Randomized, Placebo Controlled Study Of The Efficacy And Safety Of PF-02545920 In Subjects With Huntington's Disease

NCT ID: NCT02197130

Last Updated: 2017-11-17

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

272 participants

Study Classification

INTERVENTIONAL

Study Start Date

2014-09-30

Study Completion Date

2016-10-31

Brief Summary

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This study is a 26 week, randomized, parallel group, double blind comparison of PF-02545920 5 mg, PF-02545920 20 mg, and placebo dosed BID in the treatment of motor impairment of subjects with Huntington's Disease. A total of approximately 260 subjects are planned to be randomized in the study. Primary endpoint is the change from baseline in the Total Motor Score (TMS) assessment of the Unified Huntington Disease Rating Scale (UHDRS) after 26 weeks of treatment. secondary endpoints will include change from baseline in the Total Maximum Chorea (TMC) score of the UHDRS after 13 and 26 weeks of treatment and Clinical Global Impression-Improvement score after 13 and 26 weeks of treatment.

Detailed Description

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Conditions

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Huntington's Disease

Keywords

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Huntington; chorea; total motor score; CAG repeat: total functional capacity; motor cognitive and behavioral symptoms

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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20 mg PF-02545920 BID

20 mg PF-02545920 BID

Group Type EXPERIMENTAL

PF-02545920

Intervention Type DRUG

20 mg twice a day (BID) for 26 weeks. Each 20 mg dose will be taken as 4 tablets of 5 mg. The 20mg dose will be titrated as follow: 5mg BID for 7 days, 10mg BID for 7 days, 15 mg BID for 7 days and 20 mg BID to week 26. Study drug will be provided in weekly blister cards.

5 mg PF-02545920 BID

5 mg PF-02545920 BID

Group Type EXPERIMENTAL

PF-02545920

Intervention Type DRUG

5 mg twice a day (BID) for 26 weeks. Each 5 mg dose will be taken as 4 tablets: one tablet of 5 mg and 3 tablets of matching placebo. The 5mg dose will not be titrated. Study drug will be provided in weekly blister cards.

Placebo BID

Matching placebo

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type OTHER

Matching Placebo twice a day (BID) for 26 weeks. Each placebo dose will be taken as 4 tablets of matching Placebo. The placebo dose will not be titrated. Matching placebo will be provided in weekly blister cards.

Interventions

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PF-02545920

20 mg twice a day (BID) for 26 weeks. Each 20 mg dose will be taken as 4 tablets of 5 mg. The 20mg dose will be titrated as follow: 5mg BID for 7 days, 10mg BID for 7 days, 15 mg BID for 7 days and 20 mg BID to week 26. Study drug will be provided in weekly blister cards.

Intervention Type DRUG

PF-02545920

5 mg twice a day (BID) for 26 weeks. Each 5 mg dose will be taken as 4 tablets: one tablet of 5 mg and 3 tablets of matching placebo. The 5mg dose will not be titrated. Study drug will be provided in weekly blister cards.

Intervention Type DRUG

Placebo

Matching Placebo twice a day (BID) for 26 weeks. Each placebo dose will be taken as 4 tablets of matching Placebo. The placebo dose will not be titrated. Matching placebo will be provided in weekly blister cards.

Intervention Type OTHER

Eligibility Criteria

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Inclusion Criteria

* CAG repeat equal or greater than 36;
* Total motor score equal or greater than 10;
* Total functional capacity equal or greater than 7.

Exclusion Criteria

* Clinically significant neurologic disorder other than Huntington's disease;
* Other severe acute psychiatric conditions, mania and/or psychosis;
* History of neutropenia, and myeloproliferative disorders;
Minimum Eligible Age

30 Years

Maximum Eligible Age

65 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Pfizer

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Pfizer CT.gov Call Center

Role: STUDY_DIRECTOR

Pfizer

Locations

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The Kirklin Clinic of UAB Hospital

Birmingham, Alabama, United States

Site Status

The University of Alabama at Birmingham

Birmingham, Alabama, United States

Site Status

University of Alabama at Birmingham

Birmingham, Alabama, United States

Site Status

Mayo Clinic Arizona

Phoenix, Arizona, United States

Site Status

Mayo Clinic Arizona

Scottsdale, Arizona, United States

Site Status

University of California, Irvine

Irvine, California, United States

Site Status

Ronald Regan UCLA Medical Center Drug Information Center

Los Angeles, California, United States

Site Status

UCLA Neurology Clinic

Los Angeles, California, United States

Site Status

UCLA Radiology

Los Angeles, California, United States

Site Status

Rocky Mountain Movement Disorders Center

Englewood, Colorado, United States

Site Status

University of Florida Center for Movement Disorders and Neurorestoration

Gainesville, Florida, United States

Site Status

Indiana University Health Neuroscience Center

Indianapolis, Indiana, United States

Site Status

Massachusetts General Hospital

Charlestown, Massachusetts, United States

Site Status

Washington University School of Medicine

St Louis, Missouri, United States

Site Status

Albany Medical College

Albany, New York, United States

Site Status

Wake Forest Baptist Medical Center - Dept. of Neurology

Winston-Salem, North Carolina, United States

Site Status

Cleveland Clinic Foundation Hospital Pharmacy

Cleveland, Ohio, United States

Site Status

The Cleveland Clinic Foundation

Cleveland, Ohio, United States

Site Status

Davis Medical Center

Columbus, Ohio, United States

Site Status

The Wexner Medical Center at the Ohio State University

Columbus, Ohio, United States

Site Status

Wexner Medical Center at the Ohio State University

Columbus, Ohio, United States

Site Status

Baylor College of Medicine

Houston, Texas, United States

Site Status

The Centre for Huntington Disease

Vancouver, British Columbia, Canada

Site Status

Centre for Movement Disorders

Toronto, Ontario, Canada

Site Status

CHUM-Notre-Dame Hospital

Montreal, Quebec, Canada

Site Status

CHUM Notre Dame, Pharmacie

Montreal, Quebec, Canada

Site Status

Technische Universität München

München, Bavaria, Germany

Site Status

Uniklinik RWTH Aachen

Aachen, , Germany

Site Status

Charite - Universitatsmedizin Berlin

Berlin, , Germany

Site Status

Prof. Dr. Carsten Saft

Bochum, , Germany

Site Status

Friedrich-Alexander-Universität

Erlangen, , Germany

Site Status

Prof. Dr. med. Stephan Klebe

Freiburg im Breisgau, , Germany

Site Status

Universitat zu Lubeck

Lübeck, , Germany

Site Status

Philipps Universitat Marburg

Marburg, , Germany

Site Status

George Huntington Institut

Münster, , Germany

Site Status

Kbo-Isar-Amper-Klinikum gGmbH

Taufkirchen, , Germany

Site Status

Universitätsklinikum Ulm

Ulm, , Germany

Site Status

Universitatsklinikum Wuerzburg

Würzburg, , Germany

Site Status

Copernicus Podmiot Leczniczy sp. z o.o.

Gdansk, , Poland

Site Status

Krakowska Akademia Neurologii Sp. z o.o.

Krakow, , Poland

Site Status

Solumed Centrum Medyczne

Poznan, , Poland

Site Status

Instytut Psychiatrii i Neurologii

Warsaw, , Poland

Site Status

NHS Grampian, Clinical Genetics Centre

Aberdeen, Aberdeenshire, United Kingdom

Site Status

University Hospital Southampton NHS Foundation Trust

Southampton, Hampshire, United Kingdom

Site Status

Oxford University Hospitals NHS Trust

Oxford, Oxfordshire, United Kingdom

Site Status

Sheffield Teaching Hospitals NHS Foundation Trust

Sheffield, South Yorkshire, United Kingdom

Site Status

Birmingham & Solihull Mental Health NHS Foundation Trust

Birmingham, West Midlands, United Kingdom

Site Status

John Van Geest Centre for Brain Repair

Cambridge, , United Kingdom

Site Status

University of Wales Hospital

Cardiff, , United Kingdom

Site Status

NHS Greater Glasgow and Clyde

Glasgow, , United Kingdom

Site Status

Clinical Research Facility

London, , United Kingdom

Site Status

University College London Hospitals Huntington's Disease Research Centre

London, , United Kingdom

Site Status

University College London Hospitals NHS Foundation Trust

London, , United Kingdom

Site Status

Central Manchester University Hospitals NHS Foundation Trust

Manchester, , United Kingdom

Site Status

The National Institute for Health Research/Wellcome Trust Clinical Research Facility

Manchester, , United Kingdom

Site Status

St Nicholas Hospital

Newcastle upon Tyne, , United Kingdom

Site Status

Newcastle Magnetic Resonance Centre

Newcastle upon Tyne, , United Kingdom

Site Status

Countries

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United States Canada Germany Poland United Kingdom

Related Links

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https://trialinfoemail.pfizer.com/pages/landing.aspx?StudyID=A8241021

To obtain contact information for a study center near you, click here.

Other Identifiers

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2014-001291-56

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

A8241021

Identifier Type: -

Identifier Source: org_study_id