A Study of GC1111 in Hunter Syndrom Patients

NCT ID: NCT03920540

Last Updated: 2024-04-16

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

32 participants

Study Classification

INTERVENTIONAL

Study Start Date

2017-03-09

Study Completion Date

2022-02-15

Brief Summary

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The objective of this study is to evaluate the efficacy of GC1111 in Hunter Syndrome Patients

Detailed Description

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Conditions

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Hunter Syndrome

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

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GC1111

In part 1, all participants who randomized into GC1111 arm should receive the GC1111 for 52 weeks.

In part 2, all enrolled participants should receive the GC1111 for 52 weeks.

Group Type EXPERIMENTAL

GC1111

Intervention Type COMBINATION_PRODUCT

GC1111 is 0.5mg per kg of body weight once weekly to be administered slowly by intravenous infusion.

Comparator (Part 1)

In Part 1, all participants who randomized into comparator arm should receive the GC1111 for 52 weeks.

Group Type ACTIVE_COMPARATOR

Comparator

Intervention Type COMBINATION_PRODUCT

Comparator is 0.5mg per kg of body weight once weekly to be administered slowly by intravenous infusion.

Interventions

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GC1111

GC1111 is 0.5mg per kg of body weight once weekly to be administered slowly by intravenous infusion.

Intervention Type COMBINATION_PRODUCT

Comparator

Comparator is 0.5mg per kg of body weight once weekly to be administered slowly by intravenous infusion.

Intervention Type COMBINATION_PRODUCT

Eligibility Criteria

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Inclusion Criteria

* Patients diagnosed with Hunter syndrome
* Male at the age of ≥ 5
* Adequate abilities (including 6-MWT) to participate in this study in the opinion of the investigator.
* Voluntarily signed written informed consent to participation in this study
* Consent to contraception

Exclusion Criteria

* Prior treatment with iduronate-2-sulfatase ERT
* History of bronchotomy, bone marrow trasplanation, or cord blood transplanation.
* Known hypersensitivity reactions to any of the components of the invetigational product
* Prior or planned administration of other investigational products within 30 days before treatment with the investigational product in this study or duirng this study.
* Unable to perform 6-MWT.
* Female
Minimum Eligible Age

5 Years

Eligible Sex

MALE

Accepts Healthy Volunteers

No

Sponsors

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Green Cross Corporation

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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DongKyu Jin, M.D., Ph.D.

Role: PRINCIPAL_INVESTIGATOR

Samsung Medical Center

Locations

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Samsug Medical Center

Seoul, , South Korea

Site Status

Countries

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South Korea

Other Identifiers

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GC1111_P3

Identifier Type: -

Identifier Source: org_study_id

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