Study on the Use of Cinacalcet in Phosphocalcic Context.

NCT ID: NCT04126954

Last Updated: 2019-10-15

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

UNKNOWN

Total Enrollment

25 participants

Study Classification

OBSERVATIONAL

Study Start Date

2020-01-31

Study Completion Date

2023-12-31

Brief Summary

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Currently, the indications used for MA (Marketing Authorization) Cinacalcet in France are hyperparathyroidism (hyperPTH) in adults, whether primary (for patients in whom parathyroidectomy is theoretically indicated but in whom it is contraindicated or not is not clinically appropriate) or secondary to a chronic kidney disease, and parathyroid carcinomas.

In pediatric patients, data on its use are restricted due to its recent marketing authorization (2017) and limited to dialysis patients suffering from secondary hyperPTH.

Nevertheless, some patients with phosphocalcic pathologies without renal insufficiency must be treated off-label by cinacalcet in the presence of severe hyperPTH, without any other chronic treatment available to date.

The objective of this study is therefore to evaluate the use in France of cinacalcet in phosphocalcic pathologies without renal insufficiency, in order to obtain efficacy and safety data in order to improve our knowledge on the management of these orphan diseases.

Detailed Description

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Conditions

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Hyperparathyroidism, Secondary Hyperparathyroidism, Primary

Study Design

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Observational Model Type

COHORT

Study Time Perspective

RETROSPECTIVE

Study Groups

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Cinacalcet

Patients with primary or secondary hyperPTH resulting from phosphocalcic pathology treated by cinacalcet

Serum PTH concentrations results

Intervention Type OTHER

To compare serum PTH concentrations results in patients with primary or secondary hyperPTH resulting from phosphocalcic pathology before and three months after initiation of cinacalcet therapy.

Interventions

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Serum PTH concentrations results

To compare serum PTH concentrations results in patients with primary or secondary hyperPTH resulting from phosphocalcic pathology before and three months after initiation of cinacalcet therapy.

Intervention Type OTHER

Eligibility Criteria

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Inclusion Criteria

* Patients with phosphocalcic pathology without end-stage renal failure
* Patients followed in one of the hospitals of the centers of reference and competence of the diseases of the metabolism of calcium and phosphate
* For children under 18: patient and parent (s) / parent having been informed of the study and having expressed their on-opposition
* For adults: patient / legal guardian of the patient under guardianship having been informed of the study and expressing his or her non opposition

Exclusion Criteria

* Patient suffering from parathyroid cancer,
* Patient suffering from primary hyperPTH in whom parathyroidectomy would theoretically be indicated but contraindicated or clinically inappropriate,
* Patient suffering from hyperPTH secondary to end-stage renal failure
* No social security support
Maximum Eligible Age

99 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Hospices Civils de Lyon

OTHER

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Justine BACCHETTA, MD

Role: PRINCIPAL_INVESTIGATOR

Service de Néphrologie, Rhumatologie et Dermatologie Pédiatriques

Locations

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Endocrinologie Diabète et Maladies Métaboliques - Hôpital Gabriel Montpied

Clermont-Ferrand, , France

Site Status

Service de Néphrologie Pédiatrique -Hôpital Jeanne de Flandre

Lille, , France

Site Status

Service d'Endocrinologie Pédiatrique - Hôpital de la mère et de l'Enfant

Limoges, , France

Site Status

Pole Femme Mère Enfant - Pédiatrie spécialisée - Centre Hospitalier Universitaire

Montpellier, , France

Site Status

Service de Néphrologie pédiatrique - Clinique Médicale Pédiatrique

Nantes, , France

Site Status

Service d'endocrinologie et Diabétologie Pédiatrique-Hôpital Robert Debré

Paris, , France

Site Status

Service de Diabétologie et endocrinologie pédiatriques - Centre Hospitalier Universitaire

Reims, , France

Site Status

Pôle Néphrologie-Urologie-Diabétologie-Endocrinologie

Strasbourg, , France

Site Status

Service d'Endocrinologie, Maladies Osseuses, Gynécologie, Génétique

Toulouse, , France

Site Status

Unité Endocrinologie, Nutrition, Diabétologie -Hôpital Bretonneau

Tours, , France

Site Status

Countries

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France

Central Contacts

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Justine BACCHETTA, MD

Role: CONTACT

4 27 85 61 30 ext. +33

Sacha FLAMMIER, PHD

Role: CONTACT

4 27 85 66 69 ext. +33

Facility Contacts

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Igor TAUVERON, PR

Role: primary

4 73 75 15 33 ext. +33

Robert NOVO, MD

Role: primary

03.20.44.46.95 ext. +33

Anne LIENHARDT-ROUSSIE, MD

Role: primary

5.55.05.63.58 ext. +33

Cyril AMOUROUX, MD

Role: primary

4 67 33 81 12 ext. +33

Emma ALLAIN-LAUNAY, MD

Role: primary

240083660 ext. +33

Laeticia MARTINERIE, MD

Role: primary

1.40.03.53.03 ext. +33

Pierre-François SOUCHON, MD

Role: primary

Nathalie JEANDIDIER, PR

Role: primary

3 88 11 66 03 ext. +33

Jean Pierre SALLES, MD

Role: primary

534558555 ext. +33

Lise CRINIERE, MD

Role: primary

Other Identifiers

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2019_CALCI-CINA

Identifier Type: -

Identifier Source: org_study_id

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