta, Canada

Site Status

Stollery Children's Hospital

Edmonton, Alberta, Canada

Site Status

BC Children's Hospital

Vancouver, British Columbia, Canada

Site Status

Children's Hospital - VH, London Health Sciences Centre

London, Ontario, Canada

Site Status

University of Toronto Division of Hematology Oncology/The Hospital for Sick Children

Toronto, Ontario, Canada

Site Status

Countries

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United States Canada

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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E2023-A001-304

Identifier Type: -

Identifier Source: org_study_id

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