Cusatuzumab in Combination With Background Therapy for the Treatment of Participants With Acute Myeloid Leukemia

NCT ID: NCT04150887

Last Updated: 2025-04-17

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

ACTIVE_NOT_RECRUITING

Clinical Phase

PHASE1

Total Enrollment

61 participants

Study Classification

INTERVENTIONAL

Study Start Date

2019-12-23

Study Completion Date

2026-05-15

Brief Summary

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The purpose of the study is to characterize safety and tolerability of cusatuzumab in combination with various therapies used to treat acute myeloid leukemia (AML).

Detailed Description

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Conditions

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Leukemia, Myeloid, Acute

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Experimental: Cohort 2: Cusatuzumab + Venetoclax

Participants enrolled in this cohort will receive venetoclax ramp-up to 400 mg orally (as background therapy) starting on Cycle 1 Day 1 and followed by 400 mg daily dosing starting on Cycle 1 Day 4 plus cusatuzumab IV on Day 3 and Day 17 of each 28-day cycle. Cohort 2 will not be enrolled in the US.

Group Type EXPERIMENTAL

Cusatuzumab

Intervention Type DRUG

Cusatuzumab will be administered as a dose of 10mg/kg or 20mg/kg intravenously.

Venetoclax

Intervention Type DRUG

Venetoclax will be administered orally and the dose will ramp-up to 400 mg.

Cohort 3: Cusatuzumab + Venetoclax + Azacitidine (CVA)

Participants enrolled at US sites will receive cusatuzumab 10 mg/kg and potentially escalate to 20 mg/kg IV in combination with azacitidine 75 mg/m\^2 SC or IV plus venetoclax ramp-up to 400 mg orally (as background therapies). Participants enrolled from ex-US sites will receive cusatuzumab 20 mg/kg and potentially de-escalate to 10 mg/kg IV in combination with azacitidine 75 mg/m\^2 SC or IV plus venetoclax ramp-up to 400 mg orally (as background therapies).

Group Type EXPERIMENTAL

Cusatuzumab

Intervention Type DRUG

Cusatuzumab will be administered as a dose of 10mg/kg or 20mg/kg intravenously.

Azacitidine

Intervention Type DRUG

Azacitidine will be administered 75 mg/m\^2 subcutaneously or intravenously.

Venetoclax

Intervention Type DRUG

Venetoclax will be administered orally and the dose will ramp-up to 400 mg.

Interventions

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Cusatuzumab

Cusatuzumab will be administered as a dose of 10mg/kg or 20mg/kg intravenously.

Intervention Type DRUG

Azacitidine

Azacitidine will be administered 75 mg/m\^2 subcutaneously or intravenously.

Intervention Type DRUG

Venetoclax

Venetoclax will be administered orally and the dose will ramp-up to 400 mg.

Intervention Type DRUG

Other Intervention Names

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JNJ-74494550 ARGX-110 Vidaza Venclexta

Eligibility Criteria

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Inclusion Criteria

* Diagnosis of acute myeloid leukemia (AML) according to World Health Organization 2016 criteria . Participants with acute promyelocytic leukemia (APL) are not eligible
* Must be ineligible for intensive chemotherapy
* De novo or secondary AML
* Eastern Cooperative Oncology Group (ECOG) performance status of 0, 1, or 2
* Previously untreated AML except: emergency leukapheresis, hydroxyurea, and/or 1 dose 1-2 gram per meter square (g/m\^2) cytarabine during the Screening Phase to control hyperleukocytosis. These treatments must be discontinued greater than or equal to (\>=) 24 hours prior to start of study drug. Empiric all trans retinoic acid (ATRA) treatment for presumed acute promyelocytic leukemia (APL) is permitted but APL must be ruled out and ATRA must be discontinued \>=24 hours prior to the start of study drug
* Contraceptive use by men or women should be consistent with local regulations regarding the use of contraceptive methods for participants participating in clinical studies

Exclusion Criteria

* Leukemic involvement of the central nervous system
* Eligible for an allogeneic hematopoietic stem cell transplantation at study entry
* Received a live, attenuated vaccine within 4 weeks prior to initiation of study drug
* A history of human immunodeficiency virus (HIV) antibody positive or tests positive for HIV if tested at screening
* Known allergies, hypersensitivity, or intolerance to cusatuzumab, venetoclax, azacitidine, or their excipients (example: mannitol, an excipient of azacitidine)
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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argenx

INDUSTRY

Sponsor Role collaborator

Janssen Research & Development, LLC

INDUSTRY

Sponsor Role collaborator

OncoVerity, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Clayton Smith, MD

Role: STUDY_DIRECTOR

OncoVerity, Inc.

Locations

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City of Hope

Duarte, California, United States

Site Status

Norton Cancer Institute

Louisville, Kentucky, United States

Site Status

Barbara Ann Karmanos Cancer Institute

Detroit, Michigan, United States

Site Status

Roswell Park Cancer Institute

Buffalo, New York, United States

Site Status

Weill Cornell Medicine

New York, New York, United States

Site Status

Memorial Sloan Kettering Cancer Center

New York, New York, United States

Site Status

University of Rochester

Rochester, New York, United States

Site Status

University of Pittsburgh School of Medicine

Pittsburgh, Pennsylvania, United States

Site Status

The University of Texas MD Anderson Cancer Center

Houston, Texas, United States

Site Status

University of Vermont

Burlington, Vermont, United States

Site Status

Wisconsin Medical Center

Milwaukee, Wisconsin, United States

Site Status

Tom Baker Cancer Centre

Calgary, Alberta, Canada

Site Status

University of Alberta Hospital

Edmonton, Alberta, Canada

Site Status

University of Toronto

Toronto, Ontario, Canada

Site Status

McGill University Health Centre

Montreal, Quebec, Canada

Site Status

Universitaetsklinik Hamburg-Eppendorf

Hamburg, , Germany

Site Status

Universitaetsklinikum Leipzig

Leipzig, , Germany

Site Status

Klinikum der Universitaet Muenchen

München, , Germany

Site Status

Szpital Uniwersytecki w Krakowie

Krakow, , Poland

Site Status

Wojewodzkie Wielospecjalistyczne Centrum Onkologii i Traumatologii im. M. Kopernika w Lodzi

Lodz, , Poland

Site Status

Instytut Hematologii i Transfuzjologii

Warsaw, , Poland

Site Status

INSELSPITAL, Universitätsspital Bern

Bern, , Switzerland

Site Status

Kantonsspital St.Gallen

Sankt Gallen, , Switzerland

Site Status

Countries

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United States Canada Germany Poland Switzerland

References

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Pabst T, Papayannidis C, Demirkan F, Doronin V, Fogliatto LM, Guttke C, Gyan E, Hamad N, Herrera P, Hultberg A, Jacobs J, Johnson AJ, Langlois A, Ma X, Martinelli G, Arnan M, Muller R, Nottage K, Ofran Y, Ozcan M, Samoilova O, Tolbert JA, Trudel GC, Xiu L, Vey N, Wei AH. Cusatuzumab plus azacitidine in newly diagnosed acute myeloid leukaemia ineligible for intensive chemotherapy (CULMINATE): part one of a randomised, phase 2, dose optimisation study. Lancet Haematol. 2023 Nov;10(11):e902-e912. doi: 10.1016/S2352-3026(23)00207-7.

Reference Type DERIVED
PMID: 37914483 (View on PubMed)

Dewulf J, Flieswasser T, Delahaye T, Vangestel C, Miranda A, de Haard H, Jacobs J, Smits E, Van den Wyngaert T, Elvas F. Site-specific 68Ga-labeled nanobody for PET imaging of CD70 expression in preclinical tumor models. EJNMMI Radiopharm Chem. 2023 Apr 24;8(1):8. doi: 10.1186/s41181-023-00194-3.

Reference Type DERIVED
PMID: 37093350 (View on PubMed)

Other Identifiers

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2019-002808-41

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

ELEV20235

Identifier Type: OTHER

Identifier Source: secondary_id

74494550AML1003

Identifier Type: OTHER

Identifier Source: secondary_id

ELEV20235

Identifier Type: -

Identifier Source: org_study_id

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