PD-1 in Patients With Advanced Basal Cell Carcinoma Who Experienced Progression of Disease on Hedgehog Pathway Inhibitor Therapy, or Were Intolerant of Prior Hedgehog Pathway Inhibitor Therapy

NCT ID: NCT03132636

Last Updated: 2025-04-08

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

138 participants

Study Classification

INTERVENTIONAL

Study Start Date

2017-06-29

Study Completion Date

2023-04-27

Brief Summary

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The primary objective is to estimate the objective response rate (ORR) for metastatic Basal Cell Carcinoma (BCC) (group 1) and for unresectable locally advanced BCC (group 2) when treated with cemiplimab as a monotherapy

Detailed Description

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Conditions

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Carcinoma, Basal Cell

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Group 1- metastatic BCC

Administration of cemiplimab in accordance with protocol dosing regimen

Group Type EXPERIMENTAL

cemiplimab

Intervention Type DRUG

Regimen as per protocol

Group 2 - unresectable locally advanced BCC

Administration of cemiplimab in accordance with protocol dosing regimen

Group Type EXPERIMENTAL

cemiplimab

Intervention Type DRUG

Regimen as per protocol

Interventions

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cemiplimab

Regimen as per protocol

Intervention Type DRUG

Other Intervention Names

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REGN2810 Libtayo

Eligibility Criteria

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Inclusion Criteria

* Confirmed diagnosis of invasive BCC
* Progression of disease on hedgehog inhibitor (HHI) therapy or intolerance of prior HHI therapy
* At least 1 measurable lesion
* ≥18 years of age
* Hepatic function, renal function, bone marrow function in defined lab-value-ranges
* Anticipated life expectancy \>12 weeks
* Consent to provide archived tumor biopsy material (all patients)
* Group 2: consent to undergo research biopsies
* Group 2: must not be a candidate for radiation therapy or surgery
* Comply with study procedures and site visits
* Sign Subject Information Sheet and Informed Consent Form

Exclusion Criteria

* Ongoing or recent significant autoimmune disease
* Prior treatment with specific pathway-blockers (PD-1/PD-L1)
* Prior treatment with immune-modulating agents within 28 days before cemiplimab
* Untreated brain metastasis that may be considered active
* Immunosuppressive corticosteroid doses (\>10mg prednisone) within 28 days prior to treatment with cemiplimab
* Active infections requiring therapy, including HIV, hepatitis
* Pneumonitis within the last 5 years
* Cancer treatment other than radiation therapy, including investigational or standard of care, within 30 days prior to treatment with cemiplimab
* Documented allergic reactions or similar to antibody treatments
* Concurrent malignancies other than BCC, other than those with negligible risk of metastases or death
* Any acute or chronic psychiatric problems
* Having received a solid organ transplantation
* Inability to undergo contrast radiological assessments
* Breastfeeding, pregnant, women of childbearing potential not using contraception
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Sanofi

INDUSTRY

Sponsor Role collaborator

Regeneron Pharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Clinical Trial Management

Role: STUDY_DIRECTOR

Regeneron Pharmaceuticals

Locations

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The University of Arizona Cancer Centre at Dignity Health

Phoenix, Arizona, United States

Site Status

Mayo Clinic Arizona - Mayo Clinic Hospital

Phoenix, Arizona, United States

Site Status

UC San Diego Moores Cancer Center

La Jolla, California, United States

Site Status

Stanford Medicine Outpatient Center - Stanford Dermatology Clinic-Stanford University School of Medicine

Redwood City, California, United States

Site Status

UCSF Helen Dillion Family Cancer Care Center

San Francisco, California, United States

Site Status

University of Colorado Hospital, Anschutz Outpatient Pavilion

Denver, Colorado, United States

Site Status

Mount Sinai Comprehensive Cancer Center

Miami, Florida, United States

Site Status

H Lee Moffitt Cancer Center and Research Institute

Tampa, Florida, United States

Site Status

Northwestern Medical Faculty Foundation

Chicago, Illinois, United States

Site Status

Norton Cancer Institute

Louisville, Kentucky, United States

Site Status

Massachusetts General Hospital

Boston, Massachusetts, United States

Site Status

Dana Farber Cancer Institute (DFCI)

Boston, Massachusetts, United States

Site Status

Washington University School of Medicine

St Louis, Missouri, United States

Site Status

Atlantic Health System / Morristown Medical Center

Morristown, New Jersey, United States

Site Status

Overlook Medical Center

Summit, New Jersey, United States

Site Status

New York University School Of Medicine, Kaplan Comprehensive Cancer Center

New York, New York, United States

Site Status

Mount Sinai Hospital

New York, New York, United States

Site Status

Memorial Sloan Kettering Cancer Center

New York, New York, United States

Site Status

James Cancer Hospital and Solove Research Institute

Columbus, Ohio, United States

Site Status

Penn State Hershey Medical Center

Hershey, Pennsylvania, United States

Site Status

Clinical Research Center of the Carolinas

Charleston, South Carolina, United States

Site Status

University of Texas MD Anderson Cancer Center

Houston, Texas, United States

Site Status

Huntsman Cancer Institute

Salt Lake City, Utah, United States

Site Status

LKH - Universitaetsklinikum Graz

Graz, Styria, Austria

Site Status

Medizinische Universitaet Innsbruck, Universitaetsklinik fuer Dermatologie, Venerologie und Allergologie

Innsbruck, , Austria

Site Status

Cliniques Universitaires Saint-Luc

Brussels, , Belgium

Site Status

Universitaire Ziekenhuizen Leuven - Campus Gasthuisberg

Leuven, , Belgium

Site Status

Cross Cancer Institute

Edmonton, Alberta, Canada

Site Status

Odette Cancer Center-Sunnybrook Health Sciences Centre

Toronto, Ontario, Canada

Site Status

University Health Network

Toronto, Ontario, Canada

Site Status

London Regional Cancer Program, London Hsc

Toronto, Ontario, Canada

Site Status

CHU de Dijon - Hopital du Bocage

Dijon, Cedex, France

Site Status

Hopital Saint Louis

Paris, Europe, France

Site Status

Centre Hospitalier Lyon-Sud -Hospices Civils de Lyon Groupement Hospitalier Sud

Pierre-Bénite, Paris, France

Site Status

Centre Hospitalier Universitaire de Bordeaux - Groupe Hospitalier Saint-André - Hôpital Saint-André

Bordeaux, , France

Site Status

Hopital Ambroise Pare

Boulogne-Billancourt, , France

Site Status

Centre Hospitalier Universitaire de Grenoble

La Tronche, , France

Site Status

Hopital Huriez - CHRU de Lille

Lille, , France

Site Status

Centre Leon-Berard (CLB)

Lyon, , France

Site Status

CHU Hotel Dieu

Nantes, , France

Site Status

Centre Hospitalier Universitaire de Rouen-Hopital Charles Nicolle

Rouen, , France

Site Status

Institut Claudius Regaud

Toulouse, , France

Site Status

Institut Gustave Roussy

Villejuif, , France

Site Status

University Hospital Frankfurt

Frankfurt, Hessen/Germany, Germany

Site Status

Hauttumorcentrum der Charite (HTCC)-Charite Universitatsmedizin Berlin

Berlin, , Germany

Site Status

Elbekliniken Buxtehude

Buxtehude, , Germany

Site Status

University Hospital Dresden

Dresden, , Germany

Site Status

Universitaetsklinik Essen

Essen, , Germany

Site Status

SRH Wald-Kliniken Gera GmbH

Gera, , Germany

Site Status

Hannover Medical School

Hanover, , Germany

Site Status

NCT Dermatoonkologie

Heidelberg, , Germany

Site Status

University of Kiel

Kiel, , Germany

Site Status

Universitaetsmedizin der Johannes Gutenberg-Universitaet Mainz

Mainz, , Germany

Site Status

Klinik Fur Dermatologie Und Allergollogie

Quedlinburg, , Germany

Site Status

University Hospital Tubingen

Tübingen, , Germany

Site Status

National and Kapodistrian University of Athens - School of Health Sciences - Faculty of Medicine

Athens, , Greece

Site Status

National and Kapodistrian University of Athens - School of Health Sciences

Athens, , Greece

Site Status

Andreas Sygros Hosptial-University of Athen

Athens, , Greece

Site Status

University General Hospital of Ioannina - Dermatology and Venereology Department

Ioannina, , Greece

Site Status

Policlinico S.Orsola-Malpighi U.O. Dermatologia - University of Bologna

Bologna, Bo, Italy

Site Status

Azienda Ospedaliera Spedali Civili di Brescia-Universita degli Studi Di Brescia

Brescia, Province Of Brescia, Italy

Site Status

U.O.Dermatologia Azienda Sanitaria Firenze Universita' Firenze

Florence, , Italy

Site Status

University L'Aquila

L’Aquila, , Italy

Site Status

Fondazione IRCCS Istituto Nazionale dei Tumori

Milan, , Italy

Site Status

U.O.S.C Di Oncologia Medica E Terapie Innovative

Napoli, , Italy

Site Status

Catholic University of the S.Heart

Roma, , Italy

Site Status

Catalan Institute of Oncology Badalona

Badalona, , Spain

Site Status

Hospital Clinic I Provincialde Barcelona

Barcelona, , Spain

Site Status

Hospital Universitario de Torrejon

Madrid, , Spain

Site Status

Hospital Universitario Virgen Macarena

Seville, , Spain

Site Status

University Hospital Zurich Usz

Zurich, , Switzerland

Site Status

Countries

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United States Austria Belgium Canada France Germany Greece Italy Spain Switzerland

References

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Stratigos AJ, Chen CI, Ivanescu C, Lewis KD, Peris K, Bechter O, Harnett J, Mastey V, Reaney M, Daskalopoulou C, LaFontaine PR, Konidaris G, Bury D, Yoo SY, Mohan K, Coates E, Bowler T, Fury MG, Sekulic A. Quality of life in cemiplimab-treated patients with locally advanced basal cell carcinoma in a Phase II clinical trial. Future Oncol. 2024;20(30):2249-2258. doi: 10.1080/14796694.2024.2358670. Epub 2024 Jul 29.

Reference Type DERIVED
PMID: 39073799 (View on PubMed)

Lewis KD, Peris K, Sekulic A, Stratigos AJ, Dunn L, Eroglu Z, Chang ALS, Migden MR, Yoo SY, Mohan K, Coates E, Okoye E, Bowler T, Baurain JF, Bechter O, Hauschild A, Butler MO, Hernandez-Aya L, Licitra L, Neves RI, Ruiz ES, Seebach F, Lowy I, Goncalves P, Fury MG. Final analysis of phase II results with cemiplimab in metastatic basal cell carcinoma after hedgehog pathway inhibitors. Ann Oncol. 2024 Feb;35(2):221-228. doi: 10.1016/j.annonc.2023.10.123. Epub 2023 Dec 9.

Reference Type DERIVED
PMID: 38072158 (View on PubMed)

Stratigos AJ, Sekulic A, Peris K, Bechter O, Prey S, Lewis KD, Basset-Seguin N, Chang ALS, Dalle S, Fernandez Orland A, Licitra L, Robert C, Ulrich C, Hauschild A, Migden MR, Dummer R, Yoo SY, Okoye E, Bassukas I, Loquai C, De Giorgi V, Eroglu Z, Gutzmer R, Ulrich J, Puig S, Inocencio TJ, Chen CI, LaFontaine PR, Seebach F, Lowy I, Fury MG. Phase 2 open-label, multicenter, single-arm study of cemiplimab in patients with locally advanced basal cell carcinoma after hedgehog inhibitor therapy: Extended follow-up. J Am Acad Dermatol. 2024 Feb;90(2):414-418. doi: 10.1016/j.jaad.2023.08.111. Epub 2023 Oct 14. No abstract available.

Reference Type DERIVED
PMID: 37839734 (View on PubMed)

Stratigos AJ, Sekulic A, Peris K, Bechter O, Prey S, Kaatz M, Lewis KD, Basset-Seguin N, Chang ALS, Dalle S, Orland AF, Licitra L, Robert C, Ulrich C, Hauschild A, Migden MR, Dummer R, Li S, Yoo SY, Mohan K, Coates E, Jankovic V, Fiaschi N, Okoye E, Bassukas ID, Loquai C, De Giorgi V, Eroglu Z, Gutzmer R, Ulrich J, Puig S, Seebach F, Thurston G, Weinreich DM, Yancopoulos GD, Lowy I, Bowler T, Fury MG. Cemiplimab in locally advanced basal cell carcinoma after hedgehog inhibitor therapy: an open-label, multi-centre, single-arm, phase 2 trial. Lancet Oncol. 2021 Jun;22(6):848-857. doi: 10.1016/S1470-2045(21)00126-1. Epub 2021 May 14.

Reference Type DERIVED
PMID: 34000246 (View on PubMed)

Li R, Lee G, Huang M, El-Sherief A. Rare basal cell metastasis of a basal-squamous skin collision tumour to the lung and axillary lymph node. BMJ Case Rep. 2019 Oct 3;12(10):e231487. doi: 10.1136/bcr-2019-231487.

Reference Type DERIVED
PMID: 31585957 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Related Links

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https://www.trialsummaries.com/

A Plain Language Summary is available on TrialSummaries.com

Other Identifiers

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2016-003122-16

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

R2810-ONC-1620

Identifier Type: -

Identifier Source: org_study_id

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