A Study of Nivolumab in Combination With Ipilimumab in Participants With Advanced Hepatocellular Carcinoma

NCT ID: NCT04039607

Last Updated: 2025-08-03

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

ACTIVE_NOT_RECRUITING

Clinical Phase

PHASE3

Total Enrollment

732 participants

Study Classification

INTERVENTIONAL

Study Start Date

2019-09-30

Study Completion Date

2026-09-30

Brief Summary

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The main purpose of this study is to compare the overall survival (OS) of nivolumab plus ipilimumab versus standard of care (SOC) (sorafenib or lenvatinib) in all randomized participants with advanced hepatocellular carcinoma (HCC) who have not received prior systemic therapy.

Detailed Description

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Conditions

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Hepatocellular Carcinoma

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Nivolumab + Ipilimumab

Group Type EXPERIMENTAL

Nivolumab

Intervention Type DRUG

Participants will receive nivolumab as intravenous (IV) infusion.

Ipilimumab

Intervention Type DRUG

Participants will receive ipilimumab as IV infusion.

Sorafenib/lenvatinib

Group Type ACTIVE_COMPARATOR

Sorafenib

Intervention Type DRUG

Participants will receive sorafenib as oral tablets.

lenvatinib

Intervention Type DRUG

Participants will receive lenvatinib as oral capsules.

Interventions

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Nivolumab

Participants will receive nivolumab as intravenous (IV) infusion.

Intervention Type DRUG

Ipilimumab

Participants will receive ipilimumab as IV infusion.

Intervention Type DRUG

Sorafenib

Participants will receive sorafenib as oral tablets.

Intervention Type DRUG

lenvatinib

Participants will receive lenvatinib as oral capsules.

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Participants must have a diagnosis of HCC based on histological confirmation
* Participants must have an advanced HCC
* Participants must have at least one Response Evaluation Criteria in Solid Tumors (RECIST) 1.1 measurable previously untreated lesion
* Child-Pugh score 5 or 6
* Eastern Cooperative Oncology Group (ECOG) performance status(PS) 0 or 1

Exclusion Criteria

* Known fibrolamellar HCC, sarcomatoid HCC, or mixed cholangiocarcinoma and HCC
* Prior liver transplant
* Episodes of hepatic encephalopathy (greater than or equal to \[\>=\] Grade 2) within 12 months prior to randomization
* Active brain metastases or leptomeningeal metastases
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Bristol-Myers Squibb

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Bristol-Myers Squibb

Role: STUDY_DIRECTOR

Bristol-Myers Squibb

Locations

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Local Institution - 0292

Tucson, Arizona, United States

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Coronado, California, United States

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Duarte, California, United States

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Washington D.C., District of Columbia, United States

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Louisville, Kentucky, United States

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Baltimore, Maryland, United States

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Ann Arbor, Michigan, United States

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Detroit, Michigan, United States

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Newark, New Jersey, United States

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Toledo, Ohio, United States

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Pittsburgh, Pennsylvania, United States

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Dallas, Texas, United States

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Houston, Texas, United States

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Lubbock, Texas, United States

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Salt Lake City, Utah, United States

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Caba, Buenos Aires, Argentina

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Pilar, Buenos Aires, Argentina

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Rosario, Santa Fe Province, Argentina

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Buenos Aires, , Argentina

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San Miguel de Tucumán, , Argentina

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Kogarah, New South Wales, Australia

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Liverpool, New South Wales, Australia

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Westmead, New South Wales, Australia

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Birtinya, Queensland, Australia

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Herston, Queensland, Australia

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Adelaide, South Australia, Australia

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Clayton, Victoria, Australia

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Fitzroy, Victoria, Australia

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Melbourne, Victoria, Australia

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St Albans, Victoria, Australia

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Sankt Pölten, Lower Austria, Austria

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Wiener Neustadt, Lower Austria, Austria

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Graz, , Austria

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Klagenfurt, , Austria

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Vienna, , Austria

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Brussels, , Belgium

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Federal District, , Belgium

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Ghent, , Belgium

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Ghent, , Belgium

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Haine-Saint-Paul, , Belgium

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Leuven, , Belgium

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Liège, , Belgium

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Vitória, Espírito Santo, Brazil

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Salvador, Estado de Bahia, Brazil

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Salvador, Estado de Bahia, Brazil

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Brasília, Federal District, Brazil

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Ijuí, Rio Grande do Sul, Brazil

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Pelotas, Rio Grande do Sul, Brazil

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Jaú, São Paulo, Brazil

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Hospital de Base de Sao Jose do Rio Preto

São José do Rio Preto, São Paulo, Brazil

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Paranã, , Brazil

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Rio de Janeiro, , Brazil

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São Paulo, , Brazil

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São Paulo, , Brazil

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São Paulo, , Brazil

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Edmonton, Alberta, Canada

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La Serena, Coquimbo Region, Chile

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Temuco, Región de la Araucanía, Chile

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Viña del Mar, Región de Valparaíso, Chile

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Viña del Mar, Región de Valparaíso, Chile

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Santiago, RM, Chile

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Santiago, Santiago Metropolitan, Chile

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Santiago, Santiago Metropolitan, Chile

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Santiago, Santiago Metropolitan, Chile

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Hefei, Anhui, China

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Hefei, Anhui, China

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Beijing, Beijing Municipality, China

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Beijing, Beijing Municipality, China

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Fuzhou, Fujian, China

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Fuzhou, Fujian, China

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Guangzhou, Guangdong, China

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Guangzhou, Guangdong, China

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Harbin, Heilongjiang, China

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Changsha, Hunan, China

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Changsha, Hunan, China

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Nanjing, Jiangsu, China

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Nanchang, Jiangxi, China

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Nanchang, Jiangxi, China

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Changchun, Jilin, China

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Changchun, Jilin, China

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Dalian, Liaoning, China

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Shenyang, Liaoning, China

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Shenyang, Liaoning, China

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Xi'an, Shaanxi, China

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Xi'an, Shan3xi, China

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Xi'an, Shan3xi, China

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Qingdao, Shandong, China

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Shanghai, Shanghai Municipality, China

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Chongqing, Sichuan, China

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Hangzhou, Zhejiang, China

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Hangzhou, Zhejiang, China

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Prague, Prague, Czechia

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Brno, , Czechia

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Amiens, , France

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Caen, , France

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Clichy, , France

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Dijon, , France

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Grenoble, , France

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Lyon, , France

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Marseille, , France

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Montpellier, , France

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Nice, , France

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Pessac, , France

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Poitiers, , France

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Toulouse, , France

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Vandœuvre-lès-Nancy, , France

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Villejuif, , France

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Frankfurt am Main, Hesse, Germany

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Bonn, , Germany

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Cologne, , Germany

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Essen, , Germany

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Freiburg im Breisgau, , Germany

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Hamburg, , Germany

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Hanover, , Germany

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Leipzig, , Germany

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Mainz, , Germany

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Mannheim, , Germany

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München, , Germany

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North Rhine-Westphalia, , Germany

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Hong Kong, , Hong Kong

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Hong Kong, , Hong Kong

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Meldola, Forli-Cesena, Italy

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Rozzano, Milano, Italy

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Candiolo, , Italy

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Milan, , Italy

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Novara, , Italy

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Padua, , Italy

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Parma, , Italy

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Roma, , Italy

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Rome, , Italy

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Siena, , Italy

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Vicenza, , Italy

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Kashiwa-shi, Chiba, Japan

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Matsuyama, Ehime, Japan

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Kanazawa, Ishikawa-ken, Japan

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Yokohama, Kanagawa, Japan

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Yokohama, Kanagawa, Japan

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Kyoto, Kyoto, Japan

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Kashihara, Nara, Japan

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Abeno-ku, Osaka, Japan

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Sayama, Osaka, Japan

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Saga, Saga-ken, Japan

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Iruma-gun, Saitama, Japan

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Izunokuni-shi, Shizuoka, Japan

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Minato, Tokyo, Japan

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Minato-ku, Tokyo, Japan

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Mitaka, Tokyo, Japan

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Musashino-shi, Tokyo, Japan

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Chiba, , Japan

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Fukuoka, , Japan

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Hiroshima, , Japan

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Sapporo, , Japan

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Christchurch, Canterbury, New Zealand

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Auckland, , New Zealand

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Gdansk, , Poland

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Otwock, , Poland

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Warsaw, , Poland

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Rio Piedras, , Puerto Rico

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San Juan, , Puerto Rico

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Craiova, Dolj, Romania

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Bucharest, , Romania

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Cluj-Napoca, , Romania

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Craiova, , Romania

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Timișoara, , Romania

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Arkhangelsk, , Russia

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Barnaul, , Russia

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Chelyabinsk, , Russia

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Moscow, , Russia

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Pyatigorsk, , Russia

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Saint Petersburg, , Russia

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Saint Petersburg, , Russia

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Sochi, , Russia

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Singapore, , Singapore

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Singapore, , Singapore

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Singapore, , Singapore

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Seongnam-si, Gyeonggi-do, South Korea

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Guro-gu, Seoul, South Korea

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Jongno-gu, Seoul, South Korea

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Busan, , South Korea

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Gyeonggi-do, , South Korea

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Gyeongsangnam-do, , South Korea

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Seoul, , South Korea

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Seoul, , South Korea

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Seoul, , South Korea

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Barcelona, , Spain

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Barcelona, , Spain

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Barcelona, , Spain

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Córdoba, , Spain

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El Palmar, , Spain

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Madrid, , Spain

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Madrid, , Spain

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Madrid, , Spain

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Majadahonda, , Spain

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Pamplona, , Spain

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Santander, , Spain

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Zaragoza, , Spain

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Bern, , Switzerland

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Kaohsiung City, , Taiwan

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Kaohsiung City, , Taiwan

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Taichung, , Taiwan

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Taichung, , Taiwan

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Tainan City, , Taiwan

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Tainan City, , Taiwan

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Taipei, , Taiwan

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Taipei, , Taiwan

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Taoyuan District, , Taiwan

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London, Greater London, United Kingdom

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Guildford, Surrey, United Kingdom

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Local Institution - 0160

Edinburgh, , United Kingdom

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Local Institution - 0129

London, , United Kingdom

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Countries

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United States Argentina Australia Austria Belgium Brazil Canada Chile China Czechia France Germany Hong Kong Italy Japan New Zealand Poland Puerto Rico Romania Russia Singapore South Korea Spain Switzerland Taiwan United Kingdom

References

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Yau T, Galle PR, Decaens T, Sangro B, Qin S, da Fonseca LG, Karachiwala H, Blanc JF, Park JW, Gane E, Pinter M, Pena AM, Ikeda M, Tai D, Santoro A, Pizarro G, Chiu CF, Schenker M, He A, Chon HJ, Wojcik-Tomaszewska J, Verset G, Wang QQ, Stromko C, Neely J, Singh P, Jimenez Exposito MJ, Kudo M; CheckMate 9DW investigators. Nivolumab plus ipilimumab versus lenvatinib or sorafenib as first-line treatment for unresectable hepatocellular carcinoma (CheckMate 9DW): an open-label, randomised, phase 3 trial. Lancet. 2025 May 24;405(10492):1851-1864. doi: 10.1016/S0140-6736(25)00403-9. Epub 2025 May 8.

Reference Type DERIVED
PMID: 40349714 (View on PubMed)

Related Links

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Other Identifiers

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CA209-9DW

Identifier Type: -

Identifier Source: org_study_id

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