Efficacy, Safety, and Tolerability of Valbenazine for the Treatment of Chorea Associated With Huntington Disease

NCT ID: NCT04102579

Last Updated: 2023-10-11

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

128 participants

Study Classification

INTERVENTIONAL

Study Start Date

2019-11-13

Study Completion Date

2021-10-26

Brief Summary

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This is a Phase 3, randomized, double-blind, placebo-controlled study to evaluate the efficacy, safety, and tolerability of valbenazine to treat chorea in participants with Huntington disease.

Detailed Description

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Conditions

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Chorea, Huntington

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Valbenazine

Capsule, administered orally once daily for 12 weeks.

Group Type EXPERIMENTAL

Valbenazine

Intervention Type DRUG

vesicular monoamine transporter 2 (VMAT2) inhibitor

Placebo

Capsule, administered orally once daily for 12 weeks.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

non-active dosage form

Interventions

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Valbenazine

vesicular monoamine transporter 2 (VMAT2) inhibitor

Intervention Type DRUG

Placebo

non-active dosage form

Intervention Type DRUG

Other Intervention Names

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NBI-98854

Eligibility Criteria

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Inclusion Criteria

1. Have a clinical diagnosis of Huntington Disease (HD) with chorea
2. Be able to walk, with or without the assistance of a person or device
3. Participants of childbearing potential who do not practice total abstinence must agree to use hormonal or two forms of nonhormonal contraception (dual contraception) consistently while participating in the study until 30 days (females) or 90 days (males) after the last dose of the study drug
4. Be able to read and understand English

Exclusion Criteria

1. Have a history of previously established therapy with a VMAT2 inhibitor, in the judgement of the investigator
2. Have difficulty swallowing
3. Are currently pregnant or breastfeeding
4. Have a known history of long QT syndrome, cardiac tachyarrhythmia, left bundle-branch block, atrioventricular block, uncontrolled bradyarrhythmia, or heart failure
5. Have an unstable or serious medical or psychiatric illness
6. Have a significant risk of suicidal behavior
7. Have a history of substance dependence or substance (drug) or alcohol abuse, within 1 year of screening
8. If taking antidepressant therapy, be on a stable regimen
9. Have received gene therapy at any time
10. Have received an investigational drug in a clinical study within 30 days of the baseline visit or plan to use such investigational drug (other than valbenazine) during the study
11. Have had a blood loss ≥550 milliliters (mL) or donated blood within 30 days before the baseline visit
12. Had a medically significant illness within 30 days before baseline, or any history of neuroleptic malignant syndrome
Minimum Eligible Age

18 Years

Maximum Eligible Age

75 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Huntington Study Group

NETWORK

Sponsor Role collaborator

Neurocrine Biosciences

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Chief Medical Officer

Role: STUDY_DIRECTOR

Chief Medical Officer

Locations

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Neurocrine Clinical Site

Toronto, Ontario, Canada

Site Status

Neurocrine Clinical Site

Toronto, Ontario, Canada

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Neurocrine Clinical Site

Birmingham, Alabama, United States

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Neurocrine Clinical Site

Little Rock, Arkansas, United States

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Neurocrine Clinical Site

La Jolla, California, United States

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Neurocrine Clinical Site

Sacramento, California, United States

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Neurocrine Clinical Site

Aurora, Colorado, United States

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Neurocrine Clinical Site

Englewood, Colorado, United States

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Neurocrine Clinical Site

Washington D.C., District of Columbia, United States

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Neurocrine Clinical Site

Gainesville, Florida, United States

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Neurocrine Clinical Site

Miami, Florida, United States

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Neurocrine Clinical Site

Atlanta, Georgia, United States

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Neurocrine Clinical Site

Chicago, Illinois, United States

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Neurocrine Clinical Site

Chicago, Illinois, United States

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Neurocrine Clinical Site

Indianapolis, Indiana, United States

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Neurocrine Clinical Site

Iowa City, Iowa, United States

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Neurocrine Clinical Site

Kansas City, Kansas, United States

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Neurocrine Clinical Site

Wichita, Kansas, United States

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Neurocrine Clinical Site

Louisville, Kentucky, United States

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Neurocrine Clinical Site

New Orleans, Louisiana, United States

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Neurocrine Clinical Site

Boston, Massachusetts, United States

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Neurocrine Clinical Site

Boston, Massachusetts, United States

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Neurocrine Clinical Site

Charlestown, Massachusetts, United States

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Neurocrine Clinical Site

Ann Arbor, Michigan, United States

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Neurocrine Clinical Site

West Bloomfield, Michigan, United States

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Neurocrine Clinical Site

Omaha, Nebraska, United States

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Neurocrine Clinical Site

Rochester, New York, United States

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Neurocrine Clinical Site

Williamsville, New York, United States

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Neurocrine Clinical Site

Durham, North Carolina, United States

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Neurocrine Clinical Site

Fargo, North Dakota, United States

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Neurocrine Clinical Site

Cleveland, Ohio, United States

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Neurocrine Clinical Site

Columbus, Ohio, United States

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Neurocrine Clinical Site

Toledo, Ohio, United States

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Neurocrine Clinical Site

Pittsburgh, Pennsylvania, United States

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Neurocrine Clinical Site

Charleston, South Carolina, United States

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Neurocrine Clinical Site

Columbia, South Carolina, United States

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Neurocrine Clinical Site

Greenville, South Carolina, United States

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Neurocrine Clinical Site

Nashville, Tennessee, United States

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Neurocrine Clinical Site

Houston, Texas, United States

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Neurocrine Clinical Site

Salt Lake City, Utah, United States

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Neurocrine Clinical Site

Burlington, Vermont, United States

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Neurocrine Clinical Site

Charlottesville, Virginia, United States

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Neurocrine Clinical Site

Seattle, Washington, United States

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Neurocrine Clinical Site

Spokane, Washington, United States

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Neurocrine Clinical Site

Vancouver, British Columbia, Canada

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Neurocrine Clinical Site

Ottawa, Ontario, Canada

Site Status

Countries

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United States Canada

References

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Furr Stimming E, Claassen DO, Kayson E, Goldstein J, Mehanna R, Zhang H, Liang GS, Haubenberger D; Huntington Study Group KINECT-HD Collaborators. Safety and efficacy of valbenazine for the treatment of chorea associated with Huntington's disease (KINECT-HD): a phase 3, randomised, double-blind, placebo-controlled trial. Lancet Neurol. 2023 Jun;22(6):494-504. doi: 10.1016/S1474-4422(23)00127-8.

Reference Type RESULT
PMID: 37210099 (View on PubMed)

Rodrigues FB, Wild EJ. Huntington's Disease Clinical Trials Corner: April 2020. J Huntingtons Dis. 2020;9(2):185-197. doi: 10.3233/JHD-200002.

Reference Type DERIVED
PMID: 32250312 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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NBI-98854-HD3005

Identifier Type: -

Identifier Source: org_study_id

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