An Investigational Immuno-therapy Study of Nivolumab Compared to Sorafenib as a First Treatment in Patients With Advanced Hepatocellular Carcinoma

NCT ID: NCT02576509

Last Updated: 2025-02-17

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

743 participants

Study Classification

INTERVENTIONAL

Study Start Date

2015-12-07

Study Completion Date

2024-02-07

Brief Summary

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The purpose of this study is to determine if nivolumab or sorafenib is more effective in the treatment of Advanced Hepatocellular Carcinoma.

Detailed Description

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Conditions

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Hepatocellular Carcinoma

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Nivolumab

Nivolumab specified dose on specified days

Group Type EXPERIMENTAL

Nivolumab

Intervention Type DRUG

Specified Dose on Specified Days

Sorafenib

Sorafenib specified dose on specified days

Group Type ACTIVE_COMPARATOR

Sorafenib

Intervention Type DRUG

Specified Dose on Specified Days

Interventions

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Nivolumab

Specified Dose on Specified Days

Intervention Type DRUG

Sorafenib

Specified Dose on Specified Days

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Histologically confirmed advanced hepatocellular carcinoma, not eligible for surgical and/or locoregional therapies; or progressive disease after surgical and /or locoregional therapies
* Locoregional therapy for hepatocellular carcinoma (HCC) must be completed at least 4 weeks prior to the baseline scan
* Child-Pugh Class A
* Eastern Cooperative Oncology Group (ECOG) performance status (PS) 0 or 1

Exclusion Criteria

* Known fibrolamellar HCC, sarcomatoid HCC, or mixed cholangiocarcinoma and HCC
* Prior liver transplant
* Active, known, or suspected autoimmune disease
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Ono Pharmaceutical Co. Ltd

INDUSTRY

Sponsor Role collaborator

Bristol-Myers Squibb

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Bristol Myers Squibb

Role: STUDY_DIRECTOR

Bristol-Myers Squibb

Locations

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Local Institution - 0066

Birmingham, Alabama, United States

Site Status

Local Institution - 0020

Los Angeles, California, United States

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Local Institution - 0015

San Francisco, California, United States

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Local Institution - 0084

San Francisco, California, United States

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Local Institution - 0061

Chicago, Illinois, United States

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Ochsner Clinic Foundation

New Orleans, Louisiana, United States

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Local Institution - 0083

New York, New York, United States

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Local Institution - 0093

New York, New York, United States

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Local Institution - 0016

Charlotte, North Carolina, United States

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Local Institution - 0095

Philadelphia, Pennsylvania, United States

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Local Institution - 0019

Philadelphia, Pennsylvania, United States

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UT Southwestern Medical Center

Dallas, Texas, United States

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Local Institution - 0017

San Antonio, Texas, United States

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Scott & White Memorial Hospital And Clinic

Temple, Texas, United States

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Local Institution - 0026

Seattle, Washington, United States

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University of Washington - Seattle Cancer Care Alliance

Seattle, Washington, United States

Site Status

Local Institution - 0050

Madison, Wisconsin, United States

Site Status

Local Institution - 0005

Camperdown, New South Wales, Australia

Site Status

Local Institution - 0007

Adelaide, South Australia, Australia

Site Status

Local Institution - 0001

Clayton, Victoria, Australia

Site Status

Local Institution - 0002

Heidelberg, Victoria, Australia

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Local Institution - 0003

Prahran, Victoria, Australia

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Local Institution - 0008

Nedlands, Western Australia, Australia

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Local Institution - 0039

Graz, , Austria

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Local Institution - 0038

Vienna, , Austria

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Local Institution - 0075

Brussels, , Belgium

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Local Institution - 0091

Leuven, , Belgium

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Local Institution - 0077

Liège, , Belgium

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Local Institution - 0043

Calgary, Alberta, Canada

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Local Institution - 0044

Vancouver, British Columbia, Canada

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Local Institution - 0042

Québec, Quebec, Canada

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Local Institution - 0164

Hefei, Anhui, China

Site Status

Local Institution - 0139

Beijing, Beijing Municipality, China

Site Status

Local Institution - 0137

Beijing, Beijing Municipality, China

Site Status

Local Institution - 0140

Beijing, Beijing Municipality, China

Site Status

Local Institution - 0141

Beijing, Beijing Municipality, China

Site Status

Local Institution - 0152

Fuzhou, Fujian, China

Site Status

Local Institution - 0161

Guangzhou, Guangdong, China

Site Status

Local Institution - 0157

Guangzhou, Guangdong, China

Site Status

Local Institution - 0144

Guangzhou, Guangdong, China

Site Status

Local Institution - 0158

Nanning, Guangxi, China

Site Status

Local Institution - 0142

Harbin, Heilongjiang, China

Site Status

Local Institution - 0148

Changsha, Hunan, China

Site Status

Local Institution - 0162

Changsha, Hunan, China

Site Status

Local Institution - 0169

Changzhou, Jiangsu, China

Site Status

Local Institution - 0135

Nanjing, Jiangsu, China

Site Status

Local Institution - 0136

Changchun, Jilin, China

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Local Institution - 0163

Changchun, Jilin, China

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Local Institution - 0166

Dalian, Liaoning, China

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Local Institution - 0138

Xi'an, Shan3xi, China

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Local Institution - 0145

Shanghai, Shanghai Municipality, China

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Local Institution - 0151

Shanghai, Shanghai Municipality, China

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Local Institution - 0159

Tianjin, Tianjin Municipality, China

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Local Institution - 0173

Hangzhou, Zhejiang, China

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Local Institution - 0146

Hangzhou, Zhejiang, China

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Local Institution - 0029

Brno, , Czechia

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Local Institution - 0027

Hradec Králové, , Czechia

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Local Institution - 0028

Olomouc, , Czechia

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Local Institution - 0071

La Tronche, , France

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Local Institution - 0072

Lille, , France

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Local Institution - 0069

Lyon, , France

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Local Institution - 0073

Montpellier, , France

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Local Institution - 0067

Paris, , France

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Local Institution - 0068

Pessac, , France

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Local Institution - 0070

Rennes, , France

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Local Institution - 0074

Toulouse, , France

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Local Institution - 0036

Berlin, , Germany

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Local Institution - 0037

Essen, , Germany

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Local Institution - 0167

Frankfurt, , Germany

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Local Institution - 0034

Hamburg, , Germany

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Local Institution - 0031

Leipzig, , Germany

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Local Institution - 0035

Mainz, , Germany

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Local Institution - 0033

Munich, , Germany

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Local Institution - 0032

Regensburg, , Germany

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Local Institution - 0030

Tübingen, , Germany

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Local Institution - 0011

Hong Kong, , Hong Kong

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Local Institution - 0012

Hong Kong, , Hong Kong

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Local Institution - 0082

Haifa, , Israel

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Local Institution - 0060

Jerusalem, , Israel

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Local Institution - 0058

Petah Tikva, , Israel

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Local Institution - 0059

Tel Aviv, , Israel

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Local Institution - 0054

Benevento, , Italy

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Local Institution - 0062

Bergamo, , Italy

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Local Institution - 0055

Milan, , Italy

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Local Institution - 0063

Orbassano, , Italy

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Local Institution - 0064

Siena, , Italy

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Local Institution - 0100

Chiba, Chiba, Japan

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Local Institution - 0103

Matsuyama, Ehime, Japan

Site Status

Local Institution - 0107

Kurume-shi, Fukuoka, Japan

Site Status

Local Institution - 0127

Ogaki-shi, Gifu, Japan

Site Status

Local Institution - 0102

Sapporo, Hokkaido, Japan

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Local Institution - 0130

Sapporo, Hokkaido, Japan

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Local Institution - 0105

Kanazawa, Ishikawa-ken, Japan

Site Status

Local Institution - 0110

Kawasaki-shi, Kanagawa, Japan

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Local Institution - 0112

Yokohama, Kanagawa, Japan

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Local Institution - 0104

Yokohama, Kanagawa, Japan

Site Status

Local Institution - 0111

Kyoto, Kyoto, Japan

Site Status

Local Institution - 0106

Osaka-Sayama-Shi, Osaka, Japan

Site Status

Local Institution - 0113

Suita, Osaka, Japan

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Local Institution - 0115

Saga, Saga-ken, Japan

Site Status

Local Institution - 0131

Chiyoda-ku, Tokyo, Japan

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Local Institution - 0114

Mitaka-shi, Tokyo, Japan

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Local Institution - 0108

Musashino-shi, Tokyo, Japan

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Local Institution - 0126

Shinjuku-ku, Tokyo, Japan

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Local Institution - 0101

Hiroshima, , Japan

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Local Institution - 0023

Gdansk, , Poland

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Local Institution - 0056

Warsaw, , Poland

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Local Institution - 0045

Wroclaw, , Poland

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Local Institution - 0096

Moscow, , Russia

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Local Institution - 0013

Singapore, , Singapore

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Local Institution - 0014

Singapore, , Singapore

Site Status

Local Institution - 0117

Seoul, Seocho-gu, South Korea

Site Status

Local Institution - 0125

Daegu, , South Korea

Site Status

Local Institution - 0116

Goyang-si, , South Korea

Site Status

Local Institution - 0118

Jeollanam-do, , South Korea

Site Status

Local Institution - 0123

Seoul, , South Korea

Site Status

Local Institution - 0119

Seoul, , South Korea

Site Status

Local Institution - 0122

Seoul, , South Korea

Site Status

Local Institution - 0124

Seoul, , South Korea

Site Status

Local Institution - 0065

Alicante, , Spain

Site Status

Local Institution - 0085

Majadahonda - Madrid, , Spain

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Local Institution - 0009

Pamplona, , Spain

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Local Institution - 0010

Santiago Compostela, , Spain

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Local Institution - 0088

Gothenburg, , Sweden

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Local Institution - 0087

Stockholm, , Sweden

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Local Institution - 0040

Basel, , Switzerland

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Local Institution - 0041

Bern, , Switzerland

Site Status

Local Institution - 0129

Kaohsiung County, , Taiwan

Site Status

Local Institution - 0133

Taichung, , Taiwan

Site Status

Local Institution - 0121

Tainan City, , Taiwan

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Local Institution - 0132

Tainan City, , Taiwan

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Local Institution - 0099

Taipei, , Taiwan

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Local Institution - 0120

Taipei, , Taiwan

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Local Institution - 0128

Taoyuan, , Taiwan

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Local Institution - 0080

London, Greater London, United Kingdom

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Local Institution - 0078

London, Greater London, United Kingdom

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Local Institution - 0079

Glasgow, Lanarkshire, United Kingdom

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Local Institution - 0081

Liverpool, , United Kingdom

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Countries

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United States Australia Austria Belgium Canada China Czechia France Germany Hong Kong Israel Italy Japan Poland Russia Singapore South Korea Spain Sweden Switzerland Taiwan United Kingdom

References

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Zhou X, Cao J, Topatana W, Xie T, Chen T, Hu J, Li S, Juengpanic S, Lu Z, Zhang B, Wang K, Feng X, Shen J, Chen M. Evaluation of PD-L1 as a biomarker for immunotherapy for hepatocellular carcinoma: systematic review and meta-analysis. Immunotherapy. 2023 Apr;15(5):353-365. doi: 10.2217/imt-2022-0168. Epub 2023 Feb 27.

Reference Type DERIVED
PMID: 36852452 (View on PubMed)

Li Y, Liang X, Li H, Chen X. Atezolizumab plus bevacizumab versus nivolumab as first-line treatment for advanced or unresectable hepatocellular carcinoma: A cost-effectiveness analysis. Cancer. 2022 Nov 15;128(22):3995-4003. doi: 10.1002/cncr.34457. Epub 2022 Sep 16.

Reference Type DERIVED
PMID: 36111952 (View on PubMed)

Shi J, Liu J, Tu X, Li B, Tong Z, Wang T, Zheng Y, Shi H, Zeng X, Chen W, Yin W, Fang W. Single-cell immune signature for detecting early-stage HCC and early assessing anti-PD-1 immunotherapy efficacy. J Immunother Cancer. 2022 Jan;10(1):e003133. doi: 10.1136/jitc-2021-003133.

Reference Type DERIVED
PMID: 35101942 (View on PubMed)

Yau T, Park JW, Finn RS, Cheng AL, Mathurin P, Edeline J, Kudo M, Harding JJ, Merle P, Rosmorduc O, Wyrwicz L, Schott E, Choo SP, Kelley RK, Sieghart W, Assenat E, Zaucha R, Furuse J, Abou-Alfa GK, El-Khoueiry AB, Melero I, Begic D, Chen G, Neely J, Wisniewski T, Tschaika M, Sangro B. Nivolumab versus sorafenib in advanced hepatocellular carcinoma (CheckMate 459): a randomised, multicentre, open-label, phase 3 trial. Lancet Oncol. 2022 Jan;23(1):77-90. doi: 10.1016/S1470-2045(21)00604-5. Epub 2021 Dec 13.

Reference Type DERIVED
PMID: 34914889 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Related Links

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Other Identifiers

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CA209-459

Identifier Type: -

Identifier Source: org_study_id

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