Open-Label Rollover Study for Continuing Valbenazine Administration for the Treatment of Chorea Associated With Huntington Disease

NCT ID: NCT04400331

Last Updated: 2024-12-24

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

ACTIVE_NOT_RECRUITING

Clinical Phase

PHASE3

Total Enrollment

154 participants

Study Classification

INTERVENTIONAL

Study Start Date

2020-09-18

Study Completion Date

2026-03-31

Brief Summary

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This is a Phase 3, open-label study to evaluate the long-term safety and tolerability of valbenazine, and to provide participants continued access to valbenazine for the treatment of chorea associated with Huntington disease.

Detailed Description

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After completion of Week 156/early termination visit, participants in the US will be given the option to continue into an extended maintenance period for up to 104 weeks and participants in Canada will have the option to participate in a separate open-label study (Study NBI-98854-HD3022).

Conditions

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Chorea, Huntington

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Valbenazine

Capsule, administered orally once daily.

Group Type EXPERIMENTAL

Valbenazine

Intervention Type DRUG

vesicular monoamine transporter 2 (VMAT2) inhibitor

Interventions

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Valbenazine

vesicular monoamine transporter 2 (VMAT2) inhibitor

Intervention Type DRUG

Other Intervention Names

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NBI-98854

Eligibility Criteria

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Inclusion Criteria

Either #1 or #2 must be met for inclusion eligibility.

1. Have participated in Study NBI-98854-HD3005 and

a. Study drug dosing completion of Study NBI-98854-HD3005, as demonstrated by completed study drug dosing through the follow-up visit or early terminated Study NBI-98854-HD3005 for administrative reasons due to COVID-19 (for example, site closure related to COVID-19)
2. Did not participate in Study NBI-98854-HD3005 and

1. Have a clinical and genetic diagnosis of Huntington Disease (HD) with chorea
2. Be able to walk, with or without the assistance of a person or device
3. Be able to read and understand English and capable of providing consent to study participation or have a legally authorized representative providing consent and the participant providing assent
4. Participants of childbearing potential must agree to use contraception consistently while participating in the study until 30 days after last dose of the study treatment

Exclusion Criteria

1. Have difficulty swallowing
2. Are currently pregnant or breastfeeding
3. Have a known history of long QT syndrome, cardiac tachyarrhythmia, left bundle-branch block, atrioventricular (AV) block, uncontrolled bradyarrhythmia, or heart failure
4. Have an unstable or serious medical or psychiatric illness
5. Have a significant risk of suicidal behavior
6. Have a history of substance dependence or substance (drug) or alcohol abuse, within 1 year of screening
7. Have received gene therapy at any time
8. Have received an investigational drug in a clinical study (other than valbenazine) within 30 days before the baseline visit or plan to use such investigational drug (other than valbenazine) during the study
9. Have had a blood loss ≥550 mL or donated blood within 30 days before the baseline visit
10. Have a history of severe hepatic impairment or history of protocol specified hematologic abnormalities during the course of the NBI-98854-HD3005 study
11. Had a medically significant illness within 30 days before baseline, or any history of neuroleptic malignant syndrome
12. Have a known hypersensitivity to any component of the formulation of valbenazine
13. For participants who did not participate in NBI-98854-HD3005: have a history of VMAT2 inhibitor use within 30 days of baseline
Minimum Eligible Age

18 Years

Maximum Eligible Age

75 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Huntington Study Group

NETWORK

Sponsor Role collaborator

Neurocrine Biosciences

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Chief Medical Officer

Role: STUDY_DIRECTOR

Chief Medical Officer

Locations

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Neurocrine Clinical Site

Birmingham, Alabama, United States

Site Status

Neurocrine Clinical Site

Little Rock, Arkansas, United States

Site Status

Neurocrine Clinical Site

La Jolla, California, United States

Site Status

Neurocrine Clinical Site

Aurora, Colorado, United States

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Neurocrine Clinical Site

Washington D.C., District of Columbia, United States

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Neurocrine Clinical Site

Boca Raton, Florida, United States

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Neurocrine Clinical Site

Gainesville, Florida, United States

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Neurocrine Clinical Site

Atlanta, Georgia, United States

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Neurocrine Clinical Site

Chicago, Illinois, United States

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Neurocrine Clinical Site

Chicago, Illinois, United States

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Neurocrine Clinical Site

Indianapolis, Indiana, United States

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Neurocrine Clinical Site

Iowa City, Iowa, United States

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Neurocrine Clinical Site

Wichita, Kansas, United States

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Neurocrine Clinical Site

Louisville, Kentucky, United States

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Neurocrine Clinical Site

New Orleans, Louisiana, United States

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Neurocrine Clinical Site

Boston, Massachusetts, United States

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Neurocrine Clinical Site

Charlestown, Massachusetts, United States

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Neurocrine Clinical Site

Ann Arbor, Michigan, United States

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Neurocrine Clinical Site

Omaha, Nebraska, United States

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Neurocrine Clinical Site

Rochester, New York, United States

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Neurocrine Clinical Site

Williamsville, New York, United States

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Neurocrine Clinical Site

Durham, North Carolina, United States

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Neurocrine Clinical Site

Columbus, Ohio, United States

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Neurocrine Clinical Site

Toledo, Ohio, United States

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Neurocrine Clinical Site

Pittsburgh, Pennsylvania, United States

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Neurocrine Clinical Site

Charleston, South Carolina, United States

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Neurocrine Clinical Site

Columbia, South Carolina, United States

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Neurocrine Clinical Site

Greenville, South Carolina, United States

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Neurocrine Clinical Site

Nashville, Tennessee, United States

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Neurocrine Clinical Site

Houston, Texas, United States

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Neurocrine Clinical Site

Burlington, Vermont, United States

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Neurocrine Clinical Site

Vancouver, British Columbia, Canada

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Neurocrine Clinical Site

Ottawa, Ontario, Canada

Site Status

Neurocrine Clinical Site

Toronto, Ontario, Canada

Site Status

Countries

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United States Canada

Related Links

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Other Identifiers

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NBI-98854-HD3006

Identifier Type: -

Identifier Source: org_study_id