Study of Navtemadlin as Maintenance Therapy in TP53WT Advanced or Recurrent Endometrial Cancer

NCT ID: NCT05797831

Last Updated: 2024-05-02

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE2/PHASE3

Total Enrollment

268 participants

Study Classification

INTERVENTIONAL

Study Start Date

2023-07-17

Study Completion Date

2027-07-31

Brief Summary

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This study evaluates navtemadlin as maintenance treatment for patients with advanced or recurrent endometrial cancer (EC) who have achieved complete response or partial response on chemotherapy.

The study will be conducted in 2 parts. Part 1 will evaluate safety and efficacy of two different doses of navtemadlin alongside an observational control arm to determine the Phase 3 navtemadlin dose. Part 2 will evaluate the efficacy and safety of navtemadlin Phase 3 dose compared to placebo.

Detailed Description

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Conditions

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Endometrial Cancer

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Part 1 Arm 1

Navtemadlin administered orally at 180 mg, once daily (QD) on Days 1-7 in a 28-day treatment cycles.

Group Type EXPERIMENTAL

Navtemadlin

Intervention Type DRUG

Navtemadlin is an experimental MDM2 anticancer drug taken by mouth

Part 1 Arm 2

Navtemadlin administered orally at 240 mg, once daily (QD) on Days 1-7 in a 28-day treatment cycles.

Group Type EXPERIMENTAL

Navtemadlin

Intervention Type DRUG

Navtemadlin is an experimental MDM2 anticancer drug taken by mouth

Part 1 Arm 3

Observational control ("watch and wait") on a 28-day cycle.

Group Type NO_INTERVENTION

No interventions assigned to this group

Part 2 Arm A

Navtemadlin administered orally at 180 mg once daily (QD) on Days 1-7 in a 28-day treatment cycles.

Group Type EXPERIMENTAL

Navtemadlin

Intervention Type DRUG

Navtemadlin is an experimental MDM2 anticancer drug taken by mouth

Part 2 Arm B

Navtemadlin administered orally at 240 mg once daily (QD) on Days 1-7 in a 28-day treatment cycles.

Group Type EXPERIMENTAL

Navtemadlin

Intervention Type DRUG

Navtemadlin is an experimental MDM2 anticancer drug taken by mouth

Part 2 Arm C

Placebo administered orally at 180 mg once daily (QD) on Days 1-7 in a 28-day administration cycle.

Group Type PLACEBO_COMPARATOR

Navtemadlin Placebo

Intervention Type DRUG

Navtemadlin placebo is a placebo that is the same in appearance to navtemadlin drug taken by mouth

Part 2 Arm D

Placebo administered orally at 240 mg once daily (QD) on Days 1-7 in a 28-day administration cycle.

Group Type PLACEBO_COMPARATOR

Navtemadlin Placebo

Intervention Type DRUG

Navtemadlin placebo is a placebo that is the same in appearance to navtemadlin drug taken by mouth

Interventions

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Navtemadlin

Navtemadlin is an experimental MDM2 anticancer drug taken by mouth

Intervention Type DRUG

Navtemadlin Placebo

Navtemadlin placebo is a placebo that is the same in appearance to navtemadlin drug taken by mouth

Intervention Type DRUG

Other Intervention Names

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KRT-232

Eligibility Criteria

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Inclusion Criteria

* ECOG 0-1
* Histologically or cytologically confirmed diagnosis of endometrial cancer documented as TP53WT
* Subjects with advanced or recurrent disease must have completed a single line of up to 6 cycles of taxane-platinum based chemo and achieved a CR or PR per RECIST V1.1
* Adequate hematologic, hepatic and renal function (within 14 days)

Exclusion Criteria

* Has any sarcomas or small-cell carcinomas with neuroendocrine differentiation
* Prior immune therapy, cytokine therapy, or any investigational therapy (within 28 days)
* Indwelling surgical drains
* Grade 2 or higher QTc prolongation
* History of major organ transplant
* History of bleeding diathesis; major hemorrhage or intracranial hemorrhage (within 24 weeks)
Minimum Eligible Age

18 Years

Eligible Sex

FEMALE

Accepts Healthy Volunteers

No

Sponsors

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GOG Foundation

NETWORK

Sponsor Role collaborator

European Network of Gynaecological Oncological Trial Groups (ENGOT)

OTHER

Sponsor Role collaborator

Kartos Therapeutics, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Kaiser Permanente Center

Vallejo, California, United States

Site Status RECRUITING

Northside Hospital

Atlanta, Georgia, United States

Site Status RECRUITING

St. Joseph

Savannah, Georgia, United States

Site Status RECRUITING

Dr. Sudarshan K. Sharma, Ltd.

Hinsdale, Illinois, United States

Site Status RECRUITING

Parkview Research Center

Fort Wayne, Indiana, United States

Site Status RECRUITING

Indiana University

Indianapolis, Indiana, United States

Site Status RECRUITING

Maryland Oncology Hematology, P.A.

Silver Spring, Maryland, United States

Site Status RECRUITING

Minnesota Oncology Hematology, P.A.

Minneapolis, Minnesota, United States

Site Status RECRUITING

Washington University School of Medicine

St Louis, Missouri, United States

Site Status RECRUITING

Women's Cancer Center of Nevada

Las Vegas, Nevada, United States

Site Status RECRUITING

Good Samaritan Hospital Medical Center

West Islip, New York, United States

Site Status RECRUITING

FirstHealth Carolinas

Pinehurst, North Carolina, United States

Site Status RECRUITING

OhioHealth Institute

Columbus, Ohio, United States

Site Status RECRUITING

Oklahoma Cancer Specialists and Research Institute

Tulsa, Oklahoma, United States

Site Status RECRUITING

Oncology Associates of Oregon

Eugene, Oregon, United States

Site Status RECRUITING

Northwest Cancer Specialists

Portland, Oregon, United States

Site Status RECRUITING

Texas Oncology-Austin Central

Austin, Texas, United States

Site Status RECRUITING

Texas Oncology-Fort Worth Cancer Center

Fort Worth, Texas, United States

Site Status RECRUITING

Texas Oncology-San Antonio Medical Center

San Antonio, Texas, United States

Site Status RECRUITING

University Hospital Graz, Department of Gynecology and Obstetrics

Graz, , Austria

Site Status RECRUITING

Medizinische Universität Innsbruck

Innsbruck, , Austria

Site Status RECRUITING

Medizinische Universität Wien

Vienna, , Austria

Site Status RECRUITING

Cross Cancer Institute

Edmonton, , Canada

Site Status RECRUITING

CHUM - University of Montreal Hospital Centre

Montreal, , Canada

Site Status RECRUITING

Odense University Hospital

Odense, , Denmark

Site Status RECRUITING

Tartu University Hospital

Tartu, , Estonia

Site Status RECRUITING

Kuopio University Hospital

Kuopio, , Finland

Site Status RECRUITING

Turku University Hospital

Turku, , Finland

Site Status RECRUITING

LTD High Technology hospital Medcenter

Batumi, , Georgia

Site Status RECRUITING

American Hospital Network LLC

Tbilisi, , Georgia

Site Status RECRUITING

Caucasus Medical Centre

Tbilisi, , Georgia

Site Status RECRUITING

National Institute of Oncology

Budapest, , Hungary

Site Status RECRUITING

University of Debrecen Clinical Center

Debrecen, , Hungary

Site Status RECRUITING

Rambam Medical Center

Haifa, , Israel

Site Status RECRUITING

Shaare Zedek Medical Center

Jerusalem, , Israel

Site Status RECRUITING

Sourasky Medical Center

Tel Aviv, , Israel

Site Status RECRUITING

A.O. Cannizzaro

Catania, , Italy

Site Status RECRUITING

IRCCS Istituto Romangolo per lo Studio dei Tumori "Dino Amadori"

Forlì, , Italy

Site Status RECRUITING

Ospedale Policlinico San Martino

Genoa, , Italy

Site Status RECRUITING

ASST di Lecco-Ospedale Alessandro Manzoni

Lecco, , Italy

Site Status RECRUITING

Ospedale San Luca

Lucca, , Italy

Site Status RECRUITING

Osp. Niguarda

Milan, , Italy

Site Status RECRUITING

University Hospital of Parma

Parma, , Italy

Site Status RECRUITING

Ospedale Guglielmo da Saliceto

Piacenza, , Italy

Site Status RECRUITING

Ospedale di Prato S. Stefano

Prato, , Italy

Site Status RECRUITING

Ospedale Santa Maria delle Croci

Ravenna, , Italy

Site Status RECRUITING

"Azienda Unità Sanitaria Locale della Romagna - Hospital ""Infermi"" of Rimini Oncology Department"

Rimini, , Italy

Site Status RECRUITING

Policlinico Umberto

Rome, , Italy

Site Status RECRUITING

Ospedale Filippo Del Ponte

Varese, , Italy

Site Status RECRUITING

Health Sciences Kaunas Clinics

Kaunas, , Lithuania

Site Status RECRUITING

Nation Cancer Institute of Lithuania, Vilnius

Vilnius, , Lithuania

Site Status RECRUITING

Southern Hospital Sorlandet

Kristiansand, , Norway

Site Status RECRUITING

Oslo University Hospital HF

Oslo, , Norway

Site Status RECRUITING

Sykehusapotek Nord Tromsø

Tromsø, , Norway

Site Status RECRUITING

Białostockie Centrum Onkologii

Bialystok, , Poland

Site Status RECRUITING

Szpitale Pomorskie

Gdansk, , Poland

Site Status RECRUITING

Uniwersyteckie Centrum Kliniczne

Gdansk, , Poland

Site Status RECRUITING

NIO-PIB Oddzial w Gliwicach

Gliwice, , Poland

Site Status RECRUITING

Centrum Badań klinicznych Jagiellońskie Centrum Innowacji

Krakow, , Poland

Site Status RECRUITING

Siedleckie Centrum Onkologii

Olsztyn, , Poland

Site Status RECRUITING

Uniwersytecki Szpital

Poznan, , Poland

Site Status RECRUITING

NIO-PIB Klinika Gine-Onk

Warsaw, , Poland

Site Status RECRUITING

Lower Silesian Oncology, Pulmonology and Hematology Center, Department of Oncological Gynecology

Wroclaw, , Poland

Site Status RECRUITING

Bucharest CF2 Hospital

Bucharest, , Romania

Site Status RECRUITING

Ovidius Clinical Hospital SRL

Constanța, , Romania

Site Status RECRUITING

Onco Clinic Consult S.A.

Craiova, , Romania

Site Status RECRUITING

Oncology Center "Sf. Nectarie"

Craiova, , Romania

Site Status RECRUITING

Gral Medical S.R.L. - Oncofort Hospital

Piteşti, , Romania

Site Status RECRUITING

Oncocenter, Oncology Clinic SRL

Timișoara, , Romania

Site Status RECRUITING

SC Oncomed SRL

Timișoara, , Romania

Site Status RECRUITING

Institute of Oncology Ljubljana

Ljubljana, , Slovenia

Site Status RECRUITING

University Clinical Center Maribor

Maribor, , Slovenia

Site Status RECRUITING

CHUAC (Hospital de Coruña)

A Coruña, , Spain

Site Status RECRUITING

Hospital del Mar

Barcelona, , Spain

Site Status RECRUITING

Hospital Galdakao-Usansolo

Galdakao, , Spain

Site Status RECRUITING

Hospital Universitario de Jaen

Jaén, , Spain

Site Status RECRUITING

H.G.U. Jerez de la Frontera

Jerez de la Frontera, , Spain

Site Status RECRUITING

Hospital U Insular de GC

Las Palmas, , Spain

Site Status RECRUITING

Hospital de Leon

León, , Spain

Site Status RECRUITING

HCU Santiago de Compostela

Santiago de Compostela, , Spain

Site Status RECRUITING

Hospital Universitario de Valme

Seville, , Spain

Site Status RECRUITING

Linkoping University Hospital

Linköping, , Sweden

Site Status RECRUITING

Karolinska University Hospital

Stockholm, , Sweden

Site Status RECRUITING

Countries

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United States Austria Canada Denmark Estonia Finland Georgia Hungary Israel Italy Lithuania Norway Poland Romania Slovenia Spain Sweden

Central Contacts

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John Mei

Role: CONTACT

650-542-0136

Other Identifiers

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ENGOT en-21

Identifier Type: OTHER

Identifier Source: secondary_id

GOG-3089

Identifier Type: OTHER

Identifier Source: secondary_id

KRT-232-118

Identifier Type: -

Identifier Source: org_study_id

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