Efficacy and Safety on SOM3355 in Huntington's Disease Chorea

NCT ID: NCT05475483

Last Updated: 2025-08-28

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

139 participants

Study Classification

INTERVENTIONAL

Study Start Date

2022-08-02

Study Completion Date

2024-07-15

Brief Summary

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Phase IIb, randomized, double-blind, placebo-controlled study in parallel groups assessing the efficacy and safety of two doses of SOM3355 in patients suffering from Huntington's Disease with choreic movements.

Detailed Description

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Conditions

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Huntington Chorea

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Placebo

Placebo capsules were administered twice daily (BID) for at least 9 weeks at maintenance dose.

Group Type PLACEBO_COMPARATOR

Placebo capsules

Intervention Type DRUG

Treatment was blind for the whole duration of the study.

SOM3355 400 mg/day

SOM3355 200 mg capsules were administered twice daily (BID) for at least 9 weeks at maintenance dose.

Group Type EXPERIMENTAL

SOM3355 200 mg capsules

Intervention Type DRUG

Treatment was blind for the whole duration of the study.

SOM3355 600 mg/day

SOM3355 300 mg capsules were administered twice daily (BID) for at least 8 weeks at maintenance dose.

Group Type EXPERIMENTAL

SOM3355 300 mg capsules

Intervention Type DRUG

Treatment was blind for the whole duration of the study.

Interventions

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Placebo capsules

Treatment was blind for the whole duration of the study.

Intervention Type DRUG

SOM3355 200 mg capsules

Treatment was blind for the whole duration of the study.

Intervention Type DRUG

SOM3355 300 mg capsules

Treatment was blind for the whole duration of the study.

Intervention Type DRUG

Other Intervention Names

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Bevantolol hydrochloride Bevantolol hydrochloride

Eligibility Criteria

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Inclusion Criteria

Inclusion Criteria: Males or females ≥21 years old, a diagnosis of Huntington's Disease determined by a movement disorders expert and confirmed by a number of HTT gene CAG repeats ≥36, a UHDRS® Total maximal chorea (TMC) score ≥10, and a UHDRS® Total Functional Capacity (TFC) ≥7.

Exclusion Criteria: Onset of HD symptoms prior to age of 21 years (juvenile forms of HD), HD patients presenting rigid akinesia, and use of other VMAT2 inhibitors such as tetrabenazine, deutetrabenazine, or valbenazine, or other antichoreic treatment such as any neuroleptic, or amantadine, memantine, riluzole.
Minimum Eligible Age

21 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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SOM Innovation Biotech SA

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Centre Hospitalier Universitaire Angers

Angers, , France

Site Status

CHU Hôpital Henri Mondor (APHP)

Créteil, , France

Site Status

Hôpital Roger Salengro - CHU Lille

Lille, , France

Site Status

Hopital de Hautepierre

Strasbourg, , France

Site Status

Hôpital Purpan - CHU Toulouse

Toulouse, , France

Site Status

Charité - Universitätsmedizin Berlin

Berlin, , Germany

Site Status

George Huntington Institut

Münster, , Germany

Site Status

Kbo-Isar-Amper-Klinikum Taufkirchen

Taufkirchen, , Germany

Site Status

Hospital of University of Ulm

Ulm, , Germany

Site Status

IRCCS Istituto delle Scienze Neurologiche di Bologna

Bologna, , Italy

Site Status

Azienda Ospedaliera Universitaria Federico II

Napoli, , Italy

Site Status

IRCCS Casa Sollievo della Sofferenza

Roma, , Italy

Site Status

Sant'Andrea University Hospital

Roma, , Italy

Site Status

Krakowska Akademia Neurologii Sp. z o.o.

Krakow, , Poland

Site Status

Indywidualna Praktyka Lekarska Daniel Zielonka

Poznan, , Poland

Site Status

Hospital de la Santa Creu i Sant Pau

Barcelona, , Spain

Site Status

Hospital Universitario de Cruces

Bilbao, , Spain

Site Status

Hospital Universitario de Burgos

Burgos, , Spain

Site Status

Hospital Ramón y Cajal

Madrid, , Spain

Site Status

Universitaetsspital Bern - Inselspital

Bern, , Switzerland

Site Status

Cambridge University Hospitals NHS Foundation Trust Addenbrooke's Hospital

Cambridge, , United Kingdom

Site Status

NIHR Wellcome Trust Manchester Clinical Research Facility

Manchester, , United Kingdom

Site Status

Oxford University Hospitals NHS Foundation Trust

Oxford, , United Kingdom

Site Status

Countries

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France Germany Italy Poland Spain Switzerland United Kingdom

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Related Links

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http://www.sombiotech.com

SOM Biotech website

Other Identifiers

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2021-003453-28

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

SOMCT03

Identifier Type: -

Identifier Source: org_study_id

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