Trial of CPX-351 in Adult Patients With First Relapse Acute Myeloid Leukemia (AML)

NCT ID: NCT00822094

Last Updated: 2017-11-24

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

126 participants

Study Classification

INTERVENTIONAL

Study Start Date

2009-02-28

Study Completion Date

2012-01-31

Brief Summary

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The study investigates if CPX-351 will be a) more effective than the standard intensive salvage AML treatment and b) more tolerable than the standard intensive salvage treatment regimens.

The study compares the investigational product CPX-351 vs the standard intensive salvage treatment for first relapse AML patients.

Detailed Description

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This study is a randomized, open-label, parallel-arm, fixed-dose, standard therapy controlled Phase IIB trial. Study enrollment duration is expected to be approximately 12-18 months. On entry, patients are randomized to receive either CPX-351 or intensive first salvage treatment.

Patients are stratified to balance the likelihood of obtaining a CR and the duration of CR between the two arms.

Conditions

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Acute Myeloid Leukemia

Keywords

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Acute Myeloid Leukemia Adult First Relapse AML Acute Myelogenous leukemia Leukemia, Myeloid Leukemia, Myeloid, Acute Acute myelocytic leukemia

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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CPX-351 (Arm A)

First induction: 100 units/m2 on Days 1, 3, and 5 by 90-minute IV infusion Second induction: 100 units/m2 on Days 1 and 3 by 90-minute IV infusion Consolidation(s): 100 units/m2 on Days 1 and 3 by 90-minute IV infusion

Group Type EXPERIMENTAL

CPX-351

Intervention Type DRUG

Salvage Therapy (Arm B)

First induction: Investigator's choice salvage therapy administered according to local practice Second induction: Investigator's choice salvage therapy administered according to local practice Consolidation(s): Investigator's choice consolidation therapy administered according to local practice

Group Type ACTIVE_COMPARATOR

Intensive Salvage Therapy

Intervention Type DRUG

Interventions

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CPX-351

Intervention Type DRUG

Intensive Salvage Therapy

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Ability to understand and voluntarily sign an informed consent form
* Age ≥18 and ≤65 years at the time of relapse
* Pathological confirmation of relapsed AML after initial CR of \>1 month duration
* Eastern Cooperative Oncology Group (ECOG) performance status 0- 2
* Able to adhere to the study visit schedule and other protocol requirements
* Laboratory values fulfilling the following:

* Serum creatinine \< 2.0 mg/dL
* Serum total bilirubin \< 2.0 mg/dL
* Serum alanine aminotransferase or aspartate aminotransferase \<3xULN Note: If elevated liver enzymes are related to disease; contact medical monitor to discuss.
* Cardiac ejection fraction \> 50% by echocardiography or MUGA scan
* All men and women must agree to practice effective contraception during the study period and for 3 months afterward if not otherwise documented to be infertile.

Exclusion Criteria

* Patients with active second malignancies are excluded. Patients with second malignancies in remission may be eligible if there is no clinical evidence of active disease, documented by imaging, with tumor marker studies, etc., at screening. Patients maintained on long-term non-chemotherapy treatment, e.g., hormonal therapy, are eligible. In all cases, the second malignancy and its non-chemotherapy treatment must not interfere with the investigators ability to assess the safety or efficacy of the study treatment
* Patients with acute promyelocytic leukemia \[t(15;17)\]
* Total lifetime anthracycline exposure exceeding the equivalent of 368 mg/m2 of daunorubicin (or equivalent) prior to start of study therapy
* Any serious medical condition, laboratory abnormality or psychiatric illness that would prevent obtaining informed consent
* Administration of any antineoplastic therapy within 4 weeks of therapy; intended to treat first relapse. In the event of rapidly proliferative disease use of hydroxyurea is permitted until 24 hours before the start of study treatment
* Clinical evidence of active CNS leukemia
* Patients with history of and/or current evidence of myocardial impairment (e.g. cardiomyopathy, ischemic heart disease, significant valvular dysfunction, hypertensive heart disease, and congestive heart failure) resulting in New York Heart Association Class III or IV staging
* Active and uncontrolled infection. Patients with a bacterial infection receiving treatment with antibiotics may be entered into the study if they are afebrile and hemodynamically stable for \>72 hrs.
* Current evidence of invasive fungal infection (blood or tissue culture); active hepatitis C infection or known HIV infection
* Hypersensitivity to cytarabine, daunorubicin or liposomal products
* History of Wilson's disease or other copper-related disorder
* Patients with a history of severe toxicity related to receiving conventional dose cytarabine in first line treatment (approximately 100mg/m2/d for \<7 days) are excluded. Patients who experienced unacceptable toxicities while receiving high dose cytarabine (approximately 3000mg/m2 for 6 doses) will not be treated again with the same regimen, but could be randomized to treatment with conventional dose cytarabine regimens where the risk of major toxicity is less.
* Woman who are pregnant or breast feeding
Minimum Eligible Age

18 Years

Maximum Eligible Age

65 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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The Leukemia and Lymphoma Society

OTHER

Sponsor Role collaborator

Jazz Pharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Jonathan Kolitz, MD

Role: PRINCIPAL_INVESTIGATOR

North Shore University Hospital

Locations

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Arizona Cancer Center

Tucson, Arizona, United States

Site Status

UCLA

Los Angeles, California, United States

Site Status

Cedars Sinai Medical Center

Los Angeles, California, United States

Site Status

UC Davis Cancer Center

Sacramento, California, United States

Site Status

University of Colorado Cancer Center

Aurora, Colorado, United States

Site Status

Northwestern University Robert H. Lurie Comprehensive Cancer Center

Chicago, Illinois, United States

Site Status

Rush University Medical Center

Chicago, Illinois, United States

Site Status

University of Chicago Medical Center Section of Hematology/Oncology

Chicago, Illinois, United States

Site Status

St. Francis Cancer Center

Beech Grove, Indiana, United States

Site Status

University of Louisville Brown Cancer Center

Louisville, Kentucky, United States

Site Status

Maine General Medical Center Harold Alfond Center for Cancer Care

Waterville, Maine, United States

Site Status

Johns Hopkins University

Baltimore, Maryland, United States

Site Status

St. Louis University Medical Center

St Louis, Missouri, United States

Site Status

The Cancer Center, Hackensack University Medical Center

Hackensack, New Jersey, United States

Site Status

North Shore LIJ Center for Advanced Medicine Monter Cancer Center

Lake Success, New York, United States

Site Status

Weil Cornell Medical Center

New York, New York, United States

Site Status

New York Medical College

New York, New York, United States

Site Status

Montefiore Medical Center

The Bronx, New York, United States

Site Status

Blumenthal Cancer Center/Mecklenburg Medical Group

Charlotte, North Carolina, United States

Site Status

Duke Comprehensive Cancer Center

Durham, North Carolina, United States

Site Status

Jewish Hospital of Cincinatti

Cincinnati, Ohio, United States

Site Status

Oregon Health and Science University

Portland, Oregon, United States

Site Status

Oncology and Hematology at Lehigh Valley

Bethlehem, Pennsylvania, United States

Site Status

Western Pennsylvania Hospital

Pittsburgh, Pennsylvania, United States

Site Status

UTMB Comprehensive Cancer Center

Galveston, Texas, United States

Site Status

M.D. Anderson Cancer Center

Houston, Texas, United States

Site Status

Joe Arrington Cancer Center

Lubbock, Texas, United States

Site Status

Texas Tech University Health Sciences Center

Lubbock, Texas, United States

Site Status

Cancer Therapy and Research Center at The University of TX Health Science Center

San Antonio, Texas, United States

Site Status

Intermountain LDS Hospital

Salt Lake City, Utah, United States

Site Status

Medical College of Wisconsin

Milwaukee, Wisconsin, United States

Site Status

Vancouver General Hospital/ British Columbia Cancer Agency

Vancouver, British Columbia, Canada

Site Status

Cancer Care Manitoba

Winnipeg, Manitoba, Canada

Site Status

Service des Maladies du Sang CHU de Lille, Hopital Claude Huriez

Lille, , France

Site Status

Service des Maladies du Sang Hopital Haut-Leveque

Pessac, , France

Site Status

Service d'Hématologie CHU Toulouse-Hôpital Purpan

Toulouse, , France

Site Status

Service d'Hématologie et Médecine Interne CHU de Nancy-Hôpital de Brabois

Vandœuvre-lès-Nancy, , France

Site Status

Klinika Hematologii i Transplantologii

Gdansk, , Poland

Site Status

Wojewódzki Szpital Specjalistyczny im. M. Kopernika

Lodz, , Poland

Site Status

Oddział Hematologii

Opole, , Poland

Site Status

Instytut Hematologii i Transfuzjologii

Warsaw, , Poland

Site Status

Akademia Medyczna we Wroclawlu

Wroclaw, , Poland

Site Status

Countries

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United States Canada France Poland

Other Identifiers

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CLTR0308-205

Identifier Type: -

Identifier Source: org_study_id