AB8939 in Patients With Relapsed/Refractory Acute Myeloid Leukemia

NCT ID: NCT05211570

Last Updated: 2025-10-02

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE1/PHASE2

Total Enrollment

78 participants

Study Classification

INTERVENTIONAL

Study Start Date

2022-06-01

Study Completion Date

2026-12-31

Brief Summary

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The primary objective is to define the safety and tolerability of AB8939 in patients with AML by determining the dose-limiting toxicities, the maximum tolerated dose, and the recommended dose for dose expansion study.

Detailed Description

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This is a Phase 1/2, open-label, multi-center, non-randomized, 2-part study in patients with refractory and relapsed AML and refractory myelodysplastic syndrome.

Study AB18001 has a multi-stage design. The first part is a dose escalation study that aims to determine the safety, tolerability and pharmacokinetic profiles of consecutive daily intravenous administration of AB8939 in patients with refractory or relapsed AML or patients with refractory myelodysplastic syndrome, and to determine the recommended dose for the second-stage dose expansion study. This dose expansion study aims to determine the schedule for a Phase 2 trial in patients with relapsed/refractory AML and to also provide an early efficacy assessment of AB8939.

Conditions

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Acute Myeloid Leukemia Refractory Acute Myeloid Leukemia, in Relapse Myelodysplastic Syndrome Acute Myeloid Leukemia

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

SEQUENTIAL

Open-label, multi-centre, non-randomized, 2-part study
Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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AB8939

AB8939 administered as a single agent

Group Type EXPERIMENTAL

AB8939

Intervention Type DRUG

Intravenous injection (from an initial dose of 0.9 mg/m²)

AB8939 plus Venetoclax

AB8939 administered in combination with venetoclax

Group Type EXPERIMENTAL

AB8939

Intervention Type DRUG

Intravenous injection (from an initial dose of 0.9 mg/m²)

Venetoclax

Intervention Type DRUG

the recommended starting dose for AML indication is 100 mg. Dose escalating regimen as per SmPC.

Interventions

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AB8939

Intravenous injection (from an initial dose of 0.9 mg/m²)

Intervention Type DRUG

Venetoclax

the recommended starting dose for AML indication is 100 mg. Dose escalating regimen as per SmPC.

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Patients with documented diagnosis of acute myeloid leukemia (AML) based on the last version of the World Health Organization classification and eligible to second or third line of treatment.
* Patients with documented diagnosis of refractory melyodisplastic syndrome in second or third line of treatment, and with high risk at prognosis based on the IPSS-R scoring system.
* ECOG performance status ≤ 1
* Patients are able to understand, sign, and date the written informed consent form at screening visit prior to any protocol-specific procedures
* Patients are able and willing to comply with study procedures as per protocol, including bone marrow biopsies


* Patients with documented diagnosis of acute myeloid leukemia (AML) based on the last version of the World Health Organization classification and eligible to second or third line of treatment.
* ECOG performance status ≤ 2
* Patients are able to understand, sign, and date the written informed consent form at screening visit prior to any protocol-specific procedures
* Patients are able and willing to comply with study procedures as per protocol, including bone marrow biopsies

Exclusion Criteria

* Patients eligible to a standard of care
* Patients eligible to hematopoietic stem cell transplantation (HSCT) at the time of inclusion
* Patients diagnosed with acute promyelocytic leukemia (M3)
* Patients with clinically active CNS leukemia
* Patients with HSCT within 100 days prior to the first administration of AB8939
* Women who are lactating/breastfeeding or who plan to breastfeed while on study
* Women with a positive pregnancy test


EXPANSION COHORT STUDY


* Patients eligible to a standard of care
* Patients eligible to hematopoietic stem cell transplantation (HSCT) at the time of inclusion
* Patients diagnosed with acute promyelocytic leukemia (M3)
* Patients with clinically active CNS leukemia
* Patients with HSCT within 100 days prior to the first administration of AB8939
* Women who are lactating/breastfeeding or who plan to breastfeed while on study
* Women with a positive pregnancy test
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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AB Science

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Norbert Vey, MD

Role: PRINCIPAL_INVESTIGATOR

Institut Paoli Calmettes, Marseille, France

Nicholas Short, MD

Role: PRINCIPAL_INVESTIGATOR

MD Anderson Cancer Center, Houston, Texas

Locations

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MD Anderson Cancer Center

Houston, Texas, United States

Site Status NOT_YET_RECRUITING

Institut Paoli Calmettes

Marseille, , France

Site Status NOT_YET_RECRUITING

National and Kapodistrian University of Athens NKUA · Department of Hematology and Bone marrow Transplantation Unit

Athens, , Greece

Site Status RECRUITING

General University Hospital of Alicantet (Hospital General Universitario Dr. Balmis de Alicante)

Alicante, , Spain

Site Status RECRUITING

Hospital San Pedro de Alcantara

Cáceres, , Spain

Site Status RECRUITING

Hospital Universitario 12 de Octubre

Madrid, , Spain

Site Status RECRUITING

Hospital Universitario Quirónsalud

Madrid, , Spain

Site Status RECRUITING

MD Anderson Cancer Center Madrid

Madrid, , Spain

Site Status RECRUITING

Clínica Universidad de Navarra

Pamplona, , Spain

Site Status RECRUITING

Virgen del Rocío University Hospital (Hospital Universitario Virgen del Rocío)

Seville, , Spain

Site Status RECRUITING

Countries

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United States France Greece Spain

Central Contacts

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Clinical Study Coordinator

Role: CONTACT

+33(0)147200014

References

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Goubard A, Humbert M, Mansfield C, Hermine O, Dubreuil P, et al. In Vivo Assessment of the Next Generation Microtubule-Destabilizing Agent AB8939 in Patient-derived Xenograft Models of Acute Myeloid Leukemia. Blood (2019) 134 (Supplement_1): 5142. doi.org/10.1182/blood-2019-127143

Reference Type BACKGROUND

Goubard A, Humbert M, Mansfield C, Hermine O, Dubreuil P, et al. AB8939, a Microtubule-Destabilizing Agent with Potential to Overcome Multidrug Resistance, is Active Across the Range (M0-M7) of Acute Myeloid Leukemia Subtypes. Blood (2019) 134 (Supplement_1): 5154. doi.org/10.1182/blood-2019-127021

Reference Type BACKGROUND

Humbert M, Goubard A, Mansfield C, Hermine O, Dubreuil P, et al. Anticancer Activity of a Highly Potent Small Molecule Tubulin Polymerization Inhibitor, AB8939. Blood (2019) 134 (Supplement_1): 2075. doi.org/10.1182/blood-2019-122540

Reference Type BACKGROUND

Other Identifiers

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2020-005122-28

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

AB18001

Identifier Type: -

Identifier Source: org_study_id

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