A Study to Evaluate the Safety and Efficacy of Tocilizumab in Patients With Severe COVID-19 Pneumonia

NCT ID: NCT04320615

Last Updated: 2021-06-30

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

View full results

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

452 participants

Study Classification

INTERVENTIONAL

Study Start Date

2020-04-03

Study Completion Date

2020-07-28

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

This study will evaluate the efficacy, safety, pharmacodynamics, and pharmacokinetics of tocilizumab (TCZ) compared with a matching placebo in combination with standard of care (SOC) in hospitalized patients with severe COVID-19 pneumonia.

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

COVID-19 Pneumonia

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

Tocilizumab (TCZ) Arm

Participants will receive 1 intravenous (IV) infusion of TCZ, dosed at 8 mg/kg, up to a maximum dose 800 mg. Up to 1 additional dose may be given if clinical symptoms worsen or show no improvement.

Group Type EXPERIMENTAL

Tocilizumab (TCZ)

Intervention Type DRUG

Participants will receive 1 dose of IV TCZ. 1 additional dose may be given if clinical symptoms worsen or show no improvement.

Placebo Arm

Participants will receive 1 IV infusion of placebo matched to TCZ. Up to 1 additional dose may be given if clinical symptoms worsen or show no improvement.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Participants will receive 1 dose of IV placebo matched to TCZ. Up to 1 additional dose may be given if clinical symptoms worsen or show no improvement.

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

Tocilizumab (TCZ)

Participants will receive 1 dose of IV TCZ. 1 additional dose may be given if clinical symptoms worsen or show no improvement.

Intervention Type DRUG

Placebo

Participants will receive 1 dose of IV placebo matched to TCZ. Up to 1 additional dose may be given if clinical symptoms worsen or show no improvement.

Intervention Type DRUG

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

* Hospitalized with COVID-19 pneumonia confirmed per WHO criteria (including a positive PCR of any specimen; e.g., respiratory, blood, urine, stool, other bodily fluid) and evidenced by chest X-ray or CT scan
* SPO2 \</=93% or PaO2/FiO2 \<300 mmHg

Exclusion Criteria

* Known severe allergic reactions to TCZ or other monoclonal antibodies
* Active tuberculosis (TB) infection
* Suspected active bacterial, fungal, viral, or other infection (besides COVID-19)
* In the opinion of the investigator, progression to death is imminent and inevitable within the next 24 hours, irrespective of the provision of treatments
* Have received oral anti-rejection or immunomodulatory drugs (including TCZ) with the past 3 months
* Participating in other drug clinical trials (participation in COVID-19 anti-viral trials may be permitted if approved by Medical Monitor)
* Pregnant or breastfeeding, or positive pregnancy test in a pre-dose examination
* Treatment with an investigational drug within 5 half-lives or 30 days (whichever is longer) of randomization (investigational COVID-19 antivirals may be permitted if approved by Medial Monitor)
* Any serious medical condition or abnormality of clinical laboratory tests that, in the investigator's judgment, precludes the patient's safe participation in and completion of the study
* Alanine aminotransferase (ALT) or aspartate aminotransferase (AST) \> 10 x upper limit of normal (ULN) detected within 24 hours at screening (per local lab)
* Absolute neutrophil count (ANC) \< 1000/mL at screening (per local lab)
* Platelet count \< 50,000/mL at screening (per local lab)
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

Hoffmann-La Roche

INDUSTRY

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Responsibility Role SPONSOR

Principal Investigators

Learn about the lead researchers overseeing the trial and their institutional affiliations.

Clinical Trials

Role: STUDY_DIRECTOR

Hoffmann-La Roche

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

University of California San Diego

La Jolla, California, United States

Site Status

eStudySite

La Mesa, California, United States

Site Status

David Geffen School of Medicine UCLA

Los Angeles, California, United States

Site Status

Stanford University

Stanford, California, United States

Site Status

Denver Health Medical Center

Denver, Colorado, United States

Site Status

University of Miami Miller School of Medicine

Miami, Florida, United States

Site Status

Rush University Medical Center

Chicago, Illinois, United States

Site Status

University of Chicago

Chicago, Illinois, United States

Site Status

Ochsner Clinic Foundation

Baton Rouge, Louisiana, United States

Site Status

Baystate Health System

Springfield, Massachusetts, United States

Site Status

Mayo Clinic - PPDS

Rochester, Minnesota, United States

Site Status

Hackensack University Medical Center

Hackensack, New Jersey, United States

Site Status

Robert Wood Johnson University Hospital/Rutgers

New Brunswick, New Jersey, United States

Site Status

James J Peters Veterans Administration Medical Center - NAVREF

The Bronx, New York, United States

Site Status

Duke University Medical Center

Durham, North Carolina, United States

Site Status

Cleveland Clinic Foundation; Pulmonary, Allergy & Critical Care Medicine

Cleveland, Ohio, United States

Site Status

Thomas Jefferson University

Philadelphia, Pennsylvania, United States

Site Status

Baylor St. Luke's Medical Center

Houston, Texas, United States

Site Status

Ben Taub General Hospital - HCHD

Houston, Texas, United States

Site Status

Intermountain LDS Hospital

Salt Lake City, Utah, United States

Site Status

Intermountain Medical Group

St. George, Utah, United States

Site Status

Evergreen Health Infectious Disease

Kirkland, Washington, United States

Site Status

Swedish Hospital Medical Center

Seattle, Washington, United States

Site Status

Hamilton General Hospital; Pharmacy

Hamilton, Ontario, Canada

Site Status

St. Joseph's Healthcare Hamilton

Hamilton, Ontario, Canada

Site Status

University Health Network

Toronto, Ontario, Canada

Site Status

Clinical Research Institute of Montreal

Montreal, Quebec, Canada

Site Status

Rigshospitalet Copenhagen University Hospital

Copenhagen, , Denmark

Site Status

Hvidovre Hospital

Hvidovre, , Denmark

Site Status

Odense Universitetshospital

Odense C, , Denmark

Site Status

Sjællands Universitetshospital, Roskilde

Roskilde, , Denmark

Site Status

Centre Hospitalier Departemental de Vendee

La Roche-sur-Yon, , France

Site Status

Centre Hospitalier et Universitaire de Limoges

Limoges, , France

Site Status

Hôpital de La Croix Rousse

Lyon, , France

Site Status

Hotel Dieu - Nantes

Nantes, , France

Site Status

Hopital de la Pitie Salpetriere

Paris, , France

Site Status

HOPITAL COCHIN university hospital

Paris, , France

Site Status

CHRU de Tours, Pharmacie

Tours, , France

Site Status

Universitätsklinikum Köln; Innere Medizin I; Onkologie, Hämatologie

Cologne, , Germany

Site Status

Universitatsklinikum Dusseldorf

Düsseldorf, , Germany

Site Status

Medizinische Hochschule Hannover

Hanover, , Germany

Site Status

LMU Klinikum der Universitat Munchen

München, , Germany

Site Status

Azienda Ospedaliera San Gerardo di Monza

Monza MI, Lombardy, Italy

Site Status

Fondazione IRCCS Policlinico San Matteo di Pavia; S.S. Fisiopatologia Respiratoria

Pavia, Lombardy, Italy

Site Status

Amphia Ziekenhuis

Breda, , Netherlands

Site Status

St. Antonius Ziekenhuis Nieuwegein

Nieuwegein, , Netherlands

Site Status

Erasmus MC

Rotterdam, , Netherlands

Site Status

Universitair Medisch Centrum Utrecht

Utrecht, , Netherlands

Site Status

Hospital Universitario de Bellvitge

L'Hospitalet de Llobregat, Barcelona, Spain

Site Status

Hospital Universitari Vall d'Hebron

Barcelona, , Spain

Site Status

Hospital Clinic de Barcelona

Barcelona, , Spain

Site Status

Hospital Universitario La Paz

Madrid, , Spain

Site Status

Hospital Universitario Ramon y Cajal

Madrid, , Spain

Site Status

Hospital General Universitario Gregorio Maranon

Madrid, , Spain

Site Status

Hospital Universitario HM Sanchinarro-CIOCC

Madrid, , Spain

Site Status

Greater Glasgow and Clyde Health Board

Glasgow, , United Kingdom

Site Status

Leeds Teaching Hospitals NHS Trust

Leeds, , United Kingdom

Site Status

University College Hospital

London, , United Kingdom

Site Status

Royal Free Hospital

London, , United Kingdom

Site Status

St George's Clinical Research Facility

London, , United Kingdom

Site Status

Imperial College London

London, , United Kingdom

Site Status

North Manchester General Hospital

Manchester, , United Kingdom

Site Status

Countries

Review the countries where the study has at least one active or historical site.

United States Canada Denmark France Germany Italy Netherlands Spain United Kingdom

References

Explore related publications, articles, or registry entries linked to this study.

Rosas IO, Brau N, Waters M, Go RC, Malhotra A, Hunter BD, Bhagani S, Skiest D, Savic S, Douglas IS, Garcia-Diaz J, Aziz MS, Cooper N, Youngstein T, Sorbo LD, Zerda DJ, Ustianowski A, Gracian AC, Blyth KG, Carratala J, Francois B, Benfield T, Haslem D, Bonfanti P, van der Leest CH, Rohatgi N, Wiese L, Luyt CE, Bauer RN, Cai F, Lee IT, Matharu B, Metcalf L, Wildum S, Graham E, Tsai L, Bao M. Tocilizumab in patients hospitalised with COVID-19 pneumonia: Efficacy, safety, viral clearance, and antibody response from a randomised controlled trial (COVACTA). EClinicalMedicine. 2022 May;47:101409. doi: 10.1016/j.eclinm.2022.101409. Epub 2022 Apr 21.

Reference Type DERIVED
PMID: 35475258 (View on PubMed)

Tom J, Bao M, Tsai L, Qamra A, Summers D, Carrasco-Triguero M, McBride J, Rosenberger CM, Lin CJF, Stubbings W, Blyth KG, Carratala J, Francois B, Benfield T, Haslem D, Bonfanti P, van der Leest CH, Rohatgi N, Wiese L, Luyt CE, Kheradmand F, Rosas IO, Cai F. Prognostic and Predictive Biomarkers in Patients With Coronavirus Disease 2019 Treated With Tocilizumab in a Randomized Controlled Trial. Crit Care Med. 2022 Mar 1;50(3):398-409. doi: 10.1097/CCM.0000000000005229.

Reference Type DERIVED
PMID: 34612846 (View on PubMed)

Rosas IO, Brau N, Waters M, Go RC, Hunter BD, Bhagani S, Skiest D, Aziz MS, Cooper N, Douglas IS, Savic S, Youngstein T, Del Sorbo L, Cubillo Gracian A, De La Zerda DJ, Ustianowski A, Bao M, Dimonaco S, Graham E, Matharu B, Spotswood H, Tsai L, Malhotra A. Tocilizumab in Hospitalized Patients with Severe Covid-19 Pneumonia. N Engl J Med. 2021 Apr 22;384(16):1503-1516. doi: 10.1056/NEJMoa2028700. Epub 2021 Feb 25.

Reference Type DERIVED
PMID: 33631066 (View on PubMed)

Provided Documents

Download supplemental materials such as informed consent forms, study protocols, or participant manuals.

Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

2020-001154-22

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

WA42380

Identifier Type: -

Identifier Source: org_study_id

More Related Trials

Additional clinical trials that may be relevant based on similarity analysis.

A Phase I Study of XJ101 in Chinese Healthy Subjects
NCT06014736 ACTIVE_NOT_RECRUITING PHASE1