A Study of Atezolizumab Plus Bevacizumab Versus Active Surveillance as Adjuvant Therapy in Patients With Hepatocellular Carcinoma at High Risk of Recurrence After Surgical Resection or Ablation

NCT ID: NCT04102098

Last Updated: 2025-12-11

Study Results

Results available

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Basic Information

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Recruitment Status

ACTIVE_NOT_RECRUITING

Clinical Phase

PHASE3

Total Enrollment

668 participants

Study Classification

INTERVENTIONAL

Study Start Date

2019-12-31

Study Completion Date

2027-07-16

Brief Summary

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This study will evaluate the efficacy and safety of adjuvant therapy with atezolizumab plus bevacizumab compared with active surveillance in participants with completely resected or ablated hepatocellular carcinoma (HCC) who are at high risk for disease recurrence.

Detailed Description

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Conditions

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Carcinoma, Hepatocellular

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Arm A (atezolizumab plus bevacizumab)

Participants will receive Atezolizumab + Bevacizumab until disease recurrence or unacceptable toxicity.

Group Type EXPERIMENTAL

Atezolizumab

Intervention Type DRUG

Atezolizumab 1200 mg will be administered by IV infusion on Day 1 of each 21-day cycle.

Bevacizumab

Intervention Type DRUG

Bevacizumab will be administered by IV infusion at a dose of 15 mg/kg on Day 1 of each 21-day cycle.

Arm B (active surveillance)

Active surveillance of participants.

Group Type NO_INTERVENTION

No interventions assigned to this group

Interventions

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Atezolizumab

Atezolizumab 1200 mg will be administered by IV infusion on Day 1 of each 21-day cycle.

Intervention Type DRUG

Bevacizumab

Bevacizumab will be administered by IV infusion at a dose of 15 mg/kg on Day 1 of each 21-day cycle.

Intervention Type DRUG

Other Intervention Names

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Tecentriq Avastin

Eligibility Criteria

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Inclusion Criteria

* Participants with a first diagnosis of HCC who have undergone either a curative resection or ablation (radiofrequency ablation \[RFA\] or microwave ablation \[MVA\] only) within 4-12 weeks prior to randomization
* Documented diagnosis of HCC that has been completely resected or ablated (RFA or MVA only)
* Absence of major macrovascular invasion (except Vp1/Vp2) and extrahepatic spread
* Absence of extrahepatic spread as confirmed by CT or MRI scan of the chest, abdomen, pelvis, and head prior to and following curative procedure
* Full recovery from surgical resection or ablation within 4 weeks prior to randomization
* High risk for HCC recurrence after resection or ablation
* For patients who received post-operative transarterial chemoembolization: full recovery from the procedure within 4 weeks prior to randomization
* For patients with resected HCC, availability of a representative baseline tumor tissue sample
* ECOG Performance Status of 0 or 1
* Child-Pugh Class A status
* Adequate hematologic and end-organ function
* For women of childbearing potential: agreement to remain abstinent (refrain from heterosexual intercourse) or use contraceptive methods
* For men: agreement to remain abstinent (refrain from heterosexual intercourse) or use a condom, and agreement to refrain from donating sperm

Exclusion Criteria

* Known fibrolamellar HCC, sarcomatoid HCC, or mixed cholangiocarcinoma and HCC
* Evidence of residual, recurrent, or metastatic disease at randomization
* Clinically significant ascites
* History of hepatic encephalopathy
* Prior bleeding event due to untreated or incompletely treated esophageal and/or gastric varices within 6 months prior to randomization
* Have received more than 1 cycle of adjuvant TACE following surgical resection
* Active or history of autoimmune disease or immune deficiency
* History of idiopathic pulmonary fibrosis, organizing pneumonia, drug-induced pneumonitis, or idiopathic pneumonitis, or evidence of active pneumonitis on screening chest CT scan
* Significant cardiovascular disease within 3 months prior to Day 1 of Cycle 1, unstable arrhythmia, or unstable angina
* History of malignancy other than HCC within 5 years prior to screening, with the exception of malignancies with a negligible risk of metastasis or death
* Active tuberculosis
* Any other disease, metabolic dysfunction, physical examination finding, or clinical laboratory finding that contraindicates the use of an investigational drug, may affect the interpretation of the results, or may render the patient at high risk from treatment complications
* Pregnant or breastfeeding, or intending to become pregnant during the study or within 5 months after the final dose of atezolizumab or within 6 months after the final dose of bevacizumab. Women of childbearing potential must have a negative serum pregnancy test result within 14 days prior to Day 1 of Cycle 1.
* Co-infection with HBV and HCV
* Co-infection with HBV and hepatitis D viral infection
* Clinical significant uncontrolled or symptomatic hypercalcemia
* Any treatment for HCC prior to resection or ablation, including systemic therapy and locoregional therapy such as TACE
* Treatment with systemic immunostimulatory or immunosuppressive agents
* Inadequately controlled arterial hypertension
* History of hypertensive crisis or hypertensive encephalopathy
* Significant vascular disease
* Evidence of bleeding diathesis or significant coagulopathy
* Current or recent use of aspirin or full-dose oral or parenteral anticoagulants
* Core biopsy within 3 days of Day 1 of Cycle 1
* History of GI fistula, GI perforation, or intra-abdominal abscess
* Serious non-healing or dehiscing wound
* Major surgical procedure within four weeks
* Chronic daily treatment with a non-steroidal anti-inflammatory drug
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Hoffmann-La Roche

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Clinical Trials

Role: STUDY_DIRECTOR

Hoffmann-La Roche

Locations

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Kaiser Permanente Los Angeles

Los Angeles, California, United States

Site Status

Mercy Medical Center

Baltimore, Maryland, United States

Site Status

Henry Ford Health System

Detroit, Michigan, United States

Site Status

Columbia University Medical Center

New York, New York, United States

Site Status

Thomas Jefferson University

Philadelphia, Pennsylvania, United States

Site Status

The University of Texas Southwestern Medical Center at Dallas

Dallas, Texas, United States

Site Status

MD Anderson Cancer Center

Houston, Texas, United States

Site Status

Swedish Cancer Inst.

Seattle, Washington, United States

Site Status

St Vincent's Hospital Sydney

Darlinghurst, New South Wales, Australia

Site Status

Lkh-Univ. Klinikum Graz

Graz, , Austria

Site Status

Klinikum Klagenfurt am Wörtersee

Klagenfurt, , Austria

Site Status

Medizinische Universität Wien

Vienna, , Austria

Site Status

Imeldaziekenhuis

Bonheiden, , Belgium

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AZ Delta (Campus Rumbeke)

Roeselare, , Belgium

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Hospital Sao Rafael - HSR

Salvador, Estado de Bahia, Brazil

Site Status

Sociedade beneficente de senhoras Hospital Sirio Libanes

Brasília, Federal District, Brazil

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Hospital do Cancer UOPECCAN

Cascavel, Paraná, Brazil

Site Status

Hospital Alemao Oswaldo Cruz

São Paulo, São Paulo, Brazil

Site Status

Gordon & Leslie Diamond Health Care Centre

Vancouver, British Columbia, Canada

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McGill University Health Centre - Glen Site

Montreal, Quebec, Canada

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Anhui Provincial Hospital

Anhui, , China

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Beijing Cancer Hospital

Beijing, , China

Site Status

Peking Union Medical College Hospital

Beijing, , China

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Affiliated Hospital of Bengbu Medical College

Bengbu, , China

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The First Hospital of Jilin University

Changchun, , China

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West China Hospital, Sichuan University

Chengdu, , China

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Daping Hospital of Third Military Medical University

Chongqing, , China

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The Second Affiliated Hospital of Dalian Medical University

Dalian, , China

Site Status

Fujian Cancer Hospital

Fuzhou, , China

Site Status

Mengchao Hepatobiliary Hospital Of Fujian Medical University

Fuzhou, , China

Site Status

Cancer Center of Guangzhou Medical University

Guangzhou, , China

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Sun Yet-sen University Cancer Center

Guangzhou, , China

Site Status

Zhujiang Hospital, Southern Medical University

Guangzhou, , China

Site Status

Nanfang Hospital, Southern Medical University

Guangzhou, , China

Site Status

Zhejiang Cancer Hospital

Hangzhou, , China

Site Status

Harbin Medical University Cancer Hospital

Harbin, , China

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Anhui Province Cancer Hospital

Hefei, , China

Site Status

The Second Affiliated Hospital of Anhui Medical University

Hefei, , China

Site Status

Shandong Cancer Hospital

Jinan, , China

Site Status

The 81st Hospital of P.L.A.

Nanjing, , China

Site Status

Zhongda Hospital Affiliated to Southeast University

Nanjing, , China

Site Status

Nanjing Drum Tower Hospital, the Affiliated Hospital of Nanjing University Medical School

Nanjing, , China

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Guangxi Cancer Hospital of Guangxi Medical University

Nanning, , China

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The First Affiliate Hospital of Guangxi Medical University

Nanning, , China

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Fudan University Shanghai Cancer Center

Shanghai, , China

Site Status

Huashan Hospital Affiliated to Fudan University

Shanghai, , China

Site Status

Renji Hospital Affiliated to Shanghai Jiao Tong University School of Medicine

Shanghai, , China

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Zhongshan Hospital Fudan Unvierstiy

Shanghai, , China

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The First Affiliated Hospital of China Medical University

Shenyang, , China

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Shengjing Hospital of China Medical University

Shenyang, , China

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Tianjin Cancer Hospital

Tianjin, , China

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The Tumor Hospital of Xinjiang Medical University

Ürümqi, , China

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Wuhan Union Hospital Tongji Medical College, Huazhong University of Science and Technology

Wuhan, , China

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Renmin Hospital of Wuhan University

Wuhan, , China

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Zhongnan Hospital of Wuhan University

Wuhan, , China

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Northern Jangsu People's Hospital

Yangzhou, , China

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Clinica CIMCA

San José, , Costa Rica

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Fakultni nemocnice Brno

Brno, , Czechia

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Fakultni Thomayerova Nemocnice

Prague, , Czechia

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Hopital Jean Minoz

Besançon, , France

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Hôpital Avicenne - Groupement Hospitalier Universitaire Paris Seine St Denis

Bobigny, , France

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Hôpital Albert Michallon

La Tronche, , France

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Fondation Hopital Saint Joseph

Marseille, , France

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CHU Bordeaux - Hôpital Haut-Lévêque

Pessac, , France

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Hopital Robert Debre

Reims, , France

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Hopital de Pontchaillou

Rennes, , France

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CHU de Toulouse - Hôpital Rangueil

Toulouse, , France

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Hopitaux de Brabois - Gastro-Entereologie

Vandœuvre-lès-Nancy, , France

Site Status

Universitätsklinikum Bonn, Medizinische Klinik und Poliklinik I.

Bonn, , Germany

Site Status

Klinik Johann Wolfgang von Goethe Uni

Frankfurt am Main, , Germany

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Klinikum der Uni Regensburg

Regensburg, , Germany

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Universitätsklinikum Ulm

Ulm, , Germany

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Queen Mary Hospital

Hong Kong, , Hong Kong

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Prince of Wales Hospital

Shatin, , Hong Kong

Site Status

Ospedale Regionale Di Parma

Parma, Emilia-Romagna, Italy

Site Status

Ospedale Maggiore Policlinico

Milan, Lombardy, Italy

Site Status

Asst Santi Paolo E Carlo

Milan, Lombardy, Italy

Site Status

Azlenda Ospendaliero-Universitaria Pisana

Pisa, Tuscany, Italy

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Chiba University Hospital

Chiba, , Japan

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Ehime Prefectural Central Hospital

Ehime, , Japan

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Hiroshima University Hospital

Hiroshima, , Japan

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Sapporo Kosei General Hospital

Hokkaido, , Japan

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Hyogo Medical University Hospital

Hyōgo, , Japan

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Japanese Red Cross Society Himeji Hospital

Hyōgo, , Japan

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Kanazawa University Hospital

Ishikawa, , Japan

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Yokohama City University Medical Center

Kanagawa, , Japan

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Kanagawa Cancer Center

Kanagawa, , Japan

Site Status

Kitasato University Hospital

Kanagawa, , Japan

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Kumamoto University Hospital

Kumamoto, , Japan

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Osaka Red Cross Hospital

Osaka, , Japan

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Kindai University Hospital

Osaka, , Japan

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Tokushima University Hospital

Tokushima, , Japan

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Toranomon Hospital

Tokyo, , Japan

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The University of Tokyo Hospital

Tokyo, , Japan

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Japanese Red Cross Musashino Hospital

Tokyo, , Japan

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Filios Alta Medicina

Monterrey, Nuevo León, Mexico

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Oaxaca Site Management Organization

Oaxaca City, , Mexico

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Maastricht University Medical Center

Maastricht, , Netherlands

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Auckland City Hospital

Auckland, , New Zealand

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Instituto Nacional de Enfermedades Neoplasicas

Lima, , Peru

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Clínica San Gabriel

Lima, , Peru

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Narodowy Instytut Onkologii im. M. Sklodowskiej-Curie

Warsaw, , Poland

Site Status

First Moscow State Medical University n.a. I.M. Sechenov

Moscow, Moscow Oblast, Russia

Site Status

Group of companies "Medci"

Moskva, Moscow Oblast, Russia

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Clinical hospital #1, FBHI Volga district medical center, Federal Medical and Biological Agency

Nizhny Novgorod, Niznij Novgorod, Russia

Site Status

Russian Scientific Center of Radiology and Surgical Technologies

Pesochny, Sankt-Peterburg, Russia

Site Status

National Cancer Centre

Singapore, , Singapore

Site Status

Tan Tock Seng Hospital

Singapore, , Singapore

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Pusan National University Hospital

Busan, , South Korea

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Kyungpook National University Hospital

Daegu, , South Korea

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CHA Bundang Medical Center

Gyeonggi-do, , South Korea

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Seoul National University Bundang Hospital

Gyeonggi-do, , South Korea

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Ajou University Medical Center

Gyeonggi-do, , South Korea

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Seoul National University Hospital

Seoul, , South Korea

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Severance Hospital, Yonsei University Health System

Seoul, , South Korea

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Asan Medical Center

Seoul, , South Korea

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Gangnam Severance Hospital

Seoul, , South Korea

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Seoul St Mary's Hospital

Seoul, , South Korea

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Boramae Medical Center

Seoul, , South Korea

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Samsung Medical Center

Seoul, , South Korea

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Ulsan University Hosiptal

Ulsan, , South Korea

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Hospital Universitario Puerta de Hierro

Majadahonda, Madrid, Spain

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Hospital Universitario Infanta Cristina

Badajoz, , Spain

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Hospital General Universitario Gregorio Marañon

Madrid, , Spain

Site Status

Changhua Christian Hospital

Chang-hua, , Taiwan

Site Status

Kaohsiung Medical University Chung-Ho Memorial Hospital

Kaohsiung City, , Taiwan

Site Status

National Taiwan Uni Hospital

Taipei, , Taiwan

Site Status

Taipei Veterans General Hospital

Taipei, , Taiwan

Site Status

Chang Gung Medical Foundation - Linkou

Taoyuan District, , Taiwan

Site Status

Rajavithi Hospital

Bangkok, , Thailand

Site Status

Siriraj Hospital

Bangkok, , Thailand

Site Status

Chiang Rai Prachanukroh Hospital

Chiang Rai, , Thailand

Site Status

Chulabhorn Hospital

Lak Si, , Thailand

Site Status

Adana Baskent University Hospital

Adana, , Turkey (Türkiye)

Site Status

Countries

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United States Australia Austria Belgium Brazil Canada China Costa Rica Czechia France Germany Hong Kong Italy Japan Mexico Netherlands New Zealand Peru Poland Russia Singapore South Korea Spain Taiwan Thailand Turkey (Türkiye)

References

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Qin S, Chen M, Cheng AL, Kaseb AO, Kudo M, Lee HC, Yopp AC, Zhou J, Wang L, Wen X, Heo J, Tak WY, Nakamura S, Numata K, Uguen T, Hsiehchen D, Cha E, Hack SP, Lian Q, Ma N, Spahn JH, Wang Y, Wu C, Chow PKH; IMbrave050 investigators. Atezolizumab plus bevacizumab versus active surveillance in patients with resected or ablated high-risk hepatocellular carcinoma (IMbrave050): a randomised, open-label, multicentre, phase 3 trial. Lancet. 2023 Nov 18;402(10415):1835-1847. doi: 10.1016/S0140-6736(23)01796-8. Epub 2023 Oct 20.

Reference Type DERIVED
PMID: 37871608 (View on PubMed)

Hack SP, Spahn J, Chen M, Cheng AL, Kaseb A, Kudo M, Lee HC, Yopp A, Chow P, Qin S. IMbrave 050: a Phase III trial of atezolizumab plus bevacizumab in high-risk hepatocellular carcinoma after curative resection or ablation. Future Oncol. 2020 May;16(15):975-989. doi: 10.2217/fon-2020-0162. Epub 2020 Apr 30.

Reference Type DERIVED
PMID: 32352320 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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2019-002491-14

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

2023-504303-86-00

Identifier Type: CTIS

Identifier Source: secondary_id

WO41535

Identifier Type: -

Identifier Source: org_study_id

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