A Study of the Effectiveness of Venetoclax in Combination With Azacitidine or Decitabine in an Outpatient Setting in Patients With Acute Myeloid Leukemia (AML) Ineligible for Intensive Chemotherapy

NCT ID: NCT03941964

Last Updated: 2023-03-20

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

60 participants

Study Classification

INTERVENTIONAL

Study Start Date

2019-08-15

Study Completion Date

2022-03-14

Brief Summary

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A study evaluating the effectiveness and safety of venetoclax, in combination with azacitidine or decitabine, in an outpatient setting for treatment-naïve participants with AML who are ineligible for intensive chemotherapy.

Detailed Description

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Conditions

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Acute Myeloid Leukemia (AML) Cancer

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Venetoclax 400 mg + azacitidine 75 mg

Participants received venetoclax orally daily for 28-day cycles, for a maximum of 6 cycles, beginning on Cycle 1 Day 1. The venetoclax dosing ramp-up schedule was 100 mg on Cycle 1 Day 1, 200 mg on Cycle 1 Day 2, and 400 mg on Cycle 1 Days 3 -28 and 400 mg daily for each 28-day cycle thereafter. Azacitidine (75 mg/m\^2) was administered subcutaneously or intravenously per investigator's choice and institutional practice for 7 days beginning on Day 1 of each 28-day cycle.

Group Type EXPERIMENTAL

Venetoclax

Intervention Type DRUG

Venetoclax tablets were to be taken orally once daily with a meal and water in the morning at approximately the same time each day. Tablets were to be swallowed whole and not chewed, crushed, or broken prior to swallowing. On the days that the participant received either azacitidine or decitabine, venetoclax was dosed in clinic and administered prior to these agents.

Azacitidine

Intervention Type DRUG

The azacitidine infusion was prepared and administered per the package insert and given either subcutaneously or intravenously, per institutional practice.

Venetoclax 400 mg + decitabine 20 mg

Participants received venetoclax orally daily for 28-day cycles, for a maximum of 6 cycles, beginning on Cycle 1 Day 1. The venetoclax dosing ramp-up schedule was 100 mg on Cycle 1 Day 1, 200 mg on Cycle 1 Day 2, and 400 mg on Cycle 1 Days 3 -28 and 400 mg daily for each 28-day cycle thereafter. Decitabine (20 mg/m\^2) was administered intravenously per investigator's choice and institutional practice for 5 days beginning on Day 1 of each cycle.

Group Type EXPERIMENTAL

Venetoclax

Intervention Type DRUG

Venetoclax tablets were to be taken orally once daily with a meal and water in the morning at approximately the same time each day. Tablets were to be swallowed whole and not chewed, crushed, or broken prior to swallowing. On the days that the participant received either azacitidine or decitabine, venetoclax was dosed in clinic and administered prior to these agents.

Decitabine

Intervention Type DRUG

The decitabine infusion was prepared and administered per the package insert and given intravenously, per institutional practice.

Interventions

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Venetoclax

Venetoclax tablets were to be taken orally once daily with a meal and water in the morning at approximately the same time each day. Tablets were to be swallowed whole and not chewed, crushed, or broken prior to swallowing. On the days that the participant received either azacitidine or decitabine, venetoclax was dosed in clinic and administered prior to these agents.

Intervention Type DRUG

Azacitidine

The azacitidine infusion was prepared and administered per the package insert and given either subcutaneously or intravenously, per institutional practice.

Intervention Type DRUG

Decitabine

The decitabine infusion was prepared and administered per the package insert and given intravenously, per institutional practice.

Intervention Type DRUG

Other Intervention Names

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ABT-199 VENCLEXTA VENCLYXTO Vidaza Dacogen

Eligibility Criteria

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Inclusion Criteria

* Participant has confirmation of acute myeloid leukemia (AML) by World Health Organization (WHO) criteria
* Participant is deemed by the investigator to be an appropriate candidate for outpatient ramp-up of venetoclax
* Participant is not eligible to receive treatment with standard cytarabine and anthracycline induction regimens
* Participant has not received prior treatment for AML (treatment naïve) with the exception of hydroxyurea
* Participant has no evidence of spontaneous tumor lysis syndrome (TLS) at Screening
* Participant can have progressed from myelodysplastic syndrome (MDS) or be considered to have secondary AML and could have been treated with growth factors or other agents with the exception of hypomethylating agents
* Participant has adequate kidney, liver, and hematology laboratory values as detailed in the protocol
* Has an Eastern Cooperative Oncology Group (ECOG) Performance status of 0 to 3

Exclusion Criteria

Has a history of the following conditions:

* Acute promyelocytic leukemia
* Known active central nervous system involvement with AML
* Positive for HIV (HIV testing is not required)
* Positive for hepatitis B or C infection with the exception of those with an undetectable viral load within 3 months
* Cardiovascular disability status of New York Heart Association Class \> 2
* Chronic respiratory disease that requires continuous oxygen or any other medical condition that in the opinion of the investigator would adversely affect his/her participating in this study
* Malabsorption syndrome or other condition that precludes enteral route of administration

Has a history of other malignancies within 2 years prior to study entry, with the exception of:

* Adequately treated in situ carcinoma of the cervix uteri or carcinoma in situ of breast
* Basal cell carcinoma of the skin or localized squamous cell carcinoma of the skin
* Previous malignancy confined and surgically resected (or treated with other modalities) with curative intent
Minimum Eligible Age

12 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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AbbVie

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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ABBVIE INC.

Role: STUDY_DIRECTOR

AbbVie

Locations

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Texas Oncology - Austin Midtown /ID# 212780

Austin, Texas, United States

Site Status

Texas Oncology - Medical City Dallas /ID# 211503

Dallas, Texas, United States

Site Status

Texas Transplant Institute /ID# 213311

San Antonio, Texas, United States

Site Status

Texas Oncology - San Antonio Medical Center /ID# 211510

San Antonio, Texas, United States

Site Status

Texas Oncology - Northeast Texas /ID# 213908

Tyler, Texas, United States

Site Status

Arizona Oncology Associates, PC-HOPE /ID# 211509

Tempe, Arizona, United States

Site Status

Colorado Blood Cancer Institute /ID# 212800

Denver, Colorado, United States

Site Status

Rocky Mountain Cancer Centers /ID# 211508

Lone Tree, Colorado, United States

Site Status

Fort Wayne Medical Oncology /ID# 223523

Fort Wayne, Indiana, United States

Site Status

Minnesota Oncology Hematology, PA /ID# 212837

Minneapolis, Minnesota, United States

Site Status

Oncology Hematology Care, Inc. /ID# 212779

Cincinnati, Ohio, United States

Site Status

Willamette Valley Cancer Institute and Research Center /ID# 211504

Eugene, Oregon, United States

Site Status

Charleston Oncology, P.A. /ID# 211471

Charleston, South Carolina, United States

Site Status

Prisma Health Cancer Inst - Eastside /ID# 211466

Greenville, South Carolina, United States

Site Status

Tennessee Oncology - Chattanooga / McCallie /ID# 212717

Chattanooga, Tennessee, United States

Site Status

Tennessee Oncology-Nashville Centennial /ID# 210944

Nashville, Tennessee, United States

Site Status

Countries

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United States

References

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Manda S, Anz BM 3rd, Benton C, Broun ER, Yimer HA, Renshaw JS, Geils G Jr, Berdeja J, Cruz J, Melear JM, Fanning S, Fletcher L, Li Y, Duan Y, Werner ME, Potluri J, Pai MV, Donnellan WB. A phase 3b study of venetoclax and azacitidine or decitabine in an outpatient setting in patients with acute myeloid leukemia. Hematol Oncol. 2024 May;42(3):e3274. doi: 10.1002/hon.3274.

Reference Type DERIVED
PMID: 38711253 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Related Links

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Other Identifiers

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M19-072

Identifier Type: -

Identifier Source: org_study_id

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