Safety and Efficacy of Retifanlimab (INCMGA00012) Alone or in Combination With Other Therapies in Participants With Advanced or Metastatic Endometrial Cancer Who Have Progressed on or After Platinum-based Chemotherapy.

NCT ID: NCT04463771

Last Updated: 2025-12-10

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

ACTIVE_NOT_RECRUITING

Clinical Phase

PHASE2

Total Enrollment

206 participants

Study Classification

INTERVENTIONAL

Study Start Date

2021-01-26

Study Completion Date

2026-07-10

Brief Summary

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This is a multicenter, open-label, nonrandomized, Phase 2 umbrella study of retifanlimab in participants who have advanced or metastatic endometrial cancer that has progressed on or after platinum-based chemotherapy. retifanlimab will be administered as monotherapy or in combination with other immunotherapy or targeted agents.

Detailed Description

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Conditions

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Endometrial Cancer

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Group D - retifanlimab + pemigatinib

Select participants who are allowed on prior checkpoint inhibitors will be administered retifanlimab intravenously in combination with oral pemigatininb (FGFR 1,2,3 inhibitor)

Group Type EXPERIMENTAL

retifanlimab

Intervention Type DRUG

INCMGA00012 administered intravenously on Day 1 of each 28-day cycle for up to 26 cycles.

pemigatinib

Intervention Type DRUG

pemigatinib will be administered orally QD.

Group E - retifanlimab + epacadostat

Select participants naïve to checkpoint inhibitors will be administered retifanlimab intravenously in combination with oral epacadostat

Group Type EXPERIMENTAL

retifanlimab

Intervention Type DRUG

INCMGA00012 administered intravenously on Day 1 of each 28-day cycle for up to 26 cycles.

epacadostat

Intervention Type DRUG

epacadostat will be administered orally BID.

Group F - retifanlimab + INCAGN02385 and INCAGN02390

Select participants who are allowed on prior checkpoint inhibitors will be administered retifanlimab in combination with INCAGN02385 and INCAGN02390 intravenously

Group Type EXPERIMENTAL

INCAGN02385

Intervention Type DRUG

INCAGN2385 will be administered every 2 weeks

INCAGN02390

Intervention Type DRUG

INCAGN2390 will be administered every 2 weeks

Group C - retifanlimab + epacadostat

Select participants who are allowed on prior checkpoint inhibitors will be administered retifanlimab intravenously in combination with oral epacadostat (IDO1 inhibitor)

Group Type EXPERIMENTAL

retifanlimab

Intervention Type DRUG

INCMGA00012 administered intravenously on Day 1 of each 28-day cycle for up to 26 cycles.

epacadostat

Intervention Type DRUG

epacadostat will be administered orally BID.

Group A - retifanlimab

Select participants naïve to checkpoint inhibitors will be administered retifanlimab intravenously

Group Type EXPERIMENTAL

retifanlimab

Intervention Type DRUG

INCMGA00012 administered intravenously on Day 1 of each 28-day cycle for up to 26 cycles.

Group B - retifanlimab

Select participants naïve to checkpoint inhibitors will be administered retifanlimab intravenously

Group Type EXPERIMENTAL

retifanlimab

Intervention Type DRUG

INCMGA00012 administered intravenously on Day 1 of each 28-day cycle for up to 26 cycles.

Interventions

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retifanlimab

INCMGA00012 administered intravenously on Day 1 of each 28-day cycle for up to 26 cycles.

Intervention Type DRUG

epacadostat

epacadostat will be administered orally BID.

Intervention Type DRUG

pemigatinib

pemigatinib will be administered orally QD.

Intervention Type DRUG

INCAGN02385

INCAGN2385 will be administered every 2 weeks

Intervention Type DRUG

INCAGN02390

INCAGN2390 will be administered every 2 weeks

Intervention Type DRUG

Other Intervention Names

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INCMGA00012

Eligibility Criteria

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Inclusion Criteria

* Ability to comprehend and willingness to sign a written ICF for the study. Note for Germany: This excludes individuals who are housed in an institution due to official or court order Women 18 years of age or older (or as applicable per local country requirements).
* Histologically confirmed diagnosis of advanced or metastatic endometrial cancer with disease progression on or after treatment with at least 1 platinum-containing regimen for advanced or metastatic disease.
* Groups A, B, and E: Have not been previously treated with a PD-(L)1 inhibitor.
* Group A only: Tumor tissue tested as MSI-High
* Group B only: Tumor tissue tested as deficient MMR or an ultra-mutated POLE tumor.
* Group D only: Tumor tissue tested as having an FGFR 1,2,3 mutation or alteration characterized as per protocol.
* Group E: Tumor tissue tested as MSS and PD-L1 positive.
* Group F: Radiological evidence of disease progression on or after prior PD (L)1 therapy and Tumor tissue tested as MSI-H
* Must have at least 1 measurable tumor lesion per RECIST v1.1.
* Willing to provide tumor tissue sample (fresh or archived).
* ECOG performance status 0 to 1.
* Willingness to avoid pregnancy.

Exclusion Criteria

* Group A, B and E only: Histologically confirmed diagnosis of carcinosarcoma of the uterus.
* Histologically confirmed diagnosis of sarcoma of the uterus.
* Has disease eligible for potentially curative treatment.
* Receipt of anticancer therapy within 28 days of the first administration of study treatment, with the exception of localized radiotherapy.
* Toxicity of prior therapy that has not recovered to ≤ Grade 1 or baseline unless approved by the medical monitor.
* Groups C, D and F (combinations): limiting immune-related toxicity during prior checkpoint inhibitor therapy.
* Group F only: Previous treatment with LAG-# or TIM-3 therapy or lenvatinib; multiple metastases that achieved mixed tumor response to prior anti-PD-(L)1 therapy
* Has an active autoimmune disease requiring systemic immunosuppression with corticosteroids (\> 10 mg/day of prednisone or equivalent) or immunosuppressive drugs within 14 days before the first dose of study treatment.
* Receiving chronic systemic steroids (\> 10 mg/day of prednisone or equivalent):
* Known active CNS metastases and/or carcinomatous meningitis.
* Has known active hepatitis B or C.
* Has received a live vaccine within 28 days of the planned start of study treatment.
* Evidence of interstitial lung disease or active, noninfectious pneumonitis.
* Participants who are known to be HIV-positive with some protocol exceptions.
Minimum Eligible Age

18 Years

Eligible Sex

FEMALE

Accepts Healthy Volunteers

No

Sponsors

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GOG Foundation

NETWORK

Sponsor Role collaborator

European Network of Gynaecological Oncological Trial Groups (ENGOT)

OTHER

Sponsor Role collaborator

Incyte Corporation

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Mark Cornfield

Role: STUDY_DIRECTOR

Incyte Corporation

Locations

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European Institute of Oncology

Milan, , Italy

Site Status

Istituto Nazionale Tumori Irccs Fondazione Pascale

Napoli, , Italy

Site Status

Iov - Istituto Oncologico Veneto Irccs

Padua, , Italy

Site Status

Fondazione Policlinico Universitario Agostino Gemelli Irccs

Roma, , Italy

Site Status

Ospedale Santa Maria Ca Foncello

Treviso, , Italy

Site Status

Alaska Womens Cancer Care Akwcc

Anchorage, Alaska, United States

Site Status

Honorhealth

Phoenix, Arizona, United States

Site Status

Arizona Oncology Associates

Tucson, Arizona, United States

Site Status

UCLA Medical Hematology & Oncology

Los Angeles, California, United States

Site Status

Olive View Med Ctr

Sylmar, California, United States

Site Status

Broward Health Medical Center

Fort Lauderdale, Florida, United States

Site Status

Miami Cancer Institute

Miami, Florida, United States

Site Status

Mount Sinai Medical Center Comprehensive Cancer Center

Miami Beach, Florida, United States

Site Status

Advent Health Medical Group-Orlando 2501

Orlando, Florida, United States

Site Status

H. Lee Moffitt Cancer Center and Research Institute Hospital

Tampa, Florida, United States

Site Status

Georgia Cancer Center

Augusta, Georgia, United States

Site Status

Barbara Ann Karmanos Cancer Hospital

Detroit, Michigan, United States

Site Status

Minnesota Oncology-Maplewood

Coon Rapids, Minnesota, United States

Site Status

Midwest Cancer Care

Kansas City, Missouri, United States

Site Status

Washington University

St Louis, Missouri, United States

Site Status

Billings Clinic Cancer Center

Billings, Montana, United States

Site Status

Comprehensive Cancer Centers of Nevada

Henderson, Nevada, United States

Site Status

New Mexico Cancer Care Alliance

Albuquerque, New Mexico, United States

Site Status

Laura & Isaac Perlmutter Cancer Ctr

New York, New York, United States

Site Status

University of North Carolina At Chapel Hill

Chapel Hill, North Carolina, United States

Site Status

The Ohio State University Wexner Medical Center Division of Gynecologic Oncology

Hilliard, Ohio, United States

Site Status

Willamette Valley Cancer Institute

Eugene, Oregon, United States

Site Status

Texas Oncology-Tyler

Sioux Falls, South Dakota, United States

Site Status

Tennessee Oncology

Nashville, Tennessee, United States

Site Status

Texas Oncology-Austin Center

Austin, Texas, United States

Site Status

Texas Oncology-Fort Worth South Henderson

Fort Worth, Texas, United States

Site Status

Texas Oncology San Antonio

San Antonio, Texas, United States

Site Status

Texas Oncology the Woodlands

Shenandoah, Texas, United States

Site Status

Virginia Commonwealth University

Richmond, Virginia, United States

Site Status

O.L.V Ziekenhuis

Aalst, , Belgium

Site Status

Institut Jules Bordet

Brussels, , Belgium

Site Status

Ghent University Hospital

Ghent, , Belgium

Site Status

Universitaire Ziekenhuis Leuven - Gasthuisberg

Leuven, , Belgium

Site Status

Centre Hospitalier Universitaire de Liege - Sart Tilman

Liège, , Belgium

Site Status

Chu Ucl Namur de Saint Elisabeth

Namur, , Belgium

Site Status

Chu Besancon Hospital Jean Minjoz

Besançon, , France

Site Status

Institut Bergonie

Bordeaux, , France

Site Status

Hospital Cochin Cancerologie

Paris, , France

Site Status

Cario - Centre Armoricain de Radiotherapie Imagerie Medicale Et Oncologie

Plérin, , France

Site Status

Centre de Lutte Contre Le Cancer - Institut de Cancerologie de L'Ouest - Rene Gauducheau

Saint-Herblain, , France

Site Status

Institut Gustave Roussy

Villejuif, , France

Site Status

High Technology Hospital Medcenter

Batumi, , Georgia

Site Status

Jsc Evex Hospitals

Kutaisi, , Georgia

Site Status

Todua Clinic, Llc

Tbilisi, , Georgia

Site Status

Caucasus Medical Centre Llc

Tbilisi, , Georgia

Site Status

INNOVA

Tbilisi, , Georgia

Site Status

Multiprofile Clinic Consilium Medulla Llc

Tbilisi, , Georgia

Site Status

Charite - Campus Virchow-Klinikum

Berlin, , Germany

Site Status

University Clinic Carl Gustav Carus Technical University Dresden

Dresden, , Germany

Site Status

Klinikum Kassel Gmbh

Kassel, , Germany

Site Status

Universitarsfrauenklinik Ulm

Ulm, , Germany

Site Status

Alexandra General Hospital of Athens

Athens, , Greece

Site Status

University Hospital of West Attica - Attikon

Athens, , Greece

Site Status

Hygeia Hospital

Marousi, , Greece

Site Status

Euromedica General Clinic of Thessaloniki

Thessaloniki, , Greece

Site Status

Azienda Ospedaliero-Universitaria Di Bologna Policlinico S. Orsola - Malpighi

Bologna, , Italy

Site Status

Presidio Ospedaliero Di Summa Antonio Perrino

Brindisi, , Italy

Site Status

Istituto Scientifico Romagnolo Per Lo Studio E La Cura Dei Tumori

Meldola, , Italy

Site Status

Istituto Di Ricovero E Cura A Carattere Scientifico (Irccs) Ospedale San Raffaele

Milan, , Italy

Site Status

Comitato Etico Fondazione Irccs Istituto Nazionale Dei Tumori Milano

Milan, , Italy

Site Status

Countries

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United States Belgium France Georgia Germany Greece Italy

Related Links

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https://incyteclinicaltrials.com/studies/incmga-0012-204

Safety and Efficacy of Retifanlimab (INCMGA00012) Alone or in Combination With Other Therapies in Participants With Advanced or Metastatic Endometrial Cancer Who Have Progressed on or After Platinum-based Chemotherapy.

Other Identifiers

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2022-502600-79-00

Identifier Type: REGISTRY

Identifier Source: secondary_id

2020-000496-20

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

INCMGA 0012-204

Identifier Type: -

Identifier Source: org_study_id

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