A Phase III Study of Sorafenib in Patients With Advanced Hepatocellular Carcinoma

NCT ID: NCT00105443

Last Updated: 2014-10-31

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

View full results

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

602 participants

Study Classification

INTERVENTIONAL

Study Start Date

2005-03-31

Study Completion Date

2008-11-30

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

The purpose of the study is: Find out if patients receiving sorafenib will live longer. Find out if sorafenib has any effect on patient reported outcomes. Find out if sorafenib prevents the growth of or shrinks liver tumors and/or their metastases. Determine the pharmacokinetics (PK) in patients with liver cancer.

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

The following abbreviations were used in the Adverse Event section:

* international normalized ratio (inr)
* Common Terminology Criteria for Adverse Events (ctcae)
* Not Otherwise Specified (nos)
* Gastrointestinal (gi)
* Central nervous system (cns)
* Absolute Neutrophil Count (anc)
* Alanine aminotransferase (ALT)
* Aspartate aminotransferase (AST)
* Creatine phosphokinase (cpk)
* Gammaglutamyltransferase (ggt)
* Genitourinary (gu)
* Atrioventricular (av)

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

Carcinoma, Hepatocellular

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

Sorafenib (Nexavar, BAY43-9006)

Sorafenib 400 mg was administered orally at a dose of 400 mg (2 x 200 mg tablets) twice daily; 2 dose reductions to predefined levels of 400 mg once daily (OD) and 400 mg every other day were permitted for adverse events related to study treatment. Follow-up / Open Label phase: Subjects on sorafenib who continued the study, continued on the same dose of sorafenib as during the double-blind study.

Group Type EXPERIMENTAL

Sorafenib (Nexavar, BAY43-9006)

Intervention Type DRUG

Sorafenib 400 mg was administered orally at a dose of 400 mg (2 x 200 mg tablets) twice daily (bid); 2 dose reductions to predefined levels of 400 mg once daily (OD) and 400 mg every other day were permitted for adverse events related to study treatment.

Placebo

Sorafenib-matching placebo tablets were orally administered twice daily (bid). Follow-up / Open Label phase: Subjects on placebo who chose to switch to sorafenib, received an oral dose of 400 mg (2 x 200 mg tablets) bid; similar to the double-blind study.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Sorafenib-matching placebo tablets were orally administered twice daily (bid).

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

Sorafenib (Nexavar, BAY43-9006)

Sorafenib 400 mg was administered orally at a dose of 400 mg (2 x 200 mg tablets) twice daily (bid); 2 dose reductions to predefined levels of 400 mg once daily (OD) and 400 mg every other day were permitted for adverse events related to study treatment.

Intervention Type DRUG

Placebo

Sorafenib-matching placebo tablets were orally administered twice daily (bid).

Intervention Type DRUG

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

* Ages eligible for study: 18 years and above, Genders eligible for study: both
* Patients who have a life expectancy of at least 12 weeks
* Patients with histologically or cytologically documented Hepatocellular Carcinoma (HCC)
* Patients must have at least one tumor lesion that meets both of the following criteria: (1) Accurately measured in at least one dimension according to RECIST (Response Evaluation Criteria in Solid Tumors) (2) Not previously treated with local therapy
* Patients who have an ECOG (Eastern Cooperative Oncology Group) PS (Performance Status) of 0, 1, or 2

Exclusion Criteria

* Previous or concurrent cancer that is distinct in primary site or histology from HCC, EXCEPT cervical carcinoma in situ, treated basal cell carcinoma, superficial bladder tumors (Ta \[Noninvasive papillary carcinoma\], Tis \[Carcinoma in situ: "flat tumor"\] \& T1 \[Tumor invades subepithelial connective tissue\]). Any cancer curatively treated \> 3 years prior to entry is permitted
* Renal failure requiring hemo- or peritoneal dialysis
* History of cardiac disease
* Active clinically serious infections
* Known history of human immunodeficiency virus (HIV) infection
* Known central nervous system tumors including metastatic brain disease
* Patients with clinically significant gastrointestinal bleeding within 30 days prior to study entry
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

Bayer

INDUSTRY

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Responsibility Role SPONSOR

Principal Investigators

Learn about the lead researchers overseeing the trial and their institutional affiliations.

Bayer Study Director

Role: STUDY_DIRECTOR

Bayer

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

Phoenix, Arizona, United States

Site Status

Tucson, Arizona, United States

Site Status

Los Angeles, California, United States

Site Status

Los Angeles, California, United States

Site Status

Orange, California, United States

Site Status

San Francisco, California, United States

Site Status

Stanford, California, United States

Site Status

Farmington, Connecticut, United States

Site Status

New Haven, Connecticut, United States

Site Status

Gainesville, Florida, United States

Site Status

Miami, Florida, United States

Site Status

Tampa, Florida, United States

Site Status

Atlanta, Georgia, United States

Site Status

Atlanta, Georgia, United States

Site Status

Chicago, Illinois, United States

Site Status

Chicago, Illinois, United States

Site Status

Lexington, Kentucky, United States

Site Status

Ann Arbor, Michigan, United States

Site Status

Detroit, Michigan, United States

Site Status

St Louis, Missouri, United States

Site Status

Omaha, Nebraska, United States

Site Status

Manhasset, New York, United States

Site Status

New York, New York, United States

Site Status

New York, New York, United States

Site Status

New York, New York, United States

Site Status

New York, New York, United States

Site Status

Canton, Ohio, United States

Site Status

Portland, Oregon, United States

Site Status

Philadelphia, Pennsylvania, United States

Site Status

Philadelphia, Pennsylvania, United States

Site Status

Pittsburgh, Pennsylvania, United States

Site Status

Houston, Texas, United States

Site Status

Richmond, Virginia, United States

Site Status

Seattle, Washington, United States

Site Status

Seattle, Washington, United States

Site Status

Mar del Plata, Buenos Aires, Argentina

Site Status

Pilar, Buenos Aires, Argentina

Site Status

Bueno Aires, Ciudad Auton. de Buenos Aires, Argentina

Site Status

Buenos Aires, Ciudad Auton. de Buenos Aires, Argentina

Site Status

Buenos Aires, Ciudad Auton. de Buenos Aires, Argentina

Site Status

Buenos Aires, Ciudad Auton. de Buenos Aires, Argentina

Site Status

San Miguel de Tucumán, Tucumán Province, Argentina

Site Status

San Miguel de Tucumán, Tucumán Province, Argentina

Site Status

Camperdown, New South Wales, Australia

Site Status

Randwick, New South Wales, Australia

Site Status

Westmead, New South Wales, Australia

Site Status

East Bentleigh, Victoria, Australia

Site Status

Heidelberg, Victoria, Australia

Site Status

Melbourne, Victoria, Australia

Site Status

Bruges, , Belgium

Site Status

Bruxelles - Brussel, , Belgium

Site Status

Bruxelles - Brussel, , Belgium

Site Status

Bruxelles - Brussel, , Belgium

Site Status

Ghent, , Belgium

Site Status

Leuven, , Belgium

Site Status

Porto Alegre, Rio Grande do Sul, Brazil

Site Status

Porto Alegre, Rio Grande do Sul, Brazil

Site Status

São Paulo, São Paulo, Brazil

Site Status

Belo Horizonte, , Brazil

Site Status

Belo Horizonte, , Brazil

Site Status

Sofia, , Bulgaria

Site Status

Sofia, , Bulgaria

Site Status

Sofia, , Bulgaria

Site Status

Stara Zagora, , Bulgaria

Site Status

Varna, , Bulgaria

Site Status

Calgary, Alberta, Canada

Site Status

Edmonton, Alberta, Canada

Site Status

Vancouver, British Columbia, Canada

Site Status

Winnipeg, Manitoba, Canada

Site Status

London, Ontario, Canada

Site Status

Ottawa, Ontario, Canada

Site Status

Toronto, Ontario, Canada

Site Status

Montreal, Quebec, Canada

Site Status

Santiago, Santiago Metropolitan, Chile

Site Status

Santiago, , Chile

Site Status

Santiago Región Metropolitana, , Chile

Site Status

Zagreb, , Croatia

Site Status

Bondy, , France

Site Status

Bordeaux, , France

Site Status

Clichy, , France

Site Status

Dijon, , France

Site Status

Lille, , France

Site Status

Marseille, , France

Site Status

Nantes, , France

Site Status

Paris, , France

Site Status

Rennes, , France

Site Status

Vandœuvre-lès-Nancy, , France

Site Status

Freiburg im Breisgau, Baden-Wurttemberg, Germany

Site Status

Tübingen, Baden-Wurttemberg, Germany

Site Status

München, Bavaria, Germany

Site Status

München, Bavaria, Germany

Site Status

Regensburg, Bavaria, Germany

Site Status

Hamburg, City state of Hamburg, Germany

Site Status

Frankfurt am Main, Hesse, Germany

Site Status

Hanover, Lower Saxony, Germany

Site Status

Bonn, North Rhine-Westphalia, Germany

Site Status

Düsseldorf, North Rhine-Westphalia, Germany

Site Status

Essen, North Rhine-Westphalia, Germany

Site Status

Mainz, Rhineland-Palatinate, Germany

Site Status

Homburg, Saarland, Germany

Site Status

Halle, Saxony-Anhalt, Germany

Site Status

Magdeburg, Saxony-Anhalt, Germany

Site Status

Berlin, State of Berlin, Germany

Site Status

Haidari, Attica, Greece

Site Status

Thessaloniki, Thessaloniki, Greece

Site Status

Thessaloniki, Thessaloniki, Greece

Site Status

Athens, , Greece

Site Status

Ioannina, , Greece

Site Status

Thessaloniki, , Greece

Site Status

Petah Tikva, Israel, Israel

Site Status

Tel Aviv, Israel, Israel

Site Status

Zrifin, Israel, Israel

Site Status

Haifa, , Israel

Site Status

Forlì, Forlì, Italy

Site Status

Rozzano, Milano, Italy

Site Status

Avellino, , Italy

Site Status

Bologna, , Italy

Site Status

Milan, , Italy

Site Status

Milan, , Italy

Site Status

Padua, , Italy

Site Status

Palermo, , Italy

Site Status

Pavia, , Italy

Site Status

Pisa, , Italy

Site Status

Roma, , Italy

Site Status

Mexico City, Mexico City, Mexico

Site Status

México, D.F., , Mexico

Site Status

México, D.F., , Mexico

Site Status

Monterrey, , Mexico

Site Status

Auckland, , New Zealand

Site Status

Wellington South, , New Zealand

Site Status

Comas Lima, , Peru

Site Status

Lima, , Peru

Site Status

Lima Cercado, , Peru

Site Status

Gdansk, , Poland

Site Status

Poznan, , Poland

Site Status

Warsaw, , Poland

Site Status

Warsaw, , Poland

Site Status

Iași, Iaşi, Romania

Site Status

Timișoara, Timiș County, Romania

Site Status

Craiova Dolj, , Romania

Site Status

Kazan', , Russia

Site Status

Kirov, , Russia

Site Status

Krasnodar, , Russia

Site Status

Moscow, , Russia

Site Status

Moscow, , Russia

Site Status

Moscow, , Russia

Site Status

Moscow, , Russia

Site Status

Moscow, , Russia

Site Status

Moscow, , Russia

Site Status

Moscow, , Russia

Site Status

Saint Petersburg, , Russia

Site Status

Saint Petersburg, , Russia

Site Status

Saint Petersburg, , Russia

Site Status

Tolgliatti, , Russia

Site Status

Yekaterinburg, , Russia

Site Status

Yekaterinburg, , Russia

Site Status

Alicante, Alicante, Spain

Site Status

Badalona, Barcelona, Spain

Site Status

Barcelona, Barcelona, Spain

Site Status

Barcelona, Barcelona, Spain

Site Status

Barcelona, Barcelona, Spain

Site Status

Cruces/Barakaldo, Bilbao, Spain

Site Status

Córdoba, Córdoba, Spain

Site Status

Madrid, Madrid, Spain

Site Status

Madrid, Madrid, Spain

Site Status

Madrid, Madrid, Spain

Site Status

Pamplona, Pamplona, Spain

Site Status

Valencia, Valencia, Spain

Site Status

Bern, Canton of Bern, Switzerland

Site Status

Geneva, Canton of Geneva, Switzerland

Site Status

Sankt Gallen, Canton of St. Gallen, Switzerland

Site Status

Zurich, Canton of Zurich, Switzerland

Site Status

Bristol, Avon, United Kingdom

Site Status

London, London, United Kingdom

Site Status

London, London, United Kingdom

Site Status

Oxford, Oxfordshire, United Kingdom

Site Status

Glasgow, Stratchclyde, United Kingdom

Site Status

Newcastle upon Tyne, , United Kingdom

Site Status

Countries

Review the countries where the study has at least one active or historical site.

United States Argentina Australia Belgium Brazil Bulgaria Canada Chile Croatia France Germany Greece Israel Italy Mexico New Zealand Peru Poland Romania Russia Spain Switzerland United Kingdom

References

Explore related publications, articles, or registry entries linked to this study.

Llovet JM, Ricci S, Mazzaferro V, Hilgard P, Gane E, Blanc JF, de Oliveira AC, Santoro A, Raoul JL, Forner A, Schwartz M, Porta C, Zeuzem S, Bolondi L, Greten TF, Galle PR, Seitz JF, Borbath I, Haussinger D, Giannaris T, Shan M, Moscovici M, Voliotis D, Bruix J; SHARP Investigators Study Group. Sorafenib in advanced hepatocellular carcinoma. N Engl J Med. 2008 Jul 24;359(4):378-90. doi: 10.1056/NEJMoa0708857.

Reference Type RESULT
PMID: 18650514 (View on PubMed)

Wu W, Mao H, Song J, Yang F. Bibliometric analysis of hepatocellular carcinoma and tyrosine kinase inhibitors. Medicine (Baltimore). 2025 May 16;104(20):e42015. doi: 10.1097/MD.0000000000042015.

Reference Type DERIVED
PMID: 40388796 (View on PubMed)

Bruix J, Cheng AL, Meinhardt G, Nakajima K, De Sanctis Y, Llovet J. Prognostic factors and predictors of sorafenib benefit in patients with hepatocellular carcinoma: Analysis of two phase III studies. J Hepatol. 2017 Nov;67(5):999-1008. doi: 10.1016/j.jhep.2017.06.026. Epub 2017 Jul 4.

Reference Type DERIVED
PMID: 28687477 (View on PubMed)

Related Links

Access external resources that provide additional context or updates about the study.

http://www.clinicaltrialsregister.eu/

Click here to find information about studies related to Bayer Healthcare products conducted in Europe

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

2004-001773-26

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

100554

Identifier Type: -

Identifier Source: org_study_id

More Related Trials

Additional clinical trials that may be relevant based on similarity analysis.