Natural Berry Extract Treatment of Hemangiomas

NCT ID: NCT04020419

Last Updated: 2023-10-23

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

EARLY_PHASE1

Total Enrollment

12 participants

Study Classification

INTERVENTIONAL

Study Start Date

2020-12-01

Study Completion Date

2023-05-24

Brief Summary

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This is a prospective, randomized, double-blind, placebo-controlled parallel group study evaluating the use of PediaBerry for the treatment of hemangiomas in infants ≤ 4 months of corrected gestation age over a 6-month treatment period. Subjects will be followed to age 18 months. A total of 44 subjects will be PediaBerry group and 22 subjects in the placebo control group.

Detailed Description

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PediaBerry™ is a proprietary blend of powdered berry extracts. Placebo: powdered sugar plus McCormick Color from Nature Food Colors Berry and Sky Blue powdered food color (https://www.mccormick.com/spices-and-flavors/extracts-and-food-colors/food-colors/color-from-nature-assorted-food-color ).

Cream vehicle is mixed with PediaBerry™ or placebo at the time of application.Children will receive once daily topical and oral gavage dosing of PediaBerry or placebo.

The first study visit will take place within 2 weeks of subject recruitment. The subject enrollment, consenting and randomization will occur as study visit #0 and will occur at Riley Children's Hospital or Nationwide Children's Hospital. Data collection will be the same at all study visits starting with study visit #1 until the completion of the study. The first dose of PediaBerry™ or placebo will be administered prior to completion of study visit #1, and will also be given at study visits #2-6. Study visits #2-6 will occur monthly study visits until the subject completes 6 months of treatment.Subjects will be weighed and treatment doses adjusted accordingly. Study visits #7-11 to watch for signs of rebound hemangioma proliferation will occur every other month until age 12 months and then at age 15 and 18 months. Urine samples, photos and caliper measurements will occur at each study visit. Some subjects may have less than 11 study visits depending on the age at the time of subject enrollment.

Conditions

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Hemangioma

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

pilot study to determine effect size for possible FDA phase I/II trial
Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors
investigational pharmacy will have access to randomization schemes and will package study drug from bulk supplies. All other study team members and participants are blinded.

Study Groups

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Pediaberry group

PediaBerry™ is a proprietary blend powdered berry extracts

Group Type EXPERIMENTAL

PediaBerry

Intervention Type DRUG

PediaBerry or placebo will be mixed with a cream vehicle for topical administration or with water for oral administration

Placebo

Placebo: powdered sugar plus McCormick Color from Nature Food Colors Berry and Sky Blue powdered food color (https://www.mccormick.com/spices-and-flavors/extracts-and-food-colors/food-colors/color-from-nature-assorted-food-color ).

Group Type PLACEBO_COMPARATOR

PediaBerry

Intervention Type DRUG

PediaBerry or placebo will be mixed with a cream vehicle for topical administration or with water for oral administration

Interventions

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PediaBerry

PediaBerry or placebo will be mixed with a cream vehicle for topical administration or with water for oral administration

Intervention Type DRUG

Other Intervention Names

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placebo

Eligibility Criteria

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Inclusion Criteria

* Children with hemangiomas ≤ 4 months and 2 weeks of corrected gestational age
* Hemangioma size ≥ 1 cm diameter

Exclusion Criteria

* Children with hemangiomas that threaten the life of the child or development of vital structures.
* Children who are breast feeding and mother is taking beta blocker medication
* Children with previously treated hemangiomas
* Congenital hemangiomas - cannot distinguish between rapidly involuting and non-involuting congenital hemangiomas
* Hemangiomas located in the perineal/diapering area - product will get contaminated or wiped off with diapering
* Children with food allergies to blueberries or any other kind of berry
* Legal guardian unable to provide informed consent
Minimum Eligible Age

1 Month

Maximum Eligible Age

19 Weeks

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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National Institute of General Medical Sciences (NIGMS)

NIH

Sponsor Role collaborator

National Institutes of Health (NIH)

NIH

Sponsor Role collaborator

Gayle Gordillo

OTHER

Sponsor Role lead

Responsible Party

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Gayle Gordillo

Professor

Responsibility Role SPONSOR_INVESTIGATOR

Principal Investigators

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Gayle Gordillo, MD

Role: PRINCIPAL_INVESTIGATOR

Indiana University

Locations

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Riley Hospital for Children

Indianapolis, Indiana, United States

Site Status

Nationwide Children's Hospital

Columbus, Ohio, United States

Site Status

Countries

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United States

References

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Provided Documents

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Document Type: Informed Consent Form

View Document

Other Identifiers

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2R01GM095657

Identifier Type: NIH

Identifier Source: secondary_id

View Link

1810087420

Identifier Type: -

Identifier Source: org_study_id

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