Efficacy of Deutetrabenazine to Control Symptoms of Dysphagia Associated with HD

NCT ID: NCT04301726

Last Updated: 2025-02-27

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE1

Total Enrollment

36 participants

Study Classification

INTERVENTIONAL

Study Start Date

2022-01-21

Study Completion Date

2023-09-01

Brief Summary

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To determine the efficacy of deutetrabenazine to control symptoms of dysphagia associated with HD.

Detailed Description

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The primary endpoint is the change in swallow function/dysphagia from baseline to maintenance therapy.

Conditions

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Huntington Disease

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Placebo-controlled pilot study
Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Investigators Outcome Assessors

Study Groups

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Deutetrabenazine

The participants randomized to this group will receive oral deutetrabenazine for 8 weeks. Week 1: 6 mg once daily; Week 2: 6 mg twice daily (BID); Week 3: 9 mg BID; Week 4: 12 BID; Week 5: 15 mg BID; Week 6: 18 mg BID; Week 7: 21 mg BID; Week 8: 24 mg BID.

Group Type EXPERIMENTAL

Deutetrabenazine Oral Tablet [Austedo]

Intervention Type DRUG

The participants randomized to this group will receive oral deutetrabenazine for 8 weeks. Week 1: 6 mg tab once daily; Week 2: 6 mg tab (BID); Week 3: 9 mg tab (BID); Week 4: 12 mg tab (BID); Week 5: 15 mg (6 mg tab + 9 mg tab BID); Week 6: 18 mg (9 mg tab + 9 mg tab BID); Week 7: 21 mg (9 mg tab + 12 mg tab BID); Week 8: 24 mg (12 mg tab BID).

Placebo

The participants randomized to this group will receive oral placebo for 8 weeks. Week 1: 6 mg once daily; Week 2: 6 mg twice daily (BID); Week 3: 9 mg BID; Week 4: 12 BID; Week 5: 15 mg BID; Week 6: 18 mg BID; Week 7: 21 mg BID; Week 8: 24 mg BID.

Group Type PLACEBO_COMPARATOR

Placebo oral tablet

Intervention Type DRUG

The participants randomized to this group will receive oral placebo for 8 weeks. Week 1: 6 mg tab once daily; Week 2: 6 mg tab (BID); Week 3: 9 mg tab (BID); Week 4: 12 mg tab (BID); Week 5: 15 mg (6 mg tab + 9 mg tab BID); Week 6: 18 mg (9 mg tab + 9 mg tab BID); Week 7: 21 mg (9 mg tab + 12 mg tab BID); Week 8: 24 mg (12 mg tab BID).

Interventions

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Deutetrabenazine Oral Tablet [Austedo]

The participants randomized to this group will receive oral deutetrabenazine for 8 weeks. Week 1: 6 mg tab once daily; Week 2: 6 mg tab (BID); Week 3: 9 mg tab (BID); Week 4: 12 mg tab (BID); Week 5: 15 mg (6 mg tab + 9 mg tab BID); Week 6: 18 mg (9 mg tab + 9 mg tab BID); Week 7: 21 mg (9 mg tab + 12 mg tab BID); Week 8: 24 mg (12 mg tab BID).

Intervention Type DRUG

Placebo oral tablet

The participants randomized to this group will receive oral placebo for 8 weeks. Week 1: 6 mg tab once daily; Week 2: 6 mg tab (BID); Week 3: 9 mg tab (BID); Week 4: 12 mg tab (BID); Week 5: 15 mg (6 mg tab + 9 mg tab BID); Week 6: 18 mg (9 mg tab + 9 mg tab BID); Week 7: 21 mg (9 mg tab + 12 mg tab BID); Week 8: 24 mg (12 mg tab BID).

Intervention Type DRUG

Other Intervention Names

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Austedo Placebo

Eligibility Criteria

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Inclusion Criteria

* Confirmed diagnosis of HD
* Symptoms of dysphagia
* Must be able to swallow tablets

Exclusion Criteria

* Other confounding diseases that affect swallowing
* Depression
* Hepatic impairment
* Renal impairment
* Dementia
Minimum Eligible Age

21 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Fundacion Huntington Puerto Rico

OTHER

Sponsor Role lead

Responsible Party

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Sylvette Ayala-Pena

Scientific Official/Principal Investigator

Responsibility Role PRINCIPAL_INVESTIGATOR

Locations

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Fundacion Huntington Puerto Rico, Inc. - Huntington's disease Clinic

San Juan, , Puerto Rico

Site Status

Countries

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Puerto Rico

Other Identifiers

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2002027824

Identifier Type: -

Identifier Source: org_study_id

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