Study of REGN2810 in Patients With Advanced Cutaneous Squamous Cell Carcinoma

NCT ID: NCT02760498

Last Updated: 2025-05-28

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

432 participants

Study Classification

INTERVENTIONAL

Study Start Date

2016-04-07

Study Completion Date

2023-10-18

Brief Summary

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The goals of this study are to evaluate the clinical benefit and safety of cemiplimab in participants with metastatic (nodal or distant) Cutaneous Squamous Cell Carcinoma (CSCC), or unresectable locally advanced CSCC.

Detailed Description

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Conditions

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Advanced Cutaneous Squamous Cell Carcinoma

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Group 1 (Participants With mCSCC): Cemiplimab 3 mg/kg Q2W

Participants received cemiplimab 3 milligrams (mg)/kilogram (kg) intravenously (IV) every 2 weeks (Q2W) during each 8-week treatment cycle, for up to 96 weeks (12 cycles).

Group Type EXPERIMENTAL

cemiplimab

Intervention Type DRUG

Group 2 (Participants With laCSCC): Cemiplimab 3 mg/kg Q2W

Participants received cemiplimab 3 mg/kg IV Q2W during each 8-week treatment cycle, for up to 96 weeks (12 cycles).

Group Type EXPERIMENTAL

cemiplimab

Intervention Type DRUG

Group 3 (Participants With mCSCC): Cemiplimab 350 mg Q3W

Participants received cemiplimab 350 mg IV every 3 weeks (Q3W) during each 9-week treatment cycle, for up to 54 weeks (6 cycles).

Group Type EXPERIMENTAL

cemiplimab

Intervention Type DRUG

Group 4 (Participants With mCSCC and laCSCC): Cemiplimab 600 mg Q4W

Participants received cemiplimab 600 mg IV every 4 weeks (Q4W) during each 8-week treatment cycle, for up to 48 weeks (6 cycles).

Group Type EXPERIMENTAL

cemiplimab

Intervention Type DRUG

Group 5 (Participants With mCSCC and laCSCC): Cemiplimab SC + 350 mg Q3W

Participants received a single subcutaneous (SC) dose of cemiplimab followed by cemiplimab 350 mg IV Q3W during each 9-week treatment cycle, for up to 54 weeks (6 cycles).

Group Type EXPERIMENTAL

cemiplimab

Intervention Type DRUG

Group 6 (Participants With mCSCC and laCSCC): Cemiplimab 350 mg Q3W

Participants received cemiplimab 350 mg IV Q3W during each 9-week treatment cycle, for up to 108 weeks (12 cycles).

Group Type EXPERIMENTAL

cemiplimab

Intervention Type DRUG

Interventions

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cemiplimab

Intervention Type DRUG

Other Intervention Names

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REGN2810 Libtayo

Eligibility Criteria

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Inclusion Criteria

* At least 1 measurable lesion
* Eastern Cooperative Oncology Group (ECOG) performance status ≤1
* Adequate bone marrow function
* Adequate renal function
* Adequate hepatic function
* Archived or newly obtained tumor material
* Patients must consent to undergo biopsies of CSCC lesions (Groups 2, 4, and 6)
* Surgical or radiological treatment of lesions contraindicated

Exclusion Criteria

* Ongoing or recent (within 5 years) evidence of significant autoimmune disease that required treatment with systemic immunosuppressive treatments, which may suggest risk for immune-related adverse events
* Prior treatment with an agent that blocks the PD-1/PD-L1pathway
* Prior treatment with a BRAF inhibitor
* Prior treatment with other immune-modulating agents within fewer than 4 weeks prior to the first dose of cemiplimab, or associated with immune-mediated adverse events that were ≥ grade 1 within 90 days prior to the first dose of cemiplimab, or associated with toxicity that resulted in discontinuation of the immune-modulating agent. Examples of immune-modulating agents include therapeutic vaccines, cytokine treatments, or agents that target cytotoxic T-lymphocyte antigen 4 (CTLA-4), 4-1BB (CD137), or OX-40.
* Untreated brain metastasis(es) that may be considered active
* Immunosuppressive corticosteroid doses (\>10 mg prednisone daily or equivalent) within 4 weeks prior to the first dose of cemiplimab
* Infection with human immunodeficiency virus (HIV) and/or chronic/active infection with hepatitis B virus or hepatitis C virus
* History of non-infectious pneumonitis within the last 5 years
* Allergic reactions or acute hypersensitivity reaction attributed to antibody treatments
* Known allergy to doxycycline or tetracycline
* Patients with a history of solid organ transplant
* Any medical co-morbidity, physical examination finding, or metabolic dysfunction, or clinical laboratory abnormality that renders the patient unsuitable
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Regeneron Pharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Clinical Trial Management

Role: STUDY_DIRECTOR

Regeneron Pharmaceuticals

Locations

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Hospital Universitario Ramon y Cajal

Madrid, , Spain

Site Status

Hospital Universitario Fundacion Jimenez Diaz

Madrid, , Spain

Site Status

Hospital Universitario 12 de Octubre

Madrid, , Spain

Site Status

Hospital Universitario Marques de Valdecilla

Santander, , Spain

Site Status

Fundacion Instituto Valenciano de Oncología

Valencia, , Spain

Site Status

University of Arizona Cancer Center

Phoenix, Arizona, United States

Site Status

Mayo Clinic

Phoenix, Arizona, United States

Site Status

City of Hope Hospital

Duarte, California, United States

Site Status

University of California, Los Angeles

Los Angeles, California, United States

Site Status

Stanford University

Redwood City, California, United States

Site Status

University of California, San Diego

San Diego, California, United States

Site Status

University of Colorado, Denver

Aurora, Colorado, United States

Site Status

Mount Sinai Comprehensive Cancer Center

Miami Beach, Florida, United States

Site Status

H. Lee Moffitt Cancer Center

Tampa, Florida, United States

Site Status

Northwestern University

Chicago, Illinois, United States

Site Status

Norton Cancer Institute

Louisville, Kentucky, United States

Site Status

Massachusetts General Hospital

Boston, Massachusetts, United States

Site Status

Dana-Farber Cancer Institute

Boston, Massachusetts, United States

Site Status

Barbara Ann Karmanos Cancer Institute

Detroit, Michigan, United States

Site Status

St. Louis University

St Louis, Missouri, United States

Site Status

Washington University in St. Louis

St Louis, Missouri, United States

Site Status

Nebraska Methodist Hospital

Omaha, Nebraska, United States

Site Status

New York University

New York, New York, United States

Site Status

Memorial Sloan Kettering Cancer Center

New York, New York, United States

Site Status

University of Rochester Medical Center

Rochester, New York, United States

Site Status

Cleveland Clinic

Cleveland, Ohio, United States

Site Status

St. Luke's Hematology Oncology Specialists

Easton, Pennsylvania, United States

Site Status

Penn State Hershey Medical Center

Hershey, Pennsylvania, United States

Site Status

Dermatology and Laser Center of Charleston

Charleston, South Carolina, United States

Site Status

MD Anderson Cancer Center

Houston, Texas, United States

Site Status

Huntsman Cancer Institute

Salt Lake City, Utah, United States

Site Status

The Canberra Hospital

Garran, Australian Capital Territory, Australia

Site Status

Gosford Hospital

Gosford, New South Wales, Australia

Site Status

Royal North Shore Hospital

St Leonards, New South Wales, Australia

Site Status

Calvary Mater Newcastle

Waratah, New South Wales, Australia

Site Status

Royal Brisbane & Women's Hospital

Herston, Queensland, Australia

Site Status

Princess Alexandra Hospital

Woolloongabba, Queensland, Australia

Site Status

Adelaide Cancer Centre

Kurralta Park, South Australia, Australia

Site Status

Peter MacCallum Cancer Centre

Melbourne, Victoria, Australia

Site Status

Border Medical Oncology

Wodonga, Victoria, Australia

Site Status

Sir Charles Gairdner Hospital

Nedlands, Western Australia, Australia

Site Status

Hospital de Clinicas de Porto Alegre

Porto Alegre, Rio Grande do Sul, Brazil

Site Status

Liga Paranaense de Combate Ao Cancer - Hospital Erasto Gaertner

Curitiba, , Brazil

Site Status

Fundação São Francisco Xavier-Hospital Márcio Cunha

Ipatinga, , Brazil

Site Status

Animi

Lages, , Brazil

Site Status

Fundação Antônio Prudente - AC Camargo Câncer Center

São Paulo, , Brazil

Site Status

Instituto do Cancer do Estado de São Paulo ICESP

São Paulo, , Brazil

Site Status

Hôpital Claude Huriez

Lille, Nord, France

Site Status

Hopital Avicenne

Bobigny, , France

Site Status

Hôpital Saint-André

Bordeaux, , France

Site Status

CHU Dijon Bourgogne

Dijon, , France

Site Status

CHRU Grenoble

Grenoble, , France

Site Status

Hopitaux de La Timone

Marseille, , France

Site Status

Centre Hospitalier Universitaire de Nantes

Nantes, , France

Site Status

Hopital Cochin

Paris, , France

Site Status

Hôpital Saint Louis

Paris, , France

Site Status

Centre Hospitalier Lyon Sud

Pierre-Bénite, , France

Site Status

Institut Gustave Roussy

Villejuif, , France

Site Status

Universitätsklinikum Tübingen

Tübingen, Baden-Wurttemberg, Germany

Site Status

LMU Klinikum der Universität München

Munich, Bavaria, Germany

Site Status

Medizinische Hochschule Hannover

Hanover, Lower Saxony, Germany

Site Status

Universitätsklinikum Essen

Essen, North Rhine-Westphalia, Germany

Site Status

Universitätsklinikum Carl Gustav Carus

Dresden, Saxony, Germany

Site Status

Universitatsklinikum Schleswig-Holstein

Kiel, Schleswig-Holstein, Germany

Site Status

Charitè Campus Mitte

Berlin, , Germany

Site Status

SRH Wald-Klinikum Gera

Gera, , Germany

Site Status

Andreas Sygros Hosptial-University of Athen

Athens, , Greece

Site Status

Istituto Nazionale Per Lo Studio E La Cura Dei Tumori Fondazione Giovanni Pascale

Napoli, Campania, Italy

Site Status

Istituto Oncologico Veneto - I.R.C.C.S.

Padua, Veneto, Italy

Site Status

ASST degli Spedali Civili di Brescia - Spedali Civili di Brescia

Brescia, , Italy

Site Status

Ospedale San Salvatore

L’Aquila, , Italy

Site Status

Istituto Europeo Di Oncologia

Milan, , Italy

Site Status

Fondazione Policlinico Universitario A Gemelli

Roma, , Italy

Site Status

ICO l'Hospitalet - Hospital Duran i Reynals

L'Hospitalet de Llobregat, Barelona, Spain

Site Status

Hospital Clinic de Barcelona

Barcelona, Catalonia, Spain

Site Status

Hospital Universitario Vall d'Hebron

Barcelona, , Spain

Site Status

Hospital Universitario Germans Trias i Pujol

Barcelona, , Spain

Site Status

C.H. Regional Reina Sofia - PPDS

Córdoba, , Spain

Site Status

Countries

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United States Australia Brazil France Germany Greece Italy Spain

References

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Rischin D, Hughes BGM, Basset-Seguin N, Schadendorf D, Bowyer S, Trabelsi Messai S, Meier F, Eigentler TK, Casado Echarren V, Stein B, Beylot-Barry M, Dalac S, Dreno B, Migden MR, Hauschild A, Schmults CD, Lim AM, Yoo SY, Paccaly AJ, Papachristos A, Nguyen JH, Okoye E, Seebach F, Booth J, Lowy I, Fury MG, Guminski A. High response rate with extended dosing of cemiplimab in advanced cutaneous squamous cell carcinoma. J Immunother Cancer. 2024 Mar 11;12(3):e008325. doi: 10.1136/jitc-2023-008325.

Reference Type DERIVED
PMID: 38471711 (View on PubMed)

Rischin D, Khushalani NI, Schmults CD, Guminski A, Chang ALS, Lewis KD, Lim AM, Hernandez-Aya L, Hughes BGM, Schadendorf D, Hauschild A, Thai AA, Stankevich E, Booth J, Yoo SY, Li S, Chen Z, Okoye E, Chen CI, Mastey V, Sasane M, Lowy I, Fury MG, Migden MR. Integrated analysis of a phase 2 study of cemiplimab in advanced cutaneous squamous cell carcinoma: extended follow-up of outcomes and quality of life analysis. J Immunother Cancer. 2021 Aug;9(8):e002757. doi: 10.1136/jitc-2021-002757.

Reference Type DERIVED
PMID: 34413166 (View on PubMed)

Paccaly AJ, Migden MR, Papadopoulos KP, Yang F, Davis JD, Rippley RK, Lowy I, Fury MG, Stankevich E, Rischin D. Fixed Dose of Cemiplimab in Patients with Advanced Malignancies Based on Population Pharmacokinetic Analysis. Adv Ther. 2021 May;38(5):2365-2378. doi: 10.1007/s12325-021-01638-5. Epub 2021 Mar 25.

Reference Type DERIVED
PMID: 33768419 (View on PubMed)

Rischin D, Migden MR, Lim AM, Schmults CD, Khushalani NI, Hughes BGM, Schadendorf D, Dunn LA, Hernandez-Aya L, Chang ALS, Modi B, Hauschild A, Ulrich C, Eigentler T, Stein B, Pavlick AC, Geiger JL, Gutzmer R, Alam M, Okoye E, Mathias M, Jankovic V, Stankevich E, Booth J, Li S, Lowy I, Fury MG, Guminski A. Phase 2 study of cemiplimab in patients with metastatic cutaneous squamous cell carcinoma: primary analysis of fixed-dosing, long-term outcome of weight-based dosing. J Immunother Cancer. 2020 Jun;8(1):e000775. doi: 10.1136/jitc-2020-000775.

Reference Type DERIVED
PMID: 32554615 (View on PubMed)

Migden MR, Khushalani NI, Chang ALS, Lewis KD, Schmults CD, Hernandez-Aya L, Meier F, Schadendorf D, Guminski A, Hauschild A, Wong DJ, Daniels GA, Berking C, Jankovic V, Stankevich E, Booth J, Li S, Weinreich DM, Yancopoulos GD, Lowy I, Fury MG, Rischin D. Cemiplimab in locally advanced cutaneous squamous cell carcinoma: results from an open-label, phase 2, single-arm trial. Lancet Oncol. 2020 Feb;21(2):294-305. doi: 10.1016/S1470-2045(19)30728-4. Epub 2020 Jan 14.

Reference Type DERIVED
PMID: 31952975 (View on PubMed)

Migden MR, Rischin D, Schmults CD, Guminski A, Hauschild A, Lewis KD, Chung CH, Hernandez-Aya L, Lim AM, Chang ALS, Rabinowits G, Thai AA, Dunn LA, Hughes BGM, Khushalani NI, Modi B, Schadendorf D, Gao B, Seebach F, Li S, Li J, Mathias M, Booth J, Mohan K, Stankevich E, Babiker HM, Brana I, Gil-Martin M, Homsi J, Johnson ML, Moreno V, Niu J, Owonikoko TK, Papadopoulos KP, Yancopoulos GD, Lowy I, Fury MG. PD-1 Blockade with Cemiplimab in Advanced Cutaneous Squamous-Cell Carcinoma. N Engl J Med. 2018 Jul 26;379(4):341-351. doi: 10.1056/NEJMoa1805131. Epub 2018 Jun 4.

Reference Type DERIVED
PMID: 29863979 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Related Links

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https://www.trialsummaries.com/

A Plain Language Summary is available on TrialSummaries.com

Other Identifiers

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2016-000105-36

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

R2810-ONC-1540

Identifier Type: -

Identifier Source: org_study_id

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