Study Evaluating Cemiplimab Alone and Combined With RP1 in Treating Advanced Squamous Skin Cancer

NCT ID: NCT04050436

Last Updated: 2025-01-27

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

ACTIVE_NOT_RECRUITING

Clinical Phase

PHASE2

Total Enrollment

231 participants

Study Classification

INTERVENTIONAL

Study Start Date

2019-10-08

Study Completion Date

2025-09-30

Brief Summary

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To estimate the clinical benefit of cemiplimab monotherapy versus cemiplimab in combination with RP1 for patients with locally advanced or metastatic CSCC, as assessed by overall response rate (ORR) and complete response rate (CRR) according to blinded independent review.

Detailed Description

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RP1 is a selectively replication competent herpes simplex virus type 1(HSV-1). This is a Phase 1/2, open-label, multicenter repeat-dosing study of RP1 alone and in combination with nivolumab in patients with advanced malignancies, and contains both single agent dose escalation, dose expansion to include nivolumab, and the combination in multiple Phase 2 cohorts in individual tumor types.

Conditions

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Cutaneous Squamous Cell Carcinoma Advanced Cutaneous Squamous Cell Carcinoma Metastatic Cutaneous Squamous Cell Carcinoma

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Cemiplimab in combination with RP1

Cemiplimab administered intravenously every 3 weeks in combination with RP1 administered as an intratumoral injection every 3 weeks

Group Type EXPERIMENTAL

Cemiplimab

Intervention Type DRUG

Cemiplimab administered intravenously

RP1

Intervention Type BIOLOGICAL

RP1 administered intratumorally

Cemiplimab

Cemiplimab administered intravenously as a single therapy every 3 weeks

Group Type ACTIVE_COMPARATOR

Cemiplimab

Intervention Type DRUG

Cemiplimab administered intravenously

Interventions

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Cemiplimab

Cemiplimab administered intravenously

Intervention Type DRUG

RP1

RP1 administered intratumorally

Intervention Type BIOLOGICAL

Other Intervention Names

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Libtayo Genetically modified herpes simplex type 1 virus

Eligibility Criteria

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Inclusion Criteria

* Histologically confirmed locally advanced or metastatic cutaneous squamous cell carcinoma
* Patients with locally advanced disease who are not suitable candidates for surgical or radiological treatment of lesions or have refused those treatments
* At least 1 lesion that is measurable and injectable by study criteria
* Eastern Cooperative Oncology Group (ECOG) performance status ≤1. Patients with ECOG PS 2 at baseline may be allowed to enroll if PS 2 status is only related to the CSCC disease under study
* Anticipated life expectancy \>12 weeks
* All patients must consent to provide archived or newly obtained tumor material for central pathology review for confirmation of diagnosis of CSCC.

Exclusion Criteria

* Prior treatment with an oncolytic therapy
* Patients with active significant herpetic infections or prior complications of HSV-1 infection (e.g. herpetic keratitis or encephalitis)
* Patients who require intermittent or chronic use of systemic (oral or intravenous) anti-virals with known anti-herpetic activity (e.g. acyclovir)
* Ongoing or recent (within 5 years) evidence of significant autoimmune disease that required treatment with systemic immunosuppressive treatments
* Prior treatment with an agent that blocks the PD-1/PD-L1 pathway.
* Prior treatment with other immune modulating agents other than as adjuvant or neoadjuvant therapy within 3 years.
* Untreated brain metastasis(es) that may be considered active.
* Acute or chronic active hepatitis B or known history of hepatitis B or hepatitis C or human immunodeficiency virus (HIV) infection
* History of ILD/pneumonitis within the last 5 years or a history of ILD/pneumonitis requiring treatment with systemic steroids.
* Any major or surgical procedure ≤ 28 days before randomization
* Administration of live vaccines ≤ 28 days before randomization
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Regeneron Pharmaceuticals

INDUSTRY

Sponsor Role collaborator

Replimune Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Moran Mishal, MD

Role: STUDY_DIRECTOR

Lead Medical Monitor

Jeannie Hou, MD

Role: STUDY_DIRECTOR

Secondary Medical Monitor

Locations

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University of California San Diego

La Jolla, California, United States

Site Status

University of California Los Angeles

Los Angeles, California, United States

Site Status

Stanford University

Stanford, California, United States

Site Status

University of Colorado Cancer Center

Aurora, Colorado, United States

Site Status

University of Miami Health System

Miami, Florida, United States

Site Status

Orlando Health UF Health Cancer Center

Orlando, Florida, United States

Site Status

Moffitt McKinley Outpatient Center

Tampa, Florida, United States

Site Status

Winship Cancer Institute of Emory University

Atlanta, Georgia, United States

Site Status

John Theurer Cancer Center at Hackensack Univeristy Medical Center

Hackensack, New Jersey, United States

Site Status

Memorial Sloan Kettering Cancer Center

New York, New York, United States

Site Status

University Of North Carolina at Chapel Hill

Chapel Hill, North Carolina, United States

Site Status

Ohio State University Comprehensive Cancer Center

Columbus, Ohio, United States

Site Status

Prisma Health Cancer Institute

Greenville, South Carolina, United States

Site Status

MD Anderson Cancer Center

Houston, Texas, United States

Site Status

Chris O'Brien Lifehouse

Camperdown, New South Wales, Australia

Site Status

Cancer Care Wollongong Pty Limited

Wollongong, New South Wales, Australia

Site Status

Tasman Oncology Research Ltd

Southport, Queensland, Australia

Site Status

Monash Medical Centre

Clayton, Victoria, Australia

Site Status

Peter MacCallum Cancer Centre

Melbourne, Victoria, Australia

Site Status

The Alfred Hospital

Melbourne, Victoria, Australia

Site Status

Sir Charles Gairdner Hospital

Nedlands, Western Australia, Australia

Site Status

Multiprofile Hospital for Active Treatment - Uni Hospital" OOD Department of Medical Oncology

Panagyurishte, , Bulgaria

Site Status

"Complex Oncology Center - Plovdiv" EOOD Department of Medical Oncology and Cutaneous Cancer Diseases "

Plovdiv, , Bulgaria

Site Status

Sunnybrook Health Science Centre

Toronto, Ontario, Canada

Site Status

CHU Besancon - Hopital Jean Minjoz

Besançon, , France

Site Status

CHU Dijon Hopital F. Mitterrand Service de Dermatologie - UMAC

Dijon, , France

Site Status

CHU de Grenoble - Hopital A Michallon

La Tronche, , France

Site Status

CHRU de Lille

Lille, , France

Site Status

Centre Léon Bérard

Lyon, , France

Site Status

Service de Dermatologie et Cancerologie Cutanee Hopital de la Timone

Marseille, , France

Site Status

CHU Nice - Hopital de l'Archet 2

Nice, , France

Site Status

Hospital Saint Louis

Paris, , France

Site Status

Hospices Civils de Lyon

Pierre-Bénite, , France

Site Status

Institut Gustave Roussy

Villejuif, , France

Site Status

Charite Universitatsmedizin Berlin

Berlin, , Germany

Site Status

Universitatsklinikum Essen

Essen, , Germany

Site Status

Universitätsklinikum Eppendorf

Hamburg, , Germany

Site Status

Universitatsklinikum Heidelberg: National Centre for Tumour Diseases (NCT)

Heidelberg, , Germany

Site Status

University Hospital Munchen (LMU)

München, , Germany

Site Status

Universitatsklinikum Tubingen Zentrum fur Dermatoonkologie

Tübingen, , Germany

Site Status

Hippocratio General Hospital of Athens

Athens, , Greece

Site Status

Attiko University Hospital

Athens, , Greece

Site Status

Andreas Syggros Hospital

Athens, , Greece

Site Status

General Hospital of Athens "Laiko", 1st Department of Medicine, University of Athens Medical School

Athens, , Greece

Site Status

Istituto Tumori "Giovanni Paolo II" IRCCS

Bari, , Italy

Site Status

Uniwersyteckie Centrum Kliniczne; Centrum Leczenia Czerniaka w Gdańsku

Gdansk, , Poland

Site Status

Narodowy Instytut Onkologii; Panstwowy Instytut Badawczy Oddzial w Krakowie

Krakow, , Poland

Site Status

Narodowy Instytut Onkologii; Panstwowy Instytut Badawczy

Warsaw, , Poland

Site Status

Klinika Dermatologii, Wenerologii i Alergologii, USK im J. Mikulicza-Radeckiego we Wroclawiu

Wroclaw, , Poland

Site Status

Hospital Clinic Barcelona

Barcelona, , Spain

Site Status

Hospital Universitari Vall d'Hebron

Barcelona, , Spain

Site Status

Hospital Universitario 12 de Octubre

Madrid, , Spain

Site Status

Hospital Universitario Fundación Jiménez Díaz

Madrid, , Spain

Site Status

Hospital Universitario Virgen de la Arrixaca

Murcia, , Spain

Site Status

Clinica Universitaria de Navarra

Pamplona, , Spain

Site Status

Hospital General Universitario De Valencia

Valencia, , Spain

Site Status

Countries

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United States Australia Bulgaria Canada France Germany Greece Italy Poland Spain

Other Identifiers

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RPL-002-18

Identifier Type: -

Identifier Source: org_study_id

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